NCT02926833

Brief Summary

The primary objective of phase 1 is to evaluate the safety of KTE-C19 and atezolizumab combination regimens. The primary objective of phase 2 is to evaluate the efficacy of KTE-C19 and atezolizumab, as measured by complete response rate in participants with refractory diffuse large B-cell lymphoma (DLBCL). Participants who received an infusion of KTE-C19 will complete the remainder of the 15 year follow-up assessments in a separate long-term follow-up study, KT-US-982-5968 (NCT05041309).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
37

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Sep 2016

Longer than P75 for phase_1

Geographic Reach
1 country

5 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 29, 2016

Completed
6 days until next milestone

First Submitted

Initial submission to the registry

October 5, 2016

Completed
1 day until next milestone

First Posted

Study publicly available on registry

October 6, 2016

Completed
3.7 years until next milestone

Results Posted

Study results publicly available

June 26, 2020

Completed
2.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 12, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 12, 2023

Completed
Last Updated

March 6, 2024

Status Verified

February 1, 2024

Enrollment Period

6.3 years

First QC Date

October 5, 2016

Results QC Date

June 8, 2020

Last Update Submit

February 13, 2024

Conditions

Outcome Measures

Primary Outcomes (2)

  • Phase 1: Number of Participants Experiencing Dose-Limiting Toxicities (DLTs)

    A DLT was defined as the following KTE-C19-related or ATZ-related events with an onset from immediately after the first ATZ infusion through 21 days after the first ATZ infusion: Grade 4 hematologic toxicity lasting \> 30 days (except lymphopenia or B-cell aplasia); All KTE-C19- or ATZ-related Grade 3 non-hematologic toxicities lasting for \> 7 days and all KTE-C19- or ATZ-related Grade 4 non-hematologic toxicities regardless of duration.

    Baseline up to 21 days

  • Phase 1 and 2: Complete Response Rate (CRR)

    CRR was assessed based on the International Working Group Revised Response Criteria for Malignant Lymphoma (Cheson, 2007), and was defined as the percentage of participants achieving a complete response (CR) as assessed by the study investigators. CR was defined as the complete resolution of all disease-related radiological abnormalities and the disappearance of all signs and symptoms related to the disease.

    From enrollment until first occurrence of CR or PR (maximum duration: 6.2 years)

Secondary Outcomes (17)

  • Phase 1 and 2: Objective Response Rate (ORR)

    From enrollment until first occurrence of CR or PR (maximum duration: 6.2 years)

  • Phase 1 and 2: Duration of Response (DOR)

    From the date of first confirmed objective response (CR or PR) to disease progression or death regardless of cause (maximum duration: 6.2 years)

  • Phase 1 and 2: Progression-Free Survival (PFS)

    From the date of first KTE-C19 infusion to disease progression or death regardless of cause (maximum duration: 6.2 years)

  • Phase 1 and 2: Overall Survival (OS)

    From the date of first KTE-C19 infusion to the date of death regardless of cause (maximum duration: 6.2 years)

  • Phase 1 and 2: Percentage of Participants Experiencing Treatment-Emergent Adverse Events (TEAEs)

    Up to 1.8 years

  • +12 more secondary outcomes

Study Arms (4)

Phase 1 Cohort 1: KTE-C19 + ATZ (After 21 Days of KTE-C19)

EXPERIMENTAL

Participants received conditioning chemotherapy consisting of 30 mg/m\^2 fludarabine and 500 mg/m\^2 cyclophosphamide intravenous (IV) infusion per day for 3 days followed by KTE-C19 IV infusion at a target dose of 2 x 10\^6 anti-CD19 chimeric antigen receptor (CAR) T cells/kg followed by 4 doses of atezolizumab (ATZ) (1200 mg/dose) IV infusion every 21 days, beginning 21 days following KTE-C19.

Biological: KTE-C19Biological: AtezolizumabDrug: CyclophosphamideDrug: Fludarabine

Phase 1 Cohort 2: KTE-C19 + ATZ (After 14 Days of KTE-C19)

EXPERIMENTAL

Participants received conditioning chemotherapy consisting of 30 mg/m\^2 fludarabine and 500 mg/m\^2 cyclophosphamide IV infusion per day for 3 days followed by KTE-C19 IV infusion at a target dose of 2 x 10\^6 anti-CD19 CAR T cells/kg followed by 4 doses of ATZ (1200 mg/dose) IV infusion every 21 days, beginning 14 days following KTE-C19.

Biological: KTE-C19Biological: AtezolizumabDrug: CyclophosphamideDrug: Fludarabine

Phase 1 Cohort 3: KTE-C19 + ATZ (After 1 Day of KTE-C19)

EXPERIMENTAL

Participants received conditioning chemotherapy consisting of 30 mg/m\^2 fludarabine and 500 mg/m\^2 cyclophosphamide IV infusion per day for 3 days followed by KTE-C19 IV infusion at a target dose of 2 x 10\^6 anti-CD19 CAR T cells/kg followed by 4 doses of ATZ (1200 mg/dose) IV infusion every 21 days, beginning 1 day following KTE-C19.

Biological: KTE-C19Biological: AtezolizumabDrug: CyclophosphamideDrug: Fludarabine

Phase 2: KTE-C19 + ATZ (After 1 Day of KTE-C19)

EXPERIMENTAL

Participants received conditioning chemotherapy consisting of 30 mg/m\^2 fludarabine and 500 mg/m\^2 cyclophosphamide IV infusion per day for 3 days followed by KTE-C19 IV infusion at a target dose of 2 x 10\^6 anti-CD19 CAR T cells/kg followed by 4 doses of ATZ (1200 mg/dose) IV infusion every 21 days, beginning 1 day following KTE-C19.

Biological: KTE-C19Biological: AtezolizumabDrug: CyclophosphamideDrug: Fludarabine

Interventions

KTE-C19BIOLOGICAL

A single infusion of KTE-C19 CAR-T cells administered intravenously

Also known as: Axicabtagene ciloleucel, Yescarta®
Phase 1 Cohort 1: KTE-C19 + ATZ (After 21 Days of KTE-C19)Phase 1 Cohort 2: KTE-C19 + ATZ (After 14 Days of KTE-C19)Phase 1 Cohort 3: KTE-C19 + ATZ (After 1 Day of KTE-C19)Phase 2: KTE-C19 + ATZ (After 1 Day of KTE-C19)
AtezolizumabBIOLOGICAL

Administered intravenously

Phase 1 Cohort 1: KTE-C19 + ATZ (After 21 Days of KTE-C19)Phase 1 Cohort 2: KTE-C19 + ATZ (After 14 Days of KTE-C19)Phase 1 Cohort 3: KTE-C19 + ATZ (After 1 Day of KTE-C19)Phase 2: KTE-C19 + ATZ (After 1 Day of KTE-C19)

Administered intravenously

Phase 1 Cohort 1: KTE-C19 + ATZ (After 21 Days of KTE-C19)Phase 1 Cohort 2: KTE-C19 + ATZ (After 14 Days of KTE-C19)Phase 1 Cohort 3: KTE-C19 + ATZ (After 1 Day of KTE-C19)Phase 2: KTE-C19 + ATZ (After 1 Day of KTE-C19)

Administered intravenously

Phase 1 Cohort 1: KTE-C19 + ATZ (After 21 Days of KTE-C19)Phase 1 Cohort 2: KTE-C19 + ATZ (After 14 Days of KTE-C19)Phase 1 Cohort 3: KTE-C19 + ATZ (After 1 Day of KTE-C19)Phase 2: KTE-C19 + ATZ (After 1 Day of KTE-C19)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically confirmed DLBCL
  • Chemotherapy-refractory disease, defined as one or more of the following:
  • Stable disease (duration of stable disease must be less than or equal to 6 months) or progressive disease as best response to most recent chemotherapy containing regimen
  • Disease progression or recurrence less than or equal to 12 months of prior autologous stem cell transplantation (SCT)
  • Individuals must have received adequate prior therapy including at a minimum:
  • Anti-cluster of differentiate 20 (anti-CD20) monoclonal antibody unless investigator determines that tumor is CD20-negative; and
  • an anthracycline containing chemotherapy regimen
  • At least one measurable lesion per revised International Working Group (IWG) Response Criteria
  • Age 18 years or older
  • Eastern cooperative oncology group (ECOG) performance status of 0 or 1
  • Adequate organ and bone marrow function
  • All individuals or legally appointed representatives/caregivers, must personally sign and date the institutional review board (IRB)/independent ethics committee (IEC) approved consent form before initiating any study specific procedures or activities.

You may not qualify if:

  • History of malignancy other than nonmelanoma skin cancer or carcinoma in situ (e.g., cervix, bladder, breast) or follicular lymphoma unless disease free for at least 3 years
  • History of allogeneic stem cell transplantation
  • Prior CAR therapy or other genetically modified T cell therapy
  • Clinically significant active infection
  • Known history of infection with human immunodeficiency virus (HIV) or hepatitis B (HBsAg positive) or hepatitis C virus (anti-HCV positive)
  • Individuals with detectable cerebrospinal fluid malignant cells or brain metastases or with a history of cerebrospinal fluid malignant cells or brain metastases
  • History of a seizure disorder, cerebrovascular ischemia/hemorrhage, dementia, cerebellar disease, or any autoimmune disease with central nervous system (CNS) involvement
  • History of autoimmune disease. Participants with a history of autoimmune-related hypothyroidism on a stable dose of thyroid replacement hormone and participants with controlled type 1 diabetes mellitus on a stable insulin regimen may be eligible for this study.
  • History of idiopathic pulmonary fibrosis, organizing pneumonia (e.g., bronchiolitis obliterans), drug-induced pneumonitis, idiopathic pneumonitis, or evidence of active pneumonitis per chest computed tomography (CT) scan at screening. History of radiation pneumonitis in the radiation field (fibrosis) is allowed.
  • Prior treatment with Programmed Cell Death Ligand 1 (PD-L1) inhibitor, PD-1 inhibitor, anti-CTLA4, anti-CD137, anti-OX40 or other immune checkpoint blockade or activator therapy with the exception of Individuals who received atezolizumab in this study and are eligible for re-treatment
  • Prior CD19 targeted therapy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (5)

City of Hope

Duarte, California, 91010, United States

Location

Stanford Cancer Center

Palo Alto, California, 94305, United States

Location

H Lee Moffitt Cancer Center

Tampa, Florida, 33612, United States

Location

Dana Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

University of Texas MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Related Publications (3)

  • Jacobson CA, Locke FL, Miklos DB, Herrera AF, Westin JR, Lee J, et al. End of Phase 1 results for ZUMA-6: Axicabtagene ciloleucel (axi-cel) in combination with atezolizumab for the treatment of patients with refractory diffuse large B cell lymphoma. Presented at ASH, 2018.

    BACKGROUND
  • Locke FL, Westin JR, Miklos DB, Herrera AF, Jacobson CA, Lee J, et al. Phase 1 results from ZUMA-6: Axicabtagene ciloleucel (axi-cel; KTE-C19) in combination with atezolizumab for the treatment of patients with refractory diffuse large B cell lymphoma. Presented at ASH, 2018, presentation #2628.

    BACKGROUND
  • Ernst M, Oeser A, Besiroglu B, Caro-Valenzuela J, Abd El Aziz M, Monsef I, Borchmann P, Estcourt LJ, Skoetz N, Goldkuhle M. Chimeric antigen receptor (CAR) T-cell therapy for people with relapsed or refractory diffuse large B-cell lymphoma. Cochrane Database Syst Rev. 2021 Sep 13;9(9):CD013365. doi: 10.1002/14651858.CD013365.pub2.

Related Links

MeSH Terms

Conditions

Lymphoma, Large B-Cell, Diffuse

Interventions

axicabtagene ciloleucelatezolizumabCyclophosphamidefludarabine

Condition Hierarchy (Ancestors)

Lymphoma, B-CellLymphoma, Non-HodgkinLymphomaNeoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

Phosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhosphoramidesOrganophosphorus Compounds

Results Point of Contact

Title
Medical Information
Organization
Kite, A Gilead Company

Study Officials

  • Kite Study Director

    Kite, A Gilead Company

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Model Details: This study uses a single group design. The arms reported in the Arms and Intervention section are based on the atezolizumab dosing schedule in the 4 Cohorts.
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 5, 2016

First Posted

October 6, 2016

Study Start

September 29, 2016

Primary Completion

January 12, 2023

Study Completion

January 12, 2023

Last Updated

March 6, 2024

Results First Posted

June 26, 2020

Record last verified: 2024-02

Data Sharing

IPD Sharing
Will share

Qualified external researchers may request IPD for this study after study completion. For more information, please visit our website at https://www.gilead.com/science-and-medicine/research/clinical-trials-transparency-and-data-sharing-policy

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
18 months after study completion
Access Criteria
A secured external environment with username, password, and RSA code.
More information

Locations