NCT04429503

Brief Summary

The primary objective of the study is to determine if treatment with high-dose aflibercept (HD) at intervals of 12 or 16 weeks provides non-inferior best corrected visual acuity (BCVA) compared to aflibercept dosed every 8 weeks. The secondary objectives of the study are as follows:

  • To determine the effect of HD vs. aflibercept on anatomic and other visual measures of response
  • To evaluate the safety, immunogenicity, and pharmacokinetics (PK) of aflibercept

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
660

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jun 2020

Typical duration for phase_2

Geographic Reach
8 countries

138 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 26, 2020

Completed
17 days until next milestone

First Posted

Study publicly available on registry

June 12, 2020

Completed
17 days until next milestone

Study Start

First participant enrolled

June 29, 2020

Completed
1.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 30, 2022

Completed
1.5 years until next milestone

Results Posted

Study results publicly available

November 21, 2023

Completed
7 months until next milestone

Study Completion

Last participant's last visit for all outcomes

June 18, 2024

Completed
Last Updated

August 8, 2025

Status Verified

July 1, 2025

Enrollment Period

1.9 years

First QC Date

May 26, 2020

Results QC Date

July 25, 2023

Last Update Submit

July 18, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change From Baseline in Best Corrected Visual Acuity (BCVA) (Early Treatment Diabetic Retinopathy Study [ETDRS] Letter Score) in the Study Eye at Week 48

    Visual function of the study eye was assessed at a distance of 4 meters at every study visit using the Early Treatment Diabetic Retinopathy Study (ETDRS) Best Corrected Visual Acuity (BCVA) letter score. BCVA scale range is 0 (worst) to 100 (best).

    Baseline, Week 48

Secondary Outcomes (16)

  • Percentage of Participants With a ≥2 Step Improvement From Baseline in Diabetic Retinopathy Severity Scale (DRSS) Score at Week 48

    Baseline, Week 48

  • Percentage of Participants Gaining ≥15 Letters in BCVA From Baseline at Week 48

    Baseline, Week 48

  • Percentage of Participants With BCVA ≥69 Letters at Week 48

    At Week 48

  • Percentage of Participants Without Fluid at Foveal Center at Week 48

    At Week 48

  • Change From Baseline in Central Retinal Thickness (CRT) in the Study Eye at Week 48

    Baseline, Week 48

  • +11 more secondary outcomes

Study Arms (3)

aflibercept Q8

ACTIVE COMPARATOR

Administered every 8 weeks after a loading phase

Drug: aflibercept

High-Dose aflibercept Q12

EXPERIMENTAL

Administered every 12 weeks after a loading phase

Drug: High-dose aflibercept

High-Dose aflibercept Q16

EXPERIMENTAL

Administered every 16 weeks after a loading phase

Drug: High-dose aflibercept

Interventions

Intravitreally (IVT) administered as a liquid formulation in a vial

Also known as: EYLEA®, BAY86-5321
aflibercept Q8

Intravitreally (IVT) administered as a liquid formulation in a vial

High-Dose aflibercept Q12High-Dose aflibercept Q16

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diabetic macular edema (DME) with central involvement in the study eye
  • Best corrected visual acuity (BCVA) early treatment diabetic retinopathy study (ETDRS) letter score of 78 to 24 (approximate Snellen equivalent of 20/32 to 20/320) in the study eye with decreased vision determined to be primarily the result of DME
  • Willing and able to comply with clinic visits and study-related procedures
  • Provide informed consent signed by study participant or legally acceptable representative
  • Extension Phase: All randomized patients that complete visit 26, week 96, as long as the patient 1) provides informed consent and 2) no treatment for DME has been given in the study eye other than the randomized study treatment.

You may not qualify if:

  • Evidence of macular edema due to any cause other than diabetes mellitus in either eye
  • Active proliferative diabetic retinopathy in the study eye
  • IVT anti-VEGF treatment (aflibercept, ranibizumab, bevacizumab, brolucizumab, pegaptanib sodium) or panretinal laser photocoagulation (PRP) /macular laser photocoagulation within 12 weeks (84 days) or intraocular or periocular corticosteroids within 16 weeks (112 days) of the screening visit in the study eye
  • Prior IVT investigational agents in either eye (eg, anti-ang-2/anti-VEGF bispecific monoclonal antibodies, gene therapy, etc.) at any time
  • Treatment with ocriplasmin (JETREA®) in the study eye at any time

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (138)

Regeneron Study Site

Phoenix, Arizona, 85021, United States

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Regeneron Study Site

Arcadia, California, 91006, United States

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Regeneron Study Site

Beverly Hills, California, 90211, United States

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Regeneron Study Site

Campbell, California, 95008, United States

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Regeneron Study Site

Encino, California, 91436, United States

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Regeneron Study Site

Fullerton, California, 92835, United States

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Regeneron Study Site

Huntington Beach, California, 92647, United States

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Long Beach, California, 90807, United States

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Regeneron Study Site

Palo Alto, California, 94303, United States

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Pasadena, California, 91107, United States

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Regeneron Study Site

Poway, California, 92064, United States

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Rancho Cordova, California, 95670, United States

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Regeneron Study Site

Riverside, California, 92505, United States

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Regeneron Study Site

Torrance, California, 90509, United States

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Colorado Springs, Colorado, 80909, United States

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Durango, Colorado, 81301, United States

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Lakewood, Colorado, 80228, United States

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Waterford, Connecticut, 06385, United States

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Regeneron Study Site

Clearwater, Florida, 33761, United States

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Regeneron Study Site

Fort Lauderdale, Florida, 33308, United States

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Regeneron Study Site

Fort Myers, Florida, 33912, United States

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Jacksonville, Florida, 32216, United States

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Lakeland, Florida, 33805, United States

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Largo, Florida, 33770, United States

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Melbourne, Florida, 32901, United States

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Miami, Florida, 33126, United States

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Orlando, Florida, 32806, United States

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Pinellas Park, Florida, 33782, United States

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Plantation, Florida, 33324, United States

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St. Petersburg, Florida, 33711, United States

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Stuart, Florida, 34994, United States

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Winter Haven, Florida, 33880, United States

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Regeneron Study Site

Augusta, Georgia, 30909, United States

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Regeneron Study Site 1

Marietta, Georgia, 30060, United States

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Regeneron Study Site 2

Marietta, Georgia, 30060, United States

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Regeneron Study Site

‘Aiea, Hawaii, 96701, United States

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Regeneron Study Site

Oak Forest, Illinois, 60452, United States

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Regeneron Study Site

Springfield, Illinois, 62703, United States

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Springfield, Illinois, 62704, United States

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Carmel, Indiana, 46290, United States

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Shawnee Mission, Kansas, 66204, United States

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Baltimore, Maryland, 21209, United States

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Hagerstown, Maryland, 21740, United States

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Boston, Massachusetts, 02114, United States

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Royal Oak, Michigan, 48073, United States

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Southaven, Mississippi, 38671, United States

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Henderson, Nevada, 89052, United States

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Bloomfield, New Jersey, 07003, United States

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Edison, New Jersey, 08820, United States

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Teaneck, New Jersey, 07666, United States

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Great Neck, New York, 11021, United States

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Liverpool, New York, 13088, United States

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New York, New York, 11221, United States

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Oceanside, New York, 11572, United States

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Shirley, New York, 02114, United States

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Asheville, North Carolina, 28803, United States

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Charlotte, North Carolina, 28210, United States

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Beachwood, Ohio, 44122, United States

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Cincinnati, Ohio, 45202, United States

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Cincinnati, Ohio, 45242, United States

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Cleveland, Ohio, 44130, United States

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Dublin, Ohio, 43016, United States

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Edmond, Oklahoma, 73013, United States

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Tulsa, Oklahoma, 74114, United States

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Portland, Oregon, 97225, United States

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Bethlehem, Pennsylvania, 18017, United States

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Kingston, Pennsylvania, 18704, United States

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Monroeville, Pennsylvania, 15146, United States

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Beaufort, South Carolina, 29902, United States

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Ladson, South Carolina, 29456, United States

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West Columbia, South Carolina, 29169, United States

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Rapid City, South Dakota, 57701, United States

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Germantown, Tennessee, 38138, United States

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Knoxville, Tennessee, 37922, United States

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Nashville, Tennessee, 37203, United States

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Abilene, Texas, 79606, United States

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Bellaire, Texas, 77401, United States

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Regeneron Study Site 2

San Antonio, Texas, 78240, United States

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Regeneron Study Site

The Woodlands, Texas, 77384, United States

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Regeneron Study Site

Willow Park, Texas, 76087, United States

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Regeneron Study Site 1

Salt Lake City, Utah, 84107, United States

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Regeneron Study Site

Fairfax, Virginia, 22031, United States

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Norfolk, Virginia, 23502, United States

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Regeneron Study Site

Morgantown, West Virginia, 26506, United States

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Calgary, Alberta, T2H 0C8, Canada

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Mississauga, Ontario, L4W 1W9, Canada

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North York, Ontario, M3C 0G9, Canada

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Sherbrooke, Quebec, J1G 2V4, Canada

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Pardubice, 530 02, Czechia

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Prague, 100 34, Czechia

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Prague, 128 08, Czechia

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Prague, 150 00, Czechia

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Neubrandenburg, Mecklenburg-Westfalen, 17036, Germany

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Göttingen, North Rhine-Westphalia, 37075, Germany

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Regeneron Study Site

Münster, North Rhine-Westphalia, 48145, Germany

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Regeneron Study Site 1

Pécs, Baranya, H-7621, Hungary

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Regeneron Study Site

Szombathely, Vas County, H-9700, Hungary

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Zalaegerszeg, Zala County, H-8900, Hungary

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Budapest, H-1085, Hungary

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Budapest, H-1106, Hungary

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Budapest, H-1133, Hungary

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Budapest, H-1145, Hungary

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Debrecen, H-4032, Hungary

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Regeneron Study Site

Szeged, H-6720, Hungary

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Regeneron Study Site

Nagakute, Aichi-ken, 480-1195, Japan

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Regeneron Study Site

Nagoya, Aichi-ken, 466-8560, Japan

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Regeneron Study Site

Nagoya, Aichi-ken, 467-8602, Japan

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Regeneron Study Site

Yoshida-Gun, Fukui, 910-1193, Japan

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Regeneron Study Site

Kurume, Fukuoka, 830-0011, Japan

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Regeneron Study Site

Kōriyama, Fukushima, 963-8052, Japan

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Regeneron Study Site

Hakodate, Hokkaido, 041-0851, Japan

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Regeneron Study Site

Kobe, Hyōgo, 650-0017, Japan

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Regeneron Study Site

Mito, Ibaraki, 310-0845, Japan

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Regeneron Study Site

Toride, Ibaraki, 302-0014, Japan

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Regeneron Study Site

Tsuchiura-shi, Ibaraki, 300-0817, Japan

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Regeneron Study Site

Kita-gun, Kagawa-ken, 761-0793, Japan

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Regeneron Study Site

Kawasaki, Kanagawa, 216-8511, Japan

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Regeneron Study Site

Matsumoto, Nagano, 390-8621, Japan

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Regeneron Study Site

Nagasaki, Nagasaki, 852-8501, Japan

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Regeneron Study Site

Kashihara, Nara, 634-8522, Japan

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Regeneron Study Site

Hirakata, Osaka, 573-1191, Japan

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Regeneron Study Site

Tokorozawa, Saitama, 359-8513, Japan

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Regeneron Study Site

Susono, Shizuoka, 410-1102, Japan

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Regeneron Study Site

Shimotsuke-shi, Tochigi, 329-0498, Japan

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Regeneron Study Site

Chiyoda-ku, Tokyo, 101-8309, Japan

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Regeneron Study Site

Hachiōji, Tokyo, 193-0998, Japan

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Regeneron Study Site

Itabashi-ku, Tokyo, 173-0015, Japan

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Regeneron Study Site

Meguro-ku, Tokyo, 152-8902, Japan

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Regeneron Study Site

Ube, Yamaguchi, 755-8505, Japan

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Regeneron Study Site

Fukuoka, 812-0011, Japan

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Regeneron Study Site

Fukuoka, 819-8585, Japan

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Regeneron Study Site

Kagoshima, 890-8520, Japan

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Regeneron Study Site

Osaka, 545-8586, Japan

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Regeneron Study Site

Saitama, 330-8553, Japan

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Regeneron Study Site

Tokushima, 770-8503, Japan

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Regeneron Study Site

Arecibo, 00612, Puerto Rico

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Regeneron Study Site

Sunderland, Tyne and Wear, SR2 9HP, United Kingdom

Location

Regeneron Study Site

London, EC1V 2PD, United Kingdom

Location

Related Publications (3)

  • Suzuma K, Murata T, Shimura M, Yoshida S, Kishino G, Berliner AJ, Chu KW, Reed K, Vitti R, Cheng Y, Voronca D, Bhore R, Leal S, Morgan-Warren P, Schulze A, Schmidt-Ott U, Kobayashi M, Sakamoto T; PHOTON Investigators. Intravitreal aflibercept 8 mg in patients from Japan with diabetic macular edema: 48-week subgroup analysis of the PHOTON trial. Jpn J Ophthalmol. 2025 Dec 26. doi: 10.1007/s10384-025-01271-7. Online ahead of print.

  • Do DV, Wykoff CC, Sivaprasad S, Brown DM, Boyer DS, Sakamoto T, Win P, Joshi S, Salehi-Had H, Seres A, Berliner AJ, Leal S, Vitti R, Chu KW, Reed K, Cheng Y, Bhore R, Bai Z, Schmidt-Ott U, Schmelter T, Schulze A, Hasanbasic Z, Morgan-Warren PJ, Zhang X, Hirshberg B, Yancopoulos GD; PHOTON Investigators. Intravitreal Aflibercept 8 mg for Diabetic Macular Edema: Ninety-Six-Week Results from the Randomized Phase 2/3 PHOTON Trial. Ophthalmology. 2025 Nov 10:S0161-6420(25)00707-9. doi: 10.1016/j.ophtha.2025.10.028. Online ahead of print.

  • Brown DM, Boyer DS, Do DV, Wykoff CC, Sakamoto T, Win P, Joshi S, Salehi-Had H, Seres A, Berliner AJ, Leal S, Vitti R, Chu KW, Reed K, Rao R, Cheng Y, Sun W, Voronca D, Bhore R, Schmidt-Ott U, Schmelter T, Schulze A, Zhang X, Hirshberg B, Yancopoulos GD, Sivaprasad S; PHOTON Investigators. Intravitreal aflibercept 8 mg in diabetic macular oedema (PHOTON): 48-week results from a randomised, double-masked, non-inferiority, phase 2/3 trial. Lancet. 2024 Mar 23;403(10432):1153-1163. doi: 10.1016/S0140-6736(23)02577-1. Epub 2024 Mar 7.

MeSH Terms

Conditions

Diabetes Mellitus, Type 1Diabetes Mellitus, Type 2

Interventions

aflibercept

Condition Hierarchy (Ancestors)

Diabetes MellitusGlucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System DiseasesAutoimmune DiseasesImmune System Diseases

Results Point of Contact

Title
Clinical Trials Administrator
Organization
Regeneron Pharmaceuticals, Inc

Study Officials

  • Clinical Trial Management

    Regeneron Pharmaceuticals

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 26, 2020

First Posted

June 12, 2020

Study Start

June 29, 2020

Primary Completion

May 30, 2022

Study Completion

June 18, 2024

Last Updated

August 8, 2025

Results First Posted

November 21, 2023

Record last verified: 2025-07

Data Sharing

IPD Sharing
Will share

All IPD that underlie results in a publication.

Shared Documents
STUDY PROTOCOL, SAP, ICF, CSR, ANALYTIC CODE
Time Frame
Individual de-identified participant data will be made available once the indication has been approved by a regulatory body, if there is participant consent and there is not a reasonable likelihood of participant re-identification.
Access Criteria
Qualified researchers may request access to study documents (including the clinical study report, study protocol with any amendments, blank case report form, statistical analysis plan) that support the methods and findings reported in a manuscript. Individual de-identified participant data will be made available once the indication has been approved by a regulatory body, if there is participant consent and there is not a reasonable likelihood of participant re-identification.
More information

Locations