NCT04495010

Brief Summary

The purpose of this study is to evaluate the role of neoadjuvant immunotherapy and to demonstrate high pathologic complete response (pCR) and near pCR rates in melanoma participants with clinically detectable nodal disease and a high risk of recurrence. Neoadjuvant immunotherapy aims to enhance the systemic T-cell response to tumor antigens while detectable tumor is still present, inducing a stronger and broader tumor-specific immune response. Of the neoadjuvant approaches studied within melanoma, the neoadjuvant combination of nivolumab and ipilimumab has demonstrated high pCR and near pCR rates that may translate to prolonged clinical benefit.

Trial Health

62
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Timeline
17mo left

Started Mar 2021

Longer than P75 for phase_2

Geographic Reach
15 countries

113 active sites

Status
withdrawn

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress78%
Mar 2021Oct 2027

First Submitted

Initial submission to the registry

July 30, 2020

Completed
1 day until next milestone

First Posted

Study publicly available on registry

July 31, 2020

Completed
8 months until next milestone

Study Start

First participant enrolled

March 31, 2021

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 28, 2024

Completed
3.7 years until next milestone

Study Completion

Last participant's last visit for all outcomes

October 23, 2027

Expected
Last Updated

March 19, 2021

Status Verified

March 1, 2021

Enrollment Period

2.9 years

First QC Date

July 30, 2020

Last Update Submit

March 17, 2021

Conditions

Outcome Measures

Primary Outcomes (1)

  • Event-free survival (EFS)

    Up to 4 years

Secondary Outcomes (12)

  • Recurrence-free survival (RFS) Time from Surgery

    Up to 5 years

  • RFS Time from Adjuvant Therapy

    Up to 5 years

  • Pathologic response rate (pRR) by immune-related pathologic response (irPR)

    Up to 5 years

  • Concordance major pathologic response (MPR) by local and central pathology Review

    Up to 5 years

  • RFS by MPR

    Up to 5 years

  • +7 more secondary outcomes

Study Arms (3)

Neoadjuvant treatment + Adjuvant treatment

EXPERIMENTAL
Biological: NivolumabBiological: Ipilimumab

Adjuvant treatment

EXPERIMENTAL
Biological: Nivolumab

Neo treat with patho response-driven Adju treat or observation

EXPERIMENTAL

Neoadjuvant treatment with pathologic response-driven Adjuvant treatment or observation

Biological: NivolumabBiological: Ipilimumab

Interventions

NivolumabBIOLOGICAL

Specified dose on specified days

Also known as: Opdivo
Adjuvant treatmentNeo treat with patho response-driven Adju treat or observationNeoadjuvant treatment + Adjuvant treatment
IpilimumabBIOLOGICAL

Specified dose on specified days

Also known as: Yervoy
Neo treat with patho response-driven Adju treat or observationNeoadjuvant treatment + Adjuvant treatment

Eligibility Criteria

Age12 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Males and females, ≥ 12 years of age \[Except: where local regulations and/or institutional policies do not allow for participants \< 18 years of age (adolescent population) to participate. For those sites, the eligible participant population is 18 years of age or local age of majority, inclusive\]
  • Diagnosed with cytologically or histologically confirmed Stage IIIB, IIIC, or IIID cutaneous melanoma as per American Joint Committee on Cancer (AJCC) staging system, with ≥ 1 clinically detectable lymph node metastases (N1b, N2b, N3b), which are measurable according to Response Evaluation Criteria In Solid Tumors version 1.1 (RECIST 1.1)
  • Adult participants and adolescents 16 to 18 years old must have an Eastern Cooperative Oncology Group (ECOG) scale performance status of 0 or 1. Adolescents \< 16 years old must have Lanksky Play-Performance Status scale performance of ≥ 60
  • Must be treatment-naïve (ie, no prior systemic anticancer therapy as adjuvant therapy for melanoma or unresectable/metastatic melanoma)
  • Women and men must agree to follow specific methods of contraception, if applicable, while participating in the trial

You may not qualify if:

  • Women who are breastfeeding
  • Patients with serious or uncontrolled medical disorders
  • Prior treatment with an anti-programmed cell death protein 1 (PD-1), anti-programmed death-ligand 1 (PD-L1), anti-programmed death-ligand 2 (PD-L2), or anti cytotoxic T-lymphocyte antigen 4 (CTLA-4) antibody, or any other antibody or drug specifically targeting T-cell co-stimulation or checkpoint pathways

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (118)

Local Institution

Gilbert, Arizona, 85234, United States

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Tucson, Arizona, 85724, United States

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San Francisco, California, 94158, United States

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Aurora, Colorado, 80045, United States

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Tampa, Florida, 33612, United States

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Atlanta, Georgia, 30322, United States

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Atlanta, Georgia, 30342, United States

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Marietta, Georgia, 30060, United States

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Annapolis, Maryland, 21401, United States

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Boston, Massachusetts, 02114, United States

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Boston, Massachusetts, 02215, United States

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Minneapolis, Minnesota, 55407, United States

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Minneapolis, Minnesota, 55455, United States

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Hattiesburg, Mississippi, 39401, United States

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St Louis, Missouri, 63110, United States

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Morristown, New Jersey, 07960, United States

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New Brunswick, New Jersey, 08901, United States

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Cleveland, Ohio, 44195, United States

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Portland, Oregon, 97239, United States

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Houston, Texas, 77030, United States

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Salt Lake City, Utah, 84112, United States

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Charlottesville, Virginia, 22908, United States

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Seattle, Washington, 98109, United States

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North Sydney, New South Wales, 2060, Australia

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Westmead, New South Wales, 2145, Australia

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Greenslopes, Queensland, 4120, Australia

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Woolloongabba, Queensland, 4120, Australia

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Adelaide, South Australia, 5000, Australia

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Hobart, Tasmania, 7000, Australia

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Ballarat, Victoria, 3350, Australia

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Melbourne, Victoria, 3000, Australia

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Melbourne, Victoria, 3004, Australia

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Doubleview, Western Australia, 6018, Australia

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Nedlands, Western Australia, 6009, Australia

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Graz, 803 6, Austria

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Innsbruck, 6020, Austria

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Salzburg, 5020, Austria

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Sankt Pölten, 3100, Austria

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Vienna, A-1090, Austria

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Brussels, 1200, Belgium

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Ghent, 9000, Belgium

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Wilrijk, 2610, Belgium

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Fortaleza, Ceará, 60135237, Brazil

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Brasília, Federal District, 70200-730, Brazil

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Curitiba, Paraná, 80530-010, Brazil

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Porto Alegre, Rio Grande do Sul, 90035-903, Brazil

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Porto Alegre, Rio Grande do Sul, 90050-170, Brazil

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Porto Alegre, Rio Grande do Sul, 91350-200, Brazil

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Florianópolis, Santa Catarina, 88034-000, Brazil

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São José do Rio Preto, São Paulo, 15092-415, Brazil

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Rio de Janeiro, 20220-410, Brazil

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São Paulo, 01246-000, Brazil

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São Paulo, 05308-020, Brazil

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Aarhus, 8200, Denmark

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Herlev, 2730, Denmark

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Odense C, 2000, Denmark

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Bordeaux, 33075, France

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Dijon, 21079, France

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Lille, 59000, France

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Marseille, 13385, France

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Nantes, 44093, France

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Nice, 6200, France

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Paris, 75010, France

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Pierre-Bénite, 69495, France

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Rennes, 35000, France

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Sr Priest En Jarez, 42270, France

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Toulouse, 31059, France

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Villejuif, 94800, France

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Berlin, 10117, Germany

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Erlangen, 91054, Germany

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Essen, 45122, Germany

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Hanover, 30625, Germany

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Heidelberg, 69120, Germany

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Kiel, 24105, Germany

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Lübeck, 23538, Germany

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Mainz, 55131, Germany

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Regensburg, 93053, Germany

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Tübingen, 72076, Germany

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Würzburg, 97080, Germany

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Bergamo, 24127, Italy

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Meldola, 47014, Italy

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Napoli, 80131, Italy

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Novara, 28100, Italy

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Padua, 35128, Italy

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Pavia, 27100, Italy

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Amsterdam, 1066CX, Netherlands

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Amsterdam, 1081 HV, Netherlands

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Breda, 4818 CK, Netherlands

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Geleen, 6162bg, Netherlands

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Leiden, 2333 ZA, Netherlands

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Rotterdam, 3075 EA, Netherlands

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Utrecht, 3584CX, Netherlands

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Krakow, 31-115, Poland

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Warsaw, 02-781, Poland

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Wroclaw, 53-413, Poland

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Krasnodar, 350000, Russia

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Ryazan, 390011, Russia

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Saint Petersburg, 197758, Russia

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Saint Petersburg, 198255, Russia

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Barcelona, 08036, Spain

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Haddon Heights, 8035, Spain

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Madrid, 28007, Spain

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Málaga, 29010, Spain

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Oviedo, 33011, Spain

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Santiago de Compostela, 15706, Spain

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Seville, 41009, Spain

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Vaxjo, 352 34, Sweden

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Zurich, CH - 8091, Switzerland

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Cambridge, CB2 0QQ, United Kingdom

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Glasgow, G12 0YN, United Kingdom

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Guildford, GU2 7XX, United Kingdom

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Leeds, LS9 7TF, United Kingdom

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London, SE1 9RT, United Kingdom

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London, SW3 6JJ, United Kingdom

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Manchester, M20 4BX, United Kingdom

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Northwood, HA6 2RN, United Kingdom

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Oxford, OX3 7LE, United Kingdom

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Sutton, SM2 5PT, United Kingdom

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Related Publications (1)

  • Gorry C, McCullagh L, O'Donnell H, Barrett S, Schmitz S, Barry M, Curtin K, Beausang E, Barry R, Coyne I. Neoadjuvant treatment for stage III and IV cutaneous melanoma. Cochrane Database Syst Rev. 2023 Jan 17;1(1):CD012974. doi: 10.1002/14651858.CD012974.pub2.

Related Links

MeSH Terms

Conditions

Melanoma

Interventions

NivolumabIpilimumab

Condition Hierarchy (Ancestors)

Neuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Nerve TissueNevi and MelanomasSkin NeoplasmsNeoplasms by SiteSkin DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Study Officials

  • Bristol-Myers Squibb

    Bristol-Myers Squibb

    STUDY DIRECTOR
0

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 30, 2020

First Posted

July 31, 2020

Study Start

March 31, 2021

Primary Completion

February 28, 2024

Study Completion (Estimated)

October 23, 2027

Last Updated

March 19, 2021

Record last verified: 2021-03

Locations