NCT03443973

Brief Summary

This randomized, double-blind, placebo-controlled, parallel group study will evaluate the efficacy and safety of gantenerumab versus placebo in participants with early (prodromal to mild) AD. All participants must show evidence of beta-amyloid pathology. Eligible participants will be randomized 1:1 to receive either subcutaneous (SC) injection of gantenerumab or placebo. The primary efficacy assessment will be performed at the end of the double blind period at week 116. Participants will then be offered to enter into an open-label extension (OLE). Participants not willing to go to the OLE will participate in a long term follow-up period for up to 50 weeks after the last gantenerumab dose.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
975

participants targeted

Target at P75+ for phase_3 alzheimer-disease

Timeline
Completed

Started Aug 2018

Typical duration for phase_3 alzheimer-disease

Geographic Reach
19 countries

155 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 19, 2018

Completed
4 days until next milestone

First Posted

Study publicly available on registry

February 23, 2018

Completed
6 months until next milestone

Study Start

First participant enrolled

August 22, 2018

Completed
4.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 23, 2022

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

November 28, 2022

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

January 17, 2024

Completed
Last Updated

January 17, 2024

Status Verified

December 1, 2023

Enrollment Period

4.1 years

First QC Date

February 19, 2018

Results QC Date

September 22, 2023

Last Update Submit

December 22, 2023

Conditions

Outcome Measures

Primary Outcomes (6)

  • DBT Period: Change From Baseline to Week 116 in Global Outcome, as Measured by CDR-SB

    CDR was derived through semi-structured interview with the participant and an appropriate informant, and it rated impairment across six domains: memory, orientation, judgment, and problem solving, community affairs, home and hobbies, and personal care on a 5-point scale for which 0=no impairment, 0.5=questionable impairment, and 1, 2, and 3=mild, moderate, and severe impairment, respectively. The CDR-SB is based on summing each of the domain box scores with total score ranging from 0-18 with higher scores reflecting greater cognitive and functional impairment. A negative change from baseline indicates improvement.

    Baseline, Week 116

  • OLE Period: Number of Participants With Adverse Events (AEs)

    An adverse event is any untoward medical occurrence in a clinical investigation participant administered a pharmaceutical product, regardless of causal attribution.

    From day of first dose in OLE period up to 14 weeks after the last OLE dose (up to 48 weeks)

  • OLE Period: Number of Participants With Post-baseline Suicidal Ideation or Suicidal Behavior as Measured Using Columbia-Suicide Severity Rating Scale (C-SSRS)

    C-SSRS=assessment tool used to assess lifetime suicidality of a participant (at baseline) as well as any new instances of suicidality (C-SSRS since last visit). Structured interview prompts recollection of suicidal ideation, including intensity of ideation, behavior, \& attempts with actual/potential lethality. Categories have binary responses (yes/no) \& include Wish to be Dead; Non-specific Active Suicidal Thoughts; Active Suicidal Ideation with Any Methods (Not Plan) without Intent to Act; Active Suicidal Ideation with Some Intent to Act, without Specific Plan; Active Suicidal Ideation with Specific Plan and Intent, Preparatory Acts and Behavior; Aborted Attempt; Interrupted Attempt; Actual Attempt (non-fatal); Completed Suicide. Suicidal ideation/behavior is indicated by a "yes" answer to any of the listed categories. Score of 0 is assigned if no suicide risk is present. Score of 1 or higher= suicidal ideation or behavior. Categories with non-zero values are only reported here.

    From day of first dose in OLE period up to 14 weeks after the last OLE dose (up to 48 weeks)

  • OLE Period : Number of Participants With Amyloid-Related Imaging Abnormalities-Haemosiderin Deposition (ARIA-H) Confirmed by MRI

    ARIA are an identified risk with anti-amyloid antibodies, including gantenerumab. These changes can be identified on brain MRI. ARIA-H (H for hemosiderosis) are small foci of signal loss observed on MRI sequences sensitive for paramagnetic tissue properties and comprise cerebral microbleeds (small foci of bleeding in the brain parenchyma) and leptomeningeal hemosiderosis (small foci of bleeding on the surface of the brain). These changes also occur sporadically in AD.

    From day of first dose in OLE period up to 14 weeks after the last OLE dose (up to 48 weeks)

  • OLE Period: Number of Participants With Amyloid-Related Imaging Abnormalities-Edema (ARIA-E) Confirmed by Magnetic Resonance Imaging (MRI)

    ARIA are an identified risk with anti-amyloid antibodies, including gantenerumab. These changes can be identified on brain MRI. In ARIA-E, (E for oedema or effusion), oedema can be seen in different areas of the brain on MRI, representing fluid leakage into the brain parenchyma or sulcal spaces.

    From day of first dose in OLE period up to 14 weeks after the last OLE dose (up to 48 weeks)

  • OLE Period: Number of Participants With Injection-Site Reactions

    An AE is any unfavorable and unintended sign, symptom, or disease temporally associated with the use of an investigational product or other protocol-imposed intervention, regardless of attribution. Local injection reactions (or injection site reactions) are defined as AEs related to the injection site that occur during or within 24 hours after study drug administration that are judged to be related to the study drug injection.

    From day of first dose in OLE period up to 14 weeks after the last OLE dose (up to 48 weeks)

Secondary Outcomes (20)

  • DBT Period: Change From Baseline to Week 116 in Alzheimer Disease Assessment Scale-Cognition Subscale 13 (ADAS-Cog13) Score

    Baseline, Week 116

  • DBT Period: Change From Baseline to Week 116 in Alzheimer's Disease Cooperative Study- Activities of Daily Living (ADCS-ADL) Total Score

    Baseline, Week 116

  • DBT Period: Change From Baseline to Week 116 in Functional Activities Questionnaire (FAQ) Score

    Baseline, Week 116

  • DBT Period: Change From Baseline to Week 116 in Mini-Mental State Examination (MMSE) Total Score

    Baseline, Week 116

  • DBT Period: Change From Baseline to Week 116 in Alzheimer Disease Assessment Scale-Cognition Subscale 11 (ADAS-Cog11) Score

    Baseline, Week 116

  • +15 more secondary outcomes

Other Outcomes (1)

  • Plasma Concentration of Gantenerumab

    Pre-dose on Days 1, Weeks 24, 52 and 76; Post-dose on Day 4, Weeks 41, 103, and 115

Study Arms (2)

Gantenerumab

EXPERIMENTAL

Gantenerumab will be administered as SC injections with gradual uptitration.

Drug: Gantenerumab

Placebo

PLACEBO COMPARATOR

Placebo will be administered as SC injections with gradual uptitration.

Drug: Placebo

Interventions

Gantenerumab will be administered as per the schedule specified in the respective arm.

Also known as: RO4909832
Gantenerumab

Placebo matching to gantenerumab will be administered as per the schedule specified in the respective arm.

Placebo

Eligibility Criteria

Age50 Years - 90 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Meets National Institute on Aging/Alzheimer's Association (NIAAA) core clinical criteria for probable AD dementia or prodromal AD (consistent with the NIAAA diagnostic criteria and guidelines for mild cognitive impairment)
  • Evidence of the AD pathological process, as confirmed by CSF tau/A-beta42or amyloid PET scan
  • Demonstrated abnormal memory function
  • MMSE score greater than or equal to 22 (≥ 22)
  • Clinical dementia rating-global score (CDR-GS) of 0.5 or 1.0
  • Availability of a reliable study partner who accepts to participate in study procedures throughout the 2 years duration of study
  • If receiving symptomatic AD medications, the dosing regimen must have been stable for 3 months prior to screening and until randomization
  • For enrollment in the China extension, patients must have residence in mainland China, Hong Kong, or Taiwan and be of Chinese ancestry
  • For women of childbearing potential: agreement to remain abstinent (refrain from heterosexual intercourse) or use contraceptive methods

You may not qualify if:

  • Any evidence of a condition other than AD that may affect cognition
  • History of schizophrenia, schizoaffective disorder, major depression, or bipolar disorder
  • History or presence of clinically evident systemic vascular disease that in the opinion of the investigator has the potential to affect cognitive function
  • History or presence of clinically evident cerebrovascular disease
  • History or presence of posterior reversible encephalopathy syndrome
  • History or presence of any stroke with clinical symptoms within the past 12 months, or documented history within the last 6 months of an acute event that is consistent with a transient ischemic attack
  • History of severe, clinically significant CNS trauma
  • History or presence of intracranial mass (e.g., glioma, meningioma) that could potentially impair cognition
  • Presence of infections that affect brain function or history of infections that resulted in neurologic sequelae
  • History or presence of systemic autoimmune disorders that potentially cause progressive neurologic disease with associated cognitive deficits
  • At risk for suicide in the opinion of the investigator
  • Alcohol and/or substance abuse or dependants in past 2 years
  • Relevant brain hemorrhage, bleeding disorder and cerebrovascular abnormalities
  • Any contraindications to brain MRI
  • Unstable or clinically significant cardiovascular, kidney or liver disease
  • +8 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (155)

Banner Alzheimer?s Institute

Phoenix, Arizona, 85006, United States

Location

Barrow Neurological Institute

Phoenix, Arizona, 85013, United States

Location

Banner Sun Health Research Insitute

Sun City, Arizona, 85351, United States

Location

Health Initiatives Research, PLLC

Fayetteville, Arkansas, 72703, United States

Location

Fullerton Neurology and Headache Center

Fullerton, California, 92835, United States

Location

Neurology Center of North Orange County

Fullerton, California, 92835, United States

Location

Irvine Center for Clinical Research

Irvine, California, 92614, United States

Location

Desert Valley Research

Redlands, California, 92374, United States

Location

Southern California Research LLC

Simi Valley, California, 93065, United States

Location

Yale University School Of Medicine

New Haven, Connecticut, 06519, United States

Location

Georgetown University Medical Center

Washington D.C., District of Columbia, 20007, United States

Location

Accel Research Sites - CRU Tampa

Bradenton, Florida, 34201, United States

Location

ClinCloud, LLC

Maitland, Florida, 32751, United States

Location

Optimus U Corp

Miami, Florida, 33125, United States

Location

Allied Biomedical Research Institute, Inc

Miami, Florida, 33155, United States

Location

Renstar Medical Research

Ocala, Florida, 34470, United States

Location

Progressive Medical Research

Port Orange, Florida, 32127, United States

Location

Intercoastal Medical Group

Sarasota, Florida, 34239, United States

Location

Infinity Clinical Research, LLC

Sunrise, Florida, 33351, United States

Location

Axiom Clinical Research of Florida

Tampa, Florida, 33609, United States

Location

Emory University

Atlanta, Georgia, 30329, United States

Location

Rush Alzheimer's Disease Cntr.

Chicago, Illinois, 60612, United States

Location

American Health Network Institute, LLC

Avon, Indiana, 46123, United States

Location

Brigham and Womens Hospital; Center for Alzheimer Research & Treatment

Boston, Massachusetts, 02115, United States

Location

ActivMed Practices and Research

Haverhill, Massachusetts, 01830, United States

Location

Boston Center for Memory

Newton, Massachusetts, 02459, United States

Location

Quest Research Institute

Farmington Hills, Michigan, 48334, United States

Location

Missouri Memory Center

Bolivar, Missouri, 65613, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

University of Nebraska Medical Center; Dept of Neurological Sciences

Omaha, Nebraska, 68198-8440, United States

Location

Cleveland Clinic Lou Ruvo; Center for Brain Research

Las Vegas, Nevada, 89106, United States

Location

The Cognitive and Research Center of New Jersey

Springfield, New Jersey, 07081, United States

Location

AD-CARE, University of Rochester Medical Center

Rochester, New York, 14620, United States

Location

Richmond Behavioral Associates

Staten Island, New York, 10314, United States

Location

SUNY Upstate Medical University

Syracuse, New York, 13210, United States

Location

Behavioral Health Research

Charlotte, North Carolina, 28211, United States

Location

Alzheimer's Memory Center

Matthews, North Carolina, 28105, United States

Location

Raleigh Neurology Associates

Raleigh, North Carolina, 27607-6520, United States

Location

Wake Forest University

Winston-Salem, North Carolina, 27157, United States

Location

Neuro-Behavioral Clinical Research, Inc.

Canton, Ohio, 44718, United States

Location

Cleveland Clinic; Cleveland Lou Ruvo Center for Brain Health ? Neurological Institute

Cleveland, Ohio, 44195, United States

Location

Lynn Health Science Institute

Oklahoma City, Oklahoma, 73112, United States

Location

Summit Research Network Inc.

Portland, Oregon, 97210, United States

Location

Texas Neurology PA

Dallas, Texas, 75206, United States

Location

Kerwin Medical Center

Dallas, Texas, 75231, United States

Location

Alzheimers Disease & Memory Disorders Center; Department of Neurology Baylor College of Medicine

Houston, Texas, 77030, United States

Location

The University of Texas Health Science Center at Houston

Houston, Texas, 77054, United States

Location

Hospital Italiano

Buenos Aires, C1181ACH, Argentina

Location

Universidad Maimonides

Caba, C1405BCK, Argentina

Location

Instituto Geriatrico Nuestra Señora de las Nieves

Capital Federal, C1427CCP, Argentina

Location

Instituto Kremer

Córdoba, X5004AOA, Argentina

Location

CEN Centro Especializado en Neurociencias

Córdoba, X5004FJF, Argentina

Location

Instituto de Neurociencias San Agustín S.A.

La Plata, B1902AVF, Argentina

Location

Fundacion Scherbovsky

Mendoza, M5500AYB, Argentina

Location

AZ Sint Blasius (Dendermonde)

Dendermonde, 9200, Belgium

Location

UZ Gent

Ghent, 9000, Belgium

Location

Jessa Zkh (Campus Virga Jesse)

Hasselt, 3500, Belgium

Location

Psicomed Estudios Médicos

Antofagasta, 1270244, Chile

Location

Biomedica Research Group

Santiago, 7500710, Chile

Location

Especialidades Medicas LYS

Santiago, 7560356, Chile

Location

Clinical Hospital Centre Zagreb;Clinic for Neurology

Zagreb, 10000, Croatia

Location

Aarhus Universitetshospital; Neurologisk Afd. F, Demensklinikken

Aarhus N, 8200, Denmark

Location

Rigshospitalet, Hukommelsesklinikken

København Ø, 2100, Denmark

Location

Svendborg Sygehus; Neurologisk afdeling N, Demensklinik Fyn

Svendborg, 5700, Denmark

Location

Terveystalo Ruoholahti

Helsinki, 00180, Finland

Location

University of Eastern Finland

Kuopio, 70210, Finland

Location

Yachiyo Hospital

Aichi, 446-8510, Japan

Location

Nagoya Ekisaikai Hospital

Aichi, 454-8502, Japan

Location

National Center for Geriatrics and Gerontology

Aichi, 474-8511, Japan

Location

Fukuoka University Hospital

Fukuoka, 814-0180, Japan

Location

National Hospital Organization Hiroshima-Nishi Medical Center

Hiroshima, 739-0696, Japan

Location

Hyogo Prefectural HarimaHimeji General Medical Center

Hyōgo, 670-8560, Japan

Location

Tsukazaki Hospital

Hyōgo, 671-1227, Japan

Location

Matsui Dietary and Dementia Clinic

Hyōgo, 673-0891, Japan

Location

Kagawa Prefectural Central Hospital

Kagawa, 760-8557, Japan

Location

Rakuwakai Otowa Hospital

Kyoto, 607-8062, Japan

Location

Uji Takeda Hospital

Kyoto, 611-0021, Japan

Location

Rijikai Medical Corporation Katayama Medical Clinic

Okayama, 710-0813, Japan

Location

Kishiwada Tokushukai Hospital

Osaka, 596-0042, Japan

Location

National Hospital Organization Hizen Psychiatric Medical Center

Saga, 842-0192, Japan

Location

Medical corporation Ichiekai Itsuki Hospital

Tokushima, 770-0852, Japan

Location

Tokushima Hospital

Tokushima, 776-8585, Japan

Location

Mexico Centre for Clinical Research

Mexico City, Mexico CITY (federal District), 03100, Mexico

Location

Hospital Universitario Dr Jose Eleuterio Gonzalez UANL; Depto.de NeurologíaPta.BajaConsulta

Monterrey, Nuevo León, 64460, Mexico

Location

AVIX Investigación Clínica S.C

Monterrey, Nuevo León, 64710, Mexico

Location

Hospital Angeles Culiacan; Neurociencias

Culiacán, Sinaloa, 80020, Mexico

Location

Brain Research Center B.V

Amsterdam, 1081 GN, Netherlands

Location

O?rodek Badawczo-Naukowo-Dydaktyczny Chorób Ot?piennych w ?cinawie

?cinawa, 59-330, Poland

Location

Podlaskie Centrum Psychogeriatrii

Bia?ystok, 15-756, Poland

Location

NZOZ Vitamed

Bydgoszcz, 85-079, Poland

Location

KO-MED Centra Kliniczne Lublin II

Lublin, 20-362, Poland

Location

Neurologiczny NZOZ Centrum Leczenia SM; Osrodek Badan Klinicznych

Plewiska, 62-064, Poland

Location

NEURO-CARE Sp. z o.o. Sp. Komandytowa

Siemianowice ?l?skie, 41-100, Poland

Location

Senior Sp. Z O.O. Poradnia Psychogeriatryczna

Sopot, 81-855, Poland

Location

mMED Maciej Czarnecki

Warsaw, 01-684, Poland

Location

Pratia S.A.

Warsaw, 01-868, Poland

Location

NZOZ WCA

Wroc?aw, 53-659, Poland

Location

Hospital Prof. Dr. Fernando Fonseca; Servico de Neurologia

Amadora, 2720-276, Portugal

Location

Hospital de Braga; Servico de Neurologia

Braga, 4710-243, Portugal

Location

HUC; Servico de Neurologia

Coimbra, 3000-075, Portugal

Location

Hospital da Senhora da Oliveira-Guimarães; Serviço de Neurologia

Guimarães, Portugal

Location

Hospital Geral de Santo Antonio; Servico de Neurologia

Porto, 4099-001, Portugal

Location

Santa Cruz Behavioral PSC

Bayamón, 00961, Puerto Rico

Location

University of Puerto Rico - Medical Science Campus; Internal Medicine

San Juan, 00936, Puerto Rico

Location

National University Hospital (NUH); Neuroscience

Singapore, 117549, Singapore

Location

National Neuroscience Institute; Neurology

Singapore, 308433, Singapore

Location

Dong-A University Hospital

Busan, 49201, South Korea

Location

Myongji Hospital

Gyeonggi-do, 10475, South Korea

Location

Gachon University Gil Medical Center

Incheon, 21565, South Korea

Location

Inha University Hospital

Incheon, 22332, South Korea

Location

Seoul National University Bundang Hospital

Seongnam-si, 463-707, South Korea

Location

Hanyang University Seoul Hospital

Seoul, 04763, South Korea

Location

Konkuk University Medical Center

Seoul, 05030, South Korea

Location

Asan Medical Center

Seoul, 05505, South Korea

Location

Samsung Medical Center

Seoul, 06351, South Korea

Location

Seoul St Mary's Hospital

Seoul, 06591, South Korea

Location

Ewha Womans University Hospital (Seoul)

Seoul, 07804, South Korea

Location

Ewha Womans University Mokdong Hospital

Seoul, 07985, South Korea

Location

Hospital General Universitario de Elche; Servicio de Neurología

Elche, Alicante, 03203, Spain

Location

Hospital Mutua De Terrasa; Servicio de Neurologia

Terrassa, Barcelona, 08222, Spain

Location

Hospital Virgen del Puerto. Servicio de Neurología

Plasencia, Caceres, 10600, Spain

Location

Policlínica Guipuzcoa; Servicio de Neurología

Donostia / San Sebastian, Guipuzcoa, 20014, Spain

Location

Hospital Universitario de Santa Maria; Servicio de Neurología

Lleida, Lerida, 25198, Spain

Location

Hospital Quiron de Madrid; Servicio de Neurologia

Pozuelo de Alarcón, Madrid, 28223, Spain

Location

Clinica Universitaria de Navarra; Servicio de Neurología

Pamplona, Navarre, 31008, Spain

Location

Clinica Universitaria de Navarra

Pamplona, Navarre, 31008, Spain

Location

CAE OROITU; Servicio de Neurología

Getxo, Vizcaya, 48993, Spain

Location

Hospital del Mar; Servicio de Neurologia

Barcelona, 08003, Spain

Location

Fundación ACE; Servicio de Neurología

Barcelona, 08028, Spain

Location

Universitario de La Princesa; Servicio de Neurología

Madrid, 28006, Spain

Location

Hospital Victoria Eugenia; Servico Neurología

Seville, Spain

Location

Hospital Universitario la Fe; Servicio de Neurologia

Valencia, 46026, Spain

Location

Complejo Asistencial de Zamora; Servicio Psiquiatria

Zamora, 49021, Spain

Location

Skånes Universitetssjukhus Malmö, Minneskliniken

Malmo, 211 46, Sweden

Location

Sahlgrenska Academy University,Neuroscience and Physiology;Departmt of Psychiatry and Neurochemistry

Mölndal, 431 41, Sweden

Location

KAROLINSKA UNI HOSPITAL, HUDDINGE; Mottagning Kognitiv Forskning, M54

Stockholm, 141 86, Sweden

Location

Istanbul University Istanbul School of Medicine; Neurology

Istanbul, 34093, Turkey (Türkiye)

Location

Bezmialem Vakif Univ Medical

Istanbul, 34286, Turkey (Türkiye)

Location

Ondokuz Mayis Univ. Med. Fac.; Neurology

Samsun, 55139, Turkey (Türkiye)

Location

Royal Cornhill Hospital; OAP Directorate

Aberdeen, AB25 2ZH, United Kingdom

Location

The Rice Centre; Royal United Hospital

Bath, BA1 3NG, United Kingdom

Location

Re-Cognition

Birmingham, B16 8QQ, United Kingdom

Location

The Fritchie Centre, Charlton Lane Centre, Charlon Lane, Leckhampton; The Fritchie Centre

Cheltenham, GL53 9DZ, United Kingdom

Location

Surrey and Borders NHS Foundation Trust; Brain Science Research Unit

Chertsey, KT16 9AU, United Kingdom

Location

Sussex Partnership NHS Foundation Trust; Cognitive Treatment and Research unit

Crowborough, TN6 1HB, United Kingdom

Location

Ninewells Hospital

Dundee, DD12 9SY, United Kingdom

Location

Queen Elizabeth University Hospital; Clinical Research Facility

Glasgow, G51 4TF, United Kingdom

Location

St George's Hospital

London, SW17 0QT, United Kingdom

Location

RE:Cognition Health

London, W1G 9RU, United Kingdom

Location

Charing Cross Hospital

London, W6 8RF, United Kingdom

Location

Campus for Ageing and Vitality

Newcastle, NE4 5PL, United Kingdom

Location

John Radcliffe Hospital

Oxford, OX3 9DU, United Kingdom

Location

Royal Preston Hospital

Preston, PR2 9HT, United Kingdom

Location

Royal Hallamshire Hospital Sheffield Teaching Hospitals NHS Foundation Trust

Sheffield, S10 2JF, United Kingdom

Location

University Southampton NHS Foundation Trust; Wessex Neurologica Centre

Southampton, SO166YD, United Kingdom

Location

Related Publications (5)

  • Chandler JM, Lansdall CJ, Ye W, McDougall F, Belger M, Toth B, Mi X, Sink KM, Atkins AS. The Alzheimer's Disease Cooperative Study - Activities of Daily Living dependence score: revision and validation of an algorithm evaluating patient dependence across the spectrum of AD severity. J Prev Alzheimers Dis. 2025 Sep;12(8):100261. doi: 10.1016/j.tjpad.2025.100261. Epub 2025 Jul 1.

  • Asada T, Thanasopoulou A, Delmar P, Wojtowicz J, Smith J, Yoshiyama Y, Yokoi K, Watanabe C, Isozaki M, Ozaki R, Ishida T, Tatsuda H, Tamaoka A. Japanese participant data from three gantenerumab trials in early Alzheimer's disease. Alzheimers Dement. 2025 Apr;21(4):e70192. doi: 10.1002/alz.70192.

  • Bittner T, Tonietto M, Klein G, Belusov A, Illiano V, Voyle N, Delmar P, Scelsi MA, Gobbi S, Silvestri E, Barakovic M, Napolitano A, Galli C, Abaei M, Blennow K, Barkhof F. Biomarker treatment effects in two phase 3 trials of gantenerumab. Alzheimers Dement. 2025 Feb;21(2):e14414. doi: 10.1002/alz.14414. Epub 2025 Jan 30.

  • Salloway S, Wojtowicz J, Voyle N, Lane CA, Klein G, Lyons M, Rossomanno S, Mazzo F, Bullain S, Barkhof F, Bittner T, Schneider A, Grundman M, Aldea R, Boada M, Smith J, Doody R. Amyloid-Related Imaging Abnormalities (ARIA) in Clinical Trials of Gantenerumab in Early Alzheimer Disease. JAMA Neurol. 2025 Jan 1;82(1):19-29. doi: 10.1001/jamaneurol.2024.3937.

  • Bateman RJ, Smith J, Donohue MC, Delmar P, Abbas R, Salloway S, Wojtowicz J, Blennow K, Bittner T, Black SE, Klein G, Boada M, Grimmer T, Tamaoka A, Perry RJ, Turner RS, Watson D, Woodward M, Thanasopoulou A, Lane C, Baudler M, Fox NC, Cummings JL, Fontoura P, Doody RS; GRADUATE I and II Investigators and the Gantenerumab Study Group. Two Phase 3 Trials of Gantenerumab in Early Alzheimer's Disease. N Engl J Med. 2023 Nov 16;389(20):1862-1876. doi: 10.1056/NEJMoa2304430.

MeSH Terms

Conditions

Alzheimer Disease

Interventions

gantenerumab

Condition Hierarchy (Ancestors)

DementiaBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesTauopathiesNeurodegenerative DiseasesNeurocognitive DisordersMental Disorders

Results Point of Contact

Title
Medical Communications
Organization
Hoffmann-La Roche

Study Officials

  • Clinical Trials

    Hoffmann-La Roche

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 19, 2018

First Posted

February 23, 2018

Study Start

August 22, 2018

Primary Completion

September 23, 2022

Study Completion

November 28, 2022

Last Updated

January 17, 2024

Results First Posted

January 17, 2024

Record last verified: 2023-12

Data Sharing

IPD Sharing
Will share

Qualified researchers may request access to individual patient level data through the clinical study data request platform (www.clinicalstudydatarequest.com). Further details on Roche's criteria for eligible studies are available here (https://clinicalstudydatarequest.com/Study-Sponsors/Study-Sponsors-Roche.aspx). For further details on Roche's Global Policy on the Sharing of Clinical Information and how to request access to related clinical study documents, see here (https://www.roche.com/research\_and\_development/who\_we\_are\_how\_we\_work/clinical\_trials/our\_commitment\_to\_data\_sharing.htm).

Locations