NCT02980731

Brief Summary

The purpose of this open-label, single-arm study was to evaluate the impact of venetoclax on the quality of life of participants including those with with relapsed/refractory (R/R) chronic lymphocytic leukemia (CLL; a type of cancer affecting the blood and the bone marrow) with or without the 17p deletion or TP53 mutation, including participants with an unknown status, as well as R/R CLL participants who had been previously treated with B-cell receptor inhibitor (BCRi) therapy. The starting dose of venetoclax was 20 mg once daily. The dose must have been gradually increased over a period of 5 weeks up to the daily dose of 400 mg. Participants may have continued receiving venetoclax for up to 2 years. After the treatment period, participants may have continued on into a 2-year follow-up period.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
210

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Dec 2016

Longer than P75 for phase_3

Geographic Reach
10 countries

33 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 30, 2016

Completed
2 days until next milestone

First Posted

Study publicly available on registry

December 2, 2016

Completed
11 days until next milestone

Study Start

First participant enrolled

December 13, 2016

Completed
5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 29, 2021

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 29, 2021

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

February 22, 2023

Completed
Last Updated

February 22, 2023

Status Verified

January 1, 2023

Enrollment Period

5 years

First QC Date

November 30, 2016

Results QC Date

December 21, 2022

Last Update Submit

January 23, 2023

Conditions

Keywords

Relapsed CLLRefractory CLL17p deletionTP53 geneB-Cell receptor inhibitor (BCRi)European Organization of Research and Treatment of Cancer Quality of Life Core Questionnaire (EORTC QLQ-C30)Overall response rate (ORR)Duration of overall response (DOR)Complete remission rate (CR + CRi)Progression-free survival (PFS)Overall survival (OS)

Outcome Measures

Primary Outcomes (1)

  • Mean Change From Baseline to Week 48 in Global Health Status/Quality of Life (GHS/QoL) Subscale of the European Organization for Research and Treatment of Cancer Quality of Life Core Questionnaire (EORTC QLQ-C30)

    EORTC QLQ-C30 is a 30-item participant self-report questionnaire composed of both multi-item and single scales, including a global health status/quality of life (GHS/QoL) scale. Participants rate items and a score ranging from 0 to 100 is calculated. A higher score on the global health status/quality of life scale indicates a better level of functioning, and positive changes from baseline indicate improvement. A change of 5 - 10 points is considered a small change, and a change of 10 - 20 points is considered a moderate change.

    Baseline, Week 48

Secondary Outcomes (29)

  • Mean Change From Baseline in Global Health Status/Quality of Life (GHS/QoL) Subscale of the European Organization for Research and Treatment of Cancer Quality of Life Core Questionnaire (EORTC QLQ-C30)

    Baseline, Weeks 4, 8, 12, 24, 36, 48, 60, 72, 84, 96, 108, Final visit (at study drug discontinuation and/or upon discontinuation from the study, up to Week 108)

  • Mean Change From Baseline in Physical Functioning Subscale of the European Organization for Research and Treatment of Cancer Quality of Life Core Questionnaire (EORTC QLQ-C30)

    Baseline, Weeks 4, 8, 12, 24, 36, 48, 60, 72, 84, 96, 108, Final visit (at study drug discontinuation and/or upon discontinuation from the study, up to Week 108)

  • Mean Change From Baseline in Role Functioning Subscale of the European Organization for Research and Treatment of Cancer Quality of Life Core Questionnaire (EORTC QLQ-C30)

    Baseline, Weeks 4, 8, 12, 24, 36, 48, 60, 72, 84, 96, 108, Final visit (at study drug discontinuation and/or upon discontinuation from the study, up to Week 108)

  • Mean Change From Baseline in Emotional Functioning Subscale of the European Organization for Research and Treatment of Cancer Quality of Life Core Questionnaire (EORTC QLQ-C30)

    Baseline, Weeks 4, 8, 12, 24, 36, 48, 60, 72, 84, 96, 108, Final visit (at study drug discontinuation and/or upon discontinuation from the study, up to Week 108)

  • Mean Change From Baseline in Cognitive Functioning Subscale of the European Organization for Research and Treatment of Cancer Quality of Life Core Questionnaire (EORTC QLQ-C30)

    Baseline, Weeks 4, 8, 12, 24, 36, 48, 60, 72, 84, 96, 108, Final visit (at study drug discontinuation and/or upon discontinuation from the study, up to Week 108)

  • +24 more secondary outcomes

Study Arms (1)

Venetoclax

EXPERIMENTAL

Venetoclax was administered orally once daily (QD) for a planned duration of up to 2 years or until disease progression; median time on treatment was 127 weeks. The starting dose was 20 mg daily, increasing over a period of 5 weeks up to the daily dose of 400 mg.

Drug: Venetoclax

Interventions

Venetoclax tablets were to be taken orally once daily with a meal and water in the morning at approximately the same time each day. Tablets were to be swallowed whole and not chewed, crushed, or broken prior to swallowing.

Also known as: ABT-199, VENCLEXTA, VENCLYXTO
Venetoclax

Eligibility Criteria

Age18 Years - 99 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Eastern Cooperative Oncology Group (ECOG) performance score of ≤ 2
  • Participant has relapsed/refractory disease (received at least one prior therapy)
  • Diagnosis of CLL that meets published 2008 Modified International Workshop on CLL National Cancer Institute - Working Group (IWCLL NCI-WG) Guidelines and:
  • has an indication for treatment according to the 2008 Modified IWCLL NCI-WG Guidelines
  • has clinically measurable disease (lymphocytosis \> 5 × 10\^9/L and/or palpable and measurable nodes by physical exam and/or organomegaly assessed by physical exam)
  • with or without 17p deletion or TP53 mutation
  • may have been previously treated with a prior B-cell receptor inhibitor therapy
  • Adequate bone marrow function

You may not qualify if:

  • Participant has developed Richter's transformation or Prolymphocytic leukemia (PLL)
  • Participant has previously received venetoclax
  • History of active malignancies other than CLL within the past 2 years prior to first dose of venetoclax, with the exception of:
  • adequately treated in situ carcinoma of the cervix uteri
  • adequately treated basal cell carcinoma or localized squamous cell carcinoma of the skin
  • previous malignancy confined and surgically resected (or treated with other modalities) with curative intent
  • Active and uncontrolled autoimmune cytopenias (within 2 weeks prior to screening), including autoimmune hemolytic anemia (AIHA) or idiopathic thrombocytopenic purpura (ITP), despite low dose corticosteroids
  • Prior allogeneic stem cell transplant

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (33)

Hospital Italiano La Plata /ID# 150812

La Plata, Buenos Aires, 1902, Argentina

Location

Fundaleu /Id# 150811

Ciudad Autonoma de Buenos Aire, Ciuadad Autonoma de Buenos Aires, 1114, Argentina

Location

Cemic /Id# 150810

Ciudad Autonoma de Buenos Aire, Ciuadad Autonoma de Buenos Aires, 1431, Argentina

Location

Sanatorio Allende /ID# 150813

Córdoba, 5000, Argentina

Location

St George Hospital /ID# 154212

Kogarah, New South Wales, 2217, Australia

Location

Liverpool Hospital /ID# 154950

Liverpool, New South Wales, 2170, Australia

Location

Gold coast University Hospital /ID# 150833

Southport, Queensland, 4215, Australia

Location

Peter MacCallum Cancer Ctr /ID# 154948

Melbourne, Victoria, 3000, Australia

Location

Perth Blood Institute Ltd /ID# 154949

Nedlands, Western Australia, 6009, Australia

Location

UMHAT Alexandrovska EAD /ID# 162987

Sofiya, Sofia, 1431, Bulgaria

Location

UMHAT Sveti Georgi /ID# 161594

Plovdiv, 4002, Bulgaria

Location

UMHAT Sveti Ivan Rilski /ID# 163280

Sofia, 1431, Bulgaria

Location

SHAT Hematologic Diseases /ID# 161592

Sofia, 1756, Bulgaria

Location

Prince of Wales Hospital /ID# 150837

Hong Kong, 999077, Hong Kong

Location

Queen Mary Hospital /ID# 150836

Hong Kong, 999077, Hong Kong

Location

Semmelweis Egyetem /ID# 150792

Budapest, 1085, Hungary

Location

Del-pesti Centrumkorhaz Orszagos Hematologiai es Infektologiai Intezet /ID# 152842

Budapest, 1097, Hungary

Location

Centro de Investigacion Clínica Chapultepec SA de CV /ID# 163641

Morelia, Michoacán, 58260, Mexico

Location

Hospital Universitario Dr. Jose Eleuterio Gonzalez /ID# 150821

Monterrey, Nuevo León, 64460, Mexico

Location

Middlemore Clinical Trials /ID# 161526

Papatoetoe, Auckland, 2025, New Zealand

Location

North Shore Hospital /ID# 157626

Takapuna, Auckland, 0622, New Zealand

Location

Wellington Regional Hospital /ID# 157627

Newtown, Wellington Region, 6021, New Zealand

Location

Instytut Hematologii i Transfuzjologii /ID# 150878

Warsaw, Masovian Voivodeship, 02-776, Poland

Location

Szpitale Pomorskie Sp. z o.o /ID# 164097

Gdynia, Pomeranian Voivodeship, 81-519, Poland

Location

SP ZOZ Zespol Szpitali Miejskich w Chorzowie /ID# 150877

Chorzów, Silesian Voivodeship, 41-500, Poland

Location

Wojewodzkie Wielospecjalistyczne Centrum Onkologii i Traumatologii im. M. Kopern /ID# 150880

Lodz, Łódź Voivodeship, 93-513, Poland

Location

Federal State Budgetary Scientific Institution N.N. Blokhin /ID# 166610

Moscow, Moscow, 115478, Russia

Location

Moscow State budget healthcare /ID# 154806

Moscow, Moscow, 125284, Russia

Location

Regional Oncological Dispensary /ID# 154202

Penza, Penza Oblast, 440071, Russia

Location

Federal State Budgetary Ins NRC for Hematology of MoH of Russian Federation /ID# 154213

Moscow, 125167, Russia

Location

China Medical University Hospital /ID# 150839

Taichung, 40447, Taiwan

Location

National Taiwan University Hospital /ID# 150838

Taipei, 100, Taiwan

Location

Taipei Veterans General Hosp /ID# 153803

Taipei, 11217, Taiwan

Location

Related Publications (1)

  • Cochrane T, Enrico A, Gomez-Almaguer D, Hadjiev E, Lech-Maranda E, Masszi T, Nikitin E, Robak T, Weinkove R, Wu SJ, Sail KR, Pesko J, Pai M, Komlosi V, Anderson MA. Impact of venetoclax monotherapy on the quality of life of patients with relapsed or refractory chronic lymphocytic leukemia: results from the phase 3b VENICE II trial. Leuk Lymphoma. 2022 Feb;63(2):304-314. doi: 10.1080/10428194.2021.1986217. Epub 2021 Oct 11.

MeSH Terms

Conditions

Leukemia, Lymphocytic, Chronic, B-CellChromosome 17 deletion

Interventions

venetoclax

Condition Hierarchy (Ancestors)

Leukemia, B-CellLeukemia, LymphoidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Global Medical Services
Organization
AbbVie

Study Officials

  • ABBVIE INC.

    AbbVie

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 30, 2016

First Posted

December 2, 2016

Study Start

December 13, 2016

Primary Completion

December 29, 2021

Study Completion

December 29, 2021

Last Updated

February 22, 2023

Results First Posted

February 22, 2023

Record last verified: 2023-01

Data Sharing

IPD Sharing
Will share

AbbVie is committed to responsible data sharing regarding the clinical trials we sponsor. This includes access to anonymized, individual and trial-level data (analysis data sets), as well as other information (e.g., protocols and clinical study reports), as long as the trials are not part of an ongoing or planned regulatory submission. This includes requests for clinical trial data for unlicensed products and indications.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
For details on when studies are available for sharing visit https://vivli.org/ourmember/abbvie/
Access Criteria
Access to this clinical trial data can be requested by any qualified researchers who engage in rigorous independent scientific research, and will be provided following review and approval of a research proposal and statistical analysis plan and execution of a data sharing statement. Data requests can be submitted at any time after approval in the US and/or EU and a primary manuscript is accepted for publication. For more information on the process, or to submit a request, visit the following link https://www.abbvieclinicaltrials.com/hcp/data-sharing/
More information

Locations