NCT03444870

Brief Summary

This randomized, double-blind, placebo-controlled, parallel-group study will evaluate the efficacy and safety of gantenerumab versus placebo in participants with early (prodromal to mild) AD. All participants must show evidence of beta-amyloid pathology. Eligible participants will be randomized 1:1 to receive either subcutaneous (SC) injection of gantenerumab or placebo. The primary efficacy assessment will be performed at the end of the double blind period at week 116. Participants will then be offered to enter into an open-label extension (OLE). Participants not willing to go to the OLE will participate in a long term follow-up period for up to 50 weeks after the last gantenerumab dose.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
1,053

participants targeted

Target at P75+ for phase_3 alzheimer-disease

Timeline
Completed

Started Jun 2018

Longer than P75 for phase_3 alzheimer-disease

Geographic Reach
15 countries

172 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 19, 2018

Completed
4 days until next milestone

First Posted

Study publicly available on registry

February 23, 2018

Completed
3 months until next milestone

Study Start

First participant enrolled

June 6, 2018

Completed
4.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 28, 2022

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

February 17, 2023

Completed
12 months until next milestone

Results Posted

Study results publicly available

January 30, 2024

Completed
Last Updated

January 30, 2024

Status Verified

January 1, 2024

Enrollment Period

4.6 years

First QC Date

February 19, 2018

Results QC Date

December 22, 2023

Last Update Submit

January 25, 2024

Conditions

Outcome Measures

Primary Outcomes (2)

  • DBT Period: Change From Baseline to Week 116 in Global Outcome, as Measured by CDR-SB

    CDR was derived through semi-structured interview with the participant and an appropriate informant, and it rated impairment across six domains: memory, orientation, judgment, and problem solving, community affairs, home and hobbies, and personal care on a 5-point scale for which 0=no impairment, 0.5=questionable impairment, and 1, 2, and 3=mild, moderate, and severe impairment, respectively. The CDR-SB is based on summing each of the domain box scores with total score ranging from 0-18 with higher scores reflecting greater cognitive and functional impairment. A negative change from baseline indicates improvement.

    Baseline, Week 116

  • China Extension: DBT Period: Change From Baseline to Week 116 in Global Outcome, as Measured by CDR-SB

    CDR was derived through semi-structured interview with the participant and an appropriate informant, and it rated impairment across six domains: memory, orientation, judgment, and problem solving, community affairs, home and hobbies, and personal care on a 5-point scale for which 0=no impairment, 0.5=questionable impairment, and 1, 2, and 3=mild, moderate, and severe impairment, respectively. The CDR-SB is based on summing each of the domain box scores with total score ranging from 0-18 with higher scores reflecting greater cognitive and functional impairment. A negative change from baseline indicates improvement.

    Baseline, Week 116

Secondary Outcomes (36)

  • DBT Period: Change From Baseline to Week 116 in Alzheimer Disease Assessment Scale-Cognition Subscale 13 (ADAS-Cog13) Score

    Baseline, Week 116

  • DBT Period: Change From Baseline to Week 116 in Alzheimer's Disease Cooperative Study- Activities of Daily Living (ADCS-ADL) Total Score

    Baseline, Week 116

  • DBT Period: Change From Baseline to Week 116 in Functional Activities Questionnaire (FAQ) Score

    Baseline, Week 116

  • DBT Period: Change From Baseline to Week 116 in Mini-Mental State Examination (MMSE) Total Score

    Baseline, Week 116

  • DBT Period: Change From Baseline to Week 116 in Alzheimer Disease Assessment Scale-Cognition Subscale 11 (ADAS-Cog11) Score

    Baseline, Week 116

  • +31 more secondary outcomes

Study Arms (2)

Gantenerumab

EXPERIMENTAL

Gantenerumab will be administered as SC injections with gradual uptitration.

Drug: Gantenerumab

Placebo

PLACEBO COMPARATOR

Placebo will be administered as SC injections with gradual uptitration.

Drug: Placebo

Interventions

Gantenerumab will be administered as per the schedule specified in the respective arm.

Also known as: RO4909832
Gantenerumab

Placebo will be administered as per the schedule specified in the respective arm.

Placebo

Eligibility Criteria

Age50 Years - 90 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Meets National Institute on Aging/Alzheimer's Association (NIAAA) core clinical criteria for probable AD dementia or prodromal AD (consistent with the NIAAA diagnostic criteria and guidelines for mild cognitive impairment)
  • Evidence of the AD pathological process, as confirmed by CSF tau/A-beta42or amyloid PET scan
  • Demonstrated abnormal memory function
  • MMSE score greater than or equal to 22 (≥ 22)
  • Clinical dementia rating-global score (CDR-GS) of 0.5 or 1.0
  • Availability of a reliable study partner who accepts to participate in study procedures throughout the 2 years duration of study
  • If receiving symptomatic AD medications, the dosing regimen must have been stable for 3 months prior to screening and until randomization
  • For enrollment in the China extension, patients must have residence in mainland China, Hong Kong, or Taiwan and be of Chinese ancestry
  • For women of childbearing potential: agreement to remain abstinent (refrain from heterosexual intercourse) or use contraceptive methods

You may not qualify if:

  • Any evidence of a condition other than AD that may affect cognition
  • History of schizophrenia, schizoaffective disorder, major depression, or bipolar disorder
  • History or presence of clinically evident systemic vascular disease that in the opinion of the investigator has the potential to affect cognitive function
  • History or presence of clinically evident cerebrovascular disease
  • History or presence of posterior reversible encephalopathy syndrome
  • History or presence of any stroke with clinical symptoms within the past 12 months, or documented history within the last 6 months of an acute event that is consistent with a transient ischemic attack
  • History of severe, clinically significant CNS trauma
  • History or presence of intracranial mass (e.g., glioma, meningioma) that could potentially impair cognition
  • Presence of infections that affect brain function or history of infections that resulted in neurologic sequelae
  • History or presence of systemic autoimmune disorders that potentially cause progressive neurologic disease with associated cognitive deficits
  • At risk for suicide in the opinion of the investigator
  • Alcohol and/or substance abuse or dependants in past 2 years
  • Relevant brain hemorrhage, bleeding disorder and cerebrovascular abnormalities
  • Any contraindications to brain MRI
  • Unstable or clinically significant cardiovascular, kidney or liver disease
  • +8 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (172)

Center for Neurosciences

Tucson, Arizona, 85718, United States

Location

Global Clinical Trials; Irvine, CA

Irvine, California, 92614, United States

Location

Sutter Medical Group, Neurology

Sacramento, California, 95816, United States

Location

Syrentis Clinical Research

Santa Ana, California, 92705, United States

Location

California Neuroscience Research Medical Group, Inc

Sherman Oaks, California, 91403, United States

Location

Research Center for Clinical Studies, Inc.

Norwalk, Connecticut, 06851, United States

Location

JEM Research LLC

Atlantis, Florida, 33462, United States

Location

Bradenton Research Center

Bradenton, Florida, 34205, United States

Location

Brain Matters Research, Inc.

Delray Beach, Florida, 33445, United States

Location

Alzheimer?s Research and Treatment Center

Wellington, Florida, 33414, United States

Location

Columbus Memory Center

Columbus, Georgia, 31909, United States

Location

Center for Advanced Research & Education

Gainesville, Georgia, 30501, United States

Location

Southern Illinois University, School of Medicine

Springfield, Illinois, 62702, United States

Location

Fort Wayne Neurological Center

Fort Wayne, Indiana, 46805, United States

Location

Via Christi Research

Wichita, Kansas, 67214, United States

Location

Precise Research Centers

Flowood, Mississippi, 39232, United States

Location

University of Mississippi Medical Center

Jackson, Mississippi, 39216, United States

Location

Advanced Memory Research Institute of NJ

Toms River, New Jersey, 08755, United States

Location

Neurological Associates of Long Island, PC

Lake Success, New York, 11042, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

Ohio State University; College of Medicine

Columbus, Ohio, 43210, United States

Location

Abington Neurological Associates

Abington, Pennsylvania, 19001, United States

Location

The Clinical Trial Center, LLC

Jenkintown, Pennsylvania, 19046, United States

Location

Drexel University; College of Medicine

Philadelphia, Pennsylvania, 19102, United States

Location

Coastal Neurology

Port Royal, South Carolina, 29935, United States

Location

Senior Adults Specialty Research

Austin, Texas, 78757, United States

Location

Neurology Consultants of Dallas; Research Department

Dallas, Texas, 75243, United States

Location

Wasatch Clinical Research, LLC

Salt Lake City, Utah, 84107, United States

Location

University of Virginia

Charlottesville, Virginia, 22906, United States

Location

Sentara Neurology Specialists

Norfolk, Virginia, 23507, United States

Location

Neurological Associates, Inc.

Richmond, Virginia, 23229, United States

Location

National Clinical Research Inc.-Richmond

Richmond, Virginia, 23294, United States

Location

UW Wisconsin-Madison

Madison, Wisconsin, 53705, United States

Location

St Vincent's Hospital Sydney; Neurology

Darlinghurst, New South Wales, 2010, Australia

Location

Central Coast Neurosciences Research

Erina, New South Wales, 2250, Australia

Location

Southern Neurology

Kogarah, New South Wales, 2217, Australia

Location

The Queen Elizabeth Hospital; Neurology

Woodville, South Australia, 5011, Australia

Location

Heidelberg Repatriation Hospital; Medical and Cognitive Research Centre

Heidelberg West, Victoria, 3081, Australia

Location

Neuro Trials Victoria

Noble Park, Victoria, 3174, Australia

Location

Australian Alzheimer's Research Foundation

Nedlands, Western Australia, 6009, Australia

Location

Hospital Nossa Senhora das Graças; Setor de Pesquisa em Neurologia

Curitiba, Paraná, 80810-040, Brazil

Location

Instituto de Neurologia de Curitiba

Curitiba, Paraná, 81210-310, Brazil

Location

Clinica Clinilive ltda

Maringá, Paraná, 87013-250, Brazil

Location

Hospital das Clinicas - UFRGS

Porto Alegre, Rio Grande do Sul, 90035-903, Brazil

Location

Clínica Dr. Norton Sayeg LTDA - EPP

São Paulo, São Paulo, 04534-011, Brazil

Location

Hospital das Clinicas - FMUSP_X; Neurologia

São Paulo, São Paulo, 05403-000, Brazil

Location

Medical Arts Health Research Group

Penticton, British Columbia, V1Y 1Z9, Canada

Location

The Medical Arts Health Research Group - West Vancouver

Vancouver, British Columbia, V7T 2Z3, Canada

Location

Parkwood Hospital; Geriatric Medicine

London, Ontario, N6C 5J1, Canada

Location

Centre for Memory and Aging

Toronto, Ontario, M4G 3E8, Canada

Location

Sunnybrook Health Sciences Centre

Toronto, Ontario, M4N 3M5, Canada

Location

St. Michael'S Hospital

Toronto, Ontario, M5B 1W8, Canada

Location

Baycrest Health Sciences

Toronto, Ontario, M6A 2E1, Canada

Location

Devonshire Clinical Research

Woodstock, Ontario, N4S 5P5, Canada

Location

Center for Diagnosis and Research on Alzheimer's disease

Greenfield Park, Quebec, J4V 2J2, Canada

Location

Q & T Research Sherbrooke

Sherbrooke, Quebec, J1J 2G2, Canada

Location

Alpha Recherche Clinique

Québec, G3K 2P8, Canada

Location

China-Japan Friendship Hospital

Beijing, 100029, China

Location

Beijing Anding Hospital, Capital Medical University

Beijing, 100032, China

Location

Beijing Tian Tan Hospital,Capital Medical University

Beijing, 100071, China

Location

West China Hospital, Sichuan University

Chengdu, 610041, China

Location

The First Affiliated Hospital, Chongqing Medical University

Chongqing, 400016, China

Location

Fujian Medical University Union Hospital

Fuzhou, 350001, China

Location

Sun Yat-sen Memorial Hospital; Neurology

Guangzhou, 510000, China

Location

Guangdong Provincial People's Hospital; Breast

Guangzhou, 510180, China

Location

Guangzhou First Municipal People's Hospital

Guangzhou, 510180, China

Location

The Second Affiliated Hospital, Zhejiang University

Hangzhou, 310009, China

Location

Sir Run Run Shaw Hospital

Hangzhou, 310018, China

Location

Anhui Provincial Hospital

Hefei, 230001, China

Location

The First Affiliated Hospital of Anhui Medical University

Hefei, 230022, China

Location

The Second Affiliated Hospital to Nanchang University

Nanchang, 330006, China

Location

Nanjing Drum Tower Hospital, the Affiliated Hospital of Nanjing University Medical School

Nanjing, 210008, China

Location

Zhongda Hospital Affiliated to Southeast University

Nanjing, 210009, China

Location

Jiangsu Province Hospital (the First Affiliated Hospital With Nanjing Medical University)

Nanjing, 210029, China

Location

Ruijin Hospital Shanghai Jiaotong University School of Medicine

Shanghai, 200025, China

Location

Shanghai Mental Health Center

Shanghai, 200030, China

Location

Huashan Hospital Affiliated to Fudan University

Shanghai, 200040, China

Location

Shanghai First People's Hospital

Shanghai, 200080, China

Location

Xinhua Hospital Affiliated to Shanghai Jiao Tong University School of Medicine

Shanghai, 200092, China

Location

Shanghai Sixth People's Hospital Affiliated to Shanghai Jiao Tong University School of Medicine

Shanghai, 200233, China

Location

The University of Hong Kong-Shenzhen Hospital; Local Ethic Committee

Shenzhen, 518053, China

Location

Tianjin Medical University General Hospital

Tianjin, 300052, China

Location

The First Affiliated Hospital of Wenzhou Medical College

Wenzhou, 325000, China

Location

Northern Jangsu People's Hospital

Yangzhou, 225001, China

Location

Henan Provincial People's Hospital

Zhengzhou, 450003, China

Location

CHU Amiens Hopital Sud; Neurologie

Amiens Cedex1, 80054, France

Location

Hôpital Avicenne; Centre de Recherche Clinique

Bobigny, 93009, France

Location

Groupement Hospitalier Est - Hôpital Neurologique; Neurologie A (U502)

Bron, 69677, France

Location

CHU de la Timone - Hopital d Adultes; Service de Neurologie

Marseille, 13005, France

Location

Hôpital Lariboisière

Paris, 75010, France

Location

CHU Poitiers - Hopital La Miletrie

Poitiers, 86000, France

Location

CHU Strasbourg Hôpital Hautepierre

Strasbourg, 67098, France

Location

Gerontopole; Centre de Recherche clinique

Toulouse, 31059, France

Location

Hopital des Charpennes

Villeurbanne, 69100, France

Location

Ambulates Gesundheitszentrum der Charité GmbH; MVZ Neurologie Campus Benjamin Franklin

Berlin, 12200, Germany

Location

ECRC Experimental and Clinical Research Center, Charité Campus Berlin Buch, Memory Clinic

Berlin, 13125, Germany

Location

St. Josef-Hospital, Klinik für Neurologie

Bochum, 44791, Germany

Location

Universitätsklinikum Köln; Klinik und Poliklinik für Psychiatrie und Psychotherapie

Cologne, 50937, Germany

Location

PANAKEIA - Arzneimittelforschung Leipzig GmbH

Leipzig, 04275, Germany

Location

Universitätsmedizin derJohannes Gutenberg-Universität Mainz;Klinik für Psychiatrie und Psychotherapi

Mainz, 55131, Germany

Location

Klinikum rechts der Isar der TU München; Klinik für Psychiatrie und Psychotherapie

München, 81675, Germany

Location

Universitätsklinikum Münster; Klinik und Poliklinik für Neurologie

Münster, 48149, Germany

Location

Universitätsklinikum Rostock Zentrum für Nervenheilkunde

Rostock, 18147, Germany

Location

Universitätsklinikum Ulm; Klinik für Neurologie

Ulm, 89081, Germany

Location

Studienzentrum Nordwest Dr med Joachim Springub Herr Wolfgang Schwarz

Westerstede, 26655, Germany

Location

Forschungszentrum Ruhr

Witten, 58455, Germany

Location

Semmelweis University; Department of Neurology

Budapest, 1083, Hungary

Location

Nuovo Ospedale Civile S. Agostino-Estense; Clinica Neurologica ? Dipartimento di Neuroscienze

Modena, Emilia-Romagna, 41126, Italy

Location

Fondazione Santa Lucia IRCCS; Neurologia e Riabilitazione Neurologica

Rome, Lazio, 00179, Italy

Location

Umberto I Policlinico di Roma-Università di Roma La Sapienza

Rome, Lazio, 00185, Italy

Location

Ospedale San Giovanni Calibita Fatebenefratell;Neurologia

Rome, Lazio, 00186, Italy

Location

IRCCS ?Centro S. Giovanni di Dio? Fatebenefratelli -UO Alzheimer

Brescia, Lombardy, 25125, Italy

Location

IRCCS Ospedale San Raffaele; Centro Disturbi della Memoria

Milan, Lombardy, 20132, Italy

Location

ASST DI MONZA; Neurologia

Monza, Lombardy, 20900, Italy

Location

IRCCS Neuromed; Neurologia I-Centro studio e cura delle demenze e UVA

Pozzilli, Molise, 86077, Italy

Location

AO Città della Salute e della Scienza Osp.S.Giov.Battista Molinette; SC Geriatria

Turin, Piedmont, 10126, Italy

Location

Dipartimento delle Patologie Emergenti; Azienda Ospedaliera Universitaria Policlinico Paolo Giaccone

Palermo, Sicily, 90127, Italy

Location

Medical Corporation Hakuyokai Kashiwado Hospital

Chiba, 260-8656, Japan

Location

Inage Neurology and Memory Clinic

Chiba, 263-0043, Japan

Location

Juntendo University Urayasu Hospital

Chiba, 279-0021, Japan

Location

Southern Tohoku Medical Clinic

Fukushima, 963-8052, Japan

Location

Yuai Clinic

Kanagawa, 223-0059, Japan

Location

Shonan Kamakura General Hospital

Kanagawa, 247-8533, Japan

Location

Mishima Hospital

Niigata, 940-2302, Japan

Location

NHO Shizuoka Institute of Epilepsy and Neurological Disorders

Shizuoka, 420-8688, Japan

Location

Shizuoka City Shimizu Hospital

Shizuoka, 424-0911, Japan

Location

Jichiidai Station Brain Clinic

Tochigi, 329-0403, Japan

Location

Yotsuya Medical Cube

Tokyo, 102-0084, Japan

Location

Tokyo Medical and Dental University Hospital

Tokyo, 113-8519, Japan

Location

Tokyo Medical University Hospital

Tokyo, 160-0023, Japan

Location

Tokyo Metropolitan Geriatric Hospital

Tokyo, 173-0015, Japan

Location

Nozomi Memory Clinic

Tokyo, 181-0013, Japan

Location

National Center of Neurology and Psychiatry

Tokyo, 187-8551, Japan

Location

P-One Clinic

Tokyo, 192-0071, Japan

Location

Yamagata Tokusyukai Hospital

Yamagata, 990-0834, Japan

Location

Vilnius University Hospital Santariskiu Clinics; Neurology

Vilnius, 08661, Lithuania

Location

Hospital IV Alberto Sabogal Sologuren; Unidad de Investigacion

Bellavista, Callao 2, Peru

Location

Clinica Internacional; Unidad De Investigacion

Lima, 15001, Peru

Location

Hospital Nacional Dos de Mayo; Unidad de Investigacion de Neurologia

Lima, 15003, Peru

Location

Hospital Nacional Cayetano Heredia; Servicio de Neurologia

San Martín de Porres, 15102, Peru

Location

FSBHI Siberian Clinical Center of the Federal Medical and Biological Agency

Krasnoyarsk, Krasnoyarsk Krai, 660037, Russia

Location

University ?linic of headaches

Moscow, Moscow Oblast, 121467, Russia

Location

City Clin Hosp n.a. S.P.Botkin

Moscow, Moscow Oblast, 125101, Russia

Location

Central Clinical Hospital #2 N.A. Semashko OAO RJHD

Moskva, Moscow Oblast, 107150, Russia

Location

Russian Medical Military Academy n.a. S.M.Kirov; Neurology Department

Saint Petersburg, Sankt-Peterburg, 194044, Russia

Location

Vertebronevrologiya LLC

Kazan', Tatarstan Republic, 420047, Russia

Location

State autonomous institution of healthcare Inter-regional clinical and diagnostic center

Kazan', Tatarstan Republic, 420101, Russia

Location

City Clinical Hospital # 2 n.a. V.I. Razumovsky

Saratov, 410028, Russia

Location

Nebbiolo Center for Clinical Trials

Tomsk, 634009, Russia

Location

Hospital Universitari de Bellvitge; Servicio de Neurologia

L'Hospitalet de Llobregat, Barcelona, 08907, Spain

Location

Hospital General De Catalunya; Servicio de Neurologia

Sant Cugat del Vallès, Barcelona, 8195, Spain

Location

Hospital Universitario Marques de Valdecilla; Servicio de Neurología

Santander, Cantabria, 39011, Spain

Location

Hospital San Pedro; Servicio de Neurología

Logroño, La Rioja, 26006, Spain

Location

HM Universitario Puerta del Sur CINAC (C.Integ.Neuroc);; Servicio de Psiquiatría

Móstoles, Madrid, 28938, Spain

Location

Hospital General Universitario de Albacete; Servicio de Neurología

Albacete, Spain

Location

Hospital Vall d'Hebron; Servicio de Neurología

Barcelona, 08035, Spain

Location

Hospital Clinic i Provincial; Servicio de Neurologia

Barcelona, 08036, Spain

Location

Hospital de la Santa Creu i Sant Pau; Servicio de Neurologia

Barcelona, 08041, Spain

Location

Hospital Universitario Reina Sofia; Servicio de Neurologia

Córdoba, 14004, Spain

Location

Hospital Ramon y Cajal; Servicio de Neurologia

Madrid, 28034, Spain

Location

Hospital Ruber Internacional; Servicio de Neurología

Madrid, 28034, Spain

Location

Hospital Universitario 12 de Octubre; Servicio de Neurologia

Madrid, 28041, Spain

Location

Complejo Asistencial Universitario de Salamanca; Servicio de Psiquiatría

Salamanca, 37005, Spain

Location

Hospital Virgen del Rocío; Servicio de Neurología

Seville, 41013, Spain

Location

Hospital Universitario Dr. Peset; Servicio de Neurologia

Valencia, 46017, Spain

Location

Servicio de Neurología Hospital Viamed Montecanal.

Zaragoza, 50012, Spain

Location

Changhua Christian Hospital; Neurology

Changhua County, 500, Taiwan

Location

Kaohsiung Medical University Hospital; Neurology

Kaohsiung City, 807, Taiwan

Location

Chang Gung Memorial Foundation - Kaohsiung - Neurology

Niaosong Dist., 83301, Taiwan

Location

China Medical University Hospital; Neurology

North Dist., 40447, Taiwan

Location

National Taiwan University Hospital; Neurology

Taipei, 100, Taiwan

Location

Chang Gung Memorial Foundation - Linkou - Neurology

Taoyuan District, 333, Taiwan

Location

Related Publications (5)

  • Chandler JM, Lansdall CJ, Ye W, McDougall F, Belger M, Toth B, Mi X, Sink KM, Atkins AS. The Alzheimer's Disease Cooperative Study - Activities of Daily Living dependence score: revision and validation of an algorithm evaluating patient dependence across the spectrum of AD severity. J Prev Alzheimers Dis. 2025 Sep;12(8):100261. doi: 10.1016/j.tjpad.2025.100261. Epub 2025 Jul 1.

  • Asada T, Thanasopoulou A, Delmar P, Wojtowicz J, Smith J, Yoshiyama Y, Yokoi K, Watanabe C, Isozaki M, Ozaki R, Ishida T, Tatsuda H, Tamaoka A. Japanese participant data from three gantenerumab trials in early Alzheimer's disease. Alzheimers Dement. 2025 Apr;21(4):e70192. doi: 10.1002/alz.70192.

  • Bittner T, Tonietto M, Klein G, Belusov A, Illiano V, Voyle N, Delmar P, Scelsi MA, Gobbi S, Silvestri E, Barakovic M, Napolitano A, Galli C, Abaei M, Blennow K, Barkhof F. Biomarker treatment effects in two phase 3 trials of gantenerumab. Alzheimers Dement. 2025 Feb;21(2):e14414. doi: 10.1002/alz.14414. Epub 2025 Jan 30.

  • Salloway S, Wojtowicz J, Voyle N, Lane CA, Klein G, Lyons M, Rossomanno S, Mazzo F, Bullain S, Barkhof F, Bittner T, Schneider A, Grundman M, Aldea R, Boada M, Smith J, Doody R. Amyloid-Related Imaging Abnormalities (ARIA) in Clinical Trials of Gantenerumab in Early Alzheimer Disease. JAMA Neurol. 2025 Jan 1;82(1):19-29. doi: 10.1001/jamaneurol.2024.3937.

  • Bateman RJ, Smith J, Donohue MC, Delmar P, Abbas R, Salloway S, Wojtowicz J, Blennow K, Bittner T, Black SE, Klein G, Boada M, Grimmer T, Tamaoka A, Perry RJ, Turner RS, Watson D, Woodward M, Thanasopoulou A, Lane C, Baudler M, Fox NC, Cummings JL, Fontoura P, Doody RS; GRADUATE I and II Investigators and the Gantenerumab Study Group. Two Phase 3 Trials of Gantenerumab in Early Alzheimer's Disease. N Engl J Med. 2023 Nov 16;389(20):1862-1876. doi: 10.1056/NEJMoa2304430.

MeSH Terms

Conditions

Alzheimer Disease

Interventions

gantenerumab

Condition Hierarchy (Ancestors)

DementiaBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesTauopathiesNeurodegenerative DiseasesNeurocognitive DisordersMental Disorders

Results Point of Contact

Title
Medical Communications
Organization
Hoffmann-La Roche

Study Officials

  • Clinical Trials

    Hoffmann-La Roche

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 19, 2018

First Posted

February 23, 2018

Study Start

June 6, 2018

Primary Completion

December 28, 2022

Study Completion

February 17, 2023

Last Updated

January 30, 2024

Results First Posted

January 30, 2024

Record last verified: 2024-01

Data Sharing

IPD Sharing
Will share

Qualified researchers may request access to individual patient level data through the clinical study data request platform (www.clinicalstudydatarequest.com). Further details on Roche's criteria for eligible studies are available here (https://clinicalstudydatarequest.com/Study-Sponsors/Study-Sponsors-Roche.aspx). For further details on Roche's Global Policy on the Sharing of Clinical Information and how to request access to related clinical study documents, see here (https://www.roche.com/research\_and\_development/who\_we\_are\_how\_we\_work/clinical\_trials/our\_commitment\_to\_data\_sharing.htm).

Locations