NCT05536297

Brief Summary

The purpose of this study is to assess long-term safety of avacincaptad pegol intravitreal administration for patients with geographic atrophy (GA) who completed Study ISEE2008 (GATHER2) through the Month 23 visit on study treatment (either avacincaptad pegol or Sham).

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
278

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Sep 2022

Typical duration for phase_3

Geographic Reach
16 countries

115 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 7, 2022

Completed
3 days until next milestone

First Posted

Study publicly available on registry

September 10, 2022

Completed
16 days until next milestone

Study Start

First participant enrolled

September 26, 2022

Completed
2.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 10, 2025

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 10, 2025

Completed
1 year until next milestone

Results Posted

Study results publicly available

April 14, 2026

Completed
Last Updated

May 1, 2026

Status Verified

April 1, 2026

Enrollment Period

2.5 years

First QC Date

September 7, 2022

Results QC Date

March 26, 2026

Last Update Submit

April 29, 2026

Conditions

Keywords

Geographic Atrophy;Macular Degeneration;ARC1905;Avacincaptad pegol;Zimura (previous name);Izervay

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With Adverse Events (AEs)

    An AE is defined as any untoward medical occurrence in a participant including unfavorable and unintended signs, symptoms or disease temporally associated with the use of a medicinal product and which does not necessarily have to have a causal relationship to this treatment. AEs include illnesses with onset during the trial, or exacerbations of pre-existing illnesses. Exacerbation of pre-existing illness is defined as a significant increase in the severity of the illness as compared to the start of the trial and was considered when a participant requires new or additional treatment for that illness. Lack of or insufficient clinical response or efficacy was not recorded as an AE.

    Up to 18 months

Secondary Outcomes (2)

  • Number of Participants With Anti-drug Antibody (ADA)

    Up to 18 months

  • Plasma Concentrations of ACP

    Months 1, 2, 4, 7, 13, and 18

Study Arms (1)

avacincaptad pegol

EXPERIMENTAL

Participants will receive avacincaptad pegol 2 mg monthly from Month 1 to Month 17.

Drug: avacincaptad pegol

Interventions

Intravitreal Injection

Also known as: Zimura (previous name), ARC1905, Izervay
avacincaptad pegol

Eligibility Criteria

Age50 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female patients aged 50 years or greater diagnosed with GA inside and/or outside of the fovea who completed Study ISEE2008 (GATHER2) through the Month 24 visit on study treatment.
  • Patient must provide new written informed consent for this OLE trial prior to participation.
  • Patient must have the ability to return for all trial visits for the duration of the 18-month trial.

You may not qualify if:

  • Patient did not complete Study ISEE2008 (GATHER2) through the Month 24 visit on study treatment (either avacincaptad pegol or Sham).
  • Patient who had the study drug permanently withdrawn for an AE during ISEE2008 are not eligible.
  • Patient did not enroll into this OLE trial within the 90 day enrollment period.
  • Patient who is pregnant or nursing.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (117)

Retinal Diagnostic Center

Campbell, California, 95008, United States

Location

Eye Medical Center of Fresno

Fresno, California, 93720, United States

Location

Retina Consultants of Orange County

Fullerton, California, 92835, United States

Location

Jacobs Retina Center at The Shiley Eye Institute USCD

La Jolla, California, 92093, United States

Location

Jules Stein Eye Institute David Geffen School of Medicine

Los Angeles, California, 90095, United States

Location

Doheny Eye Center, UCLA

Pasadena, California, 91105, United States

Location

Retina Consultants of Southern California

Redlands, California, 92374, United States

Location

Orange County Retinal Med Group

Santa Ana, California, 92705, United States

Location

University of Colorado

Aurora, Colorado, 80045, United States

Location

Retina Consultants of Southern CO

Colorado Springs, Colorado, 80909, United States

Location

Colorado Retina Associates, PC

Lakewood, Colorado, 80228, United States

Location

Rand Eye Institute

Deerfield Beach, Florida, 33064, United States

Location

Retina Group of Florida

Fort Lauderdale, Florida, 33308, United States

Location

Florida Eye Associates

Melbourne, Florida, 32901, United States

Location

Retina Care Specialists

Palm Beach Gardens, Florida, 33410, United States

Location

Retina Associates of Sarasota

Sarasota, Florida, 34233, United States

Location

Retina Vitreous Associates of Florida

St. Petersburg, Florida, 33711, United States

Location

East Florida Eye Institute

Stuart, Florida, 34994, United States

Location

Southern Vitreoretinal Associates

Tallahassee, Florida, 32308, United States

Location

Center for Retina & Macula Disease

Winter Haven, Florida, 33880, United States

Location

Southeast Retina Center P.C.

Augusta, Georgia, 30909, United States

Location

Retina Consultants of Hawaii, Inc.

‘Aiea, Hawaii, 96701, United States

Location

Illinois Eye Center

Peoria, Illinois, 61615, United States

Location

Vitreo Retinal Consultants & Surgeons

Wichita, Kansas, 67214, United States

Location

Ochsner Clinic Foundation

New Orleans, Louisiana, 70124, United States

Location

The Retina Group of Washington

Chevy Chase, Maryland, 20815, United States

Location

Cumberland Valley Retina Consultants

Hagerstown, Maryland, 21740, United States

Location

Ophthalmic Consultants of Boston

Boston, Massachusetts, 02114, United States

Location

Retina Research Institute at New England Retina

Springfield, Massachusetts, 01107, United States

Location

Vitreoretinal Associates PC

Worcester, Massachusetts, 01605, United States

Location

Sierra Eye Associates

Reno, Nevada, 89502, United States

Location

Retina Vitreous Surgeons of Central New York

Liverpool, New York, 13088, United States

Location

Ophthalmic Consultants of Long Island

Oceanside, New York, 11572, United States

Location

Retina Associates of Western NY

Rochester, New York, 14620, United States

Location

Western Carolina Retinal Associates

Asheville, North Carolina, 28803, United States

Location

Retina & Vitreous Center of Southern Oregon, PC

Ashland, Oregon, 97520, United States

Location

Retina Northwest PC

Portland, Oregon, 97221, United States

Location

Eye Health Northwest

Portland, Oregon, 97225, United States

Location

Mid Atlantic Retina - Wills Eye Institute

Philadelphia, Pennsylvania, 19107, United States

Location

Associates in Ophthalmology

West Mifflin, Pennsylvania, 15122, United States

Location

Retina Research of Beaufort

Beaufort, South Carolina, 29902, United States

Location

Palmetto Retina Center

West Columbia, South Carolina, 29169, United States

Location

Black Hills Regional Eye Institute

Rapid City, South Dakota, 57701, United States

Location

Southeastern Retina Associates, PC

Knoxville, Tennessee, 37922, United States

Location

Retina Research Institute of Texas, LLC

Abilene, Texas, 79606, United States

Location

Southwest Retina Specialists

Amarillo, Texas, 79106, United States

Location

Austin Retina Associates

Austin, Texas, 78705, United States

Location

Retina Foundation of the Southwest

Dallas, Texas, 75231, United States

Location

Retina Center of Texas

Southlake, Texas, 76092, United States

Location

Retina Consultants of Houston

The Woodlands, Texas, 77384, United States

Location

Strategic Clinical Research Group, LLC

Willow Park, Texas, 76087, United States

Location

Retina Associates of Utah PC

Salt Lake City, Utah, 84107, United States

Location

Pacific Northwest Retina

Bellevue, Washington, 98004, United States

Location

Oftalmólogos Especialistas

Rosario, Sante Fe, S2000ANJ, Argentina

Location

Centro Oftalmológico Dr. Charles

Buenos Aires, 1116, Argentina

Location

Instituto Oftalmologico de Buenos Aires

Buenos Aires, 1830, Argentina

Location

Oftar Mendoza

Mendoza, 5500, Argentina

Location

Microcirugia Ocular

Santa Fe, Argentina

Location

Centre for Eye Research Australia

East Melbourne, 3002, Australia

Location

Sydney Retina Clinic

Sydney, 2000, Australia

Location

Medizinische Universitat Graz

Styria, 8036, Austria

Location

Medizinische Universitat Innsbruck

Tyrol, 6020, Austria

Location

Medical University of Vienna, Department of Ophthalmology and Optometry

Vienna, 1090, Austria

Location

Centre H. U. Brugmann

Brussels, 1020, Belgium

Location

Centro de Ensino e Pesquisa do Instituto de Visao

Belo Horizonte, 30330-00, Brazil

Location

Universidade Federal de Sao Paulo

São Paulo, 04023-062, Brazil

Location

IPEPO - Instituto da Visao

São Paulo, 04038-032, Brazil

Location

Calgary Retina Consultants

Calgary, Alberta, T2H 0C8, Canada

Location

St. Joseph's Health Care London

London, Ontario, N6A4V2, Canada

Location

Retina Centre of Ottawa

Ottawa, Ontario, K2B 7E9, Canada

Location

Fundacion Oftalmologica Nacional

Bogotá, 110231, Colombia

Location

Clinica de Oftalmologia Sandiego

Medellín, 00000, Colombia

Location

Clinical Hospital Osiiek, Ophthalmology Clinic

Osijek, 31000, Croatia

Location

Lékárna nad Knížecí Kováků

Smíchov, 150 00, Czechia

Location

University Hospital of Bordeaux

Bordeaux, 33000, France

Location

Hopital Intercommunal de Creteil

Créteil, 94010, France

Location

Pole Vision Val D'Ouest

Écully, 69130, France

Location

Centre Ophtalmologique Rabelais

Lyon, 69002, France

Location

Hopital de la Croix-Rousse

Lyon, 69317, France

Location

Centre Paradis-Monticelli

Marseille, 13008, France

Location

Centre D'exploration Ophtalmologique De L'odéon

Paris, 75006, France

Location

Centre d'Imagerie et Laser

Paris, 75015, France

Location

Rothschild Foundation

Paris, 75019, France

Location

Hopital Lariboisiere, Service Pharmacie

Paris, 75745, France

Location

Centre Ophtalmologique Saint Exupéry

Saint-Cyr-sur-Loire, 37540, France

Location

Universitätsklinikum Hamburg Eppendorf

Hamburg, 20251, Germany

Location

Universitätsklinik für Augenheilkunde, Medizinische Hochschule Hannover

Hanover, 30625, Germany

Location

Augenklinik der Ludwig-Maximilian Universität München

München, 80336, Germany

Location

Eye Clinic Ludwig Maximilian

München, 80336, Germany

Location

Augenzentrum am St. Franziskus-Hospital

Münster, 48145, Germany

Location

Dept. of Ophthalmology Semmelweis University Budapest

Budapest, 1085, Hungary

Location

Bajcsy Zsilinszky Korhaz Szemeszet

Budapest, 1106, Hungary

Location

Budapest Retina Associates

Budapest, 1133, Hungary

Location

Barzilai Medical Center

Ashkelon, 7830604, Israel

Location

Carmel Medical Center

Haifa, 3436212, Israel

Location

Kaplan Medical Center

Rehovot, 94410606, Israel

Location

Shamir Medical Center

Tzrifin, 70300, Israel

Location

AOU Policlinico S. Orsola-Malpighi

Bologna, 40138, Italy

Location

Clinica Oftalmologica Ospedale C. S.S. Annunziata

Chieti, 66100, Italy

Location

Ospedaliero Universitaria di Ferrara

Ferrara, 44124, Italy

Location

Ospedale Maggiore Policlinico

Milan, 20122, Italy

Location

Ospedale San Raffaele

Milan, 20132, Italy

Location

Azienda Ospedaliera Fatebenefratelli

Milan, 20157, Italy

Location

Azienda Ospedaliera U. della Campania "Vanvitelli"

Naples, 80131, Italy

Location

Policlinico Tor Vergata

Roma, 00133, Italy

Location

Azienda Ospedaliero-U.Ospedali Riuniti Umberto I

Torrette Di Ancona, 60126, Italy

Location

P. Stradins Clinical university hospital

Riga, LV-1002, Latvia

Location

Hospital Universitario Puerta de Hierro-Majadahonda

Majadahonda, Madrid, 28222, Spain

Location

Clinicade Oftalmologia Barraquer

Barcelona, 08021, Spain

Location

Institut Catala de la Retina

Barcelona, 08022, Spain

Location

Instituto Clinico Quirurgico de Oftalmologia

Bilbao, 48010, Spain

Location

Hospital La Arruzafa

Córdoba, 14003, Spain

Location

Valles Ophthalmology Research (VOR) in Hospital General de Catalunya Pedro

Sant Cugat del Vallès, 08195, Spain

Location

Instituto Oftalmológico Gómez-Ulla

Santiago de Compostela, 15706, Spain

Location

IMED Servicio Oftalmología

Valencia, 46100, Spain

Location

Rio Hortega University Hospital

Valladolid, 47012, Spain

Location

Hospital Clínico Universitario "Lozano Blesa"

Zaragoza, 50009, Spain

Location

Related Links

MeSH Terms

Conditions

Geographic AtrophyMacular Degeneration

Condition Hierarchy (Ancestors)

Retinal DegenerationRetinal DiseasesEye Diseases

Results Point of Contact

Title
Clinical Transparency
Organization
Astellas Pharma Global Development, Inc

Study Officials

  • Medical Director

    Astellas Pharma Global Development, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 7, 2022

First Posted

September 10, 2022

Study Start

September 26, 2022

Primary Completion

April 10, 2025

Study Completion

April 10, 2025

Last Updated

May 1, 2026

Results First Posted

April 14, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will share

Access to anonymized individual participant level data collected during the study, in addition to study-related supporting documentation, is planned for studies conducted with approved product indications and formulations, as well as products terminated during development. Studies conducted with product indications or formulations that remain active in development are assessed after study completion to determine if Individual Participant Data can be shared. Further details on Astellas' data sharing policy can be found at https://www.clinicaltrials.astellas.com/transparency/.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
Access to participant level data is offered to researchers after publication of the primary manuscript (if applicable) and is available as long as Astellas has legal authority to provide the data.
Access Criteria
Researchers must submit a proposal to conduct a scientifically relevant analysis of the study data. The research proposal is reviewed by an Independent Research Panel. If the proposal is approved, access to the study data is provided in a secure data sharing environment after receipt of a signed Data Sharing Agreement.
More information

Locations