NCT03235544

Brief Summary

This is a Phase 2, open-label, 2-cohort study designed to evaluate the efficacy and safety of 2 parsaclisib treatment regimens in participants with relapsed or refractory mantle cell lymphoma (MCL) previously treated either with or without a Bruton's tyrosine kinase (BTK) inhibitor.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
162

participants targeted

Target at P75+ for phase_2 lymphoma

Timeline
Completed

Started Nov 2017

Typical duration for phase_2 lymphoma

Geographic Reach
11 countries

103 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 27, 2017

Completed
5 days until next milestone

First Posted

Study publicly available on registry

August 1, 2017

Completed
4 months until next milestone

Study Start

First participant enrolled

November 20, 2017

Completed
4.2 years until next milestone

Results Posted

Study results publicly available

February 10, 2022

Completed
2.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 30, 2024

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 30, 2024

Completed
Last Updated

March 18, 2025

Status Verified

February 1, 2025

Enrollment Period

6.4 years

First QC Date

July 27, 2017

Results QC Date

January 14, 2022

Last Update Submit

February 27, 2025

Conditions

Keywords

Mantle cell lymphomanon-Hodgkin lymphomaBruton's tyrosine kinase (BTK)phosphatidylinositol 3-kinase (PI3K)

Outcome Measures

Primary Outcomes (1)

  • Objective Response Rate (ORR)

    ORR=percentage of participants with complete response(CR) or partial response(PR) per revised response criteria for lymphomas,determined by independent review committee(IRC).Criteria for CR:1.Target nodes/nodal masses of lymph nodes,extralymphatic sites regressed to≤1.5cm in longest dimension transverse diameter of lesion(LDi);2.Absence of non-measured lesion;3.Organ enlargement regressed to normal;4.No new lesions;5.Normal bone marrow morphology;if indeterminate,immunohistochemistry negative.Criteria for PR:1.Lymph nodes,extralymphatic sites- ≥50%decrease in sum of product of perpendicular diameters for multiple lesions(SPD)of up to 6 target measurable nodes,extranodal sites;if lesion is too small to measure on computed tomography(CT),assign5mm×5mm as default;if no longer visible,0×0mm.Node\>5mm×5mm but smaller than normal,use actual measurement.2.Absent/regressed non-measured lesions,no increase.3.Organ enlargement-Spleen regressed by\>50%in length beyond normal.4.No new lesions.

    Up to 1016 days

Secondary Outcomes (6)

  • Duration of Response (DOR)

    Up to 1016 days

  • Complete Response Rate (CRR)

    Up to 1016 days

  • Progression-Free Survival (PFS)

    Up to 1016 days

  • Overall Survival (OS)

    Up to 2017 days

  • Best Percent Change From Baseline in Target Lesion Size

    Up to 1016 days

  • +1 more secondary outcomes

Study Arms (4)

Cohort 1: Treatment A (Exposed to Ibrutinib)

EXPERIMENTAL

Participants received parsaclisib 20 mg tablets, orally, once daily (QD) for 8 weeks followed by 20 mg once weekly (QW) for up to 52 weeks. Participants who were exposed to ibrutinib before enrollment were included in this group.

Drug: Parsaclisib

Cohort 1: Treatment B (Exposed to Ibrutinib)

EXPERIMENTAL

Participants received parsaclisib 20 mg tablets, orally, QD for 8 weeks followed by 2.5 mg QD for up to 116 weeks. Participants who were exposed to ibrutinib before enrollment were included in this group.

Drug: Parsaclisib

Cohort 2: Treatment A (Bruton's Tyrosine Kinase Inhibitor Naïve)

EXPERIMENTAL

Participants received parsaclisib 20 mg tablets, orally, QD for 8 weeks followed by 20 mg QW for up to approximately 145 weeks. Participants who had not received a BTK inhibitor previously were included in this group.

Drug: Parsaclisib

Cohort 2: Treatment B (Bruton's Tyrosine Kinase Inhibitor Naïve)

EXPERIMENTAL

Participants received parsaclisib 20 mg tablets, orally, QD for 8 weeks followed by 2.5 mg QD for up to approximately 136 weeks. Participants who had not received a BTK inhibitor previously were included in this group.

Drug: Parsaclisib

Interventions

Parsaclisib tablets administered orally with water and without regard to food.

Also known as: INCB050465
Cohort 1: Treatment A (Exposed to Ibrutinib)Cohort 1: Treatment B (Exposed to Ibrutinib)Cohort 2: Treatment A (Bruton's Tyrosine Kinase Inhibitor Naïve)Cohort 2: Treatment B (Bruton's Tyrosine Kinase Inhibitor Naïve)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Men and women, aged 18 years or older.
  • Documented failure to achieve at least partial response (PR) with, or documented disease progression after, the most recent treatment regimen.
  • Radiographically measurable lymphadenopathy or extranodal lymphoid malignancy.
  • Eastern Cooperative Oncology Group (ECOG) performance status of ≤ 2.

You may not qualify if:

  • History of central nervous system lymphoma (either primary or metastatic).
  • Prior treatment with idelalisib, other selective phosphatidylinositol 3-kinase delta (PI3Kδ) inhibitors, or a pan PI3K inhibitor.
  • Allogeneic stem cell transplant within the last 6 months, or autologous stem cell transplant within the last 3 months before the date of first dose of study treatment.
  • Active graft-versus-host disease.
  • Liver disease: Participants positive for hepatitis B surface antigen or hepatitis B core antibody will be eligible if they are negative for hepatitis B virus-deoxyribonucleic acid (HBV-DNA). Participants positive for anti-hepatitis C virus (HCV) antibody will be eligible if they are negative for HCV-ribonucleic acid (RNA).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (103)

University of Alabama At Birmingham Comprehensive Cancer Center

Birmingham, Alabama, 35205, United States

Location

St. Joseph Heritage Healthcare

Santa Rosa, California, 95403, United States

Location

Rocky Mountain Cancer Center-Aurora

Aurora, Colorado, 80012, United States

Location

Asclepes Research Centers

Brooksville, Florida, 34613, United States

Location

Moffitt Cancer Center

Tampa, Florida, 33647, United States

Location

Bond & Steele Clinic, P.A.

Winter Haven, Florida, 33880, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

Loyola University Medical Center

Maywood, Illinois, 60153, United States

Location

Illinois Cancer Specialists

Niles, Illinois, 60714, United States

Location

Hattiesburg Clinic Hematology

Hattiesburg, Mississippi, 39401, United States

Location

Clinical Research Alliance, Inc.

New Hyde Park, New York, 11042, United States

Location

Duke University Medical Center

Durham, North Carolina, 27705, United States

Location

Oncology Hematology Care, Inc.

Cincinnati, Ohio, 45230, United States

Location

Willamette Valley Cancer Institute

Eugene, Oregon, 97401, United States

Location

Kaiser Permanente - Northwest

Portland, Oregon, 97227, United States

Location

Gettysburg Cancer Center

Gettysburg, Pennsylvania, 17325, United States

Location

Texas Oncology

Austin, Texas, 78705, United States

Location

Texas Oncology San Antonio

San Antonio, Texas, 78240, United States

Location

Renovatio Clinical

The Woodlands, Texas, 77380, United States

Location

Texas Oncology - Tyler

Tyler, Texas, 75702, United States

Location

Yakima Valley Memorial Hospital/North Star

Yakima, Washington, 98902, United States

Location

Universitair Ziekenhuis Gent

Ghent, Oost-Vlaanderen, 9000, Belgium

Location

Institut Jules Bordet

Brussels, Belgium

Location

Hopital de Jolimont

La Louvière, 07100, Belgium

Location

Universitaire Ziekenhuis Leuven - Gasthuisberg

Leuven, 03000, Belgium

Location

Fakultni Nemocnice Hradec Kralove

Hradec Králové, 500 05, Czechia

Location

Fakultni Nemocnice Kralovske Vinohadry, Interni Hematologicka Klinika

Prague, 10034, Czechia

Location

Charles University General Hospital

Prague, 128 08, Czechia

Location

Fakultni Nemocnice Kralovske Vinohrady

Prague, 500 05, Czechia

Location

Aalborg University Hospital

Aalborg, 09000, Denmark

Location

Aarhus Universitets Hospital

Aarhus, DK-8000, Denmark

Location

Odense Universitetshospital (Ouh) (Odense University Hospital)

Odense C, 05000, Denmark

Location

Zealand University Hospital

Roskilde, 04000, Denmark

Location

Avicenne Hospital

Bobigny, 93000, France

Location

Chu de Clermont - Ferrand- Hospital Estaing

Clermont-Ferrand, 63230, France

Location

Centre Hospitalier Universitaire Henri Mondor

Créteil, 94010, France

Location

University Hospital Grenoble

Grenoble, 38043, France

Location

Centre Hospitalier Departemental - La-Roche-Sur-Yon - Les Oudairies

La Roche-sur-Yon, 85925, France

Location

Centre Hospitalier Universitaire de Grenoble

La Tronche, 38700, France

Location

Centre Hospitalier de Versailles

Le Chesnay, 78157, France

Location

Hospices Civils de Lyon Centre Hospitalier Lyon Sud

Lyon, 69008, France

Location

Centre Antoine Lacassagne

Nice, 06189, France

Location

Hopital Saint-Louis

Paris, 75010, France

Location

H�Pital Universitaire Piti�-Salp�Tri�Re

Paris, 75013, France

Location

Centre Hospitalier Lyon-Sud

Pierre-Bénite, 69310, France

Location

Centre Hospitalier Universitaire de Poitiers

Poitiers, 86021, France

Location

Centre Henri Becquerel

Rouen, 76038, France

Location

Chru Hopitaux de Tours, Hospital Bretonneau

Tours, 37044, France

Location

Institute Gustave Roussy (Igr)

Villejuif, 94805, France

Location

Praxis Brudler, Heinrich, Bangerter

Augsburg, 86150, Germany

Location

Universitaetsklinikum Essen

Essen, 45122, Germany

Location

Universit�Tsklinikum Essen

Essen, 45147, Germany

Location

Justus-Liebig University

Giessen, 35392, Germany

Location

Universitatsmedizin Der Johannes Gutenberg-Universitat Mainz Iii

Mainz, 55131, Germany

Location

Kliniken Maria Hilf

Mönchengladbach, 41063, Germany

Location

Rotkreuzklinikum Munich

München, 80634, Germany

Location

Universit�Tsklinikum Ulm

Ulm, 89081, Germany

Location

Rambam Medical Center

Haifa, 31096, Israel

Location

Hadassah Hebrew University Medical Center

Jerusalem, 90000, Israel

Location

Hadassah Hebrew University Medical Center Ein Karem Hadassah

Jerusalem, 91120, Israel

Location

Rabin Medical Center - Beilinson Hospital

Petah Tikva, 4841492, Israel

Location

Tel Aviv Sourasky Medical Center

Tel Aviv, 64239, Israel

Location

Fondazione Irccs Istituto Nazionale Dei Tumori

Milan, MI, 20133, Italy

Location

Centro Ricerche Cliniche

Bologna, 40138, Italy

Location

Azienda Policlinico Vittorio Emanuele

Catania, 95123, Italy

Location

Grande Ospedale Metropolitano Niguarda

Milan, 20162, Italy

Location

Ospedale Niguarda Ca Granda

Milan, 22162, Italy

Location

A.O.U. Di Modena - Policlinico

Modena, 41124, Italy

Location

A.O.U. Federico Ii

Napoli, 80131, Italy

Location

Aou Maggiore Della Carita

Novara, 28100, Italy

Location

Ospedali Riuniti Villa Sofia Cervello

Palermo, 90146, Italy

Location

Sapienza University

Rome, 00161, Italy

Location

Azienda Ospedaliera Universitaria Senese Policlinico Santa Maria Alle Scotte

Siena, 53100, Italy

Location

Azienda Ospedaliero Universitaria Citta Della Salute E Della Scienza

Torino, 10126, Italy

Location

Beskidzkie Centrum Onkologii Im.Jana Pawla Ii

Bielsko-Biala, 43-300, Poland

Location

Szpital Specjalistyczny W Brzozowie, Podkarpacki Osrodek Onkologiczny Im.Ks.B.Markiewicza

Brzozów, 36-200, Poland

Location

University Clinical Center

Gdansk, 80-952, Poland

Location

Pratia McM Krakow

Krakow, 30-510, Poland

Location

Nu-Med Centrum Diagnostykii I Terapii Onkologicznej

Tomaszów Mazowiecki, 97-200, Poland

Location

Centrum Onkologii-Instytut Im. Marii Sklodowskiej-Curie

Warsaw, 02-781, Poland

Location

Hospital Del Mar

Barcelona, 08003, Spain

Location

Hospital General Universitari Vall D Hebron

Barcelona, 08035, Spain

Location

Hospital Universitari Mutua Terrassa

Barcelona, 08221, Spain

Location

Institut Catala D Oncologia

Barcelona, 08916, Spain

Location

Hospital Universitario de Burgos

Burgos, 09006, Spain

Location

Hospital General Universitario Gregorio Maranon

Madrid, 28007, Spain

Location

Md Anderson Cancer Centre Madrid

Madrid, 28033, Spain

Location

Hospital Universitario Ramon Y Cajal

Madrid, 28034, Spain

Location

Fundacion Jimenez Diaz University Hospital

Madrid, 28040, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, 28041, Spain

Location

Hospital Universitario de La Paz

Madrid, 28046, Spain

Location

Hospital General Universitario Morales Meseguer

Murcia, 30008, Spain

Location

Complejo Hospitalario de Navarra

Pamplona, 31008, Spain

Location

Hospital Clinico Universitario de Salamanca

Salamanca, 37007, Spain

Location

Hospital Universitario Virgen del Rocio

Seville, 41005, Spain

Location

Hospital Arnau de Vilanova

Valencia, 46015, Spain

Location

Hospital Universitario Dr. Peset

Valencia, 46017, Spain

Location

Hospital Universitario Y Politecnic La Fe

Valencia, 46026, Spain

Location

Birmingham Heartlands Hospital

Birmingham, B9 5SS, United Kingdom

Location

Western General Hospital

Edinburgh, EH4 2XU, United Kingdom

Location

University College London Hospitals (Uclh)

London, NW1 2PG, United Kingdom

Location

Derriford Hospital

Plymouth, PL6 8DH, United Kingdom

Location

Royal Hallamshire Hospital

Sheffield, S10 2JF, United Kingdom

Location

MeSH Terms

Conditions

LymphomaLymphoma, Mantle-CellLymphoma, Non-Hodgkin

Interventions

parsaclisib

Condition Hierarchy (Ancestors)

Neoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Results Point of Contact

Title
Study Director
Organization
Incyte Corporation

Study Officials

  • Fred Zheng, MD

    Incyte Corporation

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 27, 2017

First Posted

August 1, 2017

Study Start

November 20, 2017

Primary Completion

April 30, 2024

Study Completion

April 30, 2024

Last Updated

March 18, 2025

Results First Posted

February 10, 2022

Record last verified: 2025-02

Data Sharing

IPD Sharing
Will share

Individual participant data (IPD) will be made available to interested researchers after the end of study, a thorough analysis, and the publication of the data in the clinical study report (CSR). As required, results of the data will be posted to ClinicalTrials.gov. Upon request, individual investigators may obtain IPD from the sponsor. The format for data delivery will be determined between sponsor and investigator.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
Data will be shared after the primary publication or 2 years after the study has ended for market authorized products and indications.
Access Criteria
Data from eligible studies will be shared with qualified researchers according to the criteria and process described in the Data Sharing section of the www.incyteclinicaltrials.com website. For approved requests, the researchers will be granted access to anonymized data under the terms of a data sharing agreement.
More information

Locations