NCT04291105

Brief Summary

This is a Phase 2 study designed to determine the preliminary anti-tumor activity and confirm the safety of VV1 in combination with cemiplimab. The study will enroll patients with three distinct separate tumor cohorts. The cancers types are colorectal, head and neck carcinoma, and melanoma that are progressing on CPI treatment.

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
87

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Apr 2020

Longer than P75 for phase_2

Geographic Reach
2 countries

27 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 25, 2020

Completed
6 days until next milestone

First Posted

Study publicly available on registry

March 2, 2020

Completed
2 months until next milestone

Study Start

First participant enrolled

April 24, 2020

Completed
5.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2025

Completed
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2025

Completed
Last Updated

March 26, 2025

Status Verified

March 1, 2025

Enrollment Period

5.1 years

First QC Date

February 25, 2020

Last Update Submit

March 25, 2025

Conditions

Keywords

Solid Tumor

Outcome Measures

Primary Outcomes (1)

  • Objective response rate (ORR) per imaging assessment

    Percentage of participants with objective response is assessed every six weeks from Cycle 1 Day 1 through disease progression, by investigator review based on RECIST version 1.1

    within 24 months

Secondary Outcomes (3)

  • Incidence of Treatment-Emergent Adverse Events assessed by CTCAE v5.0

    within 24 months

  • Serum concentration time

    within 24 months

  • To investigate the pharmacodynamics (PD) of VV1 by measuring serum IFNβ

    within 24 months

Study Arms (3)

Melanoma intratumoral

EXPERIMENTAL

Melanoma, IT VV1 + IV cemiplimab Patients will receive both treatments on Day 1 and every 3 weeks thereafter until lack of clinical benefit or limiting toxicity. VV1 or cemiplimab can continue after the first dose in combination or as a single agent treatment in subsequent doses.

Biological: VV1Biological: Cemiplimab

Head and Neck SCC intratumoral

EXPERIMENTAL

HNSCC, IT VV1 + IV cemiplimab, Patients will receive both treatments on Day 1 and every 3 weeks thereafter until lack of clinical benefit or limiting toxicity. VV1 or cemiplimab can continue after the first dose in combination or as a single agent treatment in subsequent doses.

Biological: VV1Biological: Cemiplimab

Colo-rectal Carcinoma intratumoral (Arm closed)

EXPERIMENTAL

(CLOSED) IT VV1 + IV cemiplimab, Patients will receive both treatments on Day 1 and every 3 weeks thereafter until lack of clinical benefit or limiting toxicity. VV1 or cemiplimab can continue after the first dose in combination or as a single agent treatment in subsequent doses.

Biological: VV1Biological: Cemiplimab

Interventions

VV1BIOLOGICAL

VV1 is to be administered on Day 1 and every 3 weeks as long as there is clinical benefit

Also known as: VSV-IFNβ-NIS, Voyager V1, VV1
Colo-rectal Carcinoma intratumoral (Arm closed)Head and Neck SCC intratumoralMelanoma intratumoral
CemiplimabBIOLOGICAL

Cemiplimab should be given on Day 8 of Cycle 1 (28 days) and then Day 1 of each subsequent 21-day cycle.

Also known as: Libtayo
Colo-rectal Carcinoma intratumoral (Arm closed)Head and Neck SCC intratumoralMelanoma intratumoral

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age ≥18 years on day of signing informed consent.
  • Specific by tumor cohorts:
  • a. For the HSNCC cohort, histologically confirmed diagnosis of advanced and/or metastatic HSNCC suitable for first line immunotherapy.
  • i. HPV+ and HPV- patients are allowed.
  • ii. Primary tumor locations of oropharynx, oral cavity, hypopharynx, or larynx. Participants may not have a primary tumor site of nasopharynx (any histology) or salivary gland tumors.
  • iii. PD-L1 status ≥ 1% per local CPS score. Samples should be provided to central lab for post-hoc centralized testing.
  • iv. At least 12 months between last dose of prior adjuvant therapy and date of relapse diagnosis (if given). For the purposes of this protocol, "prior adjuvant therapy" only applies to full dose systemic chemotherapy (such as pre-operative systemic induction chemotherapy), but does not include radiation + surgery, or radiation + low or partial dose platinum radiosensitization. There is no time limit (washout) between the end of any prior radiation/ chemoradiation and the start of study drug v. No prior anti-PD-(L)1 treatment for HNSCC.
  • b. For the melanoma cohorts, histologically confirmed diagnosis of advanced and/or metastatic cutaneous melanoma for which no existing options are considered to provide clinical benefit.
  • i. Best response of uPR, SD or PD to an anti-PD-(L)1-containing regimen.
  • ii. Prior anti-PD-(L)1 therapy must have lasted ≥ 12 weeks.
  • iii. Radiological progression was demonstrated during or after therapy with a PD-(L)1 immune CPI (only one prior line of PD-(L)1 therapy is permitted.
  • iv. If patient received anti-PD-1 as prior adjuvant therapy, patient should have relapsed during therapy or within the subsequent 6 months after last dose. Note: Progression on ipilimumab is not required.
  • v. Patients with BRAF V600-positive tumor(s) should have received prior treatment with a BRAF inhibitor (alone or in combination with a MEK inhibitor) in addition to treatment with an anti-PD-1 or to have declined targeted therapy. Note: Patients with BRAF V600-positive tumors with no clinically significant tumor-related symptoms nor evidence of rapidly progressive disease are not required to be treated with a BRAF inhibitor (alone or in combination with a MEK inhibitor) based on investigator's decision
  • c. For the CRC cohort, a histologically confirmed diagnosis of advanced and/or metastatic CRC.
  • i. Received or are not eligible for standard of care fluoropyrimidine(s), oxaliplatin, irinotecan, anti-VEGF and EGFR-targeted therapies.
  • +8 more criteria

You may not qualify if:

  • Availability of and patient acceptance of an alternative curative therapeutic option.
  • Patients with tumor lesion(s) \> 5cm in diameter.
  • Recent or ongoing serious infection, including any active Grade 3 or higher per the NCI CTCAE, v5.0 viral, bacterial, or fungal infection within 2 weeks of registration.
  • Patients who have a diagnosis of ocular, mucosal or acral melanoma.
  • Known seropositivity for and with active infection with HIV.
  • Seropositive for and with evidence of active viral infection with HBV.
  • Seropositive for and with active viral infection with HCV.
  • Known history of active or latent TB.
  • Any concomitant serious health condition, which, in the opinion of the investigator, would place the patient at undue risk from the study, including uncontrolled hypertension and/or diabetes, clinically significant pulmonary disease (e.g., chronic obstructive pulmonary disease requiring hospitalization within 3 months) or neurological disorder (e.g., seizure disorder active within 3 months).
  • Prior therapy within the following timeframe before the planned start of study treatment as follows:
  • Small molecule inhibitors, and/or other investigational agent: ≤ 2 weeks or 5 half-lives, whichever is shorter.
  • Chemotherapy, other monoclonal antibodies, antibody-drug conjugates, or other similar experimental therapies: ≤ 3 weeks or 5 half-lives, whichever is shorter.
  • Radioimmunoconjugates or other similar experimental therapies ≤ 6 weeks or 5 half-lives, whichever is shorter.
  • NYHA classification III or IV, known symptomatic coronary artery disease, or symptoms of coronary artery disease on systems review, or known cardiac arrhythmias (atrial fibrillation or SVT).
  • Any known or suspected active organ-threatening autoimmune disease, such as inflammatory bowel disease, autoimmune hepatitis, lupus, or pneumonitis, with the exception of hypothyroidism and type 1 diabetes that are controlled with treatment
  • +7 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (27)

Mayo Clinical

Phoenix, Arizona, 85054, United States

WITHDRAWN

City of Hope Medical Center

Durate, California, 91010, United States

WITHDRAWN

USC Norris Comprehensive Cancer Center

Los Angeles, California, 90033, United States

WITHDRAWN

HOAG Memorial Hospital Presbyterian

Newport Beach, California, 92663, United States

WITHDRAWN

Saint John's Health Center - John Wayne Cancer Institute (JWCI)

Santa Monica, California, 90404, United States

TERMINATED

Stanford Health Care

Stanford, California, 94305, United States

WITHDRAWN

Yale University

New Haven, Connecticut, 06520-8032, United States

RECRUITING

Georgetown University Medical Center

Washington D.C., District of Columbia, 20007, United States

WITHDRAWN

Mayo Clinical

Jacksonville, Florida, 32224, United States

WITHDRAWN

University of Miami

Miami, Florida, 33136, United States

COMPLETED

Ochsner Clinic Foundation

New Orleans, Louisiana, 70121, United States

RECRUITING

Massachusetts General Hospital Cancer Center

Boston, Massachusetts, 02114, United States

WITHDRAWN

Masonic Cancer Center, University of Minnesota

Minneapolis, Minnesota, 55455, United States

WITHDRAWN

Mayo Clinic

Rochester, Minnesota, 55905, United States

RECRUITING

Billings Clinic Montana Cancer Consortium

Billings, Montana, 59101, United States

TERMINATED

Atlantic Health

Morristown, New Jersey, 07960, United States

WITHDRAWN

Rutgers Cancer Institute of New Jersey

New Brunswick, New Jersey, 08901, United States

WITHDRAWN

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

RECRUITING

University of Cincinnati Medical Center

Cincinnati, Ohio, 45219, United States

RECRUITING

Ohio State University

Columbus, Ohio, 43210, United States

WITHDRAWN

UPMC

Pittsburgh, Pennsylvania, 15213, United States

WITHDRAWN

Sanford Cancer Center

Sioux Falls, South Dakota, 57104, United States

RECRUITING

UT Health San Antonio MD Anderson Cancer Center

San Antonio, Texas, 78229, United States

WITHDRAWN

Hospital Sao Rafael

Salvador, BR, 41253-190, Brazil

RECRUITING

INCA

Rio de Janeiro, Rio de Janeiro, 20231-050, Brazil

RECRUITING

Hospital Moinhos de Vento

Porto Alegre, Rio Grande do Sul, 90035-000, Brazil

RECRUITING

Hospital de Amor de Barretos

Barretos, São Paulo, 14.784-400, Brazil

ACTIVE NOT RECRUITING

MeSH Terms

Conditions

MelanomaSquamous Cell Carcinoma of Head and NeckColonic Neoplasms

Interventions

cemiplimab

Condition Hierarchy (Ancestors)

Neuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Nerve TissueNevi and MelanomasSkin NeoplasmsNeoplasms by SiteSkin DiseasesSkin and Connective Tissue DiseasesCarcinoma, Squamous CellCarcinomaNeoplasms, Glandular and EpithelialHead and Neck NeoplasmsColorectal NeoplasmsIntestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal Diseases

Study Officials

  • Alice Bexon, MD

    CMO

    STUDY CHAIR
  • Stephen J Russell, MD, Ph.D.

    Clinical Lead

    STUDY DIRECTOR

Central Study Contacts

Jennifer boughton

CONTACT

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 25, 2020

First Posted

March 2, 2020

Study Start

April 24, 2020

Primary Completion

June 1, 2025

Study Completion

December 1, 2025

Last Updated

March 26, 2025

Record last verified: 2025-03

Data Sharing

IPD Sharing
Will not share

Locations