NCT05210803

Brief Summary

This is a prospective, observational study designed to evaluate the long-term safety and efficacy of RGX-314. Eligible participants are those who were previously enrolled in a clinical study of nAMD in which they received suprachoroidal space (SCS) administration of RGX-314. Enrollment of each participant in the current study should occur after the participant has completed either the end of study or early discontinuation visit in the previous (parent) clinical study. Participants will be followed for up to 5 years after RGX-314 administration (inclusive of the parent study). As such, the total study duration for each participant may vary depending on when they enroll in the current study following RGX-314 administration in the parent study.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
115

participants targeted

Target at P50-P75 for all trials

Timeline
22mo left

Started Dec 2021

Longer than P75 for all trials

Geographic Reach
1 country

16 active sites

Status
enrolling by invitation

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress71%
Dec 2021Mar 2028

Study Start

First participant enrolled

December 20, 2021

Completed
25 days until next milestone

First Submitted

Initial submission to the registry

January 14, 2022

Completed
13 days until next milestone

First Posted

Study publicly available on registry

January 27, 2022

Completed
6.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2028

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2028

Last Updated

June 18, 2025

Status Verified

June 1, 2025

Enrollment Period

6.2 years

First QC Date

January 14, 2022

Last Update Submit

June 16, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • To evaluate the long-term safety of RGX-314

    Incidences of ocular Adverse Events and Serious Adverse Events, and all Adverse Events of Special Interest

    5 years inclusive of parent study

Secondary Outcomes (4)

  • • To evaluate the persistence of effect of RGX-314 on best corrected visual acuity (BCVA)

    5 years inclusive of parent study

  • • To evaluate the persistence of effect of RGX-314 on central retinal thickness (CRT), as measured by spectral domain-optical coherence tomography (SD-OCT)

    5 years inclusive of parent study

  • • To assess the need for supplemental anti-vascular endothelial growth factor (anti-VEGF) therapy

    5 years inclusive of parent study

  • • To assess the need of clinic visits for management of nAMD

    5 years inclusive of parent study

Study Arms (1)

Roll over

No intervention All subjects that previously received RGX-314 in a parent study

Other: No intervention.

Interventions

All subjects that previously received RGX-314 in a parent study

Roll over

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodProbability Sample
Study Population

The sample sizes were determined by the parent studies and all participants who received an SCS administration of RGX-314 will be invited to participate in the long-term follow-up study. All Enrolled Population: Includes all participants who are enrolled in the long-term follow-up study.

You may qualify if:

  • Must provide written, signed informed consent for this study.
  • Must have been enrolled in a previous clinical study of RGX-314 in the treatment of nAMD and must have received an SCS injection of RGX-314 in that study.
  • Must be willing and able to comply with all study procedures.

You may not qualify if:

  • \. None

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (16)

Retinal Research Institute, LLC

Phoenix, Arizona, 85014, United States

Location

California Retina Consultants

Bakersfield, California, 93309, United States

Location

Retina-Vitreous Associates Medical Group

Beverly Hills, California, 90211, United States

Location

Northern California Retina Vitreous Associates Medical Group Inc

Mountain View, California, 94040, United States

Location

Retina Consultants San Diego

Poway, California, 92064, United States

Location

California Retina Consultants

Santa Barbara, California, 93103, United States

Location

Southeast Retina Center PC

Augusta, Georgia, 30909, United States

Location

Johns Hopkins University

Baltimore, Maryland, 21205, United States

Location

Ophthalmic Consultants of Boston

Boston, Massachusetts, 02114, United States

Location

Vitreoretinal Surgery PLLC

Edina, Minnesota, 55435, United States

Location

Sierra eye Associates

Reno, Nevada, 89502, United States

Location

Vision Research Center Eye Associates of New Mexico

Albuquerque, New Mexico, 87109, United States

Location

Retinovitreous Associates, LTD

Philadelphia, Pennsylvania, 19107, United States

Location

Charles Retina Institute, P.C

Germantown, Tennessee, 38138, United States

Location

Tennessee Retina, PC

Nashville, Tennessee, 37203, United States

Location

Retina Consultants of Texas

The Woodlands, Texas, 77384, United States

Location

Study Design

Study Type
observational
Observational Model
OTHER
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 14, 2022

First Posted

January 27, 2022

Study Start

December 20, 2021

Primary Completion (Estimated)

March 1, 2028

Study Completion (Estimated)

March 1, 2028

Last Updated

June 18, 2025

Record last verified: 2025-06

Locations