NCT05296447

Brief Summary

This is a prospective, observational study designed to evaluate the long-term safety and efficacy of RGX-314. Eligible participants are those who were previously enrolled in a clinical study of DR without center involved-diabetic macular edema (CI-DME) in which they received SCS administration of RGX-314. Enrollment of each participant in the current study should occur after the participant has completed either the end of study or early discontinuation visit in the previous (parent) clinical study. Participants will be followed for a total of 5 years post-RGX-314 administration (inclusive of the parent study). As such, the total study duration for each participant may vary depending on when they enroll in the current study following RGX-314 administration in the parent study.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
100

participants targeted

Target at P50-P75 for all trials

Timeline
23mo left

Started Apr 2022

Longer than P75 for all trials

Geographic Reach
1 country

19 active sites

Status
enrolling by invitation

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress69%
Apr 2022May 2028

First Submitted

Initial submission to the registry

March 16, 2022

Completed
9 days until next milestone

First Posted

Study publicly available on registry

March 25, 2022

Completed
10 days until next milestone

Study Start

First participant enrolled

April 4, 2022

Completed
6.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2028

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2028

Last Updated

June 18, 2025

Status Verified

June 1, 2025

Enrollment Period

6.1 years

First QC Date

March 16, 2022

Last Update Submit

June 16, 2025

Conditions

Keywords

Diabetic Retinopathy, DR

Outcome Measures

Primary Outcomes (1)

  • To evaluate the long-term safety of RGX-314

    Incidence of overall and ocular adverse events, serious adverse events, and all adverse events of special interest

    5 years inclusive of the parent study

Secondary Outcomes (8)

  • Mean change from baseline (ie, prior to RGX-314 administration in the parent study) in DR by ETDRS-DRSS on 4-widefield digital stereoscopic fundus photography

    5 years, inclusive of the parent study

  • Proportion of participants achieving 0-step (no change), a 1-step or greater, a 2-step or greater, or a 3-step or greater improvement in DR per ETDRS-DRSS on 4-widefield digital stereoscopic fundus photography from baseline

    5 years, inclusive to the parent study

  • Mean change from baseline (ie, prior to RGX-314 administration in the parent study) in BCVA

    5 years, inclusive to the parent study

  • Proportion of participants gaining or losing ≥5, 10 and 15 letters in BCVA compared with baseline (ie, prior to RGX-314 administration in the parent study)

    5 years, inclusive to the parent study

  • Mean change from baseline (ie, prior to RGX-314 administration in the parent study) in central subfield thickness as measured by SD-OCT

    5 years, inclusive to the parent study

  • +3 more secondary outcomes

Study Arms (1)

Roll Over

No intervention - all subjects that previously received RGX-314 in a parent study

Other: No Intervention

Interventions

All subjects that previously received RGX-314 in a parent study

Roll Over

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodProbability Sample
Study Population

Study population includes participants who received RGX-314 in a parent study of DR without center involved-diabetic macular edema

You may qualify if:

  • Must provide written, signed informed consent for this study
  • Must have been enrolled in a previous clinical study of RGX-314 for the treatment of DR without CI-DME and must have received an SCS injection of RGX-314 in that study
  • Must be willing and able to comply with all study procedures

You may not qualify if:

  • None

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (19)

Retinal Research Institute, LLC

Phoenix, Arizona, 85014, United States

Location

California Retina Consultants

Bakersfield, California, 93309, United States

Location

Retina-Vitreous Associates Medical Group

Beverly Hills, California, 90211, United States

Location

American Institute of Research

Los Angeles, California, 90017, United States

Location

Northern California Retina Vitreous Associates Medical Group Inc

Mountain View, California, 94040, United States

Location

California Eye Specialists Medical Group, Inc

Pasadena, California, 91107, United States

Location

Retina Consultants San Diego

Poway, California, 92064, United States

Location

California Retina Consultants CRC

Santa Barbara, California, 93103, United States

Location

University Retina and Macula Associates, PC

Oak Forest, Illinois, 60452, United States

Location

Cumberland Valley Retina Consultants

Hagerstown, Maryland, 21740, United States

Location

Ophthalmic Consultants of Boston

Boston, Massachusetts, 02114, United States

Location

Sierra eye Associates

Reno, Nevada, 89502, United States

Location

New Jersey Retina

Teaneck, New Jersey, 07666, United States

Location

Vision Research Center Eye Associates of New Mexico

Albuquerque, New Mexico, 87109, United States

Location

Duke University

Durham, North Carolina, 27705, United States

Location

Retinovitreous Associates, LTD

Philadelphia, Pennsylvania, 19107, United States

Location

Charles Retina Institute, P.C

Germantown, Tennessee, 38138, United States

Location

Austin Clinical Research

Austin, Texas, 78750, United States

Location

Retina Consultants of Texas

The Woodlands, Texas, 77384, United States

Location

MeSH Terms

Conditions

Diabetic Retinopathy

Condition Hierarchy (Ancestors)

Retinal DiseasesEye DiseasesDiabetic AngiopathiesVascular DiseasesCardiovascular DiseasesDiabetes ComplicationsDiabetes MellitusEndocrine System Diseases

Study Design

Study Type
observational
Observational Model
OTHER
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 16, 2022

First Posted

March 25, 2022

Study Start

April 4, 2022

Primary Completion (Estimated)

May 1, 2028

Study Completion (Estimated)

May 1, 2028

Last Updated

June 18, 2025

Record last verified: 2025-06

Data Sharing

IPD Sharing
Will not share

Locations