NCT04756687

Brief Summary

The primary objective of the study is to describe absolute lymphocyte count (ALC) reconstitution after Dimethyl fumarate (DMF) discontinuation, in Relapsing-Remitting Multiple Sclerosis (RRMS) participants with lymphopenia. The secondary objectives of the study are characterization of lymphopenia in overall population; characterization of lymphopenia in participant with DMF discontinuation ; description of the evolution of ALC during DMF treatment; description of the time to reach a discontinuation of DMF treatment; exploration of the time to reach clinical outcomes (Expanded Disability Status Scale \[EDSS\] and relapse) according to lymphopenia; description of the event rate of the serious or opportunistic infections in overall population from DMF initiation and according to DMF discontinuation and lymphopenia; description of the event rate of serious and opportunistic infections in overall population from DMF initiation and according to lymphopenia; estimation of the associations between the baseline demographic and clinical characteristics and the risk to reach a lymphopenia; estimation of the associations between the baseline demographics and clinical characteristics and the risk to reach an ALC reconstitution after DMF discontinuation in participants with lymphopenia; and investigation of the changes of absolute cluster of differentiation 4 (CD4) and cluster of differentiation 8 (CD8) count in overall population on DMF if available.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,507

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Mar 2021

Shorter than P25 for all trials

Geographic Reach
1 country

32 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 12, 2021

Completed
4 days until next milestone

First Posted

Study publicly available on registry

February 16, 2021

Completed
22 days until next milestone

Study Start

First participant enrolled

March 10, 2021

Completed
3 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 15, 2021

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 15, 2021

Completed
Last Updated

October 23, 2023

Status Verified

October 1, 2023

Enrollment Period

3 months

First QC Date

February 12, 2021

Last Update Submit

October 20, 2023

Conditions

Outcome Measures

Primary Outcomes (1)

  • Time to ALC Reconstitution After DMF Discontinuation

    Up to end of study (121 days)

Secondary Outcomes (13)

  • Time From DMF Initiation to Lymphopenia Initiation Assessed in Participants With and Without DMF Discontinuation

    Up to end of study (121 days)

  • Time From DMF Initiation to Lymphopenia Assessed at Time of DMF Discontinuation

    Up to end of study (121 days)

  • Percent Change in ALC Over Time From DMF Initiation to DMF Discontinuation or End of Study

    Up to end of study (121 days)

  • Time From DMF Initiation to DMF Discontinuation

    Up to end of study (121 days)

  • Percentage of Participants with Discontinuation of DMF Treatment

    Up to end of study (121 days)

  • +8 more secondary outcomes

Study Arms (1)

All Participants

RRMS participants treated with DMF will be identified in the Observatoire Français de la Sclérose en Plaques (OFSEP) database for OFSEP sites.

Drug: Dimethyl fumarate

Interventions

Administered as specified in the treatment arm.

All Participants

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodProbability Sample
Study Population

All RRMS participants treated with DMF who fulfil the inclusion criteria are eligible to participate in the study.

You may qualify if:

  • Clinical diagnosis of RRMS at DMF initiation
  • Minimum of 3 months of continuous treatment with DMF\*
  • Initiation of DMF between January 1st, 2016 and December 15th, 2020
  • Minimum of 2 ALC assessments:
  • ALC at DMF initiation (or within 6 months before DMF initiation); or under DMF treatment
  • ALC before the database extraction (15/06/2021).
  • to avoid the early DMF discontinuations for reasons other than lymphopenia.

You may not qualify if:

  • Participants will be excluded from the study entry if they express their opposition to collect the data upon the information.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (32)

Research Site

Amiens, France

Location

Research Site

Besançon, France

Location

Research Site

Bordeaux, France

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Research Site

Brest, France

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Research Site

Caen, France

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Research Site

Clermont-Ferrand, France

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Research Site

Dijon, France

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Research Site

Grenoble, France

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Research Site

Île-de-France - Bicêtre, France

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Research Site

Île-de-France - Créteil, France

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Research Site

Île-de-France - Poissy St-Germain, France

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Research Site

Île-de-France - Pontoise, France

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Research Site

Île-de-France - Rothschild, France

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Research Site

Île-de-France - Saint-Antoine, France

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Research Site

Île-de-France - Saint-Denis, France

Location

Research Site

Île-de-France - Salpêtrière, France

Location

Research Site

Lille, France

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Research Site

Limoges, France

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Research Site

Lyon, France

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Research Site

Marseille, France

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Research Site

Montpellier, France

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Research Site

Nancy, France

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Research Site

Nantes, France

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Research Site

Nice, France

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Research Site

Nîmes, France

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Research Site

Poitiers, France

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Research Site

Rennes, France

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Research Site

Rouen, France

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Research Site

Saint-Etienne, France

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Research Site

Strasbourg, France

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Research Site

Toulouse, France

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Research Site

Tours, France

Location

Related Publications (1)

  • de Seze J, Labauge P, Liblau R, Martinez M, Moreau T, Suchet L, Vermersch P, Vukusic S, Mathey G, Michel L, Ciron J, Ruet A, Maillart E, Zephir H, Papeix C, Defer G, Cohen M, Laplaud DA, Berger E, Clavelou P, Thouvenot E, Heinzlef O, Pelletier J, Giannesini C, Casez O, Bourre B, Wahab A, Magy L, Camdessanche JP, Doghri I, Labeyrie C, Hankiewicz K, Neau JP, Pottier C, Dobay P, Li H, Levin S, Gros M, Ruiz M, Rollot F. LymphoTEC: a Retrospective Real-World Study on Lymphocyte Reconstitution After Lymphopenia in Patients with Multiple Sclerosis Treated with Dimethyl Fumarate in France. Adv Ther. 2025 Apr;42(4):1760-1782. doi: 10.1007/s12325-024-03092-5. Epub 2025 Feb 19.

MeSH Terms

Conditions

Multiple SclerosisMultiple Sclerosis, Relapsing-Remitting

Interventions

Dimethyl Fumarate

Condition Hierarchy (Ancestors)

Demyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesDemyelinating DiseasesAutoimmune DiseasesImmune System Diseases

Intervention Hierarchy (Ancestors)

FumaratesDicarboxylic AcidsAcids, AcyclicCarboxylic AcidsOrganic Chemicals

Study Officials

  • Medical Director

    Biogen

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
CASE ONLY
Time Perspective
RETROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 12, 2021

First Posted

February 16, 2021

Study Start

March 10, 2021

Primary Completion

June 15, 2021

Study Completion

June 15, 2021

Last Updated

October 23, 2023

Record last verified: 2023-10

Data Sharing

IPD Sharing
Will share

In accordance with Biogen's Clinical Trial Transparency and Data Sharing Policy on https://www.biogentrialtransparency.com/

More information

Locations