NCT04740905

Brief Summary

This is a Phase III, multicenter, randomized, double-masked, active comparator-controlled, parallel-group study evaluating the efficacy, safety, and pharmacokinetics of faricimab administered by intravitreal (IVT) injection at 4-week intervals until Week 24, followed by a double-masked period of study without active control to evaluate faricimab administered according to a personalized treatment interval (PTI) dosing regimen in participants with macular edema due to branch retinal vein occlusion (BRVO).

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
553

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Mar 2021

Geographic Reach
21 countries

144 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 3, 2021

Completed
2 days until next milestone

First Posted

Study publicly available on registry

February 5, 2021

Completed
25 days until next milestone

Study Start

First participant enrolled

March 2, 2021

Completed
1.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 6, 2022

Completed
11 months until next milestone

Study Completion

Last participant's last visit for all outcomes

June 12, 2023

Completed
7 months until next milestone

Results Posted

Study results publicly available

January 18, 2024

Completed
Last Updated

August 6, 2024

Status Verified

July 1, 2024

Enrollment Period

1.3 years

First QC Date

February 3, 2021

Results QC Date

November 22, 2023

Last Update Submit

July 11, 2024

Conditions

Keywords

BRVO

Outcome Measures

Primary Outcomes (1)

  • Part 1: Change From Baseline in Best Corrected Visual Acuity (BCVA) in the Study Eye at Week 24

    Best Corrected Visual Acuity (BCVA) was measured on the Early Treatment Diabetic Retinopathy Study (ETDRS) chart at a starting distance of 4 meters. The BCVA letter score ranges from 0 to 100 (best score), and a gain in BCVA from baseline indicates an improvement in visual acuity. The Mixed Model of Repeated Measures (MMRM) analysis included the categorical covariates of treatment arm, visit, visit-by-treatment arm interaction, baseline BCVA (continuous), and randomization stratification factors \[baseline BCVA (≥55 and ≤54 letters), and region (U.S. and Canada, Asia, and rest of the world)\] as fixed effects. An unstructured covariance structure was used. Missing data were implicitly imputed by MMRM model assuming missing at random. Treatment policy strategy (i.e., all observed values used) was applied to all intercurrent events (discontinuation of treatment due to AEs or lack of efficacy, use of prohibited therapy). 95% CI is a rounding of 95.03% CI.

    From Baseline through Week 24

Secondary Outcomes (47)

  • Part 1: Change From Baseline in BCVA in the Study Eye at Specified Timepoints Through Week 24

    Baseline, Weeks 4, 8, 12, 16, 20, and 24

  • Part 1: Percentage of Participants Gaining ≥15 Letters in BCVA From Baseline in the Study Eye at Week 24

    Baseline and Week 24

  • Part 1: Percentage of Participants Gaining ≥15 Letters in BCVA From Baseline in the Study Eye at Specified Timepoints Through Week 24

    Baseline, Weeks 4, 8, 12, 16, 20, and 24

  • Part 1: Percentage of Participants Gaining ≥10 Letters in BCVA From Baseline in the Study Eye at Specified Timepoints Through Week 24

    Baseline, Weeks 4, 8, 12, 16, 20, and 24

  • Part 1: Percentage of Participants Gaining ≥5 Letters in BCVA From Baseline in the Study Eye at Specified Timepoints Through Week 24

    Baseline, Weeks 4, 8, 12, 16, 20, and 24

  • +42 more secondary outcomes

Study Arms (2)

Arm A: Faricimab Q4W (Part 1), Faricimab PTI (Part 2)

EXPERIMENTAL

In Part 1 (Day 1 through Week 24), participants randomly assigned to Arm A will receive faricimab 6 milligrams (mg) by IVT injection once every 4 weeks (Q4W) from Day 1 through Week 20 (a total of 6 injections). In Part 2 (from Week 24 to Week 72), participants will receive faricimab 6 mg by IVT injection according to a personalized treatment interval (PTI) dosing regimen. To preserve masking for Part 2, a sham procedure will be administered during study visits at which no faricimab treatment is administered (according to the PTI dosing regimen).

Drug: FaricimabProcedure: Sham Procedure

Arm B: Aflibercept Q4W (Part 1), Faricimab PTI (Part 2)

ACTIVE COMPARATOR

In Part 1 (Day 1 through Week 24), participants randomly assigned to Arm B will receive aflibercept 2 milligrams (mg) by IVT injection once every 4 weeks (Q4W) from Day 1 through Week 20 (a total of 6 injections). In Part 2 (from Week 24 to Week 72), participants will receive faricimab 6 mg by IVT injection according to a personalized treatment interval (PTI) dosing regimen. To preserve masking for Part 2, a sham procedure will be administered during study visits at which no faricimab treatment is administered (according to the PTI dosing regimen).

Drug: FaricimabDrug: AfliberceptProcedure: Sham Procedure

Interventions

Faricimab will be administered by intravitreal (IVT) injection as specified in each treatment arm.

Also known as: VABYSMO®, faricimab-svoa, RO6867461, RG7716
Arm A: Faricimab Q4W (Part 1), Faricimab PTI (Part 2)Arm B: Aflibercept Q4W (Part 1), Faricimab PTI (Part 2)

Aflibercept 2 mg will be administered by IVT injection once every 4 weeks (Q4W) from Day 1 through Week 20 (a total of 6 injections).

Also known as: Eylea
Arm B: Aflibercept Q4W (Part 1), Faricimab PTI (Part 2)

The sham is a procedure that mimics an intravitreal (IVT) injection, but involves the blunt end of an empty syringe (without a needle) being pressed against the anesthetized eye. It will be administered to participants in both treatments arms at applicable visits to maintain masking.

Arm A: Faricimab Q4W (Part 1), Faricimab PTI (Part 2)Arm B: Aflibercept Q4W (Part 1), Faricimab PTI (Part 2)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Foveal center-involved macular edema due to branch retinal vein occlusion (BRVO), diagnosed no longer than 4 months prior to the screening visit
  • Best-corrected visual acuity (BCVA) of 73 to 19 letters, inclusive (20/40 to 20/400 approximate Snellen equivalent) on Day 1
  • Sufficiently clear ocular media and adequate pupillary dilatation to allow acquisition of good quality retinal images to confirm diagnosis
  • For women of childbearing potential: agreement to remain abstinent or use contraception, and agreement to refrain from donating eggs during the treatment period and for 3 months after the final dose of study treatment

You may not qualify if:

  • Any major illness or major surgical procedure within 1 month before screening
  • Uncontrolled blood pressure
  • Stroke (cerebral vascular accident) or myocardial infarction within 6 months prior to Day 1
  • Pregnant or breastfeeding, or intending to become pregnant during the study
  • History of previous episodes of macular edema due to RVO or persistent macular edema due to RVO diagnosed more than 4 months before screening
  • Any current ocular condition which, in the opinion of the investigator, is currently causing or could be expected to contribute to irreversible vision loss due to a cause other than macular edema due to RVO in the study eye (e.g., ischemic maculopathy, Irvine-Gass syndrome, foveal atrophy, foveal fibrosis, pigment abnormalities, dense subfoveal hard exudates, or other non-retinal conditions)
  • Macular laser (focal/grid) in the study eye at any time prior to Day 1
  • Panretinal photocoagulation in the study eye within 3 months prior to Day 1 or anticipated within 3 months of study start on Day 1
  • Any prior or current treatment for macular edema; macular neovascularization, including diabetic macular edema (DME) and neovascular age-related macular degeneration (nAMD); and vitreomacular-interface abnormalities, including, but not restricted to, IVT treatment with anti-VEGF, steroids, tissue plasminogen activator, ocriplasmin, C3F8, air or periocular injection
  • Any prior intervention with verteporfin photodynamic therapy, diode laser, transpupillary thermotherapy, or vitreo-retinal surgery including sheatotomy
  • Any prior steroid implant use including dexamethasone intravitreal implant (Ozurdex) and fluocinolone acetonide intravitreal implant (Iluvien)
  • Prior IVT administration of faricimab in either eye
  • History of idiopathic or autoimmune-associated uveitis in either eye
  • Active periocular, ocular or intraocular inflammation or infection (including suspected) in either eye on Day 1

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (150)

Retinal Research Institute, LLC

Phoenix, Arizona, 85014, United States

Location

Retina Associates Southwest PC

Tucson, Arizona, 85704, United States

Location

Retinal Diagnostic Center

Campbell, California, 95008, United States

Location

The Retina Partners

Encino, California, 91436, United States

Location

California Eye Specialists Medical group Inc.

Pasadena, California, 91107, United States

Location

Retina Consultants, San Diego

Poway, California, 92064, United States

Location

Retina Consultants of Southern Colorado PC

Colorado Springs, Colorado, 80909, United States

Location

Retina Group of New England

Waterford, Connecticut, 06385, United States

Location

Florida Eye Associates

Melbourne, Florida, 32901, United States

Location

Fort Lauderdale Eye Institute

Plantation, Florida, 33324, United States

Location

Retina Vitreous Assoc of FL

St. Petersburg, Florida, 33711, United States

Location

Southern Vitreoretinal Assoc

Tallahassee, Florida, 32308, United States

Location

Retina Associates of Florida, LLC

Tampa, Florida, 33609, United States

Location

Southeast Retina Center

Augusta, Georgia, 30909, United States

Location

Georgia Retina PC

Marietta, Georgia, 30060-1137, United States

Location

Retina Consultants of Hawaii

‘Aiea, Hawaii, 96701, United States

Location

University Retina and Macula Associates, PC

Oak Forest, Illinois, 60452, United States

Location

Prairie Retina Center

Springfield, Illinois, 62704, United States

Location

Cumberland Valley Retina PC

Hagerstown, Maryland, 21740, United States

Location

Tufts Medical Center; Ophthalmology

Boston, Massachusetts, 02111, United States

Location

Assoc Retinal Consultants PC

Royal Oak, Michigan, 48073, United States

Location

VitreoRetinal Surgery, PLLC.; DBA Retina Consultants of Minnesota

Edina, Minnesota, 55435, United States

Location

Midwest Vision Research Foundation

Chesterfield, Missouri, 63017, United States

Location

Sierra Eye Associates

Reno, Nevada, 89502, United States

Location

Retina Associates of NJ

Teaneck, New Jersey, 07666, United States

Location

Long Is. Vitreoretinal Consult

Hauppauge, New York, 11788, United States

Location

Retina Vit Surgeons/Central NY

Liverpool, New York, 13088, United States

Location

Graystone Eye

Hickory, North Carolina, 28602, United States

Location

Cincinnati Eye Institute

Cincinnati, Ohio, 45242, United States

Location

Black Hills Eye Institute

Rapid City, South Dakota, 57701, United States

Location

Charles Retina Institute

Germantown, Tennessee, 38138, United States

Location

Tennessee Retina PC

Nashville, Tennessee, 37203, United States

Location

Retina Res Institute of Texas

Abilene, Texas, 79606, United States

Location

Austin Retina Associates

Austin, Texas, 78705-1169, United States

Location

Retina & Vitreous of Texas

Bellaire, Texas, 77401-3510, United States

Location

Texas Retina Associates

Dallas, Texas, 75231, United States

Location

Retina Consultants of Texas

The Woodlands, Texas, 77384-4167, United States

Location

Strategic Clinical Research Group, LLC

Willow Park, Texas, 76087, United States

Location

Retina Associates of Utah, PLLC

Salt Lake City, Utah, 84107, United States

Location

Fundacion Zambrano

CABA, C1017AAO, Argentina

Location

Centro Oftalmológico Dr. Charles S.A.

Capital Federal, C1015ABO, Argentina

Location

Oftalmos

Capital Federal, C1120AAN, Argentina

Location

Hospital Italiano; Ophtalmology

Capital Federal, C1199ABC, Argentina

Location

Buenos Aires Mácula

Ciudad Autonoma Buenos Aires, C1061AAE, Argentina

Location

Oftar

Mendoza, M5500GGK, Argentina

Location

Centro Oftalmólogos Especialistas

Rosario, S2000ANJ, Argentina

Location

Grupo Laser Vision

Rosario, S2000DLA, Argentina

Location

Organizacion Medica de Investigacion

San Nicolás, C1015ABO, Argentina

Location

Strathfield Retina Clinic

Strathfield, New South Wales, 2135, Australia

Location

Save Sight Institute

Sydney, New South Wales, 2000, Australia

Location

Sydney Retina Clinic and Day Surgery

Sydney, New South Wales, 2000, Australia

Location

Centre For Eye Research Australia

East Melbourne, Victoria, 3002, Australia

Location

Retina Specialists Victoria

Rowville, Victoria, 3178, Australia

Location

The Lions Eye Institute

Nedlands, Western Australia, 6009, Australia

Location

LKH-Univ.Klinikum Graz; Universitäts-Augenklinik

Graz, 8036, Austria

Location

Hospital das Clinicas - UFRGS

Porto Alegre, Rio Grande do Sul, 90035-903, Brazil

Location

Botelho Hospital da Visao

Blumenau, Santa Catarina, 89052-504, Brazil

Location

Universidade Federal de Sao Paulo - UNIFESP*X; Oftalmologia

São Paulo, São Paulo, 04023-062, Brazil

Location

Hosp de Olhos de Sorocaba

Sorocaba, São Paulo, 18031-060, Brazil

Location

Beijing Hospital of Ministry of Health

Beijing, 100730, China

Location

The Second Hospital of Jilin University

Changchun, 130041, China

Location

West China Hospital, Sichuan University

Chengdu, 610041, China

Location

Zhongshan Ophthalmic Center, Sun Yat-sen University

Guangzhou, 510060, China

Location

The 2nd Affiliated Hospital of Harbin Medical University

Harbin, 150001, China

Location

The Affiliated Eye Hospital of Nanjing Medical University

Nanjing, 210029, China

Location

Shanghai Tenth People's Hospital

Shanghai, 200072, China

Location

Shanghai First People's Hospital

Shanghai, 200080, China

Location

He Eye Specialist Shenyang Hospital

Shenyang, 110034, China

Location

Tianjin Eye Hospital

Tianjin, 300050, China

Location

Tianjin Medical University Eye Hospital

Tianjin, 300070, China

Location

Eye Hospital, Wenzhou Medical University

Wenzhou, 325027, China

Location

Renmin Hospital of Wuhan University

Wuhan, 430060, China

Location

Henan Provincial Eye Hosptial

Zhengzhou, China

Location

Faculty Hospital Ostrava; Ophthalmology clinic

Ostrava, 708 52, Czechia

Location

Faculty Hospital Kralovske Vinohrady; Ophthalmology clinic

Prague, 100 34, Czechia

Location

AXON Clinical

Prague, Czechia

Location

Nemocnice Sokolov

Sokolov, 356 01, Czechia

Location

Chi De Creteil; Ophtalmologie

Créteil, 94010, France

Location

Hopital Lariboisiere; Ophtalmologie

Paris, 75010, France

Location

Universitätsklinikum Freiburg, Klinik für Augenheilkunde

Freiburg im Breisgau, 79106, Germany

Location

Universitätsmedizin Göttingen Georg-August-Universität; Klinik für Augenheilkunde

Göttingen, 37075, Germany

Location

Klinikum der Stadt Ludwigshafen am Rhein gGmbH; Augenklinik

Ludwigshafen, 67063, Germany

Location

Queen Mary Hospital; Department of Ophthalmology

Hong Kong, Hong Kong

Location

Hong Kong Eye Hospital; CUHK Eye Centre

Mong Kok, Hong Kong

Location

Budapest Retina Associates Kft.

Budapest, 1133, Hungary

Location

Debreceni Egyetem Klinikai Kozpont; Szemeszeti Klinika

Debrecen, 4032, Hungary

Location

Ganglion Medial Center

Pécs, 7621, Hungary

Location

Szegedi Tudományegyetem ÁOK; Department of Ophtalmology

Szeged, 6720, Hungary

Location

Rambam Medical Center; Opthalmology

Haifa, 3109601, Israel

Location

Hadassah MC; Ophtalmology

Jerusalem, 9112001, Israel

Location

Rabin MC; Ophtalmology

Petah Tikva, 4941492, Israel

Location

Kaplan Medical Center; Ophtalmology

Rehovot, 7660101, Israel

Location

Tel Aviv Sourasky MC; Ophtalmology

Tel Aviv, 6423906, Israel

Location

Fondazione Ptv Policlinico Tor Vergata Di Roma;U.O.S.D. Patologie Renitiche

Rome, Lazio, 00133, Italy

Location

Fondazione Irccs Ca' Granda Ospedale Maggiore Policlinico-Clinica Regina Elena;U.O.C Oculistica

Milan, Lombardy, 20100, Italy

Location

Azienda Ospedaliero-Universitaria Careggi; S.O.D. Oculistica

Florence, Tuscany, 50134, Italy

Location

Sugita Eye Hospital

Aichi, 460-0008, Japan

Location

Nagoya University Hospital

Aichi, 466-8560, Japan

Location

Nagoya City University Hospital

Aichi, 467-8602, Japan

Location

Aichi Medical University Hospital

Aichi, 480-1195, Japan

Location

Toho University Sakura Medical Center

Chiba, 285-8741, Japan

Location

Hayashi Eye Hospital

Fukuoka, 812-0011, Japan

Location

Southern TOHOKU Eye Clinic

Fukushima, 963-8052, Japan

Location

Asahikawa Medical University Hospital

Hokkaido, 078-8510, Japan

Location

Hyogo Prefectural Amagasaki General Medical Center (Hyogo AGMC)

Hyōgo, 660-8550, Japan

Location

Hyogo Medical University Hospital

Hyōgo, 663-8501, Japan

Location

Kozawa eye hospital and diabetes center

Ibaraki, 310-0845, Japan

Location

Kyoto University Hospital

Kyoto, 606-8507, Japan

Location

Tokushima University Hospital

Tokushima, 770-8503, Japan

Location

Nihon University Hospital

Tokyo, 101-8309, Japan

Location

Tokyo Medical University Hachioji Medical Center

Tokyo, 193-0998, Japan

Location

Specjalistyczny O?rodek Okulistyczny Oculomedica

Bydgoszcz, 85-870, Poland

Location

Szpital Specjalistyczny nr 1; Oddzial Okulistyki

Bytom, 41-902, Poland

Location

Dobry Wzrok Sp Z O O

Gda?sk, 80-402, Poland

Location

Poradnia Okulistyczna i Salon Optyczny w Gliwicach- PRYZMAT

Gliwice, 44-100, Poland

Location

Gabinet Okulistyczny Prof Edward Wylegala

Katowice, 40-594, Poland

Location

Centrum Medyczne Dietla 19 Sp. Z O.O.

Krakow, 31-070, Poland

Location

Centrum Medyczne Pulawska SP. z o.o.

Piaseczno, 05-500, Poland

Location

Lens Clinic

Rybnik, 44-203, Poland

Location

Caminomed

Tarnowskie Góry, 42-600, Poland

Location

Centrum Zdrowia MDM

Warsaw, 00-189, Poland

Location

Centro Hospitalar E Universitário de Coimbra EPE - Serviço Oftalmologia; Serviço Oftalmologia

Coimbra, 3000-075, Portugal

Location

Espaco Medico Coimbra

Coimbra, 3030-163, Portugal

Location

Centro Hospitalar Universitário do Porto ? Hospital de Santo António; Servico de Oftalmologia

Porto, 4099-001, Portugal

Location

Clinic Optimed

Ufa, Bashkortostan Republic, 450059, Russia

Location

Clinics of Eye Diseases, LLC

Kazan', Tatarstan Republic, 420066, Russia

Location

?Intersec. Research and Technology Complex ?Eye Microsurgery? n a Fyodorov Irkutsk branch

Irkutsk, 664033, Russia

Location

Singapore Eye Research Institute

Singapore, 168751, Singapore

Location

Tan Tock Seng Hospital; Ophthalmology Department

Singapore, 308433, Singapore

Location

Pusan National University Hospital

Busan, 602-739, South Korea

Location

Yeungnam University Medical Center

Daegu, 42415, South Korea

Location

Seoul National University Bundang Hospital

Seongnam-si, 463-707, South Korea

Location

Kyung Hee University Hospital

Seoul, 02447, South Korea

Location

Asan Medical Center

Seoul, 05505, South Korea

Location

Samsung Medical Center

Seoul, 06351, South Korea

Location

Clinica Universitaria de Navarra; Servicio de Oftalmologia

Pamplona, Navarre, 31008, Spain

Location

Oftalvist Valencia

Burjassot, Valencia, 46100, Spain

Location

Hospital dos de maig; servicio de oftalmologia

Barcelona, 08025, Spain

Location

Clinica Baviera; Servicio Oftalmologia

Madrid, 28046, Spain

Location

Hospital Universitario Rio Hortega; Servicio de Oftalmologia

Valladolid, 47012, Spain

Location

Changhua Christian Hospital; Department of Ophthalmology

Changhua, 500, Taiwan

Location

Taipei Veterans General Hospital; Ophthalmology

Taipei, 11217, Taiwan

Location

Chang Gung Medical Foundation - Linkou; Ophthalmology

Taoyuan District, 333, Taiwan

Location

National Taiwan University Hospital; Ophthalmology

Zhongzheng Dist., 10002, Taiwan

Location

Belfast Health and Social Care Trust, ROYAL VICTORIA HOSPITAL

Belfast, BT12 6BA, United Kingdom

Location

Bristol Eye Hospital;Retinal Treatment and Research Unit

Bristol, BS1 2LX, United Kingdom

Location

University Hospital of Wales

Cardiff, CF14 4XW, United Kingdom

Location

Gloucestershire Hospitals NHS Foundation Trust

Gloucestershire, GL1 3NN, United Kingdom

Location

St James University Hospital

Leeds, LS9 7TF, United Kingdom

Location

Central Middlesex Hospital

London, NW10 7NS, United Kingdom

Location

Related Publications (1)

  • Romano F, Lamanna F, Gabrielle PH, Teo KYC, Battaglia Parodi M, Iacono P, Fraser-Bell S, Cornish EE, Nassisi M, Viola F, Agarwal A, Samanta A, Chhablani J, Staurenghi G, Invernizzi A. Update on Retinal Vein Occlusion. Asia Pac J Ophthalmol (Phila). 2023 Mar-Apr 01;12(2):196-210. doi: 10.1097/APO.0000000000000598. Epub 2023 Feb 14.

MeSH Terms

Conditions

Macular EdemaRetinal Vein Occlusion

Interventions

faricimabaflibercept

Condition Hierarchy (Ancestors)

Macular DegenerationRetinal DegenerationRetinal DiseasesEye DiseasesVenous ThrombosisThrombosisEmbolism and ThrombosisVascular DiseasesCardiovascular Diseases

Results Point of Contact

Title
Medical Communications
Organization
Hoffmann-La Roche

Study Officials

  • Clinical Trials

    Hoffmann-La Roche

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 3, 2021

First Posted

February 5, 2021

Study Start

March 2, 2021

Primary Completion

July 6, 2022

Study Completion

June 12, 2023

Last Updated

August 6, 2024

Results First Posted

January 18, 2024

Record last verified: 2024-07

Data Sharing

IPD Sharing
Will share

For eligible studies, qualified researchers may request access to individual patient level clinical data. See Roche's commitment to transparency of clinical study information here: https://go.roche.com/data\_sharing

Locations