NCT03583710

Brief Summary

This phase III trial studies how well mitotane alone works compared to mitotane with cisplatin and etoposide when given after surgery in treating patients with adrenocortical cancer that has a high risk of coming back (recurrence). Cortisol can cause the growth of adrenocortical tumor cells. Antihormone therapy, such as mitotane, may lessen the amount of cortisol made by the body. Drugs used in chemotherapy, such as cisplatin and etoposide, work in different ways to stop the growth of tumor cells, either by killing the cells, by stopping them from dividing, or by stopping them from spreading. It is not yet known whether mitotane alone or mitotane with cisplatin and etoposide after surgery works better in treating patients with adrenocortical carcinoma.

Trial Health

80
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
240

participants targeted

Target at P50-P75 for phase_3

Timeline
32mo left

Started Aug 2018

Longer than P75 for phase_3

Geographic Reach
4 countries

25 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress74%
Aug 2018Jan 2029

First Submitted

Initial submission to the registry

June 28, 2018

Completed
13 days until next milestone

First Posted

Study publicly available on registry

July 11, 2018

Completed
1 month until next milestone

Study Start

First participant enrolled

August 20, 2018

Completed
10.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2029

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2029

Last Updated

January 30, 2026

Status Verified

January 1, 2026

Enrollment Period

10.4 years

First QC Date

June 28, 2018

Last Update Submit

January 28, 2026

Conditions

Outcome Measures

Primary Outcomes (3)

  • Recurrence-free survival (RFS)

    Starting from the date of randomization until documentation of radiological evidence of local recurrence, radiological evidence of distant recurrence, or death from any cause (whichever occurs first), RFS will be compared using the log-rank test between the two arms.

    From the time of randomization up to 2 years

  • Local recurrence of adrenocortical carcinoma (ACC)

    Up to 6 months

  • Distant recurrence of ACC

    Up to 6 months

Secondary Outcomes (1)

  • Overall survival (OS)

    From the time of randomization up to 2 years

Study Arms (2)

Arm A (mitotane)

EXPERIMENTAL

Patients receive mitotane PO daily on days 1-21. Cycles repeat every 21 days for 2 years in the absence of disease progression or unacceptable toxicity.

Drug: MitotaneOther: Quality-of-Life Assessment

Arm B (mitotane, etoposide, cisplatin)

EXPERIMENTAL

Patients receive mitotane as in Arm A. Patients also receive cisplatin IV over 2 hours on day 1 and etoposide IV over 2 hours on days 1-3. Treatment repeats every 21 days for up to 4 cycles in the absence of disease progression or unacceptable toxicity.

Drug: CisplatinDrug: EtoposideDrug: MitotaneOther: Quality-of-Life Assessment

Interventions

Given IV

Also known as: Abiplatin, Blastolem, Briplatin, CDDP, Cis-diammine-dichloroplatinum, Cis-diamminedichloridoplatinum, Cis-diamminedichloro Platinum (II), Cis-diamminedichloroplatinum, Cis-dichloroammine Platinum (II), Cis-platinous Diamine Dichloride, Cis-platinum, Cis-platinum II, Cis-platinum II Diamine Dichloride, Cismaplat, Cisplatina, Cisplatinum, Cisplatyl, Citoplatino, Citosin, Cysplatyna, DDP, Lederplatin, Metaplatin, Neoplatin, Peyrone''s Chloride, Peyrone''s Salt, Placis, Plastistil, Platamine, Platiblastin, Platiblastin-S, Platinex, Platinol, Platinol- AQ, Platinol-AQ, Platinol-AQ VHA Plus, Platinoxan, Platinum, Platinum Diamminodichloride, Platiran, Platistin, Platosin
Arm B (mitotane, etoposide, cisplatin)

Ancillary studies

Also known as: Quality of Life Assessment
Arm A (mitotane)Arm B (mitotane, etoposide, cisplatin)

Given IV

Also known as: Demethyl Epipodophyllotoxin Ethylidine Glucoside, EPEG, Lastet, Toposar, Vepesid, VP 16, VP 16-213, VP-16, VP-16-213, VP16
Arm B (mitotane, etoposide, cisplatin)

Given PO

Also known as: (o,p)-DDD, 1, 1-Dichloro-2-(o-chlorophenyl)-2-(p-chlorophenyl)ethane, 1-Chloro-2-[2,2-dichloro-1-(4-chlorophenyl)ethyl]benzene, 2, 2-Bis(2-chlorophenyl-4-chlorophenyl)-1,1-dichloroethane, 2, 4''-Dichlorodiphenyldichloroethane, CB 313, CB-313, Chloditan, Chlodithane, DDD, Ethane, 2-(o-chlorophenyl)-2-(p-chlorophenyl)-1,1-dichloro-, Khloditan, Lisodren, Lysodren, Mytotan, o,p'' - DDD, o,p''-DDD, Ortho,para-DDD, WR-13045
Arm A (mitotane)Arm B (mitotane, etoposide, cisplatin)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Have a histologically confirmed diagnosis of ACC (Weiss score of \>= 3). (LinWeiss-Bisceglia system will be used for oncocytic ACC).
  • Have a high risk of relapse defined as: Stage I-III ACC (according to the European Network for the Study of Adrenal Tumors \[ENSAT\] classification) within 90 days of surgical resection of primary tumor with curative intent with either microscopically complete resection (R0, defined as no evidence of microscopic residual disease according to surgical reports, histopathology, and perioperative imaging), microscopically positive margins (R1), or undetermined margins (RX, based on surgical or pathological reports without unequivocal evidence of metastasis in the perioperative imaging). Each participating center will determine the pathological stages and resection margins AND Ki67 \> 10% (to be determined by an experienced pathologist in each participating center and preferably via quantitative imaging analysis).
  • Have perioperative imaging (computed tomography \[CT\] with contrast, magnetic resonance imaging \[MRI\] of the chest/abdomen/pelvis, or fluorodeoxyglucose positron emission tomography \[FDG-PET\] CT) without unequivocal evidence of disease within 8 weeks before randomization. Patients with indeterminate non-specific nodules (\< 1 cm for soft tissue lesions and \< 1.5 cm in the short dimension for lymph nodes) will be permitted to participate in this study.
  • Have an Eastern Cooperative Oncology Group (ECOG) performance status 0-2.
  • Be able to comply with the protocol procedures.
  • Provide written informed consent.

You may not qualify if:

  • The time between primary surgery and randomization \> 90 days.
  • Gross residual disease after surgery (R2 resection)
  • High suspicion for metastatic disease on perioperative imaging
  • They have undergone repeated surgery for recurrence of disease.
  • They have a history of recent or active prior malignancy, except for cured non-melanoma skin cancer, cured in situ cervical carcinoma, breast ductal carcinoma in situ, or other treated malignancies where there has been no evidence of disease for at least 2 years.
  • They have renal insufficiency (estimated glomerular filtration rate \[GFR\] \< 50 mL/min/1.73 m\^2).
  • They have significant liver insufficiency (serum bilirubin \> 2 times the upper normal range)
  • They have significant liver insufficiency (serum alanine aminotransferase \[ALT\] or aspartate aminotransferase \[AST\] \> 3 times the upper normal range)
  • Impaired bone marrow reserve (neutrophils \< 1000/mm\^3)
  • Impaired bone marrow reserve (platelets \< 100,000/mm\^3)
  • Pregnancy or breast feeding.
  • They have known congestive heart failure (ejection fraction \< 45%). The extent of cardiac testing will depend on the judgment of the local principal investigator (PI). In general, in patients with a history of cardiac disease, it is recommended to obtain a baseline two-dimensional echocardiogram as standard of care to document ejection fraction. In patients without prior cardiac disease, a baseline electrocardiogram (EKG) is sufficient if there is no evidence of acute ischemic changes or prior evidence of myocardial infarction. If EKG results are abnormal (ischemic changes, significant arrhythmia, or suggestion of prior myocardial infarction), a two-dimensional echocardiogram will be obtained to assess ejection fraction. Cardiac imaging and EKG may not be needed in patients assigned to mitotane who do not have prior cardiac history and have low suspicion for cardiac symptoms to reflect standards of clinical practice. Similarly, utilizing cardiac imaging and EKG within the past 12 months is permitted if there is no suspicion for cardiac issues.
  • They have preexisting grade 2 peripheral neuropathy.
  • They underwent previous or current treatment with mitotane or other antineoplastic drugs for ACC.
  • They underwent previous radiotherapy for ACC.
  • +1 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (25)

University of Michigan Comprehensive Cancer Center

Ann Arbor, Michigan, 48109, United States

RECRUITING

Siteman Cancer Center at Washington University

St Louis, Missouri, 63110, United States

ACTIVE NOT RECRUITING

M D Anderson Cancer Center

Houston, Texas, 77030, United States

RECRUITING

Institut de Cancérologie de l'Ouest (ICO)

Angers, 49055, France

NOT YET RECRUITING

CHU Angers, Hôpital Larrey

Angers, 49933, France

NOT YET RECRUITING

CHU Besançon, Hôpital Jean Minjoz

Besançon, 25000, France

RECRUITING

CHU Brest, Hôpital La Cavale Blanche

Brest, 29200, France

ACTIVE NOT RECRUITING

Centre Georges François Leclerc

Dijon, 25000, France

RECRUITING

HCL Hôpital Louis Pradel

Lyon, 69877, France

NOT YET RECRUITING

CHU Nantes, Hôpital René et Guillaume Laënnec

Nantes, 44093, France

RECRUITING

CHU Nantes, Hôpital René et Guillaume Laënnec

Nantes, 44093, France

RECRUITING

Hôpital Cochin, AP-HP

Paris, 75014, France

RECRUITING

Hôpital Cochin, AP-HP

Paris, 75014, France

RECRUITING

CHU Bordeaux - Hôpital Haut Lévèque

Pessac, 33600, France

RECRUITING

CHU Poitiers

Poitiers, 86000, France

RECRUITING

CHU Reims

Reims, 51092, France

RECRUITING

HUS, Hôpital Hautepierre

Strasbourg, 67000, France

NOT YET RECRUITING

ICANS Institut de cancérologie Strasbourg Europe

Strasbourg, 67200, France

NOT YET RECRUITING

CHU Toulouse, Hôpital Larrey

Toulouse, 31059, France

RECRUITING

CHU Toulouse, Hôpital Rangueil

Toulouse, 31400, France

RECRUITING

Gustave Roussy

Villejuif, 94805, France

RECRUITING

Maria Sklodowska-Curie National Research Institute of Oncology

Gliwice, 44-102, Poland

RECRUITING

Sahlgrenska University Hospital

Gothenburg, Sweden

RECRUITING

Karolinska University Hospital

Stockholm, Sweden

RECRUITING

Akademiska Sjukhuset

Uppsala, Sweden

RECRUITING

Related Links

MeSH Terms

Interventions

Cisplatin1,2-diaminocyclohexaneplatinum II citratePlatinumEtoposideMitotaneDichlorodiphenyldichloroethaneEthane

Intervention Hierarchy (Ancestors)

Chlorine CompoundsInorganic ChemicalsNitrogen CompoundsPlatinum CompoundsMetals, HeavyElementsTransition ElementsMetalsPodophyllotoxinTetrahydronaphthalenesNaphthalenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsPolycyclic CompoundsGlucosidesGlycosidesCarbohydratesHydrocarbons, ChlorinatedHydrocarbons, HalogenatedAlkanesHydrocarbons, Acyclic

Study Officials

  • Jeena Varghese

    M.D. Anderson Cancer Center

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 28, 2018

First Posted

July 11, 2018

Study Start

August 20, 2018

Primary Completion (Estimated)

January 1, 2029

Study Completion (Estimated)

January 1, 2029

Last Updated

January 30, 2026

Record last verified: 2026-01

Locations