NCT03814187

Brief Summary

The purpose of this extension study was to evaluate the efficacy, safety, and tolerability of long-term dosing of Inclisiran. The study was a global multicenter study.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
3,275

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Apr 2019

Typical duration for phase_3

Geographic Reach
13 countries

238 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 17, 2019

Completed
6 days until next milestone

First Posted

Study publicly available on registry

January 23, 2019

Completed
3 months until next milestone

Study Start

First participant enrolled

April 16, 2019

Completed
3.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 13, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 13, 2023

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

March 6, 2024

Completed
Last Updated

March 6, 2024

Status Verified

February 1, 2024

Enrollment Period

3.8 years

First QC Date

January 17, 2019

Results QC Date

February 9, 2024

Last Update Submit

February 9, 2024

Conditions

Keywords

Inclisiran sodiumASCVDLDL-CHeFHHoFH

Outcome Measures

Primary Outcomes (2)

  • Proportion of Subjects Achieving Global Lipid Targets for Their Level of ASCVD Risk

    The primary objective of the study is to evaluate the effect of inclisiran treatment on the proportion of subjects achieving prespecified LDL-C targets at end of study (EOS). Target is \<70 mg/dL for atherosclerotic cardiovascular disease (ASCVD) subjects and \<100 mg/dL for ASCVD risk equivalent subjects. Risk equivalent subjects are defined as either type 2 diabetes, familial hypercholesterolemia or a 10-year risk of a cardiovascular event ≥20% as assessed by the Framingham Risk Score or equivalent; without a medical history of coronary heart disease , cerebrovascular disease or peripheral artery disease.

    From ORION-8 Day 1 to the end of study (up to 1080 days)

  • Incidence of Treatment-emergent Adverse Events (TEAEs)

    Safety assessments include adverse events and serious adverse events until the end of study. End of study visit occured at least 90 days following the last inclisiran dose once a decision was made to end the study (either by the subject, investigator or sponsor). For subjects prematurely and permanently discontinued from study treatment, who were not willing to return within the 90 day timeframe, the EOS visit was scheduled as soon as possible, or if decision to discontinue and not return was made at a specific visit, this visit became the EOS visit.

    From ORION-8 Day 1 to the end of study (up to 1080 days)

Secondary Outcomes (4)

  • Absolute Change in LDL-C From the Initial Feeder Study Baseline

    Feeder study baseline, ORION-8 baseline, Day 1080/EOS (ORION-8) (up to a maximum of 2340 days)

  • Percentage Change in LDL-C From the Initial Feeder Study Baseline

    Feeder study baseline, ORION-8 baseline, Day 1080/EOS (ORION-8) (up to a maximum of 2340 days)

  • Absolute Change From the Initial Feeder Study Baseline in Total Cholesterol, Triglycerides and HDL-C

    Feeder study baseline, ORION-8 baseline, Day 1080/EOS (ORION-8) (up to a maximum of 2340 days)

  • Percentage Change From the Initial Feeder Study Baseline in Total Cholesterol, Triglycerides and HDL-C

    Feeder study baseline, ORION-8 baseline, Day 1080/EOS (ORION-8) (up to a maximum of 2340 days)

Study Arms (1)

Inclisiran

EXPERIMENTAL

Inclisiran sodium 300 milligrams (mg) was administered as a single SC injection on Day 1\*, 90, then every 180 days to Day 990. \*Subjects who received blinded placebo in the feeder study received blinded inclisiran and subjects who received blinded inclisiran in the feeder study received blinded placebo on Day 1 in ORION-8. Subjects from the open label ORION-3 study did not receive any injection of study drug on Day 1. Their first dose of study medication was at day 90

Drug: Inclisiran Sodium

Interventions

Inclisiran is a small interfering ribonucleic acid (RNA) that inhibits PCSK9 synthesis.

Inclisiran

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Completion on a previously qualifying inclisiran Phase II trial MDCO-PCS-16-01 (ORION-3), or Phase III lipid lowering ORION feeder study \[MDCO-PCS-17-03 (ORION-9), MDCO-PCS-17-4 (ORION-10), or MDCO-PCS-17-08 (ORION-11)\] meaning the subject received the last dose of study drug and completed the final study visit per applicable protocol.
  • On current lipid-lowering therapies (such as a statin and/or ezetimibe) from previous study with no planned medication or dose change during study participation.
  • Willing and able to give informed consent before initiation of any study-related procedures and willing to comply with all required study procedures.

You may not qualify if:

  • Any uncontrolled or serious disease, or any medical or surgical condition, that may either interfere with participation in the clinical study, and/or put the subject at significant risk \[according to investigator's (or delegate's) judgment\] if he/she participates in the clinical study.
  • An underlying known disease, or surgical, physical, or medical condition that, in the opinion of the investigator (or delegate) might interfere with interpretation of the clinical study results.
  • Severe concomitant noncardiovascular disease that carries the risk of reducing life expectancy to less than 3 years,
  • Active liver disease defined as any known current infectious, neoplastic, or metabolic pathology of the liver or unexplained alanine aminotransferase (ALT), aspartate aminotransferase (AST), elevation \>3x the upper limit of normal (ULN), or total bilirubin (TBIL) elevation \>2x ULN at the last recorded visit in the feeder study prior to study entry visit.
  • Females who are pregnant or nursing, or who are of childbearing potential and unwilling to use at least one method of acceptable effective contraception (eg, oral contraceptives, barrier methods, approved contraceptive implant, long-term injectable contraception, intrauterine device) for the entire duration of the study. Exemptions from this criterion:
  • Women \>2 years postmenopausal (defined as 1 year or longer since last menstrual period) and more than 55 years of age.
  • Postmenopausal women (as defined above) and less than 55 years of age with a negative pregnancy test within 24 hours of randomization.
  • Women who are surgically sterilized at least 3 months prior to enrollment.
  • Planned use of other investigational medicinal products other than inclisiran or devices during the course of the study.
  • Any condition that according to the investigator could interfere with the conduct of the study, such as but not limited to:
  • Subjects who are unable to communicate or to cooperate with the investigator
  • Unable to understand the protocol requirements, instructions and study-related restrictions, the nature, scope, and possible consequences of the study (including subjects whose cooperation is doubtful due to drug abuse or alcohol dependency)
  • Unlikely to comply with the protocol requirements, instructions, and study-related restrictions (eg, uncooperative attitude, inability to return for follow-up visits, and improbability of completing the study)
  • Have any medical or surgical condition, which in the opinion of the investigator would put the subject at increased risk from participating in the study
  • Persons directly involved in the conduct of the study.
  • +1 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (238)

Research Site 10001-015

Birmingham, Alabama, 35211, United States

Location

Research Site 10001-138

Foley, Alabama, 36535, United States

Location

Research Site 10001-113

Huntsville, Alabama, 35801, United States

Location

Research Site 10001-058

Mobile, Alabama, 36608, United States

Location

Research Site 10001-037

Montgomery, Alabama, 36117, United States

Location

Research Site 10001-076

Saraland, Alabama, 36571, United States

Location

Research Site 10001-013

Chandler, Arizona, 85224, United States

Location

Research Site 10001-077

Mesa, Arizona, 85213, United States

Location

Research Site 10001-136

Phoenix, Arizona, 85014, United States

Location

Research Site 10001-051

Surprise, Arizona, 85374, United States

Location

Research Site 10001-019

Tucson, Arizona, 85712, United States

Location

Research Site 10001-004

Tucson, Arizona, 85741, United States

Location

Research Site 10001-132

Tucson, Arizona, 85745, United States

Location

Research Site 10001-073

Beverly Hills, California, 90211, United States

Location

Research Site 10001-050

Canoga Park, California, 91303, United States

Location

Research Site 10001-011

Carlsbad, California, 92008, United States

Location

Research Site 10001-065

El Cajon, California, 92020, United States

Location

Research Site 10001-150

Los Angeles, California, 90022, United States

Location

Research Site 90001-005

Mission Viejo, California, 92691, United States

Location

Research Site 10001-043

Northridge, California, 91324, United States

Location

Research Site 10001-022

Northridge, California, 91325, United States

Location

Research Site 10001-033

Sacramento, California, 95821-2134, United States

Location

Research Site 10001-105

San Ramon, California, 94582, United States

Location

Research Site 10001-008

Santa Rosa, California, 95405, United States

Location

Research Site 10001-153

Spring Valley, California, 91978, United States

Location

Research Site 90001-015

Stanford, California, 94305, United States

Location

Research Site 10001-044

Torrance, California, 90502, United States

Location

Research Site 90001-047

Boca Raton, Florida, 33434, United States

Location

Research Site 10001-084

Clearwater, Florida, 33756, United States

Location

Research Site 10001-155

Clearwater, Florida, 33756, United States

Location

Research Site 10001-099

Clearwater, Florida, 33761, United States

Location

Research Site 10001-127

Daytona Beach, Florida, 32117, United States

Location

Research Site 10001-119

Fleming Island, Florida, 32003, United States

Location

Research Site 10001-070

Fort Lauderdale, Florida, 33308, United States

Location

Research Site 10001-067

Hialeah, Florida, 33012, United States

Location

Research Site 10001-139

Jacksonville, Florida, 32204, United States

Location

Research Site 10001-039

Jacksonville, Florida, 32216, United States

Location

Research Site 10001-098

Jacksonville, Florida, 32216, United States

Location

Research Site 10001-081

Miami, Florida, 33126, United States

Location

Research Site 10001-140

Miami, Florida, 33126, United States

Location

Research Site 10001-142

Miami, Florida, 33126, United States

Location

Research Site 10001-030

Miami, Florida, 33165, United States

Location

Research Site 10001-116

Miami, Florida, 33183, United States

Location

Research Site 10001-080

Miami Springs, Florida, 33166, United States

Location

Research Site 10001-027

Pembroke Pines, Florida, 33024, United States

Location

Research Site 10001-115

Pembroke Pines, Florida, 33027, United States

Location

Research Site 10001-048

Pembroke Pines, Florida, 33029, United States

Location

Research Site 10001-147

Pembroke Pines, Florida, 33029, United States

Location

Research Site 10001-003

Pinellas Park, Florida, 33781, United States

Location

Research Site 10001-104

Ponte Vedra, Florida, 32081, United States

Location

Research Site 10001-090

Saint Augustine, Florida, 32086, United States

Location

Research Site 10001-123

Sarasota, Florida, 34239-3513, United States

Location

Research Site 10001-102

St. Petersburg, Florida, 33713, United States

Location

Research Site 10001-143

Tampa, Florida, 33614, United States

Location

Research Site 10001-069

Atlanta, Georgia, 30342, United States

Location

Research Site 10001-137

Dunwoody, Georgia, 30338, United States

Location

Research Site 10001-092

Macon, Georgia, 31210, United States

Location

Research Site 10001-059

Arlington Heights, Illinois, 60005, United States

Location

Research Site 10001-158

Chicago, Illinois, 60652, United States

Location

Research Site 10001-036

Evanston, Illinois, 60201, United States

Location

Research Site 10001-082

Indianapolis, Indiana, 46260, United States

Location

Research Site 10001-040

Valparaiso, Indiana, 46383, United States

Location

Research Site 10001-074

West Des Moines, Iowa, 50266, United States

Location

Research Site 10001-028

Hutchinson, Kansas, 67502, United States

Location

Research Site 10001-125

Lexington, Kentucky, 40503, United States

Location

Research Site 10001-108

Lexington, Kentucky, 40504, United States

Location

Research Site 10001-107

Owensboro, Kentucky, 42303, United States

Location

Research Site 10001-144

Crowley, Louisiana, 70526, United States

Location

Research Site 10001-041

Lake Charles, Louisiana, 70601, United States

Location

Research Site 10001-101

Monroe, Louisiana, 71201, United States

Location

Research Site 90001-004

Boston, Massachusetts, 02114, United States

Location

Research Site 10001-024

Flint, Michigan, 48504, United States

Location

Research Site 10001-095

Grandville, Michigan, 49418, United States

Location

Research Site 10001-078

Sterling Heights, Michigan, 48310, United States

Location

Research Site 10001-034

Troy, Michigan, 48098, United States

Location

Research Site 10001-018

Edina, Minnesota, 55435, United States

Location

Research Site 90001-056

Saint Paul, Minnesota, 55102, United States

Location

Research Site 10001-156

St Louis, Missouri, 63136, United States

Location

Research Site 10001-007

St Louis, Missouri, 63141, United States

Location

Research Site 90001-012

Butte, Montana, 59701, United States

Location

Research Site 10001-053

Omaha, Nebraska, 68134, United States

Location

Research Site 10001-021

Omaha, Nebraska, 68144, United States

Location

Research Site 90001-112

Las Vegas, Nevada, 89119, United States

Location

Research Site 10001-124

Las Vegas, Nevada, 89121, United States

Location

Research Site 10001-060

Bridgewater, New Jersey, 08807, United States

Location

Research Site 90001-014

Summit, New Jersey, 07901, United States

Location

Research Site 10001-055

Warren Township, New Jersey, 07059, United States

Location

Research Site 10001-054

Albany, New York, 12206, United States

Location

Research Site 10001-122

Binghamton, New York, 13901, United States

Location

Research Site 10001-128

Endwell, New York, 13760, United States

Location

Research Site 10001-042

New Windsor, New York, 12553, United States

Location

Research Site 10001-129

Poughkeepsie, New York, 12601, United States

Location

Research Site 10001-110

Williamsville, New York, 14221, United States

Location

Research Site 10001-063

Cary, North Carolina, 27518, United States

Location

Research Site 10001-064

Greensboro, North Carolina, 27401, United States

Location

Research Site 10001-145

Mooresville, North Carolina, 28117, United States

Location

Research Site 10001-046

Shelby, North Carolina, 28150, United States

Location

Research Site 10001-016

Akron, Ohio, 443311, United States

Location

Research Site 10001-120

Cincinnati, Ohio, 45219, United States

Location

Research Site 90001-002

Cincinnati, Ohio, 45227, United States

Location

Research Site 10001-010

Cincinnati, Ohio, 45236, United States

Location

Research Site 10001-134

Cincinnati, Ohio, 45246, United States

Location

Research Site 10001-014

Columbus, Ohio, 43212, United States

Location

Research Site 10001-141

Dayton, Ohio, 45419, United States

Location

Research Site 10001-148

Marion, Ohio, 43302, United States

Location

Research Site 10001-109

Wyomissing, Pennsylvania, 19610, United States

Location

Research Site 10001-001

Anderson, South Carolina, 29621, United States

Location

Research Site 10001-006

Greer, South Carolina, 29651, United States

Location

Research Site 10001-075.

Greer, South Carolina, 29651, United States

Location

Research Site 10001-111

Myrtle Beach, South Carolina, 29588, United States

Location

Research Site 10001-133

Pelzer, South Carolina, 29669, United States

Location

Research Site 10001-103

Rapid City, South Dakota, 57701, United States

Location

Research Site 10001-146

Athens, Tennessee, 37303, United States

Location

Research Site 10001-130

Kingsport, Tennessee, 37660, United States

Location

Research Site 10001-118

Knoxville, Tennessee, 37909, United States

Location

Research Site 10001-106

Knoxville, Tennessee, 37917, United States

Location

Research Site 10001-100

Amarillo, Texas, 79106, United States

Location

Research Site 10001-087

Austin, Texas, 78726, United States

Location

Research Site 10001-117

Austin, Texas, 78756, United States

Location

Research Site 10001-009

Dallas, Texas, 75234, United States

Location

Research Site 10001-068

Edinburg, Texas, 78503, United States

Location

Research Site 10001-031

Houston, Texas, 77002, United States

Location

Research Site 10001-088

Houston, Texas, 77024, United States

Location

Research Site 10001-091

Houston, Texas, 77027, United States

Location

Research Site 10001-061

Houston, Texas, 77058, United States

Location

Research Site 10001-032

Houston, Texas, 77070, United States

Location

Research Site 10001-057

New Braunfels, Texas, 78130, United States

Location

Research Site 10001-079

Round Rock, Texas, 78681, United States

Location

Research Site 10001-071

San Antonio, Texas, 78229, United States

Location

Research Site 10001-083

Schertz, Texas, 78154, United States

Location

Research Site 10001-149

Shavano Park, Texas, 78231, United States

Location

Research Site 10001-045

Tomball, Texas, 77375, United States

Location

Research Site 10001-005

Layton, Utah, 84041, United States

Location

Research Site 10001-002

Salt Lake City, Utah, 84123, United States

Location

Research Site 10001-052

Salt Lake City, Utah, 94107, United States

Location

Research Site 10001-093

Falls Church, Virginia, 22042, United States

Location

Research Site 10001-085

Manassas, Virginia, 20110, United States

Location

Research Site 10001-094

Midlothian, Virginia, 23114, United States

Location

Research Site 10001-023

Richmond, Virginia, 23294, United States

Location

Research Site 10001-029

Suffolk, Virginia, 23435, United States

Location

Research Site 10001-114

Tacoma, Washington, 98405, United States

Location

Research Site 90011-005

Chicoutimi, Quebec, G7H 7K9, Canada

Location

Research Site 90011-001

Montreal, Quebec, H2W 1R7, Canada

Location

Research Site 90011-002

Québec, Quebec, GIV 4W2, Canada

Location

Research Site 11420-002

Chomutov, 430 02, Czechia

Location

Research Site 90420-001

Prague, 140 21, Czechia

Location

Research Site 90420-006

Prague, 180 81, Czechia

Location

Research Site 11420-003

Uherské Hradiště, 686 01, Czechia

Location

Research Site 90045-001

Aalborg, North Denmark, 9000, Denmark

Location

Research Site 90045-004

Esbjerg, 6700, Denmark

Location

Research Site 90045-003

Herning, 7400, Denmark

Location

Research Site 90045-006

Hvidovre, 2650, Denmark

Location

Research Site 90045-002

Roskilde, 4000, Denmark

Location

Research Site 90045-005

Viborg, 8800, Denmark

Location

Research Site 11049-006

Berlin, 12627, Germany

Location

Research Site 11049-002

Bochum, 47787, Germany

Location

Research Site 11049-003

Frankfurt, 60313, Germany

Location

Research Site 11049-001

Heidelberg, 69120, Germany

Location

Research Site 11049-007

Heidelberg, 69120, Germany

Location

Research Site 11036-001

Budapest, Hungary

Location

Research Site 11036-004

Debrecen, Hungary

Location

Research Site 11036-002

Hatvan, Hungary

Location

Research Site 11036-003

Zalaegerszeg, Hungary

Location

Research Site 90031-001

Amersfoort, 3813 TZ, Netherlands

Location

Research Site 90031-003

Amsterdam, 1105 AZ, Netherlands

Location

Research Site 90031-006

Goes, 4462 RA, Netherlands

Location

Research Site 90031-009

Hoorn, 1624 NP, Netherlands

Location

Research Site 90031-005

Utrecht, Netherlands

Location

Research SIte 11048-016

Brzozowie, Poland

Location

Research Site 11048-018

Bydgoszcz, 85-079, Poland

Location

Research Site 11048-011

Bydgoszcz, Poland

Location

Research Site 11048-004

Gdansk, Poland

Location

Research Site 11048-005

Gdynia, Poland

Location

Research Site 11048-007

Katowice, Poland

Location

Research SIte 11048-012

Katowice, Poland

Location

Research Site 11048-003

Krakow, Poland

Location

Research SIte 11048-014

Krakow, Poland

Location

Research Site 11048-008

Lublin, Poland

Location

Research Site 11048-001

Poznan, Poland

Location

Research Site 11048-019

Ruda Śląska, 41-709, Poland

Location

Research SIte 11048-013

Rzeszów, Poland

Location

Research SIte 11048-015

Tarnów, Poland

Location

Research Site 11048-006

Warsaw, Poland

Location

Research Site 11048-009

Warsaw, Poland

Location

Research Site 11048-002

Wroclaw, Poland

Location

Research Site 11048-010

Wroclaw, Poland

Location

Research Site 90027-008

Bellville, Cape Town, 7530, South Africa

Location

Research Site 90027-007

Lyttelton, Cape Town, 0157, South Africa

Location

Research Site 90027-003

Bloemfontein, Free State, 9301, South Africa

Location

Research Site 90027-010

Johannesburg, Gauteng, 2193, South Africa

Location

Research Site 11027-005

Kempton Park, Gauteng, 1619, South Africa

Location

Research Site 90027-006

Pretoria, Gauteng, 0184, South Africa

Location

Research Site 90027-009

Witbank, Gauteng, 1035, South Africa

Location

Research Site 90027-001

Cape Town, Western Cape, 7500, South Africa

Location

Research Site 11027-007

Kuils River, Western Cape, 7580, South Africa

Location

Research Site 11027-013

Paarl, Western Cape, 7646, South Africa

Location

Research Site 90027-004

Somerset West, Western Cape, 7130, South Africa

Location

Research Site 90027-005

Somerset West, Western Cape, 7130, South Africa

Location

Research Site 90034-004

Córdoba, Andalusia, 14004, Spain

Location

Research Site 90034-002

Zaragoza, Aragon, 5009, Spain

Location

Research Site 90034-005

Barcelona, Catalonia, 08036, Spain

Location

Research Site 90034-006

Barcelona, Catalonia, 08907, Spain

Location

Research Site 90034-001

Reus, Catalonia, 43204, Spain

Location

Research Site 90034-003

A Coruña, Galicia, 15002, Spain

Location

Research Site 90046-002

Gothenburg, SE-41346, Sweden

Location

Research Site 90046-001

Stockholm, SE-11446, Sweden

Location

Research Site 90046-003

Stockholm, SE-14186, Sweden

Location

Research Site 11380-005

Cherkasy, Ukraine

Location

Research Site 11380-008

Kharkiv, 61176, Ukraine

Location

Research Site 11380-001

Kyiv, 02002, Ukraine

Location

Research Site 11380-002

Kyiv, 03037, Ukraine

Location

Research Site 11380-003

Kyiv, 03049, Ukraine

Location

Research Site 11380-004

Kyiv, Ukraine

Location

Research Site 11380-006

Uzhhorod, 88000, Ukraine

Location

Research Site 11380-009

Zaporizhzhya, Ukraine

Location

Research Site 11044-028

Bollington, Cheshire, SK10 5JH, United Kingdom

Location

Research Site 11044-026

Bury, United Kingdom

Location

Research Site 11044-024

Cheadle Hulme, United Kingdom

Location

Research Site 11044-014

Chorley, United Kingdom

Location

Research Site 11044-012

Cornwell, United Kingdom

Location

Research Site 11044-010

Derby, United Kingdom

Location

Research Site 11044-006

Edgbaston, United Kingdom

Location

Research Site 11044-009

Exeter, United Kingdom

Location

Research Site 11044-001

Glasgow, United Kingdom

Location

Research Site 11044-008

Hexham, United Kingdom

Location

Research SIte 11044-020

Macclesfield, United Kingdom

Location

Research Site 11044-005

Manchester, United Kingdom

Location

Research Site 11044-025

Manchester, United Kingdom

Location

Research Site 11044-027

Manchester, United Kingdom

Location

Research Site 11044-029

Manchester, United Kingdom

Location

Research Site 11044-019

Plymouth, United Kingdom

Location

Research Site 11044-003

Reading, United Kingdom

Location

Research Site 11044-022

Sale, United Kingdom

Location

Research Site 11044-023

Sale, United Kingdom

Location

Research Site 11044-002

Stockton-on-Tees, United Kingdom

Location

Research Site 11044-021

Timperley, United Kingdom

Location

Research Site 11044-007

Wales, United Kingdom

Location

Research Site 11044-004

Waterloo, United Kingdom

Location

Related Publications (2)

  • Wright RS, Raal FJ, Koenig W, Landmesser U, Leiter LA, Vikarunnessa S, Lesogor A, Maheux P, Talloczy Z, Zang X, Schwartz GG, Ray KK. Inclisiran administration potently and durably lowers LDL-C over an extended-term follow-up: the ORION-8 trial. Cardiovasc Res. 2024 Oct 14;120(12):1400-1410. doi: 10.1093/cvr/cvae109.

  • Warden BA, Duell PB. Inclisiran: A Novel Agent for Lowering Apolipoprotein B-containing Lipoproteins. J Cardiovasc Pharmacol. 2021 Aug 1;78(2):e157-e174. doi: 10.1097/FJC.0000000000001053.

MeSH Terms

Conditions

HypercholesterolemiaHomozygous Familial Hypercholesterolemia

Condition Hierarchy (Ancestors)

HyperlipidemiasDyslipidemiasLipid Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesHyperlipoproteinemia Type IILipid Metabolism, Inborn ErrorsMetabolism, Inborn ErrorsGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesHyperlipoproteinemias

Results Point of Contact

Title
Study Director
Organization
Novartis Pharmaceuticals

Study Officials

  • Scott Wright, MD

    Mayo Clinic

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 17, 2019

First Posted

January 23, 2019

Study Start

April 16, 2019

Primary Completion

February 13, 2023

Study Completion

February 13, 2023

Last Updated

March 6, 2024

Results First Posted

March 6, 2024

Record last verified: 2024-02

Data Sharing

IPD Sharing
Will share

Novartis is committed to sharing access to patient-level data and supporting clinical documents from eligible studies with qualified external researchers. Requests are reviewed and approved by an independent review panel on the basis of scientific merit. All data provided is anonymized to protect the privacy of patients who have participated in the trial in line with applicable laws and regulations. This trial data availability is according to the criteria and process described on www.clinicalstudydatarequest.com

Locations