NCT04027309

Brief Summary

Activating mutations in the fms like tyrosine kinase 3 (FLT3) gene are observed in approximately 30% of patients with newly diagnosed acute myeloid leukemia (AML). Addition of the multitargeted kinase inhibitor midostaurin to standard chemotherapy prolongs event-free survival (EFS) and overall survival (OS) in patients with a FLT3 mutation. Gilteritinib is a more potent and more specific inhibitor of mutant FLT3 in comparison to midostaurin and has shown promising clinical activity in AML.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
777

participants targeted

Target at P75+ for phase_3

Timeline
86mo left

Started Dec 2019

Longer than P75 for phase_3

Geographic Reach
12 countries

169 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress47%
Dec 2019Jun 2033

First Submitted

Initial submission to the registry

July 18, 2019

Completed
1 day until next milestone

First Posted

Study publicly available on registry

July 19, 2019

Completed
5 months until next milestone

Study Start

First participant enrolled

December 20, 2019

Completed
5.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2025

Completed
7.7 years until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2033

Expected
Last Updated

December 17, 2024

Status Verified

September 1, 2024

Enrollment Period

5.8 years

First QC Date

July 18, 2019

Last Update Submit

December 12, 2024

Conditions

Outcome Measures

Primary Outcomes (1)

  • Overal survival (OS)

    Overall survival (OS), defined as the time from date of randomization to the date of death due to any cause. Patients still alive or lost to follow up will be censored at the time they were last known to be alive.

    Approximately up to 70 months following first patient enrolment

Secondary Outcomes (14)

  • Event-free survival (EFS)

    Approximately up to 70 months following first patient enrolment

  • CR rate after remission induction

    Approximately up to 70 months following first patient enrolment

  • EFS with modified CR (mEFS)

    Approximately up to 70 months following first patient enrolment

  • CR and CRi rates after induction cycle 1 and after induction cycle 2

    Approximately up to 70 months following first patient enrolment

  • Relapse-free survival (RFS) after CR

    Approximately up to 70 months following first patient enrolment

  • +9 more secondary outcomes

Study Arms (2)

Arm A (Midostaurin)

ACTIVE COMPARATOR

Midostaurin (50 mg BID PO) - Cycle 1 (day 8-21), Cycle 2 (day 8-21), Consolidation (only during chemo consolidation (day 8-21 - with max of 3 cycles), Maintenance (day 1-365)

Drug: Midostaurin

Arm B (Gilteritinib)

EXPERIMENTAL

Gilteritinib (120 mg QD PO) - Cycle 1 (day 8-21), Cycle 2 (day 8-21), Consolidation (only during chemo consolidation (day 8-21 - with max of 3 cycles), Maintenance (day 1-365)

Drug: Gilteritinib

Interventions

Patients with a FLT3 mutation w ill be randomized to receive either the investigational drug gilteritinib or midostaurin given sequentially to standard induction and consolidation chemotherapy. After completing induction and consolidation treatment, patients who achieve CR/CRi/MLFS will receive maintenance therapy with gilteritinib or midostaurin

Also known as: ASP2215
Arm B (Gilteritinib)

Patients with a FLT3 mutation w ill be randomized to receive either the investigational drug gilteritinib or midostaurin given sequentially to standard induction and consolidation chemotherapy. After completing induction and consolidation treatment, patients who achieve CR/CRi/MLFS will receive maintenance therapy with gilteritinib or midostaurin

Also known as: Rydapt
Arm A (Midostaurin)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age ≥18 years
  • Newly diagnosed AML or MDS with excess of blasts-2 (EB2) defined according to WHO criteria (appendix A), with centrally documented FLT3 gene mutation (either TKD or ITD or both). AML may be secondary to prior hematological disorders, including MDS, and/or therapy-related. Patients may have had previous treatment with erythropoiesis stimulating agents (ESA) or hypomethylating agents (HMAs) for an antecedent phase of MDS. ESA and HMAs have to be stopped at least four weeks before registration.
  • FLT3 mutation as assessed by DNA fragment analysis PCR for FLT3-ITD and FLT3-TKD mutation. Positivity is defined as a FLT3-ITD or FLT3-TKD / FLT3-WT ratio of ≥ 0.05 (5%).
  • Considered to be eligible for intensive chemotherapy
  • Patient is suitable for oral administration of study drug
  • WHO/ECOG performance status ≤ 2
  • Adequate hepatic function as evidenced by
  • Serum total bilirubin ≤ 2.5 × upper limit of normal (ULN) unless considered due to leukemic involvement following written approval by the (co) Principal Investigator
  • Aspartate aminotransferase (AST), alanine aminotransferase (ALT), and alkaline phosphatase (ALP) ≤ 3.0 × ULN, unless considered due to leukemic involvement following written approval by the (co) Principal Investigator
  • Adequate renal function as defined by creatinine clearance \> 40 mL/min based on the Cockroft-Gault glomerular filtration rate (GFR)
  • Written informed consent
  • Patient is capable of giving informed consent
  • Female patient must either:
  • Be of nonchildbearing potential:
  • Postmenopausal (defined as at least 1 year without any menses) prior to screening, or
  • +18 more criteria

You may not qualify if:

  • Prior chemotherapy for AML or MDS-EB2, including prior treatment with hypomethylating agents. Hydroxyurea is allowed for the control of peripheral leukemic blasts in patients with leukocytosis (e.g., white blood cell \[WBC\] counts \> 30 x 10\^9/L)
  • Acute promyelocytic leukemia (APL) with PML-RARA or one of the other pathognomonic variant fusion genes/chromosome translocations
  • Blast crisis after CML
  • Known or suspected hypersensitivity to midostaurin or gilteritinib and/or any excipients
  • Patient requires treatment with concomitant drugs that are strong inducers of cytochrome P450 (CYP) 3A
  • Breast feeding at start of study treatment
  • Active infection, including hepatitis B or C or HIV infection that is uncontrolled at randomization. An infection controlled with an approved or closely monitored antibiotic/antiviral/antifungal treatment is allowed.
  • Patients with a currently active second malignancy. Patients are not considered to have a currently active malignancy if they have completed therapy and are considered by their physician to be at less than 30% risk of relapse within one year. However, patients with the following history/concurrent conditions are allowed:
  • Basal or squamous cell carcinoma of the skin;
  • Carcinoma in situ of the cervix;
  • Carcinoma in situ of the breast;
  • Incidental histologic finding of prostate cancer
  • Significant active cardiac disease within 6 months prior to the start of study treatment, including:
  • New York Heart Association (NYHA) Class III or IV congestive heart failure;
  • Myocardial infarction;
  • +9 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (193)

AU-Adelaide-FLINDERS

Adelaide, Australia

Location

AU-Adelaide-RAH

Adelaide, Australia

Location

AU-Brisbane-PAH

Brisbane, Australia

Location

AU-Brisbane-RBWH

Brisbane, Australia

Location

AU-Camperdown-RPA

Camperdown, Australia

Location

AU-Douglas-TOWNSVILLE

Douglas, Australia

Location

AU-Geelong VIC-BARWONHEALTH

Geelong, Australia

Location

AU-Gosford NSW-GOSFORDHOSPITAL

Gosford, Australia

Location

AU-Hobart TAS-RHOBART

Hobart, Australia

Location

AU-Melbourne-ALFRED

Melbourne, Australia

Location

AU-Melbourne-AUSTIN

Melbourne, Australia

Location

AU-Melbourne-BOXHILL

Melbourne, Australia

Location

AU-Melbourne-MONASH

Melbourne, Australia

Location

AU-Melbourne-RMELBOURNE

Melbourne, Australia

Location

AU-Melbourne-SVHM

Melbourne, Australia

Location

AU-Perth-FSH

Perth, Australia

Location

AU-Perth-RPH

Perth, Australia

Location

AU-Perth-SCGH

Perth, Australia

Location

AU-Sydney-CONCORD

Sydney, Australia

Location

AU-Sydney-NEPEAN

Sydney, Australia

Location

AU-Sydney-RNSH

Sydney, Australia

Location

AU-Sydney-WSAH

Sydney, Australia

Location

St George Hospital

Sydney, Australia

Location

AU-Waratah-CALVARYMATER

Waratah, Australia

Location

AT-Graz-MEDUNIGRAZ

Graz, Austria

Location

AT-Innsbruck-IMED

Innsbruck, Austria

Location

AT-Linz-KEPLER

Linz, Austria

Location

AT-Linz-ORDENSKLINIKUM

Linz, Austria

Location

AT-Salzburg-SALK

Salzburg, Austria

Location

AT-Vienna-HANUSCH

Vienna, Austria

Location

BE-Antwerpen-ZNASTUIVENBERG

Antwerp, Belgium

Location

BE-Brugge-AZBRUGGE

Bruges, Belgium

Location

BE-Brussel-BORDET

Brussels, Belgium

Location

BE-Bruxelles-STLUC

Brussels, Belgium

Location

BE-Gent-UZGENT

Ghent, Belgium

Location

BE-Haine-Saint-Paul-JOLIMONT

Haine-Saint-Paul, Belgium

Location

BE-Hasselt-VIRGAJESSE

Hasselt, Belgium

Location

BE-Leuven-UZLEUVEN

Leuven, Belgium

Location

BE-Liege-CHRCITADELLE

Liège, Belgium

Location

BE-Liege-CHULIEGE

Liège, Belgium

Location

BE-Mons-AMBROISE

Mons, Belgium

Location

BE-Roeselare-AZDELTA

Roeselare, Belgium

Location

BE-Yvoir-MONTGODINNE

Yvoir, Belgium

Location

FI-Helsinki-HUS

Helsinki, Finland

Location

FI-Tampere-TAYS

Tampere, Finland

Location

FR-Amiens-CHUAMIENS

Amiens, France

Location

FR-Angers-CHUANGERS

Angers, France

Location

FR-Argenteuil-CHARGENTEUIL

Argenteuil, France

Location

FR-Bayonne-CHCOTEBASQUE

Bayonne, France

Location

FR-Besançon Cedex-JEANMINJOZ

Besançon, France

Location

FR-Bobigny-AVICENNE

Bobigny, France

Location

FR-Le Chesnay cedex-CHVERSAILLES

Chesnay, France

Location

FR-Clamart-HIAPERCY

Clamart, France

Location

FR-Clermont-Ferrand-ESTAING

Clermont-Ferrand, France

Location

FR-Grenoble cedex 9-CHUGRENOBLE

Grenoble, France

Location

FR-Lille-CHULILLE

Lille, France

Location

FR-Limoges-CHULIMOGES

Limoges, France

Location

FR-Lyon Pierre Benite cedex-LYONSUD

Lyon, France

Location

FR-Lyon-LEONBERARD

Lyon, France

Location

FR-Marseille-IPC

Marseille, France

Location

FR-Montpellier-STELOI

Montpellier, France

Location

FR-Nantes-CHUNANTES

Nantes, France

Location

FR-Nice-CAL

Nice, France

Location

FR-Nice-LARCHET

Nice, France

Location

FR-Paris cedex 10-SAINTLOUIS

Paris, France

Location

FR-Paris cedex 15-NECKER

Paris, France

Location

FR-Pessac Cedex-CHUBORDEAUX

Pessac, France

Location

FR-Poitiers-CHUPOITERS

Poitiers, France

Location

FR-Reims-CHREIMS

Reims, France

Location

FR-Rennes cedex 9-CHURENNES

Rennes, France

Location

FR-Rouen cedex-BECQUEREL

Rouen, France

Location

FR-Saint-Priest-en-Jarez-ICLOIRE

Saint-Priest-en-Jarez, France

Location

FR-Strasbourg cedex-HAUTEPIERRE

Strasbourg, France

Location

FR-Toulouse-CHUTOULOUSE

Toulouse, France

Location

FR-Tours cedex-BRETONNEAU

Tours, France

Location

FR-Vandoeuvre Les Nancy-CHRUNANCY

Vandœuvre-lès-Nancy, France

Location

FR-Villejuif-GUSTAVEROUSSY

Villejuif, France

Location

DE-Aschaffenburg-KLINIKUMAB

Aschaffenburg, Germany

Location

DE-Bad Saarow-HELIOSBADSAAROW

Bad Saarow, Germany

Location

DE-Berlin-CAMPUSBENFRANKLIN

Berlin, Germany

Location

DE-Berlin-CAMPUSMITTE

Berlin, Germany

Location

DE-Berlin-CAMPUSVIRCHOW

Berlin, Germany

Location

DE-Berlin-VIVANTESNEUKOLLN

Berlin, Germany

Location

DE-Berlin-VIVANTESURBAN

Berlin, Germany

Location

DE-Bochum-RUB

Bochum, Germany

Location

DE-Bonn-UNIBONN

Bonn, Germany

Location

DE-Braunschweig-KLINIKUMBRAUNSCHWEIG

Braunschweig, Germany

Location

DE-Bremen-KBM

Bremen, Germany

Location

DE-Darmstadt-KLINIKUMDARMSTADT

Darmstadt, Germany

Location

DE-Dortmund-JOHODORTMUND

Dortmund, Germany

Location

DE-Düsseldorf-MEDUNIDUESSELDORF

Düsseldorf, Germany

Location

DE-Essen-KEM

Essen, Germany

Location

DE-Esslingen-KLINIKUMESSLINGEN

Esslingen am Neckar, Germany

Location

DE-Flensburg-MALTESER

Flensburg, Germany

Location

DE-Frankfurt-KLINIKUMFRANKFURT

Frankfurt, Germany

Location

DE-Giessen-UKGM

Giessen, Germany

Location

DE-Goch-KKLE

Goch, Germany

Location

DE-Greifswald-UNIGREIFSWALD

Greifswald, Germany

Location

DE-Hamburg-ASKLEPIOSSTGEORG

Hamburg, Germany

Location

DE-Hamburg-ASKLEPIOS

Hamburg, Germany

Location

DE-Hamburg-UKE

Hamburg, Germany

Location

DE-Hamm-EVKHAMM

Hamm, Germany

Location

DE-Hanau-KLINIKUMHANAU

Hanau, Germany

Location

DE-Hannover-MHHANNOVER

Hanover, Germany

Location

DE-Hannover-SILOAHKRH

Hanover, Germany

Location

DE-Heilbronn-SLK

Heilbronn, Germany

Location

DE-Herne-MARIENHOSPITALHERNE

Herne, Germany

Location

DE-Homburg-UNIKLINIKSAARLAND

Homburg, Germany

Location

DE-Kaiserslautern-WESTPFALZ

Kaiserslautern, Germany

Location

DE-Karlsruhe-KLINIKUMKARLSRUHE

Karlsruhe, Germany

Location

DE-Lemgo-KLINIKUMLIPPE

Lemgo, Germany

Location

DE-Ludwigshafen-KLILU

Ludwigshafen, Germany

Location

DE-Lübeck-UKSHLUBECK

Lübeck, Germany

Location

DE-Luedenscheid-KLINIKUMLUEDENSCHEID

Lüdenscheid, Germany

Location

DE-Magdeburg-OVGU

Magdeburg, Germany

Location

DE-Mainz-UNIMEDIZINMAINZ

Mainz, Germany

Location

DE-Meschede-HOCHSAUERLAND

Meschede, Germany

Location

DE-Minden-MUEHLENKREISKLINKEN

Minden, Germany

Location

DE-München-IRZTUM

München, Germany

Location

DE-Offenburg-ORTENAUKLINIKUM

Offenburg, Germany

Location

DE-Oldenburg-KLINIKUMOLDENBURG

Oldenburg, Germany

Location

DE-Passau-KLINIKUMPASSAU

Passau, Germany

Location

DE-Regensburg-UKR

Regensburg, Germany

Location

DE-Saarbrücken-CARITASKLINIKUM

Saarbrücken, Germany

Location

DE-Stuttgart-DIAKSTUTTGART

Stuttgart, Germany

Location

DE-Stuttgart-KLINIKUMSTUTTGART

Stuttgart, Germany

Location

DE-Trier-MUTTERHAUS

Trier, Germany

Location

DE-Tübingen-MEDUNITUEBINGEN

Tübingen, Germany

Location

DE-Ulm-UNIKLINKULM

Ulm, Germany

Location

DE-Villingen-Schwenningen-SBKVS

Villingen-Schwenningen, Germany

Location

DE-Wuppertal-HELIOSGESUNDHEIT

Wuppertal, Germany

Location

IE-Cork-CUH

Cork, Ireland

Location

IE-Dublin 24-TUH

Dublin, Ireland

Location

IE-Dublin 4-SVUH

Dublin, Ireland

Location

IE-Dublin 7-MATER

Dublin, Ireland

Location

IE-Dublin 8-STJAMES

Dublin, Ireland

Location

IE-Dublin 9-BEAUMONT

Dublin, Ireland

Location

IE-Galway-UHGALWAY

Galway, Ireland

Location

IE-Co. Limerick-UHL

Limerick, Ireland

Location

LT-Vilnius-SANTA

Vilnius, Lithuania

Location

NL-Den Bosch-JBZ

's-Hertogenbosch, Netherlands

Location

NL-Amersfoort-MEANDERMC

Amersfoort, Netherlands

Location

NL-Amsterdam-AMC

Amsterdam, Netherlands

Location

NL-Amsterdam-OLVG

Amsterdam, Netherlands

Location

NL-Amsterdam-VUMC

Amsterdam, Netherlands

Location

NL-Arnhem-RIJNSTATE

Arnhem, Netherlands

Location

NL-Breda-AMPHIA

Breda, Netherlands

Location

NL-Delft-RDGG

Delft, Netherlands

Location

NL-Dordrecht-ASZ

Dordrecht, Netherlands

Location

NL-Eindhoven-MAXIMAMC

Eindhoven, Netherlands

Location

NL-Enschede-MST

Enschede, Netherlands

Location

NL-Groningen-UMCG

Groningen, Netherlands

Location

NL-Leeuwarden-MCL

Leeuwarden, Netherlands

Location

NL-Leiden-LUMC

Leiden, Netherlands

Location

NL-Maastricht-MUMC

Maastricht, Netherlands

Location

NL-Nieuwegein-ANTONIUS

Nieuwegein, Netherlands

Location

NL-Nijmegen-RADBOUDUMC

Nijmegen, Netherlands

Location

NL-Rotterdam-ERASMUSMC

Rotterdam, Netherlands

Location

NL-Den Haag-HAGA

The Hague, Netherlands

Location

NL-Utrecht-UMCUTRECHT

Utrecht, Netherlands

Location

NL-Zwolle-ISALA

Zwolle, Netherlands

Location

NO-Bergen-HELSEBERGEN

Bergen, Norway

Location

NO-Oslo-OSLOUH

Oslo, Norway

Location

NO-Stavanger-HELSESTAVANGER

Stavanger, Norway

Location

NO-Tromsø-NORTHNOORWEGEN

Tromsø, Norway

Location

NO-Trondheim-STOLAV

Trondheim, Norway

Location

ES-Barcelona-CLINICUB

Barcelona, Spain

Location

ES-Barcelona-GERMANTRIALS

Barcelona, Spain

Location

ES-Barcelona-ICODURANREYNALS

Barcelona, Spain

Location

ES-Barcelona-MUTUATERRASSA

Barcelona, Spain

Location

ES-Barcelona-PARCDESALUTMAR

Barcelona, Spain

Location

ES-Barcelona-SANTPAU

Barcelona, Spain

Location

ES-Barcelona-VHEBRON

Barcelona, Spain

Location

ES-Girona-ICSTRUETA

Girona, Spain

Location

ES-Lleida-ICSVILANOVA

Lleida, Spain

Location

ES-Madrid-CSGREGORIOMARANON

Madrid, Spain

Location

ES-Palma-HSLL

Palma, Spain

Location

ES-Palma-SSIB

Palma, Spain

Location

ES-Tarragona-JOAN

Tarragona, Spain

Location

ES-Valencia-MALVARROSA

Valencia, Spain

Location

SE-Lund-SUH

Lund, Sweden

Location

SE-Stockholm-KAROLINSKAHUDDINGE

Stockholm, Sweden

Location

SE-Uppsala-UPPSALAUH

Uppsala, Sweden

Location

CH-Aarau-KSA

Aarau, Switzerland

Location

CH-Basel-USB

Basel, Switzerland

Location

CH-Bellinzona-IOSI

Bellinzona, Switzerland

Location

CH-Bern-INSEL

Bern, Switzerland

Location

CH-Fribourg-HFR

Fribourg, Switzerland

Location

CH-Geneve (14)-HCUGE

Geneva, Switzerland

Location

CH-Lausanne-CHUV

Lausanne, Switzerland

Location

CH-Luzern-LUKS

Lucerne, Switzerland

Location

CH-St. Gallen-KSSG

Sankt Gallen, Switzerland

Location

CH-Zürich-USZ

Zurich, Switzerland

Location

Related Links

MeSH Terms

Conditions

Leukemia, Myeloid, Acute

Interventions

gilteritinibmidostaurin

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic Diseases

Study Officials

  • M. Raaijmakers, Prof. Dr.

    Erasmus MC / HOVON

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 18, 2019

First Posted

July 19, 2019

Study Start

December 20, 2019

Primary Completion

October 1, 2025

Study Completion (Estimated)

June 1, 2033

Last Updated

December 17, 2024

Record last verified: 2024-09

Data Sharing

IPD Sharing
Will not share

Locations