NCT04988191

Brief Summary

This is a trial investigating the efficacy and safety of Toripalimab combined with bevacizumab and chemotherapy as neoadjuvant therapy in patients with advanced microsatellite instability-high (MSI-H) or DNA mismatch repair-deficient (dMMR) colorectal cancer.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
44

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Dec 2020

Typical duration for phase_1

Geographic Reach
1 country

1 active site

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

December 24, 2020

Completed
7 months until next milestone

First Submitted

Initial submission to the registry

July 31, 2021

Completed
3 days until next milestone

First Posted

Study publicly available on registry

August 3, 2021

Completed
1.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 24, 2023

Completed
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 24, 2023

Completed
Last Updated

August 3, 2021

Status Verified

July 1, 2021

Enrollment Period

2.5 years

First QC Date

July 31, 2021

Last Update Submit

July 31, 2021

Conditions

Outcome Measures

Primary Outcomes (1)

  • Pathological complete response rate based on blinded, independent, central review

    Percentage of patients who achieve pathological complete response (pCR) based on blinded, independent, central review (BICR).

    10 weeks

Secondary Outcomes (12)

  • R0 recession rate

    10 weeks

  • Time to surgery

    10 weeks

  • Pathological complete response rate assessed by local investigator

    10 weeks

  • Pathological complete response rate based on blinded, independent, central review (BICR) and the assessment of local investigator

    10 weeks

  • Tumor regression grade (TRG)

    10 weeks

  • +7 more secondary outcomes

Study Arms (1)

Toripalimab combined with bevacizumab and chemotherapy

EXPERIMENTAL
Drug: ToripalimabDrug: BevacizumabDrug: Irinotecan

Interventions

Neoadjuvant therapy: Toripalimab is given by intravenous infusion at 3mg/kg d1 every 2 weeks for 3 cycles. Adjuvant therapy: Toripalimab is given by intravenous infusion at a dose of 240mg every 3 weeks for up to 9 cycles.

Toripalimab combined with bevacizumab and chemotherapy

Neoadjuvant therapy: Bevacizumab is given by intravenous infusion at 5mg/kg d1 every 2 weeks for 3 cycles.

Toripalimab combined with bevacizumab and chemotherapy

Neoadjuvant therapy: Irinotecan is given by intravenous infusion at 180mg/m2 d1 every 2 weeks for 2 cycles.

Toripalimab combined with bevacizumab and chemotherapy

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically confirmed colorectal adenocarcinoma meeting any of the following criterion: a) T3-4 resectable rectal cancer; b) T1-2 rectal cancer located within 12 cm from the anal verge and refusing direct surgery or radiation therapy; c) T4a-b resectable colon cancer.
  • Microsatellite instability-high (MSI-H) or DNA mismatch repair-deficient (dMMR).
  • Measurable disease according to the Response Evaluation Criteria In Solid Tumors (RECIST) 1.1 criteria and haven't received any local treatment.
  • Eastern Cooperative Oncology Group (ECOG) 0-1.
  • Fully aware of this study and having signed informed consent.
  • Age 18 to 75 years old without gender limitation.
  • Good compliance.
  • Absolute neutrophil count ≥1500/mm3, platelet ≥100,000/mm3, Hb ≥10g/dl, serum creatinine ≤1.5 times ULN, creatinine clearance rate ≥50mL/min, ALT and AST ≤2.5 times ULN, INR or aPTT ≤1.5 times ULN (INR ≤2 times ULN and aPTT in normal range for patients who are on prophylactic anticoagulant therapy within 14 days before study treatment), total bilirubin level ≤2 times ULN (within 7 days before study treatment).
  • Women of childbearing age should confirm that serum pregnancy test is negative and agree to use effective contraceptive methods during study treatment and the following 60 days.

You may not qualify if:

  • Previously received anti-PD1 or anti-PDL1 or anti-PDL2 or anti-CTLA4.
  • Uncontrolled active bleeding from the primary tumor or intestinal obstruction.
  • Contraindications of bevacizumab or irinotecan.
  • Hypersensitivity to other monoclonal antibodies.
  • Any active, known or suspected autoimmune disease.
  • Uncontrolled pleural effusion, pericardial effusion, or ascites to a moderate or greater extent.
  • History of one of the following dieases: idiopathic pulmonary fibrosis, organized pneumonia (eg. bronchiolitis obliterans), drug-induced pneumonia, idiopathic pneumonia and interstitial pneumonia, or evidence of active pneumonia through enhanced chest CT screening.
  • Major surgery within 4 weeks before enrollment and haven't fully recovered from the previous surgery.
  • Active bleeding or abnormal coagulation (aPTT \>43s or INR \>1.5 times ULN), or having a tendency to bleed or receiving thrombolytic or anticoagulant therapy.
  • Previously received allogeneic stem cell or parenchymal organ transplantation.
  • Any significant clinical or laboratory abnormality that the investigator considers to influence the safety assessment, eg. uncontrolled active infection, uncontrolled diabetes, hypertension that cannot be reduced to normal range with monotherapy, grade II or above peripheral neuropathy, congestive heart failure, heart disease (class II or higher) as defined by the New York College of Cardiology, myocardial infarction within 3 months prior to enrollment, unstable arrhythmias, unstable angina pectinis, chronic kidney disease, abnormal thyroid function and previous or co-existing malignancies.
  • History of uncorrected serum electrolyte disturbances such as potassium, calcium and magnesium.
  • HIV infection.
  • Active hepatitis B or hepatitis C.
  • Pregnancy or lactation period, or unwilling to use contraception during the trial.
  • +7 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Peking University Cancer Hospital and Institute

Beijing, Beijing Municipality, 100142, China

RECRUITING

Related Publications (1)

  • Wang Z, Wang X, Zhang X, Leng J, Cui M, Zhang J, Wang Q, Sun Y, Xu T, Chen M, Li J, Shen L. Toripalimab, bevacizumab, and irinotecan in dMMR/MSI locally advanced colorectal cancer: First-stage results from a phase 1b/2 trial. Cell Rep Med. 2025 Sep 16;6(9):102296. doi: 10.1016/j.xcrm.2025.102296. Epub 2025 Aug 15.

MeSH Terms

Conditions

Colorectal Neoplasms

Interventions

toripalimabBevacizumabIrinotecan

Condition Hierarchy (Ancestors)

Intestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsCamptothecinAlkaloidsHeterocyclic Compounds

Study Officials

  • Lin Shen, Professor

    Peking University Cancer Hospital & Institute

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Lin Shen, Professor

CONTACT

Jian Li, Professor

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Professor

Study Record Dates

First Submitted

July 31, 2021

First Posted

August 3, 2021

Study Start

December 24, 2020

Primary Completion

June 24, 2023

Study Completion

December 24, 2023

Last Updated

August 3, 2021

Record last verified: 2021-07

Locations