NCT04437511

Brief Summary

The reason for this study is to see how safe and effective the study drug donanemab is in participants with early Alzheimer's disease. Additional participants will be enrolled to an addendum safety cohort. The participants will be administered open-label donanemab. Trial participants who were dosed with donanemab in the main study will be enrolled to a 3-year follow up addendum. No study drug will be administered during this follow up.

Trial Health

82
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,736

participants targeted

Target at P75+ for phase_3 alzheimer-disease

Timeline
30mo left

Started Jun 2020

Longer than P75 for phase_3 alzheimer-disease

Geographic Reach
9 countries

274 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress70%
Jun 2020Nov 2028

First Submitted

Initial submission to the registry

June 17, 2020

Completed
1 day until next milestone

First Posted

Study publicly available on registry

June 18, 2020

Completed
1 day until next milestone

Study Start

First participant enrolled

June 19, 2020

Completed
2.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 14, 2023

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

May 20, 2024

Completed
4.5 years until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2028

Expected
Last Updated

August 29, 2025

Status Verified

August 1, 2025

Enrollment Period

2.8 years

First QC Date

June 17, 2020

Results QC Date

April 10, 2024

Last Update Submit

August 11, 2025

Conditions

Keywords

Alzheimer'sDementiaCognitive ImpairmentAmyloid Plaque

Outcome Measures

Primary Outcomes (2)

  • Change From Baseline on the Integrated Alzheimer's Disease Rating Scale (iADRS) (Overall Population)

    Integrated Alzheimer's Disease Rating Scale is used to assess whether donanemab slows down the clinical decline associated with AD compared with placebo. iADRS is an integrated assessment of cognition and daily function comprised of items from the ADAS-Cog13 and the Alzheimer's disease cooperative study-instrumental activities of daily living scale (ADCS-iADL). The scale ranges from 0 to 144, where lower scores indicate worse performance and higher score indicates better performance. Least Squares (LS) Mean value was adjusted for basis expansion terms (two terms), basis expansion term-by-treatment interaction, and covariates for age at baseline, pooled investigator, baseline tau level, and baseline acetylcholinesterase inhibitor (AchI)/Memantine use.

    Baseline, Week 76

  • Change From Baseline on the Integrated Alzheimer's Disease Rating Scale (iADRS) (Intermediate (Low-medium) Tau Population)

    Integrated Alzheimer's Disease Rating Scale is used to assess whether donanemab slows down the clinical decline associated with AD compared with placebo. iADRS is an integrated assessment of cognition and daily function comprised of items from the Alzheimer's disease assessment scale-cognitive subscale (ADAS-Cog13) and the Alzheimer's disease cooperative study-instrumental activities of daily living scale (ADCS-iADL). The scale ranges from 0 to 144, where lower scores indicate worse performance and higher score indicates better performance. LS Mean value was adjusted for basis expansion terms (two terms), basis expansion term-by-treatment interaction, and covariates for age at baseline, pooled investigator, and baseline AchI/Memantine use.

    Baseline, Week 76

Secondary Outcomes (13)

  • Change From Baseline on the Mini Mental State Examination (MMSE) Score (Overall Population)

    Baseline, Week 76

  • Change From Baseline on the Mini Mental State Examination (MMSE) Score (Intermediate (Low-medium) Tau Population)

    Baseline, Week 76

  • Change From Baseline on the Alzheimer's Disease Assessment Scale - Cognitive Subscale (ADAS-Cog13) (Overall Population)

    Baseline, Week 76

  • Change From Baseline on the Alzheimer's Disease Assessment Scale - Cognitive Subscale (ADAS-Cog13) (Intermediate (Low-medium) Tau Population)

    Baseline, Week 76

  • Change From Baseline on the Clinical Dementia Rating Scale-Sum of Boxes (CDR-SB) (Overall Population)

    Baseline, Week 76

  • +8 more secondary outcomes

Study Arms (2)

Donanemab

EXPERIMENTAL

Participants received 700 milligram (mg) Donanemab every 4 weeks (Q4W) x 3 doses, then 1400 mg Q4W given intravenously (IV) for up to 72 weeks

Drug: Donanemab

Placebo

PLACEBO COMPARATOR

Participants received placebo given IV.

Drug: Placebo

Interventions

Given IV

Also known as: LY3002813
Donanemab

Given IV

Placebo

Eligibility Criteria

Age60 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Gradual and progressive change in memory function reported by participants or informants for ≥ 6 months
  • MMSE score of 20 to 28 (inclusive) at baseline
  • Meet 18F flortaucipir PET scan (central read) criteria - does not apply to safety cohort
  • Meet 18F florbetapir PET scan (central read) criteria
  • Have a study partner who will provide written informed consent to participate

You may not qualify if:

  • Contraindication to MRI or PET scans
  • Current treatment with immunoglobulin G (IgG) therapy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (274)

Gilbert Neurology

Gilbert, Arizona, 85297, United States

Location

Xenoscience

Phoenix, Arizona, 85004, United States

Location

Banner Alzheimer's Institute

Phoenix, Arizona, 85006, United States

Location

Perseverance Research Center

Scottsdale, Arizona, 85254, United States

Location

Banner Sun Health Research Institute

Sun City, Arizona, 85351, United States

Location

Banner Alzheimer's Institute Tucson

Tucson, Arizona, 85718, United States

Location

Center for Neurosciences

Tucson, Arizona, 85718, United States

Location

Health Initiatives Research

Fayetteville, Arkansas, 72703, United States

Location

North County Neurology Associates

Carlsbad, California, 92011, United States

Location

Wr- Pri, Llc

Encino, California, 91316, United States

Location

Neuro-Pain Medical Center

Fresno, California, 93710, United States

Location

Neurology Center of North Orange County

Fullerton, California, 92835, United States

Location

Irvine Clinical Research

Irvine, California, 92614, United States

Location

Kaizen Brain Center

La Jolla, California, 92037, United States

Location

Senior Clinical Trials, Inc.

Laguna Hills, California, 92653, United States

Location

Collaborative Neuroscience Research, LLC

Los Alamitos, California, 90720, United States

Location

USC Keck School of Medicine

Los Angeles, California, 90033, United States

Location

Clinical Research Institute

Los Angeles, California, 90048, United States

Location

Neurovations

Napa, California, 94558, United States

Location

Hoag Memorial Hospital Presbyterian

Newport Beach, California, 92663, United States

Location

Stanford Neuroscience Health Center

Palo Alto, California, 94304, United States

Location

SC3 Research - Pasadena

Pasadena, California, 91105, United States

Location

PCND Neurology

Poway, California, 92064, United States

Location

Anderson Clinical Research

Redlands, California, 92374, United States

Location

Artemis Institute for Clinical Research

San Diego, California, 92103, United States

Location

Pacific Research Network

San Diego, California, 92103, United States

Location

Sharp Neurocognitive Research Center

San Diego, California, 92123, United States

Location

UCSF Memory and Aging Center

San Francisco, California, 94158, United States

Location

Syrentis Clinical Research

Santa Ana, California, 92705, United States

Location

California Neuroscience Research Medical Group, Inc.

Sherman Oaks, California, 91403, United States

Location

Tilda Research

Tustin, California, 92780, United States

Location

Mountain Neurological Research Center

Basalt, Colorado, 81621, United States

Location

Alpine Clinical Research Center

Boulder, Colorado, 80301, United States

Location

Colorado Springs Neurological Associates

Colorado Springs, Colorado, 80907, United States

Location

Colorado Neurological Research Center, PC

Denver, Colorado, 80210, United States

Location

Institute for Neurodegenerative Disorders

New Haven, Connecticut, 06510, United States

Location

Yale University, Alzheimer's Disease Research Unit

New Haven, Connecticut, 06510, United States

Location

Research Center for Clinical Studies

Norwalk, Connecticut, 06851, United States

Location

Ki Health Partners, LLc, dba New England Institute for Clinical Research

Stamford, Connecticut, 06905, United States

Location

Georgetown University Medical Center

Washington D.C., District of Columbia, 20007, United States

Location

JEM Research Institute

Atlantis, Florida, 33462, United States

Location

VIN-Julie Schwartzbard

Aventura, Florida, 33180, United States

Location

Neurology Offices of South Florida

Boca Raton, Florida, 33428, United States

Location

SFM Clinical Research

Boca Raton, Florida, 33487, United States

Location

Brain Matters Research

Delray Beach, Florida, 33445, United States

Location

Cohen Medical Associates

Delray Beach, Florida, 33446, United States

Location

Integrity Clinical Research

Doral, Florida, 33166, United States

Location

Neuropsychiatric Research Center of Southwest Florida

Fort Myers, Florida, 33912, United States

Location

Finlay Medical Research

Greenacres City, Florida, 33467, United States

Location

MD Clinical

Hallandale, Florida, 33009, United States

Location

AGA Clinical Trials

Hialeah, Florida, 33012, United States

Location

Indago Research & Health Center, Inc

Hialeah, Florida, 33012, United States

Location

Infinity Clinical Research, LLC

Hollywood, Florida, 33024, United States

Location

Encore Research Group- Jacksonville Center for Clinical Research

Jacksonville, Florida, 32216, United States

Location

Accel Research Sites - Lakeland Clinical Research Unit

Lakeland, Florida, 33803, United States

Location

ClinCloud - Maitland

Maitland, Florida, 32751, United States

Location

Merritt Island Medical Research, LLC

Merritt Island, Florida, 32952, United States

Location

Homestead Associates in Research

Miami, Florida, 33032, United States

Location

Finlay Medical Research

Miami, Florida, 33126, United States

Location

Optimus U Corporation

Miami, Florida, 33135, United States

Location

Miami Jewish health

Miami, Florida, 33137, United States

Location

Future Care Solution

Miami, Florida, 33142, United States

Location

Allied Biomedical Research Institute

Miami, Florida, 33155, United States

Location

New Horizon Research Center

Miami, Florida, 33165, United States

Location

Florida International Research Center

Miami, Florida, 33173, United States

Location

Ezy Medical Research

Miami, Florida, 33175, United States

Location

Miami Dade Medical Research Institute, LLC

Miami, Florida, 33176, United States

Location

The Neurology Research Group

Miami, Florida, 33176, United States

Location

VIN-Victor Faradji

Miami, Florida, 33176, United States

Location

Mount Sinai Cancer Center

Miami Beach, Florida, 33140, United States

Location

Goji Group - Research Trials Group

Miami Lakes, Florida, 33016, United States

Location

Collier Neurologic Specialists

Naples, Florida, 34105, United States

Location

Suncoast Clinical Research, Inc.

New Port Richey, Florida, 34652, United States

Location

Renstar Medical Research

Ocala, Florida, 34470, United States

Location

Sensible Healthcare, LLC

Ocoee, Florida, 34761, United States

Location

Medical Research Group of Central Florida

Orange City, Florida, 32763, United States

Location

Synexus Clinical Research US, Inc.

Orlando, Florida, 32806, United States

Location

Headlands Research Orlando

Orlando, Florida, 32819, United States

Location

IMIC, Inc.

Palmetto Bay, Florida, 33157, United States

Location

Emerald Coast Neurology - Airport Boulevard

Pensacola, Florida, 32504, United States

Location

Quantum Laboratories Clinical Research

Pompano Beach, Florida, 33064, United States

Location

Progressive Medical Research

Port Orange, Florida, 32127, United States

Location

Intercoastal Medical Group

Sarasota, Florida, 34239, United States

Location

Roskamp Institute Clinical Trials Division

Sarasota, Florida, 34243, United States

Location

Suncoast Neuroscience Associates, Inc.

St. Petersburg, Florida, 33713, United States

Location

Alzheimer's Research and Treatment Center

Stuart, Florida, 34997, United States

Location

Brain Matters Research

Stuart, Florida, 34997, United States

Location

Tallahassee Neurological Clinic

Tallahassee, Florida, 32308, United States

Location

Axiom Clinical Research of Florida

Tampa, Florida, 33609, United States

Location

Stedman Clinical Trials

Tampa, Florida, 33613, United States

Location

USF Health Byrd Alzheimer's Institute

Tampa, Florida, 33613, United States

Location

Charter Research - Lady Lake

The Villages, Florida, 32162, United States

Location

Synexus Clinical Research US, Inc.

The Villages, Florida, 32162, United States

Location

Alzheimer's Research and Treatment Center

Wellington, Florida, 33414, United States

Location

Palm Beach Neurology

West Palm Beach, Florida, 33407, United States

Location

Conquest Research

Winter Park, Florida, 32789, United States

Location

Charter Research - Winter Park

Winter Park, Florida, 32803, United States

Location

Gwinnett Research Institute

Buford, Georgia, 30519, United States

Location

Columbus Memory Center, LLC

Columbus, Georgia, 31909, United States

Location

NeuroStudies

Decatur, Georgia, 30030, United States

Location

Center for Advanced Research & Education

Gainesville, Georgia, 30501, United States

Location

Northwest Clinical Trials

Boise, Idaho, 83704, United States

Location

Great Lakes Clinical Trials - Andersonville

Chicago, Illinois, 60640, United States

Location

AMITA Health - Alexian Brothers Neurosciences Institute Clinical Research

Elk Grove Village, Illinois, 60007, United States

Location

Advocate Medical Group

Park Ridge, Illinois, 60068, United States

Location

Southern Illinois University School of Medicine

Springfield, Illinois, 62702, United States

Location

Indiana University

Indianapolis, Indiana, 46202, United States

Location

Josephson Wallack Munshower Neurology, PC

Indianapolis, Indiana, 46256, United States

Location

McFarland Clinic, PC

Ames, Iowa, 50010, United States

Location

Covenant Medical Center

Waterloo, Iowa, 50702, United States

Location

The University of Kansas - Clinical Research Center

Fairway, Kansas, 66205, United States

Location

College Park Family Care Center/Multi Specialty Clinical Res

Overland Park, Kansas, 66212, United States

Location

Cotton O'Neil Clinical Research Center - Central Office

Topeka, Kansas, 66606, United States

Location

Ascension Via Christi Research

Wichita, Kansas, 67214, United States

Location

Maine Medical Center-Maine Medical Partners Neurology

Scarborough, Maine, 04074, United States

Location

Brigham and Women's Hospital

Boston, Massachusetts, 02115, United States

Location

Boston Clinical Trials

Boston, Massachusetts, 02131, United States

Location

NECCR PrimaCare Research

Fall River, Massachusetts, 02721, United States

Location

BTC Network

New Bedford, Massachusetts, 02740, United States

Location

Boston Center for Memory

Newton, Massachusetts, 02459, United States

Location

Donald S. Marks M.D., P.C.

Plymouth, Massachusetts, 02360, United States

Location

Alzheimers Disease Center

Quincy, Massachusetts, 02169, United States

Location

MedVadis Research Corporation

Waltham, Massachusetts, 02451, United States

Location

Adams Clinical

Watertown, Massachusetts, 02472, United States

Location

QUEST Research Institute

Farmington Hills, Michigan, 48334, United States

Location

Precise Research Centers

Flowood, Mississippi, 39232, United States

Location

Citizens Memorial Hospital District

Bolivar, Missouri, 65613, United States

Location

Clinical Research Professionals

Chesterfield, Missouri, 63005, United States

Location

North Kansas City Hospital

North Kansas City, Missouri, 64116, United States

Location

Sharlin Health and Neurology

Ozark, Missouri, 65721, United States

Location

Arch Clinical Trials

St Louis, Missouri, 63141, United States

Location

Las Vegas Medical Research

Las Vegas, Nevada, 89128, United States

Location

The Cognitive and Research Center of New Jersey

Springfield, New Jersey, 07081, United States

Location

Advanced Memory Research Institute of New Jersey

Toms River, New Jersey, 08755, United States

Location

Bio Behavioral Health

Toms River, New Jersey, 08755, United States

Location

Albany Medical College

Albany, New York, 12208, United States

Location

Neurological Associates Albany

Albany, New York, 12208, United States

Location

Dent Neurologic Institute

Amherst, New York, 14226, United States

Location

University at Buffalo - UBMD Neurology

Buffalo, New York, 14203, United States

Location

Clarity Clinical Research

East Syracuse, New York, 13057, United States

Location

NYU Langone Health

New York, New York, 10016, United States

Location

University of Rochester Medical Center

Rochester, New York, 14642, United States

Location

Richmond Behavioral Associates

Staten Island, New York, 10312, United States

Location

SUNY Upstate Medical University

Syracuse, New York, 13210, United States

Location

CHS-Behavioral Health Research

Charlotte, North Carolina, 28211, United States

Location

Guilford Neurologic Associates, Inc

Greensboro, North Carolina, 27405, United States

Location

AMC Research

Matthews, North Carolina, 28105, United States

Location

Carteret Medical Group

Morehead City, North Carolina, 28557, United States

Location

Accellacare - Winston-Salem

Winston-Salem, North Carolina, 27103, United States

Location

NeuroScience Research Center

Canton, Ohio, 44718, United States

Location

Valley Medical Research

Centerville, Ohio, 45459, United States

Location

Rapid Medical Research

Cleveland, Ohio, 44122, United States

Location

Ohio State University

Columbus, Ohio, 43210, United States

Location

University of Cincinnati Physicians Company, LLC

Dayton, Ohio, 45417, United States

Location

Neurology Diagnostics, Inc.

Dayton, Ohio, 45459, United States

Location

IPS Research Company

Oklahoma City, Oklahoma, 73106, United States

Location

Lynn Health Science Institute

Oklahoma City, Oklahoma, 73112, United States

Location

Central States Research

Tulsa, Oklahoma, 74136, United States

Location

Summit Headlands

Portland, Oregon, 97210, United States

Location

Center for Cognitive Health

Portland, Oregon, 97225, United States

Location

Abington Neurological Associates, Ltd.

Abington, Pennsylvania, 19001, United States

Location

Penn Medicine: University of Pennsylvania Health System

Philadelphia, Pennsylvania, 19104, United States

Location

Keystone Clinical Studies

Plymouth Meeting, Pennsylvania, 19462, United States

Location

Rhode Island Mood & Memory Research Institute

East Providence, Rhode Island, 02914, United States

Location

Prism Health Richland Department of Neurology Research

Columbia, South Carolina, 29203, United States

Location

Neurology Clinic, P.C.

Cordova, Tennessee, 38018, United States

Location

Clinical Neuroscience Solutions, Inc. dba CNS Healthcare

Memphis, Tennessee, 38119, United States

Location

Senior Adults Specialty Research

Austin, Texas, 78757, United States

Location

Gadolin Research

Beaumont, Texas, 77702, United States

Location

Kerwin Medical Center

Dallas, Texas, 75231, United States

Location

Neurology Consultants of Dallas, PA

Dallas, Texas, 75243, United States

Location

InSite Clinical Research

DeSoto, Texas, 75115, United States

Location

Houston Methodist Hospital

Houston, Texas, 77030, United States

Location

The University of Texas Health Science Center at Houston

Houston, Texas, 77030, United States

Location

Central Texas Neurology Consultants

Round Rock, Texas, 78681, United States

Location

Glenn Biggs Institute for Alzheimers & Neurodegenerative Diseases

San Antonio, Texas, 78229-3900, United States

Location

The Memory Clinic

Bennington, Vermont, 05201-9810, United States

Location

Integrated Neurology Services - Falls Church

Arlington, Virginia, 22207, United States

Location

Sentara Norfolk General Hospital

Norfolk, Virginia, 23510, United States

Location

National Clinical Research, Inc

Richmond, Virginia, 23294, United States

Location

Northwest Clinical Research Center

Bellevue, Washington, 98007, United States

Location

EvergreenHealth Medical Center

Kirkland, Washington, 98034, United States

Location

University of Washington - Harborview Medical Center

Seattle, Washington, 98104, United States

Location

Kingfisher Cooperative

Spokane, Washington, 99201, United States

Location

Universal Research Group

Tacoma, Washington, 98405, United States

Location

Central Coast Neurosciences Research

Erina, New South Wales, 2250, Australia

Location

St Vincent's Hospital

Sydney, New South Wales, 2010, Australia

Location

HammondCare Greenwich Hospital

Sydney, New South Wales, 2065, Australia

Location

KARA Institute for Neurological Diseases

Sydney, New South Wales, 2113, Australia

Location

NeuroCentrix

Carlton, Victoria, 3053, Australia

Location

Delmont Private Hospital

Glen Iris, Victoria, 3146, Australia

Location

HammondCare

Malvern, Victoria, 3144, Australia

Location

The Alfred Hospital

Melbourne, Victoria, 3004, Australia

Location

The Royal Melbourne Hospital

Parkville, Victoria, 3050, Australia

Location

OCT Research ULC

Kelowna, British Columbia, V1Y 1Z9, Canada

Location

True North Clinical Research

Halifax, Nova Scotia, B3S 1N2, Canada

Location

True North Clinical Research

New Minas, Nova Scotia, B4N 3R7, Canada

Location

SKDS Research Inc.

Newmarket, Ontario, L3Y 5G8, Canada

Location

Ottawa Memory Clinic

Ottawa, Ontario, K1Z 1G3, Canada

Location

Bruyère Research Institute

Ottawa, Ontario, Canada

Location

Kawartha Centre - Redefining Healthy Aging

Peterborough, Ontario, K9H 2P4, Canada

Location

Bluewater Clinical Research Group Inc.

Sarnia, Ontario, N7T 4X3, Canada

Location

Toronto Memory Program

Toronto, Ontario, M3B 2S7, Canada

Location

Sunnybrook Health Sciences Centre

Toronto, Ontario, M4N 3M5, Canada

Location

Baycrest Health Sciences

Toronto, Ontario, M6A 2E1, Canada

Location

Clinique de la Mémoire de l'Outaouais

Gatineau, Quebec, K1Z 1G3, Canada

Location

MoCA Research and Innovation Inc.

Greenfield Park, Quebec, J4V 2J2, Canada

Location

Q&T Research Sherbrooke Inc.

Sherbrooke, Quebec, J1J 2G2, Canada

Location

Diex Recherche Sherbrooke Inc.

Sherbrooke, Quebec, J1L 0H8, Canada

Location

Alpha Recherche Clinique

Québec, G2J 0C4, Canada

Location

ALPHA Recherche Clinique

Québec, G3K 2P8, Canada

Location

Clinline Services

Hostivice, Central Bohemia, 253 01, Czechia

Location

Brain-Soul Therapy

Kladno, Central Bohemia, 272 01, Czechia

Location

A-Shine

Pilsen, Plzeň-město, 30100, Czechia

Location

Clintrial s.r.o.

Prague, Praha 10, 100 00, Czechia

Location

Neurologická Ambulance - Forbeli

Prague, Praha 6, 160 00, Czechia

Location

Neuropsychiatrie

Prague, Praha 6, 160 00, Czechia

Location

Nagoya Ekisaikai Hospital

Nagoya, Aichi-ken, 454-8502, Japan

Location

Chubu Rosai Hospital

Nagoya, Aichi-ken, 455-8530, Japan

Location

Kojunkai Daido Clinic

Nagoya, Aichi-ken, 4570818, Japan

Location

National Center for Geriatrics and Gerontology

Ōbu, Aichi-ken, 474-8511, Japan

Location

Inage Neurology and Memory Clinic

Inage, Chiba, 263-0043, Japan

Location

Matsui e-clinic

Akashi, Hyōgo, 673-0891, Japan

Location

Himeji Central Hospital Affiliated Clinic

Himeji, Hyōgo, 672-8043, Japan

Location

Kobe University Hospital

Kobe, Hyōgo, 650-0017, Japan

Location

Kobe City Medical Center General Hospital

Kobe, Hyōgo, 650-0047, Japan

Location

Kakigi Dementia Happiness Clinic

Kobe, Hyōgo, 657-0825, Japan

Location

Tokyo Medical University Ibaraki Medical Center

Inashiki, Ibaraki, 300-0332, Japan

Location

Memory Clinic Toride

Toride, Ibaraki, 302-0004, Japan

Location

Yokohama City Minato Red Cross Hospital

Yokohama, Kanagawa, 231-0801, Japan

Location

Oita University Hospital

Yufu, Oita Prefecture, 879-5593, Japan

Location

Katayama Medical Clinic

Kurashiki, Okayama-ken, 710-0813, Japan

Location

Honmachi Clinic

Ikeda, Osaka, 563-0058, Japan

Location

Takatsuki General Hospital

Takatsuki, Osaka, 569-1192, Japan

Location

Medical Corporation Chiseikai Tokyo Center Clinic

Chuo-ku, Tokyo, 103-0028, Japan

Location

Moriyama Neuro Center Hospital

Edogawa-ku, Tokyo, 134-0088, Japan

Location

P-One Clinic

Hachiōji, Tokyo, 192-0071, Japan

Location

Clinical Research Hospital Tokyo

Shinjuku-ku, Tokyo, 162-0053, Japan

Location

Tokyo Metro Bokutoh Hospital

Sumida-ku, Tokyo, 130-0022, Japan

Location

Hiroshima Neurology Clinic

Hiroshima, 732-0822, Japan

Location

Koseikai Takeda Hospital

Kyoto, 600-8558, Japan

Location

Ishikawa Clinic

Kyoto, 606-0851, Japan

Location

National hospital Organization Utano National Hospital

Kyoto, 616-8255, Japan

Location

Oita Prefectural Hospital

Ōita, 870-0855, Japan

Location

Itsuki Hospital

Tokushima, 770-0852, Japan

Location

Tokyo Asbo Clinic

Tokyo, 104-0031, Japan

Location

Nippon Medical School Hospital

Tokyo, 113-8603, Japan

Location

Makita General Hospital

Tokyo, 143-0016, Japan

Location

Brain Research Center Den Bosch B.V.

's-Hertogenbosch, North Brabant, 5223 LA, Netherlands

Location

Brain Research Center

Amsterdam, North Holland, 1081 GN, Netherlands

Location

Brain Research Center Zwolle

Zwolle, Overijssel, 8025 AZ, Netherlands

Location

QPS Netherlands B.V

Leeuwarden, Provincie Friesland, 8934 AD, Netherlands

Location

Nzoz Neuro-Kard Ilkowski i Partnerzy SPL

Poznan, Greater Poland Voivodeship, 61-853, Poland

Location

Centrum Medyczne NEUROMED

Bydgoszcz, Kuyavian-Pomeranian Voivodeship, 85-163, Poland

Location

Diamond Clinic

Krakow, Lesser Poland Voivodeship, 31-559, Poland

Location

Ośrodek Badawczo Naukowo Dydaktyczny Chorób Otępiennych Im Księdza Henryka Kardynała Gulbinowicza Uniwersy -T

Ścinawa, Lower Silesian Voivodeship, 59-330, Poland

Location

Wroclawskie Centrum Alzheimerowskie

Wroclaw, Lower Silesian Voivodeship, 53-659, Poland

Location

Private Practice - Dr. Urszula Chyrchel- Paszkiewicz

Lublin, Lublin Voivodeship, 20-093, Poland

Location

FutureMeds Warszawa Centrum

Warsaw, Masovian Voivodeship, 00-215, Poland

Location

Centrum Medyczne NeuroProtect

Warsawawa, Masovian Voivodeship, 01-684, Poland

Location

KLIMED Marek Klimkiewicz

Bialystok, Podlaskie Voivodeship, 15-704, Poland

Location

Podlaskie Centrum Psychogeriatrii

Bialystok, Podlaskie Voivodeship, 15-756, Poland

Location

Centrum Badan Klinicznych PI-House sp. z o.o.

Gdansk, Pomeranian Voivodeship, 80-546, Poland

Location

Centrum Medyczne SENIOR

Sopot, Pomeranian Voivodeship, 81-855, Poland

Location

Klinika Neuro-Care

Katowice, Silesian Voivodeship, 40-749, Poland

Location

Centrum Medyczne Euromedis

Szczecin, West Pomeranian Voivodeship, 70-111, Poland

Location

SCB Research Center

Bayamón, 00961, Puerto Rico

Location

INSPIRA Clinical Research

San Juan, 00918, Puerto Rico

Location

Instituto De Neurologia Dra. Ivonne Fraga

San Juan, 00918, Puerto Rico

Location

Barbara Diaz-Hernandez MD Research, Inc.

San Juan, 00926, Puerto Rico

Location

Glasgow Memory Clinic

Motherwell, Great Britain, ML1 4UF, United Kingdom

Location

Re:Cognition Health - London

London, London, City of, W1G 9JF, United Kingdom

Location

Re:Cognition Health Guildford

Guildford, Surrey, GU2 7YD, United Kingdom

Location

Re:Cognition Health - Birmingham

Birmingham, B16 8LT, United Kingdom

Location

Related Publications (9)

  • Zimmer JA, Sims JR, Evans CD, Nery ESM, Wang H, Wessels AM, Tronchin G, Sato S, Raket LL, Andersen SW, Sapin C, Paget MA, Gueorguieva I, Ardayfio P, Khanna R, Brooks DA, Matthews BR, Mintun MA; Alzheimer's Disease Neuroimaging Initiative. Donanemab in early symptomatic Alzheimer's disease: results from the TRAILBLAZER-ALZ 2 long-term extension. J Prev Alzheimers Dis. 2026 Feb;13(2):100446. doi: 10.1016/j.tjpad.2025.100446. Epub 2025 Dec 1.

  • Lu M, Kim MJ, Collins EC, Shcherbinin S, Ellinwood AK, Yokoi Y, Brooks DA, Hansson O, Knopman DS, Sims JR, Mintun MA. Posttreatment Amyloid Levels and Clinical Outcomes Following Donanemab for Early Symptomatic Alzheimer Disease: A Secondary Analysis of the TRAILBLAZER-ALZ 2 Randomized Clinical Trial. JAMA Neurol. 2025 Dec 1;82(12):1251-1256. doi: 10.1001/jamaneurol.2025.3869.

  • Chandler JM, Lansdall CJ, Ye W, McDougall F, Belger M, Toth B, Mi X, Sink KM, Atkins AS. The Alzheimer's Disease Cooperative Study - Activities of Daily Living dependence score: revision and validation of an algorithm evaluating patient dependence across the spectrum of AD severity. J Prev Alzheimers Dis. 2025 Sep;12(8):100261. doi: 10.1016/j.tjpad.2025.100261. Epub 2025 Jul 1.

  • Zimmer JA, Ardayfio P, Wang H, Khanna R, Evans CD, Lu M, Sparks J, Andersen S, Lauzon S, Nery ESM, Battioui C, Engle SE, Biffi A, Svaldi D, Salloway S, Greenberg SM, Sperling RA, Mintun M, Brooks DA, Sims JR. Amyloid-Related Imaging Abnormalities With Donanemab in Early Symptomatic Alzheimer Disease: Secondary Analysis of the TRAILBLAZER-ALZ and ALZ 2 Randomized Clinical Trials. JAMA Neurol. 2025 May 1;82(5):461-469. doi: 10.1001/jamaneurol.2025.0065.

  • Boustani M, Doty EG, Garrison LP Jr, Smolen LJ, Klein TM, Murphy DR, Spargo AW, Belger M, Johnston JA. Estimating the Economically Justifiable Price of Limited-Duration Treatment with Donanemab for Early Symptomatic Alzheimer's Disease in the United States. Neurol Ther. 2024 Dec;13(6):1641-1659. doi: 10.1007/s40120-024-00649-y. Epub 2024 Sep 18.

  • Sato S, Hatakeyama N, Fujikoshi S, Katayama S, Katagiri H, Sims JR. Donanemab in Japanese Patients with Early Alzheimer's Disease: Subpopulation Analysis of the TRAILBLAZER-ALZ 2 Randomized Trial. Neurol Ther. 2024 Jun;13(3):677-695. doi: 10.1007/s40120-024-00604-x. Epub 2024 Apr 6.

  • Klein EG, Schroeder K, Wessels AM, Phipps A, Japha M, Schilling T, Zimmer JA. How donanemab data address the coverage with evidence development questions. Alzheimers Dement. 2024 Apr;20(4):3127-3140. doi: 10.1002/alz.13700. Epub 2024 Feb 7.

  • Sims JR, Zimmer JA, Evans CD, Lu M, Ardayfio P, Sparks J, Wessels AM, Shcherbinin S, Wang H, Monkul Nery ES, Collins EC, Solomon P, Salloway S, Apostolova LG, Hansson O, Ritchie C, Brooks DA, Mintun M, Skovronsky DM; TRAILBLAZER-ALZ 2 Investigators. Donanemab in Early Symptomatic Alzheimer Disease: The TRAILBLAZER-ALZ 2 Randomized Clinical Trial. JAMA. 2023 Aug 8;330(6):512-527. doi: 10.1001/jama.2023.13239.

  • Brodtmann A, Darby D, Oboudiyat C, Mahoney CJ, Le Heron C, Panegyres PK, Brew B. Assessing preparedness for Alzheimer disease-modifying therapies in Australasian health care systems. Med J Aust. 2023 Apr 3;218(6):247-249. doi: 10.5694/mja2.51880. Epub 2023 Mar 19. No abstract available.

Related Links

MeSH Terms

Conditions

Alzheimer DiseaseDementiaCognitive DysfunctionPlaque, Amyloid

Interventions

donanemab

Condition Hierarchy (Ancestors)

Brain DiseasesCentral Nervous System DiseasesNervous System DiseasesTauopathiesNeurodegenerative DiseasesNeurocognitive DisordersMental DisordersCognition DisordersPathological Conditions, AnatomicalPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Chief Medical Officer
Organization
Eli Lilly and Company

Study Officials

  • Call 1-877-CTLILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 9 AM - 5 PM Eastern time (UTC/GMT - 5 hours, EST)

    Eli Lilly and Company

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 17, 2020

First Posted

June 18, 2020

Study Start

June 19, 2020

Primary Completion

April 14, 2023

Study Completion (Estimated)

November 1, 2028

Last Updated

August 29, 2025

Results First Posted

May 20, 2024

Record last verified: 2025-08

Data Sharing

IPD Sharing
Will share

Anonymized individual patient level data will be provided in a secure access environment upon approval of a research proposal and a signed data sharing agreement.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
Data are available 6 months after the primary publication and approval of the indication studied in the US and EU, whichever is later. Data will be indefinitely available for requesting.
Access Criteria
A research proposal must be approved by an independent review panel and researchers must sign a data sharing agreement.
More information

Locations