NCT04837677

Brief Summary

This is a Phase 1 dose-escalation study of PRT1419, a myeloid cell leukemia 1 (MCL1) inhibitor, in patients with advanced solid tumors. The purpose of this study is to define the dosing schedule, maximally tolerated dose and/or estimate the optimal biological dose to be used in subsequent development of PRT1419.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
26

participants targeted

Target at P25-P50 for phase_1

Timeline
Completed

Started Aug 2021

Geographic Reach
1 country

7 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 5, 2021

Completed
3 days until next milestone

First Posted

Study publicly available on registry

April 8, 2021

Completed
4 months until next milestone

Study Start

First participant enrolled

August 11, 2021

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 6, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 6, 2023

Completed
Last Updated

March 15, 2023

Status Verified

March 1, 2023

Enrollment Period

1.5 years

First QC Date

April 5, 2021

Last Update Submit

March 14, 2023

Conditions

Keywords

MCL1

Outcome Measures

Primary Outcomes (3)

  • Dose limiting toxicities (DLT) of PRT1419

    Dose limiting toxicities will be evaluated through the first cycle

    Baseline through Day 28

  • Maximally tolerated dose (MTD) and/or optimal biological dose (OBD)

    The MTD and/or OBD will be established for further investigation in participants with advanced solid tumors.

    Baseline through approximately 2 years

  • Recommended phase 2 dose (RP2D) and schedule of PRT1419

    The RP2D will be established for further investigation in participants with advanced solid tumors.

    Baseline through approximately 2 years

Secondary Outcomes (4)

  • Safety and tolerability of PRT1419: AEs, SAEs, CTCAE assessments

    Baseline through approximately 2 years

  • Pharmacokinetic profile of PRT1419: maximum observed plasma concentration

    Baseline through approximately 2 years

  • Anti-tumor activity of PRT1419: measurement of objective responses

    Baseline through approximately 2 years

  • Progression-free survival

    Baseline through approximately 2 years

Study Arms (1)

PRT1419

EXPERIMENTAL

PRT1419 will be administered by intravenous infusion

Drug: PRT1419

Interventions

PRT1419 will be administered by intravenous infusion

PRT1419

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Eastern Cooperative Oncology Group (ECOG) performance status of ≤ 2
  • Adequate organ function (bone marrow, hepatic, renal, cardiovascular)
  • Left ventricular ejection fraction of ≥ 50%
  • Female patients of childbearing potential must have a negative pregnancy test within 7 days of the start of treatment and must agree to use a highly effective method of contraception during the trial
  • Patients must have recovered from the effects of any prior cancer related therapy, radiotherapy or surgery (toxicity ≤ Grade 1)
  • All patients on prior investigational agents must wait at least 5 half-lives of the agent in question, or 28 days, whichever is longer before study entry
  • Most recent lab values meet the following criteria:
  • Absolute neutrophil count \> 1.0 x 10\^3/μL;
  • Platelet count \> 75,000/μL;
  • Hemoglobin \> 9.0 g/dL
  • Histologically confirmed advanced or metastatic solid tumor indicated below that is relapsed, refractory, or intolerant to available therapies with known benefit:
  • Sarcoma not amendable to curative treatment with surgery or radiotherapy;
  • Melanoma (non-resectable or metastatic);
  • Small cell lung cancer (extensive-stage);
  • Non-small cell lung cancer;
  • +4 more criteria

You may not qualify if:

  • Known hypersensitivity to any of the components of PRT1419
  • Primary malignancies of the CNS, or uncontrolled CNS metastases, including impending spinal cord compression
  • Female patients who are pregnant or lactating
  • Inflammatory disorders of the gastrointestinal tract, or subjects with GI malabsorption
  • Mean QTcF interval of \>480 msec
  • History of heart failure, additional risk factors for arrhythmias or requiring concomitant medications that prolong the QT/QTc interval
  • HIV positive; known active hepatitis B or C
  • Uncontrolled intercurrent illnesses
  • Treatment with strong inhibitors of CYP2C8
  • Prior exposure to an MCL1 inhibitor
  • History of another malignancy except:
  • Malignancy treated with curative intent with no known active disease for \>2 years at study entry;
  • Adequately treated non-melanoma skin cancer or lentigo maligna without evidence of disease;
  • Adequately treated carcinoma in situ without evidence of disease;
  • Other concurrent low-grade malignancies (i.e chronic lymphocytic leukemia (Rai 0)) may be considered after consultation with Sponsor.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (7)

Sarah Cannon Research Institute at HealthONE

Denver, Colorado, 80218, United States

Location

Florida Cancer Specialists

Lake Mary, Florida, 32746, United States

Location

Florida Cancer Specialists

Sarasota, Florida, 34232, United States

Location

University of Iowa Hospitals and Clinics

Iowa City, Iowa, 52242, United States

Location

Thomas Jefferson University, Sidney Kimmel Cancer Center

Philadelphia, Pennsylvania, 19107, United States

Location

UPMC Hillman Cancer Center

Pittsburgh, Pennsylvania, 15232, United States

Location

Tennessee Oncology

Nashville, Tennessee, 37203, United States

Location

MeSH Terms

Conditions

SarcomaMelanomaLung NeoplasmsBreast NeoplasmsEsophageal NeoplasmsUterine Cervical NeoplasmsHead and Neck Neoplasms

Condition Hierarchy (Ancestors)

Neoplasms, Connective and Soft TissueNeoplasms by Histologic TypeNeoplasmsNeuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms, Nerve TissueNevi and MelanomasSkin NeoplasmsNeoplasms by SiteSkin DiseasesSkin and Connective Tissue DiseasesRespiratory Tract NeoplasmsThoracic NeoplasmsLung DiseasesRespiratory Tract DiseasesBreast DiseasesGastrointestinal NeoplasmsDigestive System NeoplasmsDigestive System DiseasesEsophageal DiseasesGastrointestinal DiseasesUterine NeoplasmsGenital Neoplasms, FemaleUrogenital NeoplasmsUterine Cervical DiseasesUterine DiseasesGenital Diseases, FemaleFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesGenital Diseases

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 5, 2021

First Posted

April 8, 2021

Study Start

August 11, 2021

Primary Completion

February 6, 2023

Study Completion

February 6, 2023

Last Updated

March 15, 2023

Record last verified: 2023-03

Locations