NCT04482309

Brief Summary

This is an open-label, multi-center, multi-cohort, Phase 2 study to evaluate the efficacy and safety of trastuzumab deruxtecan (T-DXd) for the treatment of selected HER2-expressing tumors. This study will consist of Part 1 which includes 7 cohorts of: urothelial bladder cancer, biliary tract cancer, cervical cancer, endometrial cancer, ovarian cancer, pancreatic cancer, and rare tumors; and Part 2 which includes 5 cohorts A to E of: A) any tumor type that is HER2 IHC 3+ (excluding breast, gastric cancer, and colorectal cancer), B) any tumor type that is HER2 IHC 2+/ISH+ (excluding breast, gastric cancer, and colorectal cancer), C) HER2 IHC 2+ or 1+ endometrial cancer, D) HER2 IHC 2+ or 1+ ovarian cancer, and E) HER2 IHC 2+ or 1+ cervical cancer. Study hypothesis: Trastuzumab deruxtecan will show meaningful clinical activity and a favorable risk benefit profile in selected HER2-expressing solid tumors.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
477

participants targeted

Target at P75+ for phase_2

Timeline
10mo left

Started Aug 2020

Longer than P75 for phase_2

Geographic Reach
17 countries

89 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress87%
Aug 2020Mar 2027

First Submitted

Initial submission to the registry

July 20, 2020

Completed
2 days until next milestone

First Posted

Study publicly available on registry

July 22, 2020

Completed
27 days until next milestone

Study Start

First participant enrolled

August 18, 2020

Completed
6.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 23, 2027

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 23, 2027

Last Updated

April 9, 2026

Status Verified

April 1, 2026

Enrollment Period

6.6 years

First QC Date

July 20, 2020

Last Update Submit

April 8, 2026

Conditions

Keywords

T-DXd, DS-8201a, Trastuzumab Deruxtecan, HER2

Outcome Measures

Primary Outcomes (1)

  • Objective Response Rate (ORR)

    Confirmed ORR per RECIST 1.1 is the percentage of patients with Complete Response or Partial Response that is subsequently confirmed.

    An average of approximately 6 months

Secondary Outcomes (9)

  • Duration of response (DoR)

    An average of approximately 6 months

  • Disease control rate (DCR)

    An average of approximately 6 months

  • Progression free survival (PFS)

    An average of approximately 6 months

  • Proportion of patients alive and progression-free at 6 months and 12 months

    Up to 12 months

  • Overall survival (OS)

    An average of approximately 14 months

  • +4 more secondary outcomes

Study Arms (12)

Part 1 Cohort 1

EXPERIMENTAL

Biliary tract cancer

Drug: Trastuzumab deruxtecan

Part 1 Cohort 2

EXPERIMENTAL

Bladder cancer

Drug: Trastuzumab deruxtecan

Part 1 Cohort 3

EXPERIMENTAL

Cervical cancer

Drug: Trastuzumab deruxtecan

Part 1 Cohort 4

EXPERIMENTAL

Endometrial cancer

Drug: Trastuzumab deruxtecan

Part 1 Cohort 5

EXPERIMENTAL

Ovarian cancer

Drug: Trastuzumab deruxtecan

Part 1 Cohort 6

EXPERIMENTAL

Pancreatic cancer

Drug: Trastuzumab deruxtecan

Part 1 Cohort 7

EXPERIMENTAL

Rare tumors

Drug: Trastuzumab deruxtecan

Part 2 Cohort A

EXPERIMENTAL

Any tumor type that is HER2 IHC 3+ (excluding breast, gastric cancer, and colorectal cancer)

Drug: Trastuzumab deruxtecan

Part 2 Cohort B

EXPERIMENTAL

Any tumor type that is HER2 IHC 2+/ISH+ (excluding breast, gastric cancer, and colorectal cancer)

Drug: Trastuzumab deruxtecan

Part 2 Cohort C

EXPERIMENTAL

HER2 IHC 2+ or 1+ endometrial cancer

Drug: Trastuzumab deruxtecan

Part 2 Cohort D

EXPERIMENTAL

HER2 IHC 2+ or 1+ ovarian cancer

Drug: Trastuzumab deruxtecan

Part 2 Cohort E

EXPERIMENTAL

HER2 IHC 2+ or 1+ cervical cancer

Drug: Trastuzumab deruxtecan

Interventions

Trastuzumab deruxtecan by intravenous infusion

Also known as: DS-8201a, T-DXd
Part 1 Cohort 1Part 1 Cohort 2Part 1 Cohort 3Part 1 Cohort 4Part 1 Cohort 5Part 1 Cohort 6Part 1 Cohort 7Part 2 Cohort APart 2 Cohort BPart 2 Cohort CPart 2 Cohort DPart 2 Cohort E

Eligibility Criteria

Age18 Years - 120 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Locally advanced, unresectable, or metastatic disease based on most recent imaging.
  • Cohort 1: Biliary tract cancer
  • Cohort 2: Bladder cancer
  • Cohort 3: Cervical cancer
  • Cohort 4: Endometrial cancer
  • Cohort 5: Epithelial ovarian cancer
  • Cohort 6: Pancreatic cancer
  • Cohort 7: Rare tumors: This cohort will consist of patients with tumors that express HER2, excluding the tumors mentioned above, and breast, non-small cell lung cancer, gastric cancer, and colorectal cancer.
  • Cohort A: Metastatic or advanced solid tumors that are HER2 IHC 3+ (excluding breast, gastric cancer, and colorectal cancer). Patients with non-small cell lung cancer can be included.
  • Cohort B: Metastatic or advanced solid tumors that are HER2 IHC 2+/ISH+ any tumor type (excluding breast, gastric cancer, and colorectal cancer). Patients with non-small cell lung cancer can be included.
  • Cohort C: Metastatic or advanced solid endometrial cancer that is HER2 IHC 2+ or 1+.
  • Cohort D: Metastatic or advanced ovarian cancer that is HER2 IHC 2+ or 1+.
  • Cohort E: Metastatic or advanced solid cervical cancer that is HER2 IHC 2+ or 1+.
  • Progressed following prior treatment or who have no satisfactory alternative treatment option.
  • Prior HER2 targeting therapy is permitted.
  • +5 more criteria

You may not qualify if:

  • History of non-infectious pneumonitis/ILD that required steroids, current ILD, or where suspected ILD that cannot be ruled out by imaging at screening
  • Lung-specific intercurrent clinically significant severe illnesses
  • Uncontrolled infection requiring intravenous (IV) antibiotics, antivirals, or antifungals
  • Pleural effusion, ascites or pericardial effusion that requires drainage, peritoneal shunt, or Cell-free and Concentrated Ascites Reinfusion Therapy (CART
  • Known Somatic DNA mutation of HER2 (ERBB2) without tumoral HER2 protein expression.
  • Primary diagnosis of adenocarcinoma of the breast, adenocarcinoma of the colon or rectum, adenocarcinoma of the gastric body or gastro-esophageal junction, or non-small cell lung cancer for Part 1. For Part 2, patients with primary diagnosis of adenocarcinoma of the breast, adenocarcinoma of the colon or rectum, adenocarcinoma of the gastric body or gastro-esophageal junction will be excluded.
  • Medical conditions that may interfere with the subject's participation in the study.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (89)

Research Site

Duarte, California, 91010, United States

Location

Research Site

Santa Rosa, California, 95403, United States

Location

Research Site

Chicago, Illinois, 60637, United States

Location

Research Site

Muncie, Indiana, 47303, United States

Location

Research Site

Boston, Massachusetts, 02215, United States

Location

Research Site

Middletown, New Jersey, 07748, United States

Location

Research Site

Harrison, New York, 10604, United States

Location

Research Site

New York, New York, 10029, United States

Location

Research Site

New York, New York, 10065, United States

Location

Research Site

Durham, North Carolina, 27710, United States

Location

Research Site

Houston, Texas, 77030, United States

Location

Research Site

Seattle, Washington, 98195, United States

Location

Research Site

Auchenflower, 4066, Australia

Location

Research Site

Blacktown, 2148, Australia

Location

Research Site

Camperdown, 2050, Australia

Location

Research Site

Heidelberg, 3084, Australia

Location

Research Site

Melbourne, 3000, Australia

Location

Research Site

Nedlands, 6009, Australia

Location

Research Site

Brussels, 1090, Belgium

Location

Research Site

Leuven, 3000, Belgium

Location

Research Site

Liège, 4000, Belgium

Location

Research Site

Porto Alegre, 90035-000, Brazil

Location

Research Site

São Paulo, 01246-000, Brazil

Location

Research Site

Vitória, 29043-272, Brazil

Location

Research Site

Kelowna, British Columbia, V1Y 5L3, Canada

Location

Research Site

Ottawa, Ontario, K1H 8L6, Canada

Location

Research Site

Québec, Quebec, G1J 1Z4, Canada

Location

Research Site

Montreal, H3T 1E2, Canada

Location

Research Site

Brno, 656 53, Czechia

Location

Research Site

Hradec Králové, 500 05, Czechia

Location

Research Site

Olomouc, 77900, Czechia

Location

Research Site

Prague, 150 06, Czechia

Location

Research Site

Prague, 180 81, Czechia

Location

Research Site

Delhi, 110085, India

Location

Research Site

Gūrgaon, 122001, India

Location

Research Site

Kolkata, 700160, India

Location

Research Site

Mumbai, 400012, India

Location

Research Site

Milan, 20162, Italy

Location

Research Site

Milan, 20141, Italy

Location

Research Site

Naples, 80131, Italy

Location

Research Site

Rome, 168, Italy

Location

Research Site

Chūōku, 104-0045, Japan

Location

Research Site

Kashiwa, 277-8577, Japan

Location

Research Site

Suita-shi, 565-0871, Japan

Location

Research Site

Amsterdam, 1066CX, Netherlands

Location

Research Site

Delft, 2625 AD, Netherlands

Location

Research Site

Groningen, 9700, Netherlands

Location

Research Site

Bydgoszcz, 85-796, Poland

Location

Research Site

Gdansk, 80-952, Poland

Location

Research Site

Krakow, 31-501, Poland

Location

Research Site

Poznan, 60-355, Poland

Location

Research Site

Warsaw, 02-781, Poland

Location

Research Site

Kaluga, 248007, Russia

Location

Research Site

Moscow, 115419, Russia

Location

Research Site

Moscow, 115478, Russia

Location

Research Site

Moscow, 117997, Russia

Location

Research Site

Moscow, 121205, Russia

Location

Research Site

Moscow, 143423, Russia

Location

Research Site

Moscow, 143442, Russia

Location

Research Site

Saint Petersburg, 195271, Russia

Location

Research Site

Saint Petersburg, 197758, Russia

Location

Research Site

Seoul, 03080, South Korea

Location

Research Site

Seoul, 03722, South Korea

Location

Research Site

Seoul, 06351, South Korea

Location

Research Site

Seoul, 5505, South Korea

Location

Research Site

Barcelona, 8035, Spain

Location

Research Site

Córdoba, 14004, Spain

Location

Research Site

Madrid, 28027, Spain

Location

Research Site

Madrid, 28040, Spain

Location

Research Site

Madrid, 28041, Spain

Location

Research Site

Madrid, 28046, Spain

Location

Research Site

Valencia, 46014, Spain

Location

Research Site

Taichung, 40705, Taiwan

Location

Research Site

Tainan, 736, Taiwan

Location

Research Site

Taipei, 100, Taiwan

Location

Research Site

Taipei, 10449, Taiwan

Location

Research Site

Taipei, 11217, Taiwan

Location

Research Site

Taoyuan District, 333, Taiwan

Location

Research Site

Bangkok, 10210, Thailand

Location

Research Site

Bangkok, 10330, Thailand

Location

Research Site

Bangkok, 10400, Thailand

Location

Research Site

Chiang Mai, 50200, Thailand

Location

Research Site

Hat Yai, 90110, Thailand

Location

Research Site

Khon Kaen, 40002, Thailand

Location

Research Site

Muang, 50200, Thailand

Location

Research Site

Ongkharak, 26120, Thailand

Location

Research Site

London, SW2 6JJ, United Kingdom

Location

Research Site

Manchester, M20 4BX, United Kingdom

Location

Research Site

Sutton, SM2 5PT, United Kingdom

Location

Related Publications (2)

  • Oaknin A, Lee JY, Makker V, Oh DY, Banerjee S, Gonzalez-Martin A, Jung KH, Lugowska I, Manso L, Manzano A, Melichar B, Siena S, Stroyakovskiy D, Fielding A, Puvvada S, Smith A, Meric-Bernstam F. Efficacy of Trastuzumab Deruxtecan in HER2-Expressing Solid Tumors by Enrollment HER2 IHC Status: Post Hoc Analysis of DESTINY-PanTumor02. Adv Ther. 2024 Nov;41(11):4125-4139. doi: 10.1007/s12325-024-02975-x. Epub 2024 Sep 11.

  • Meric-Bernstam F, Makker V, Oaknin A, Oh DY, Banerjee S, Gonzalez-Martin A, Jung KH, Lugowska I, Manso L, Manzano A, Melichar B, Siena S, Stroyakovskiy D, Fielding A, Ma Y, Puvvada S, Shire N, Lee JY. Efficacy and Safety of Trastuzumab Deruxtecan in Patients With HER2-Expressing Solid Tumors: Primary Results From the DESTINY-PanTumor02 Phase II Trial. J Clin Oncol. 2024 Jan 1;42(1):47-58. doi: 10.1200/JCO.23.02005. Epub 2023 Oct 23.

MeSH Terms

Conditions

Pancreatic NeoplasmsColorectal Neoplasms

Interventions

trastuzumab deruxtecan

Condition Hierarchy (Ancestors)

Digestive System NeoplasmsNeoplasms by SiteNeoplasmsEndocrine Gland NeoplasmsDigestive System DiseasesPancreatic DiseasesEndocrine System DiseasesIntestinal NeoplasmsGastrointestinal NeoplasmsGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal Diseases

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Masking Details
This study is Open-Label Study.
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: This study will consist of Part 1 which includes 7 cohorts of: urothelial bladder cancer, biliary tract cancer, cervical cancer, endometrial cancer, ovarian cancer, pancreatic cancer, and rare tumors; and Part 2 which includes 5 cohorts A to E of: A) any tumor type that is HER2 IHC 3+ (excluding breast, gastric cancer, and colorectal cancer), B) any tumor type that is HER2 IHC 2+/ISH+ (excluding breast, gastric cancer, and colorectal cancer), C) HER2 IHC 2+ or 1+ endometrial cancer, D) HER2 IHC 2+ or 1+ ovarian cancer, and E) HER2 IHC 2+ or 1+ cervical cancer.
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 20, 2020

First Posted

July 22, 2020

Study Start

August 18, 2020

Primary Completion (Estimated)

March 23, 2027

Study Completion (Estimated)

March 23, 2027

Last Updated

April 9, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal. All request will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure. Yes, indicates that AZ are accepting requests for IPD, but this does not mean all requests will be shared.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA Pharma Data Sharing Principles. For details of our timelines, please rerefer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Access Criteria
When a request has been approved AstraZeneca will provide access to the de-identified individual patient-level data in an approved sponsored tool . Signed Data Sharing Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information. Additionally, all users will need to accept the terms and conditions of the SAS MSE to gain access. For additional details, please review the Disclosure Statements at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
More information

Locations