NCT02966756

Brief Summary

This is a Phase 2, open-label, multicenter study, evaluating the efficacy of venetoclax in participants with relapsed or refractory Chronic Lymphocytic Leukemia (CLL)/Small Lymphocytic Lymphoma (SLL) either in presence of 17p deletion (Cohort 1) or those who have failed a B-receptor signaling pathway inhibitor (BCRI) therapy and who have also failed, or were unable to receive chemoimmunotherapy (CIT) irrespective of 17p status (Cohort 2).

Trial Health

80
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
110

participants targeted

Target at P50-P75 for phase_2

Timeline
37mo left

Started Oct 2017

Longer than P75 for phase_2

Geographic Reach
4 countries

31 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress74%
Oct 2017May 2029

First Submitted

Initial submission to the registry

November 15, 2016

Completed
2 days until next milestone

First Posted

Study publicly available on registry

November 17, 2016

Completed
11 months until next milestone

Study Start

First participant enrolled

October 12, 2017

Completed
11.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2029

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2029

Last Updated

December 24, 2025

Status Verified

December 1, 2025

Enrollment Period

11.6 years

First QC Date

November 15, 2016

Last Update Submit

December 18, 2025

Conditions

Keywords

Relapsed chronic lymphocytic leukemia (CLL)Refractory chronic lymphocytic leukemia (CLL)17p deletionVenetoclaxLeukemiaLymphoproliferative DisordersSmall Lymphocytic Lymphoma (SLL)Venclexta

Outcome Measures

Primary Outcomes (1)

  • Overall Response Rate (ORR)

    ORR is the proportion of participants with an overall response (complete remission \[CR\], plus complete remission with incomplete bone marrow recovery \[CRi\], plus nodular partial remission \[nPR\], plus partial remission \[PR\]) per the National Cancer Institute-Working Group (NCI-WG) guidelines as assessed by the Independent Review Committee (IRC).

    Measured up to 2 years after the last participant has enrolled in the study.

Secondary Outcomes (7)

  • Complete Response Rate (CRR)

    Measured up to 2 years after the last participant has enrolled into the study.

  • Duration of Overall Response (DOR)

    Measured up to 2 years after the last participant has enrolled into the study.

  • Progression Free Survival (PFS)

    Measured up to 5 years after the last participant has enrolled into the study.

  • Event Free Survival (EFS)

    Measured up to 5 years after the last participant has enrolled into the study.

  • Time to Progression (TTP)

    Measured up to 5 years after the last participant has enrolled into the study.

  • +2 more secondary outcomes

Study Arms (2)

Cohort 1: Venetoclax

EXPERIMENTAL

Participants with 17p deletion status will receive various doses of venetoclax once daily (QD).

Drug: Venetoclax

Cohort 2: Venetoclax

EXPERIMENTAL

Participants who have failed a B-Cell Receptor Signaling Pathway Inhibitor (BCRI) therapy and who have also failed, or were unable to receive chemoimmunotherapy (CIT) irrespective of 17p status will receive various doses of venetoclax once daily (QD).

Drug: Venetoclax

Interventions

Tablet; Oral

Also known as: ABT-199, GDC-0199, Venclexta
Cohort 1: VenetoclaxCohort 2: Venetoclax

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participant must have a diagnosis of relapsed or refractory chronic lymphocytic leukemia (CLL)/Small Lymphocytic Lymphoma (SLL) that meets 2008 Modified International Workshop for Chronic Lymphocytic Leukemia (iwCLL) National Cancer Institute-Working Group (NCI-WG) Guidelines and the following:
  • Participant must have an indication for treatment according to the 2008 Modified iwCLL NCI-WG Guidelines.
  • SLL participant must have measurable disease (B-lymphocytosis greater than 5 Ă— 10\^9/L or an enlarged lymph node(s) (Longest Diameter (LDi) \> 1.5 cm at baseline) or hepatomegaly or splenomegaly due to CLL).
  • SLL participant must have presence of lymphadenopathy and absence of cytopenias caused by a clonal marrow infiltrate.
  • Participant must have relapsed or refractory CLL/SLL after receiving at least one prior line of therapy.
  • Participants (in Cohort 1) must have 17p deletion, assessed by a central laboratory.
  • Participants (in Cohort 2) must meet both of the following:
  • Relapsed/refractory disease to B-Cell Receptor Signaling Pathway Inhibitor (BCRI) treatment;
  • And either of the following: (a) relapsed/refractory disease to chemoimmunotherapy (CIT), or (b) ineligible to receive CIT, defined as having known 17p deletion or TP53 mutation, or Cumulative Illness Rating Scale (CIRS) \>6 or calculated creatinine clearance \<70 mL/min, or participants in whom the investigator evaluated that the use of CIT was inappropriate.
  • Participant must have an Eastern Cooperative Oncology Group (ECOG) performance score of less than or equal to 2.
  • Participant must have adequate bone marrow function, coagulation profile, renal, and hepatic function, per laboratory reference range at Screening.
  • No known active severe acute respiratory syndrome coronavirus 2 (SARS-CoV-2) infection.

You may not qualify if:

  • Participant has undergone an allogeneic stem cell transplant.
  • Participant has developed Richter's transformation confirmed by biopsy.
  • Participant has prolymphocytic leukemia.
  • Participant has active and uncontrolled autoimmune cytopenias (for 2 weeks prior to screening), including autoimmune hemolytic anemia (AIHA) and idiopathic thrombocytopenic purpura (ITP).
  • Participant has previously received venetoclax or other BCL-2 inhibitors.
  • Participant is known to be positive for Human Immunodeficiency Virus (HIV).
  • Participant has received a biologic agent for anti-neoplastic intent within 30 days prior to the first dose of study drug.
  • Participant has received any of the following within 14 days or 5 half-lives (whichever is shorter) prior to the first dose of venetoclax, or has not recovered to less than Common Toxicity Criteria for Adverse Events (CTCAE) grade 2 clinically significant adverse effect(s)/toxicity(s) of the previous therapy:
  • Any anti-cancer therapy including chemotherapy, immunotherapy, radiotherapy or targeted small molecule agents.
  • Investigational therapy, including targeted small molecule agents.
  • Participant has known allergy to both xanthine oxidase inhibitors and rasburicase.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (31)

Concord Repatriation General Hospital /ID# 201261

Concord, New South Wales, 2139, Australia

RECRUITING

St George Hospital /ID# 206484

Kogarah, New South Wales, 2217, Australia

RECRUITING

Monash Health - Monash Medical Centre /ID# 201263

Clayton, Victoria, 3168, Australia

COMPLETED

Anhui Provincial Cancer Hospital /ID# 209458

Hefei, Anhui, 230031, China

RECRUITING

Peking University People's Hospital /ID# 156575

Beijing, Beijing Municipality, 100044, China

RECRUITING

Peking Union Medical College Hospital (East) - Dongdan Campus /ID# 156576

Beijing, Beijing Municipality, 100730, China

RECRUITING

Fujian Medical University Union Hospital /ID# 156579

Fuzhou, Fujian, 350001, China

RECRUITING

Guangdong Provincial Peoples Hospital /ID# 160509

Guangzhou, Guangdong, 510080, China

RECRUITING

Nanfang Hospital of Southern Medical University /ID# 156571

Guangzhou, Guangdong, 510515, China

RECRUITING

The Second Hospital of Hebei Medical University /ID# 159143

Shijiazhuang, Hebei, 050000, China

COMPLETED

Henan Cancer Hospital /ID# 156573

Zhengzhou, Henan, 450008, China

RECRUITING

Tongji Hospital Tongji Medical College of HUST /ID# 156589

Wuhan, Hubei, 430030, China

RECRUITING

Xiangya Hospital Central South University /ID# 208913

Changsha, Hunan, 410008, China

RECRUITING

Jiangsu Province Hospital /ID# 156577

Nanjing, Jiangsu, 210029, China

RECRUITING

The First Affiliated Hospital of Soochow University /ID# 156536

Suzhou, Jiangsu, 215006, China

RECRUITING

The First Affiliated Hospital of Nanchang University /ID# 159142

Nanchang, Jiangxi, 330006, China

RECRUITING

The First Hospital of Jilin University /ID# 156532

Changchun, Jilin, 130021, China

RECRUITING

Shandong Provincial Hospital /ID# 156574

Jinan, Shandong, 250021, China

RECRUITING

Ruijin Hospital, Shanghai Jiaotong University School of Medicine /ID# 156572

Shanghai, Shanghai Municipality, 200065, China

RECRUITING

West China Hospital, Sichuan University /ID# 156537

Chengdu, Sichuan, 610041, China

RECRUITING

The General Hospital of Western Theater Command PLA /ID# 159145

Chengdu, Sichuan, 610083, China

RECRUITING

Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sc /ID# 157762

Tianjin, Tianjin Municipality, 300020, China

RECRUITING

Tianjin Medical University Cancer Institute & Hospital /ID# 156542

Tianjin, Tianjin Municipality, 300060, China

RECRUITING

The First Affiliated Hospital, Zhejiang University School of Medicine /ID# 156578

Hangzhou, Zhejiang, 310003, China

RECRUITING

North Shore Hospital /ID# 204637

Takapuna, Auckland, 0622, New Zealand

RECRUITING

Christchurch Hospital. /ID# 201650

Christchurch, Canterbury, 8011, New Zealand

COMPLETED

National Taiwan University Hospital /ID# 210733

Taipei City, Taipei, 100, Taiwan

RECRUITING

Changhua Christian Hospital /ID# 202768

Changhua City, Changhua County, 50006, Taiwan

COMPLETED

Kaohsiung Medical University Chung-Ho Memorial Hospital /ID# 202765

Kaohsiung City, 807, Taiwan

RECRUITING

China Medical University Hospital /ID# 202767

Taichung, 40447, Taiwan

RECRUITING

Linkou Chang Gung Memorial Hospital /ID# 203636

Taoyuan, 333, Taiwan

RECRUITING

Related Links

MeSH Terms

Conditions

Leukemia, Lymphocytic, Chronic, B-CellChromosome 17 deletionLeukemiaLymphoproliferative Disorders

Interventions

venetoclax

Condition Hierarchy (Ancestors)

Leukemia, B-CellLeukemia, LymphoidNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Study Officials

  • ABBVIE INC.

    AbbVie

    STUDY DIRECTOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 15, 2016

First Posted

November 17, 2016

Study Start

October 12, 2017

Primary Completion (Estimated)

May 1, 2029

Study Completion (Estimated)

May 1, 2029

Last Updated

December 24, 2025

Record last verified: 2025-12

Data Sharing

IPD Sharing
Will share

AbbVie is committed to responsible clinical trial data sharing. This includes access to anonymized, individual and trial-level data (analysis data sets), as well as other information.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
For details on when studies are available for sharing visit https://vivli.org/ourmember/abbvie/
Access Criteria
To learn more about the process, or to submit a request, visit the following link https://www.abbvieclinicaltrials.com/hcp/data-sharing/
More information

Locations