NCT03491683

Brief Summary

Phase 1/2 trial to evaluate safety, immunogenicity and preliminary efficacy of INO-5401 and INO-9012 in combination with cemiplimab (REGN2810), with radiation and chemotherapy, in subjects with newly-diagnosed glioblastoma (GBM).

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
52

participants targeted

Target at P50-P75 for phase_1

Timeline
8mo left

Started May 2018

Longer than P75 for phase_1

Geographic Reach
1 country

21 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress92%
May 2018Dec 2026

First Submitted

Initial submission to the registry

April 2, 2018

Completed
7 days until next milestone

First Posted

Study publicly available on registry

April 9, 2018

Completed
2 months until next milestone

Study Start

First participant enrolled

May 31, 2018

Completed
8.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 31, 2026

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2026

Last Updated

May 4, 2026

Status Verified

May 1, 2026

Enrollment Period

8.6 years

First QC Date

April 2, 2018

Last Update Submit

May 1, 2026

Conditions

Keywords

GlioblastomaimmunotherapyDNA therapycheckpoint inhibitor

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants with Adverse Events (AEs)

    From Day 0 to 30 days after the last dose of study treatment (non-serious AEs) and to 6 months after the last dose of study treatment (immune-related AEs, AEs of special interest and serious AEs) up to approximately 24 months

Secondary Outcomes (5)

  • Overall survival at 18 months (OS18)

    At Month 18

  • Change from Baseline in Interferon-gamma Secreting T Lymphocytes in Peripheral Blood Mononuclear Cells (PBMCs)

    From Day 0 to last dose of study treatment up to approximately 18 months

  • Change from Baseline in T-Cell Phenotypes in PBMCs

    From Day 0 to last dose of study treatment up to approximately 18 months

  • Change from Baseline in T Cell Receptor (TCR) Subtypes in PBMCs

    From Day 0 to last dose of study treatment up to approximately 18 months

  • Change from Baseline in Antigen-Specific Humoral Response

    From Day 0 to last dose of study treatment up to approximately 18 months

Study Arms (2)

Cohort A: Unmethylated MGMT Promoter

EXPERIMENTAL

Cohort A will include participants with a glioblastoma tumor with an unmethylated MGMT promoter. Participants will receive INO-5401 and INO-9012 and cemiplimab as well as radiation and temozolomide (TMZ; only during radiation therapy), if clinically indicated.

Biological: INO-5401Biological: INO-9012Biological: CemiplimabRadiation: Radiation TherapyDrug: Temozolomide

Cohort B: Methylated MGMT Promoter

EXPERIMENTAL

Cohort B will include participants with a glioblastoma tumor with a methylated MGMT promoter or with indeterminate MGMT status. Participants will receive INO-5401 and INO-9012 and cemiplimab as well as radiation and temozolomide (TMZ), if clinically indicated. Participants will continue to receive TMZ following radiation therapy, for up to six additional cycles, if clinically indicated.

Biological: INO-5401Biological: INO-9012Biological: CemiplimabRadiation: Radiation TherapyDrug: Temozolomide

Interventions

INO-5401BIOLOGICAL

INO-5401 is a combination of 3 separate DNA plasmids targeting Wilms tumor gene-1 (WT1) antigen, prostate-specific membrane antigen (PSMA) and human telomerase reverse transcriptase (hTERT) genes. Starting on Day 0 three milligrams (mg) of each plasmid will be delivered IM followed by EP using the CELLECTRA® 2000 EP device every three weeks for four doses, and then every 9 weeks until disease progression as defined by immunotherapy Response Assessment in Neuro-Oncology (iRANO), unacceptable toxicity, withdrawal of consent, or death.

Cohort A: Unmethylated MGMT PromoterCohort B: Methylated MGMT Promoter
INO-9012BIOLOGICAL

INO-9012 is a DNA plasmid for expression of human interleukin-12 (IL-12). Starting on Day 0 one mg plasmid will be delivered IM followed by EP using the CELLECTRA® 2000 EP device every three weeks for four doses, and then every 9 weeks until disease progression as defined by iRANO, unacceptable toxicity, withdrawal of consent, or death.

Cohort A: Unmethylated MGMT PromoterCohort B: Methylated MGMT Promoter
CemiplimabBIOLOGICAL

Cemiplimab is an antibody to programmed death-1 (PD-1) protein. Starting on Day 0 cemiplimab will be administered intravenously (IV) every three weeks at a dose of 350 mg per dose in the absence of dose holding, until disease progression as defined by iRANO, unacceptable toxicity, withdrawal of consent, or death.

Also known as: REGN2810
Cohort A: Unmethylated MGMT PromoterCohort B: Methylated MGMT Promoter

Radiation therapy (RT) will begin no later than 42 days after surgical intervention, and should start approximately 2 weeks after Day 0. RT will be given for three weeks.

Cohort A: Unmethylated MGMT PromoterCohort B: Methylated MGMT Promoter

Temozolomide (TMZ) will be given daily during radiation therapy (RT) at a dose of 75 milligrams per square meter (mg/m\^2).

Cohort A: Unmethylated MGMT PromoterCohort B: Methylated MGMT Promoter

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Newly-diagnosed brain cancer with histopathological diagnosis of GBM;
  • Karnofsky Performance Status (KPS) rating of \>/=70 at baseline;
  • Receive dexamethasone equivalent dose \</=2 mg per day, stable or decreased for \>/= three days prior to Day 0;
  • Recovery from the effects of prior GBM surgery as defined by the Investigator;
  • Electrocardiogram (ECG) with no clinically significant findings as assessed by the Investigator;
  • Adequate organ function as demonstrated by hematological, renal, hepatic laboratory assessments;
  • Agree that during the trial, men will not father a child, and women cannot be or become pregnant. Participants must be of non-child bearing potential or agree to use one highly effective or combined contraceptive methods that result in a failure rate of \<1% per year during the treatment period and at least through week 12 after last dose;
  • Ability to tolerate magnetic resonance imaging (MRI).

You may not qualify if:

  • Presence of greater than 1 cm x 1 cm residual tumor enhancement on postoperative MRI;
  • Multifocal disease or leptomeningeal disease (LM) disease on post-operative MRI;
  • Not scheduled to start radiation within 42 days of surgical resection of tumor;
  • Dexamethasone equivalent dose \>2 mg per day;
  • Prior treatment with an agent that blocks the PD-1/PD-Ligand 1 pathway;
  • Receipt of previous approved or investigative immune modulatory agent within 28 days of receiving the first dose of treatment;
  • Prior treatment with idelalisib;
  • Past, current or planned treatment with tumor treatment fields; oncolytic viral treatment; or prior exposure to an investigational agent or device within 28 days of receiving the first dose of treatment;
  • Allergy or hypersensitivity to cemiplimab or to any of its excipients;
  • History of documented allergic reactions or acute hypersensitivity reaction attributed to antibody treatments;
  • Ongoing or recent (within 5 years) evidence of autoimmune disease that required treatment with systemic immunosuppressive treatments;
  • History of clinically significant, medically unstable disease which, in the judgment of the investigator, would jeopardize the safety of the subject, interfere with trial assessments or endpoint evaluation, or otherwise impact the validity of the trial results.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (21)

City of Hope

Duarte, California, 91010, United States

Location

Stanford University, School of Medicine

Palo Alto, California, 94304, United States

Location

University of California, San Francisco

San Francisco, California, 94143, United States

Location

University of Miami - Sylvester Comprehensive Cancer Center

Miami, Florida, 33136, United States

Location

Moffitt Cancer Center

Tampa, Florida, 33612, United States

Location

Emory University School of Medicine

Atlanta, Georgia, 30322, United States

Location

Dana-Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

Henry Ford Health System

Detroit, Michigan, 48202, United States

Location

Rutgers University - Cancer Institute of New Jersey

New Brunswick, New Jersey, 08901, United States

Location

New York University Langone Medical Center; Perlmutter Cancer Center

New York, New York, 10016, United States

Location

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

Location

Columbia University Medical Center The Neurological Institute of New York

New York, New York, 10032, United States

Location

New York-Presbyterian Hospital/Weill Cornell Medical Center

New York, New York, 10065, United States

Location

University of North Carolina School of Medicine

Chapel Hill, North Carolina, 27599, United States

Location

Stephenson Cancer Center

Oklahoma City, Oklahoma, 73104, United States

Location

Oregon Health & Science University

Portland, Oregon, 97239, United States

Location

University of Pennsylvania Health System: Penn Medicine

Philadelphia, Pennsylvania, 19104, United States

Location

UPMC Cancer Center Neuro-Oncology; UPMC Cancer Pavilion

Pittsburgh, Pennsylvania, 15232, United States

Location

Texas Oncology

Austin, Texas, 78705, United States

Location

Baylor College of Medicine

Houston, Texas, 77030, United States

Location

Huntsman Cancer Institute

Salt Lake City, Utah, 84112, United States

Location

MeSH Terms

Conditions

Glioblastoma

Interventions

rocakinogene sifuplasmidcemiplimabRadiotherapyTemozolomide

Condition Hierarchy (Ancestors)

AstrocytomaGliomaNeoplasms, NeuroepithelialNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Glandular and EpithelialNeoplasms, Nerve Tissue

Intervention Hierarchy (Ancestors)

TherapeuticsDacarbazineTriazenesOrganic ChemicalsImidazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Study Officials

  • Jeffrey Skolnik, MD

    Inovio Pharmaceuticals

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 2, 2018

First Posted

April 9, 2018

Study Start

May 31, 2018

Primary Completion (Estimated)

December 31, 2026

Study Completion (Estimated)

December 31, 2026

Last Updated

May 4, 2026

Record last verified: 2026-05

Locations