NCT05949593

Brief Summary

This Phase 3, multicenter, double-masked, parallel-group, placebo-controlled, randomized, fixed-dose clinical study is designed to evaluate the efficacy and safety of tinlarebant (LBS-008) in subjects diagnosed with GA.

Trial Health

82
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
429

participants targeted

Target at P50-P75 for phase_3

Timeline
16mo left

Started Jul 2023

Typical duration for phase_3

Geographic Reach
8 countries

49 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress68%
Jul 2023Aug 2027

First Submitted

Initial submission to the registry

July 10, 2023

Completed
8 days until next milestone

First Posted

Study publicly available on registry

July 18, 2023

Completed
9 days until next milestone

Study Start

First participant enrolled

July 27, 2023

Completed
3.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 30, 2027

Expected
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

August 31, 2027

Last Updated

January 7, 2026

Status Verified

January 1, 2026

Enrollment Period

3.9 years

First QC Date

July 10, 2023

Last Update Submit

January 5, 2026

Conditions

Keywords

LBS-008TinlarebantGA

Outcome Measures

Primary Outcomes (1)

  • To measure the rate of change (growth rate slope) in geographic atrophy (GA) lesion size

    From baseline to Month 24]

Secondary Outcomes (2)

  • To measure the change in best-corrected visual acuity (BCVA) as assessed using the Early Treatment Diabetic Retinopathy Study (ETDRS) scale

    From baseline to Month 24

  • To measure changes in the area and size of the inner/outer segment junction of photoreceptors by spectral domain optical coherence tomography (SD-OCT)

    From baseline to Month 24

Study Arms (2)

LBS-008, Tinlarebant

EXPERIMENTAL
Drug: Tinlarebant

Placebo

PLACEBO COMPARATOR
Drug: Placebo

Interventions

5 mg tablet taken orally once a day

LBS-008, Tinlarebant

Placebo tablets for tinlarebant 5 mg prepared similarly.

Placebo

Eligibility Criteria

Age60 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Subjects must have a confirmed diagnosis of GA with atrophic lesions in 1 or both eyes.
  • Minimum BCVA is required in the study eye

You may not qualify if:

  • The presence of diabetic macular edema or macular disease in either eye.
  • Diabetic retinopathy more advanced than mild nonproliferative diabetic retinopathy, or any other retinal vascular disease in either eye.
  • Uncontrolled diagnosed glaucoma in the study eye

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (49)

Belite Study Site

Phoenix, Arizona, 85020, United States

Location

Belite Study Site

Arcadia, California, 91007, United States

Location

Belite Study Site

Beverly Hills, California, 90211, United States

Location

Belite Study Site

Huntington Beach, California, 92467, United States

Location

Belite Study Site

Los Angeles, California, 90033, United States

Location

Belite Study Site

Palo Alto, California, 94303, United States

Location

Belite Study Site

San Diego, California, 92093, United States

Location

Belite Study Site

Lakeland, Florida, 33805, United States

Location

Belite Study Site

Hagerstown, Maryland, 21740, United States

Location

Belite Study Site

Saint Louis Park, Minnesota, 55416, United States

Location

Belite Study Site

Westbury, New York, 11590, United States

Location

Belite Study Site

Cary, North Carolina, 27511, United States

Location

Belite Study Site

Durham, North Carolina, 27710, United States

Location

Belite Study Site

Wake Forest, North Carolina, 27587, United States

Location

Belite Study Site

Portland, Oregon, 97239, United States

Location

Belite Study Site

Philadelphia, Pennsylvania, 19107, United States

Location

Belite Study Site

Sewickley, Pennsylvania, 15143, United States

Location

Belite Study Site

Germantown, Tennessee, 38138, United States

Location

Belite Study Site

Abilene, Texas, 79606, United States

Location

Belite Study Site

Dallas, Texas, 75231, United States

Location

Belite Study Site

San Antonio, Texas, 78240, United States

Location

Belite Study Site

Warrenton, Virginia, 20186, United States

Location

Belite Study Site

Chatswood, New South Wales, 2067, Australia

Location

Belite Study Site

Strathfield, New South Wales, 2135, Australia

Location

Belite Study Site

Brisbane, Queensland, 4101, Australia

Location

Belite Study Site

Adelaide, South Australia, 5000, Australia

Location

Belite Study Site

East Melbourne, Victoria, 3002, Australia

Location

Belite Study Site

Crawley, Western Australia, 6009, Australia

Location

Belite Study Site

Beijing, Beijing Municipality, 100044, China

Location

Belite Study Site

Chengdu, Sichuan, 610093, China

Location

Belite Study Site

Beijing, 10005, China

Location

Belite Study Site

Beijing, 100730, China

Location

Belite Study Site

Guandong, 510060, China

Location

Belite Study Site

Zhejiang, 325027, China

Location

Belite Study Site

Ostrava, 70852, Czechia

Location

Belite Study Site

Prague, 14000, Czechia

Location

Belite Study Site

Prague, 14059, Czechia

Location

Belite Study Site

Dijon, 21000, France

Location

Belite Study Site

Écully, 69130, France

Location

Belite Study Site

Lyon, 69317, France

Location

Belite Study Site

Marseille, 130008, France

Location

Belite Study Site

Basel, 4031, Switzerland

Location

Belite Study Site

Lausanne, 1001, Switzerland

Location

Belite Study Site

Taichung, 40447, Taiwan

Location

Belite Study Site

Taipei, 100, Taiwan

Location

Belite Study Site

Taoyuan District, 33305, Taiwan

Location

Belite Study Site

Great Yarmouth, NR31 6LA, United Kingdom

Location

Belite Study Site

Harrow, HA1 3UJ, United Kingdom

Location

Belite Study Site

London, EC1V 2PD, United Kingdom

Location

MeSH Terms

Conditions

Geographic Atrophy

Condition Hierarchy (Ancestors)

Macular DegenerationRetinal DegenerationRetinal DiseasesEye Diseases

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Masking Details
Eligible subjects will be randomly assigned to begin treatment in 2:1 ratio to receive the study drug (either Tinlarebant 5 mg or matching placebo)
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 10, 2023

First Posted

July 18, 2023

Study Start

July 27, 2023

Primary Completion (Estimated)

June 30, 2027

Study Completion (Estimated)

August 31, 2027

Last Updated

January 7, 2026

Record last verified: 2026-01

Data Sharing

IPD Sharing
Will not share

Locations