NCT02668653

Brief Summary

Quizartinib is an experimental drug. It is not approved for regular use. It can only be used in medical research. Adults might be able to join this study after bone marrow tests show they have a certain kind of blood cancer (FLT3-ITD AML). Participants will have an equal chance of receiving quizartinib or placebo along with their chemotherapy.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
539

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Sep 2016

Longer than P75 for phase_3

Geographic Reach
28 countries

244 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 22, 2016

Completed
7 days until next milestone

First Posted

Study publicly available on registry

January 29, 2016

Completed
7 months until next milestone

Study Start

First participant enrolled

September 1, 2016

Completed
5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 13, 2021

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

October 5, 2022

Completed
8 months until next milestone

Study Completion

Last participant's last visit for all outcomes

June 16, 2023

Completed
Last Updated

August 6, 2024

Status Verified

July 1, 2024

Enrollment Period

5 years

First QC Date

January 22, 2016

Results QC Date

August 12, 2022

Last Update Submit

August 2, 2024

Conditions

Keywords

Newly diagnosed Acute Myeloid LeukemiaFLT3-ITD positiveChemotherapyInduction chemotherapyConsolidation chemotherapyQuizartinibFeline McDonough sarcoma (FMS)-like tyrosine kinase 3AC220FLT3-ITDAML

Outcome Measures

Primary Outcomes (1)

  • Overall Survival in Participants With Newly Diagnosed FLT3-ITD (+) Acute Myeloid Leukemia

    Overall survival is defined as the time from randomization until death from any cause.

    Date of randomization to the date of death due to any cause, up to approximately 3 years after enrollment

Secondary Outcomes (9)

  • Event-free Survival in Participants With Newly Diagnosed FLT3-ITD (+) Acute Myeloid Leukemia

    Date of randomization to the date of refractory disease, relapse, or death, up to approximately 3 years after enrollment

  • Complete Remission (CR) Rate at the End of Induction in Participants With Newly Diagnosed FLT3-ITD (+) Acute Myeloid Leukemia

    Approximately Cycle 1 Day 21 (Induction) to end of Induction, up to approximately 120 days (each Induction cycle is up to 60 days)

  • Composite CR Rate at the End of Induction in Participants With Newly Diagnosed FLT3-ITD (+) Acute Myeloid Leukemia

    Approximately Cycle 1 Day 21 (Induction) to end of Induction, up to approximately 120 days (each Induction cycle is up to 60 days)

  • Number of Participants With Treatment-emergent Adverse Events Occurring in ≥10% Participants With Newly Diagnosed FLT3-ITD (+) Acute Myeloid Leukemia

    Date of first dose up to 30 days after last dose, up to 36 cycles following continuation (approximately 6 years 11 months, each cycle is 28 days)

  • Number of Participants Achieving CR With FLT3-ITD Minimal Residual Disease Negativity at the End of Induction in Participants With Newly Diagnosed FLT3-ITD (+) Acute Myeloid Leukemia

    Approximately Cycle 1 Day 21 (Induction phase) to end of Induction phase, up to approximately 120 days (each Induction cycle is up to 60 days)

  • +4 more secondary outcomes

Study Arms (2)

Chemotherapy plus quizartinib

EXPERIMENTAL

Induction: up to 2 cycles with cytarabine and daunorubicin/idarubicin, followed by the experimental drug quizartinib Consolidation: up to 4 cycles of cytarabine followed by the experimental drug quizartinib and/or hematopoeitic stem cell transplant Continuation: up to 36 cycles with the experimental drug quizartinib

Drug: ChemotherapyDrug: Quizartinib

Chemotherapy plus placebo

ACTIVE COMPARATOR

Induction: up to 2 cycles with cytarabine and daunorubicin/idarubicin, followed by placebo Consolidation: up to 4 cycles of cytarabine followed by placebo and/or hematopoeitic stem cell transplant Continuation: up to 36 cycles with placebo

Drug: ChemotherapyDrug: Placebo

Interventions

Also known as: Cytarabine, Daunorubicin, Idarubicin
Chemotherapy plus placeboChemotherapy plus quizartinib
Also known as: Test Product
Chemotherapy plus quizartinib
Also known as: Placebo Control
Chemotherapy plus placebo

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Must be competent and able to comprehend, sign, and date an Ethics Committee (EC) or Institutional Review Board approved Informed Consent Form (ICF) before performance of any study-specific procedures or tests;
  • Is ≥18 years or the minimum legal adult age (whichever is greater) and ≤75 years (at Screening);
  • Newly diagnosed, morphologically documented primary AML or AML secondary to myelodysplastic syndrome or a myeloproliferative neoplasm, based on the World Health Organization (WHO) 2008 classification (at Screening);
  • Eastern Cooperative Oncology Group (ECOG) performance status 0-2 (at the time the participant signs their first ICF);
  • Presence of FLT3-ITD activating mutation in bone marrow (allelic ratio of ≥3% FLT3-ITD/total FLT3);
  • Participant is receiving standard "7+3" induction chemotherapy regimen as specified in the protocol;
  • Adequate renal function defined as:
  • a. Creatinine clearance \>50 mL/min, as calculated with the modified Cockcroft Gault equation
  • Adequate hepatic function defined as:
  • Total serum bilirubin (TBL) ≤1.5 × upper limit of normal (ULN) unless the participant has documented Gilbert's syndrome or the increase is related to increased unconjugated (indirect) bilirubin due to hemolysis;
  • Serum alkaline phosphatase, aspartate transaminase (AST) and alanine transaminase (ALT) ≤2.5 × ULN;
  • Serum electrolytes within normal limits: potassium, calcium (total, or corrected for serum albumin in case of hypoalbuminemia or ionized calcium) and magnesium. If outside of normal limits, participant will be eligible when electrolytes are corrected;
  • If a woman of childbearing potential, must have a negative serum pregnancy test upon entry into this study and must be willing to use highly effective birth control upon enrollment, during the treatment period and for 6 months following the last dose of investigational drug or cytarabine, whichever is later. A woman is considered of childbearing potential following menarche and until becoming postmenopausal (no menstrual period for a minimum of 12 months);
  • If male, must be surgically sterile or willing to use highly effective birth control upon enrollment, during the treatment period, and for 6 months following the last dose of investigational drug or cytarabine, whichever is later.

You may not qualify if:

  • Diagnosis of acute promyelocytic leukemia (APL), French-American-British classification M3 or WHO classification of APL with translocation, t(15;17)(q22;q12), or breakpoint cluster region-Abelson murine leukemia viral oncogene homolog 1 (BCR-ABL) positive leukemia (ie, chronic myelogenous leukemia in blast crisis); participants who undergo diagnostic workup for APL and treatment with all-trans retinoic acid (ATRA), but who are found not to have APL, are eligible (treatment with ATRA must be discontinued before starting induction chemotherapy).
  • Diagnosis of AML secondary to prior chemotherapy or radiotherapy for other neoplasms;
  • Prior treatment for AML, except for the following allowances:
  • Leukapheresis;
  • Treatment for hyperleukocytosis with hydroxyurea;
  • Cranial radiotherapy for central nervous system (CNS) leukostasis;
  • Prophylactic intrathecal chemotherapy;
  • Growth factor/cytokine support;
  • Prior treatment with quizartinib or other FLT3-ITD inhibitors;
  • Prior treatment with any investigational drug or device within 30 days prior to Randomization (within 2 weeks for investigational or approved immunotherapy) or currently participating in other investigational procedures;
  • History of known CNS leukemia, including cerebrospinal fluid positive for AML blasts; lumbar puncture is recommended for participants with symptoms of CNS leukemia to rule out extramedullary CNS involvement;
  • History of other malignancies, except adequately treated non-melanoma skin cancer, curatively treated in-situ disease, or other solid tumors curatively treated with no evidence of disease for at least 2 years;
  • Uncontrolled or significant cardiovascular disease, including any of the following:
  • Bradycardia of less than 50 beats per minute, unless the participant has a pacemaker;
  • Fridericia's Heart Rate Correction Formula (QTcF) interval \>450 msec;
  • +14 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (244)

University of Florida (UF) Health Shands Hospital

Gainesville, Florida, 90095, United States

Location

The University of Chicago Medical Center

Chicago, Illinois, 60637, United States

Location

Franciscan St. Francis Health Indianapolis

Indianapolis, Indiana, 46237, United States

Location

University of Kentucky Chandler Medical Center

Lexington, Kentucky, 40536, United States

Location

John Theurer Cancer Center at Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

NY Medical College - Hudson Valley Hematology Oncology Associates

Valhalla, New York, 10595, United States

Location

Duke Clinical Research Institute

Durham, North Carolina, 27710, United States

Location

University Hospitals Seidman Cancer Center

Cleveland, Ohio, 44106, United States

Location

Hospital of the University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Thomas Jefferson University Hospital

Philadelphia, Pennsylvania, 19107, United States

Location

West Virginia University Hospitals, Inc.

Morgantown, West Virginia, 26506, United States

Location

Sanatorio Britanico

Rosario, Santa Fe Province, S2000CVB, Argentina

Location

Sanatorio Allende

Córdoba, X5000JHQ, Argentina

Location

Calvary Mater Newcastle

Waratah, New South Wales, 2298, Australia

Location

Townsville Hospital (TTH)

Douglas, Queensland, 4814, Australia

Location

Princess Alexandra Hospital

Woolloongabba, Queensland, 4102, Australia

Location

Fiona Stanley Hospital

Murdoch, Western Australia, 6150, Australia

Location

AZ Sint-Jan Brugge-Oostende AV

Bruges, 8000, Belgium

Location

Universitair Ziekenhuis Gent

Ghent, 9000, Belgium

Location

UCL Mont-Godinne

Yvoir, 5530, Belgium

Location

Hospital Amaral Carvalho

Brasília, 70750-521, Brazil

Location

Hospital do CEPON

Brasília, 70750-521, Brazil

Location

Instituto do Cancer do Estado de São Paulo

Brasília, 70750-521, Brazil

Location

Santa Casa de Misericórdia de Porto Alegre

Brasília, 70750-521, Brazil

Location

Hospital da Cidade de Passo Fundo

Passo Fundo, 99010-260, Brazil

Location

Hospital de Clínicas de Porto Alegre

Porto Alegre, 90035-903, Brazil

Location

University Multiprofile Hospital for Active Treatment "Dr. G. Stranski" EAD

Pleven, 5800, Bulgaria

Location

University Multiprofile Hospital for Active Treatment "Sveti Georgi" EAD

Sofia, 1000, Bulgaria

Location

Tom Baker Cancer Centre

Calgary, Alberta, T2N 4N2, Canada

Location

University of Alberta Hospital

Edmonton, Alberta, T6G-3G3, Canada

Location

Vancouver General Hospital (VGH)

Vancouver, British Columbia, V5Z 1M9, Canada

Location

Princess Margaret Cancer Centre

Toronto, Ontario, M5G 1X5, Canada

Location

Peking University First Hospital

Beijing, 100034, China

Location

The General Hospital of People's Liberation Army (301 Hospital)

Beijing, 100853, China

Location

Fujian Medical University Union Hospital

Fuzhou, 350001, China

Location

Guangdong General Hospital

Guangzhou, 510030, China

Location

Lanzhou University Second Hospital

Lanzhou, 730030, China

Location

Ruijin Hospital Affiliated to The Shanghai Jiao Tong University Medical School

Shanghai, 200025, China

Location

West China Hospital, Sichuan University

Taiyuan, 30001, China

Location

Institute of Hematology and Blood Diseases Hospital Chinese Academy of Medical Sciences

Tianjin, 300020, China

Location

The First Affiliated Hospital of Wenzhou Medical University

Wenzhou, 325015, China

Location

Tang Du Hospital, Fourth Military Medical University

Xi'an, 710038, China

Location

Henan Cancer Hospital

Zhengzhou, 450008, China

Location

Klinička Bolnica Dubrava

Zagreb, 10000, Croatia

Location

Klinička Bolnica Merkur

Zagreb, 10000, Croatia

Location

Klinički Bolnički Centar Zagreb

Zagreb, 10000, Croatia

Location

Fakultní Nemocnice Hradec Králové

Hradec Králové, 500 05, Czechia

Location

Fakultní Nemocnice Olomouc

Olomouc, 775 20, Czechia

Location

Fakultní Nemocnice Ostrava

Ostrava, 708 52, Czechia

Location

Fakultni Nemocnice Plzen

Pilsen, 304 60, Czechia

Location

Vseobecna Fakultni Nemocnice, Ustav hematologie a krevni transfuze (UHKT)

Prague, 128 20, Czechia

Location

Hospital A. Michallon

Grenoble, 38043, France

Location

Centre Hospitalier de Versailles - Hôpital André Mignot

Le Chesnay, 78150, France

Location

Centre Hospitalier Régional Universitaire de Lille (CHRU) - Hôpital Claude Huriez

Lille, 59037, France

Location

Centre Léon Bérard

Lyon, 69373, France

Location

L'Institut Paoli - Calmettes

Marguerittes, 13009, France

Location

Hôpital de la Conception

Marseille, 13385, France

Location

CHRU Montpellier - Saint Eloi

Montpellier, 34295, France

Location

Hôpital Saint-Antoine

Paris, 75012, France

Location

Hôpital Saint-Louis

Paris, 75475, France

Location

Hôpital Haut-Lévêque

Pessac, 33604, France

Location

Centre Hospitalier Lyon-Sud

Pierre-Bénite, 69495, France

Location

Centre Henri Becquerel - Centre de Lutte Contre le Cancer

Rouen, 76038, France

Location

Centre Hospitalier Universitaire de Toulouse - Hôpital Purpan

Toulouse, 31059, France

Location

HELIOS Klinikum Bad Saarow

Bad Saarow, 15526, Germany

Location

Charité - Universitätsmedizin Berlin

Berlin, 10117, Germany

Location

Städtisches Klinikum Braunschweig gGmbH

Braunschweig, 38114, Germany

Location

Marien Hospital Düsseldorf GmbH

Düsseldorf, 40479, Germany

Location

Universitätsklinikum Essen

Essen, 45122, Germany

Location

Universitätsklinikum Frankfurt

Frankfurt am Main, 60590, Germany

Location

Universitätsklinikum Halle (Saale)

Halle, 6120, Germany

Location

Evangelisches Krankenhaus Hamm gGmbH

Hamm, 59063, Germany

Location

Medizinische Hochschule Hannover (MHH)

Hannover, 30625, Germany

Location

Universitätsklinikum Münster

Heidelberg, 69115, Germany

Location

Universitätsklinikum Tübingen

Heidelberg, 69115, Germany

Location

Universitätsklinikum Heidelberg

Heidelberg, 69120, Germany

Location

Universitätsklinikum Leipzig

Leipzig, 4103, Germany

Location

Stauferklinikum Schwäbisch Gmünd

Mutlangen, 73557, Germany

Location

HELIOS Klinikum Wuppertal

Wuppertal, 42283, Germany

Location

Prince of Wales Hospital

Shatin, Hong Kong

Location

Markusovszky Egyetemi Oktatókórház

Budapest, 1051, Hungary

Location

Szegedi Tudományegyetem

Budapest, 1051, Hungary

Location

Semmelweis Egyetem

Budapest, 1083, Hungary

Location

Debreceni Egyetem Klinikai Központ

Debrecen, 4032, Hungary

Location

Pecsi Tudomanyegyetem Klinikai Központ

Pécs, 7624, Hungary

Location

Markusovszky Egyetemi Oktatókórház

Szombathely, 9700, Hungary

Location

Assaf Harofeh Medical Center

Be’er Ya‘aqov, Tsifrin, 70300, Israel

Location

Bnai Zion Medical Center

Haifa, 31048, Israel

Location

Rambam Medical Center

Haifa, 31096, Israel

Location

Hadassah University Medical Center

Jerusalem, 91120, Israel

Location

Rabin Medical Center - Beilinson Hospital

Petah Tikva, 49100, Israel

Location

The Chaim Sheba Medical Center

Ramat Gan, 52621, Israel

Location

Tel Aviv Sourasky Medical Center

Tel Aviv, 64239, Israel

Location

Azienda Ospedaliera Nazionale SS.Antonio e Biagio e Cesare Arrigo

Alessandria, 15121, Italy

Location

Azienda Sanitaria Locale 13 - Ospedale "C. e G. Mazzoni"- Ascoli Piceno

Ascoli Piceno, 63100, Italy

Location

Azienda Ospedaliero - Universitaria Consorziale Policlinico di Bari

Bari, 70124, Italy

Location

Azienda Ospedaliero-Universitaria di Bologna Policlinico S. Orsola-Malpighi

Bologna, 40138, Italy

Location

IRCCS AOU San Martino - IST

Genova, 16132, Italy

Location

ASST Grande Ospedale Metropolitano Niguarda

Milan, 20162, Italy

Location

A.O.R.N. "A. Cardarelli"

Napoli, 80131, Italy

Location

Azienda Ospedaliero Universitaria Maggiore della Carità di Novara

Novara, 28100, Italy

Location

Azienda Ospedaliero - Universitaria San Luigi Gonzaga

Orbassano, 10043, Italy

Location

Azienda Ospedaliera Ospedali Riuniti Villa Sofia - Cervello

Palermo, 90146, Italy

Location

Ospedale S. Maria delle Croci - Ravenna

Ravenna, 48121, Italy

Location

Fondazione Policlinico Universitario Agostino Gemelli

Roma, 133, Italy

Location

Ospedale S. Eugenio

Roma, 133, Italy

Location

Policlinico Tor Vergata

Roma, 133, Italy

Location

IRCCS Ospedale San Raffaele

Roma, 20132, Italy

Location

Azienda Ospedaliero-Universitaria Careggi

Roma, 50134, Italy

Location

Azienda Ospedaliero Universitaria Pisana - Ospedale Santa Chiara

Roma, 56126, Italy

Location

Azienda Ospedaliera Universitaria "Federico II"

Roma, 80131, Italy

Location

Istituto Clinico Humanitas

Rozzano, 20089, Italy

Location

Azienda Ospedaliera Universitaria OO.RR. San Giovanni di Dio Ruggi d'Aragona

Salerno, 84131, Italy

Location

Azienda Ospedaliera Universitaria Senese

Siena, 53100, Italy

Location

Azienda Ospedaliera Universitaria Citta della Salute e della Scienza di Torino - Ospedale Molinette

Torino, 10126, Italy

Location

Azienda Ospedaliera Ordine Mauriziano di Torino

Torino, 10128, Italy

Location

ASST dei Sette Laghi - Ospedale di Circolo e Fondazione Macchi Varese

Varese, 21100, Italy

Location

National Hospital Organization Nagoya Medical Center

Nagoya, Aichi-ken, 460-0001, Japan

Location

Nagoya University Hospital

Nagoya, Aichi-ken, 466-8560, Japan

Location

Toyohashi Municipal Hospital

Toyohashi, Aichi-ken, 441-8570, Japan

Location

Ehime Prefectural Central Hospital

Matsuyama, Ehime, 790-0024, Japan

Location

University of Fukui Hospital

Yoshida, Fukui, 910-1193, Japan

Location

Kyushu University Hospital

Higashi, Fukuoka, 812-8582, Japan

Location

Gunmaken Saiseikai Maebashi Hospital

Maebashi, Gunma, 371-0821, Japan

Location

Gunma University Hospital

Maebashi, Gunma, 371-8511, Japan

Location

Chugoku Central Hospital

Fukuyama, Hiroshima, 720-0001, Japan

Location

Sapporo Hokuyu Hospital

Sapporo, Hokkaido, 003-0006, Japan

Location

Yokohama City University Hospital

Yokohama, Kanagawa, 236-0004, Japan

Location

National Hospital Organization Sendai Medical Center

Sendai, Miagi, 983-8520, Japan

Location

Tenri Hospital

Tenri, Nara, 632-8552, Japan

Location

Hamamatsu University Hospital

Hamamatsu, Shizuoka, 431-3192, Japan

Location

Tokyo Metropolitan Cancer and Infectious Diseases Center, Komagome Hospital

Bunkyō-Ku, Tokyo, 113-8677, Japan

Location

The Jikei University Hospital

Minato-Ku, Tokyo, 105-0003, Japan

Location

Akita University Hospital

Akita, 010-8543, Japan

Location

Aomori Prefectural Central Hospital

Aomori, 030-8553, Japan

Location

Chiba Aoba Municipal Hospital

Chiba, 260-0852, Japan

Location

Kameda Medical Center - Kameda General Hospital

Chiba, 296-0041, Japan

Location

National Hospital Organization Kyushu Cancer Center

Fukuoka, 811-1395, Japan

Location

Gifu Municipal Hospital

Gifu, 500-8513, Japan

Location

National Hospital Organization Kagoshima Medical Center

Kagoshima, 892-0853, Japan

Location

Kobe City Medical Center General Hospital

Kobe, 650-0047, Japan

Location

National Hospital Organization Kumamoto Medical Center

Kumamoto, 860-0008, Japan

Location

Nagasaki University Hospital

Nagasaki, 852-8501, Japan

Location

Osaka City General Hospital

Osaka, 534-0021, Japan

Location

Osaka Red Cross Hospital

Osaka, 543-8555, Japan

Location

NTT Medical Center Tokyo

Tokyo, 141-8625, Japan

Location

Szpital Uniwersytecki w Krakowie

Krakow, 31-501, Poland

Location

Wojewódzki Szpital Specjalistyczny im. Janusza Korczaka

Słupsk, 76-200, Poland

Location

Instytut Hematologii i Transfuzjologi

Warsaw, 00-957, Poland

Location

Samodzielny Publiczny Szpital Kliniczny Nr. 1 we Wrocławiu

Warsaw, 50367, Poland

Location

Centro Hospitalar e Universitário de Coimbra, EPE - Hospitais da Universidade de Coimbra

Coimbra, 3000-075, Portugal

Location

Centro Hospitalar Lisboa Central, EPE - Hospital Santo António dos Capuchos

Lisbon, 1169050, Portugal

Location

Centro Hospitalar do Porto, EPE - Hospital Geral de Santo António

Porto, 4099-001, Portugal

Location

Instituto Português Oncologia do Porto Francisco Gentil, EPE

Porto, 4200-072, Portugal

Location

Centro Hospitalar de São João, EPE - Hospital de São João

Porto, 4200-319, Portugal

Location

Institutul Regional de Oncologie Iași

Bucharest, 20125, Romania

Location

Spitalul Clinic Colentina

Bucharest, 20125, Romania

Location

Spitalul Clinic Coltea

Bucharest, 20125, Romania

Location

Spitalul Universitar de Urgenta Bucuresti

Bucharest, 20125, Romania

Location

Institutul Clinic Fundeni

Bucharest, 22328, Romania

Location

Institutul Oncologic "Prof. Dr. Ion Chiricuţă" Cluj Napoca

Cluj-Napoca, 400124, Romania

Location

Spitalul Clinic Municipal Filantropia Craiova

Craiova, 200143, Romania

Location

Spitalul Clinic Judetean de Urgenta Târgu-Mureş (4005)

Târgu Mureş, 540042, Romania

Location

Spitalul Clinic Judetean de Urgenta Târgu-Mureş (4008)

Târgu Mureş, 540136, Romania

Location

Nizhny Novgorod Regional Clinical Hospital

Nizhny Novgorod, 603126, Russia

Location

Penza Regional Oncology Dispensary

Penza, 440071, Russia

Location

Republican Hospital n.a.V.A. Baranov

Petrozavodsk, 185019, Russia

Location

Ryazan Regional Clinical Hospital

Ryazan, 390039, Russia

Location

Russian Research Institute of Hematology and Blood Transfusion

Saint Petersburg, 191024, Russia

Location

Leningrad Regional Clinic and Hospital

Saint Petersburg, 194291, Russia

Location

Almazov Federal North-West Medical Research Centre

Saint Petersburg, 197341, Russia

Location

Saratov State Medical University named after V.I. Razumovsky

Saratov, 410012, Russia

Location

Tula Regional Clinical Hospital

Tula, 300053, Russia

Location

Klinički Centar Srbije

Belgrade, 11000, Serbia

Location

Klinički Centar Niš

Niš, 18000, Serbia

Location

Klinički Centar Vojvodine

Novi Sad, 21101, Serbia

Location

National University Hospital (S) Pte Ltd

Singapore, 119074, Singapore

Location

Singapore General Hospital

Singapore, 138543, Singapore

Location

Inje University Haeundae Paik Hospital

Busan, 48108, South Korea

Location

Pusan National University Hospital

Busan, 49241, South Korea

Location

Kyungpook National University Hospital

Daegu, 41944, South Korea

Location

Yeungnam University Medical Center

Daegu, 42415, South Korea

Location

Daegu Catholic University Medical Center

Daegu, 42472, South Korea

Location

Chonnam National University Hwasun Hospital

Hwasun, 58128, South Korea

Location

Gachon University Gil Hospital

Incheon, 21565, South Korea

Location

Seoul National University Bundang Hospital

Seongnam-si, 13620, South Korea

Location

Seoul National University Hospital

Seoul, 3080, South Korea

Location

Severance Hospital

Seoul, 3722, South Korea

Location

SoonChunHyang University Seoul Hospital

Seoul, 4401, South Korea

Location

Konkuk University Medical Center

Seoul, 5030, South Korea

Location

Asan Medical Center

Seoul, 5505, South Korea

Location

Samsung Medical Center

Seoul, 6351, South Korea

Location

The Catholic University of Korea, Seoul St. Mary's Hospital

Seoul, 6591, South Korea

Location

Korea University Guro Hospital

Seoul, 8308, South Korea

Location

Ajou University Hospital

Sŏwŏn, 16499, South Korea

Location

Ulsan University Hospital (UUH)

Ulsan, 44033, South Korea

Location

Hospital Universitari Son Espases

Palma, Mallorca, 7014, Spain

Location

Complexo Hospitalario Universitario A Coruña

A Coruña, 15006, Spain

Location

Complejo Hospitalario Universitario de Albacete - Hospital General Universitario

Albacete, 2006, Spain

Location

Hospital General Universitario de Alicante

Alicante, 3010, Spain

Location

Catalan Institute of Oncology (ICO)

Badalona, 8916, Spain

Location

Hospital del Mar

Barcelona, 8003, Spain

Location

Hospital Universitario Vall d'Hebron

Barcelona, 8035, Spain

Location

Hospital Clinic i Provincial

Barcelona, 8036, Spain

Location

Hospital Duran i Reynals

Barcelona, 8907, Spain

Location

Hospital de Basurto

Bilbao, 48013, Spain

Location

Hospital San Pedro de Alcántara

Cáceres, 10002, Spain

Location

Hospital Universitario Reina Sofía

Córdoba, 14004, Spain

Location

Hospital Universitari de Girona Doctor Josep Trueta

Girona, 17007, Spain

Location

Complejo Hospitalario Universitario Granada

Granada, 18014, Spain

Location

Hospital Dr. Negrín

Las Palmas de Gran Canaria, 35010, Spain

Location

Hospital General Universitario Gregorio Marañón

Madrid, 28007, Spain

Location

Hospital Universitario Ramón y Cajal

Madrid, 28034, Spain

Location

Hospital Clínico San Carlos

Madrid, 28040, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, 28041, Spain

Location

Hospital Quirón Madrid

Madrid, 28223, Spain

Location

Hospital Universitario Puerta de Hierro - Majadahonda

Majadahonda, 28222, Spain

Location

Hospital Regional Universitario de Málaga - Hospital General

Málaga, 29010, Spain

Location

Hospital Universitario Central de Asturias

Oviedo, 33011, Spain

Location

Complejo Hospitalario de Navarra

Pamplona, 31008, Spain

Location

Fundación Jiménez Díaz

Pamplona, 31008, Spain

Location

Hospital Clínico Universitario "Lozano Blesa"

Pamplona, 31008, Spain

Location

Hospital General Universitario Morales Meseguer

Pamplona, 31008, Spain

Location

Hospital Universitario Miguel Servet

Pamplona, 31008, Spain

Location

Hospital Álvaro Cunqueiro

Pamplona, 31008, Spain

Location

Hosp Universitario Salamanca

Salamanca, 37007, Spain

Location

Hospital Universitario Marqués de Valdecilla

Santander, 39008, Spain

Location

Complexo Hospitalario Universitario de Santiago (CHUS) - Hospital Clínico Universitario

Santiago de Compostela, 15706, Spain

Location

Hospital Universitario Virgen del Rocío

Seville, 41013, Spain

Location

Hospital Universitari Joan XXIII de Tarragona

Tarragona, 43005, Spain

Location

Hospital Clinico Universitario de Valencia

Valencia, 46010, Spain

Location

Hospital Universitario Dr. Peset

Valencia, 46017, Spain

Location

Hospital Universitari i Politècnic La Fe

Valencia, CP 46026, Spain

Location

Chang Gung Medical Foundation - Kaohsiung Branch

Kaohsiung City, Niaosong District, 83301, Taiwan

Location

China Medical University Hospital

Taichung, 40447, Taiwan

Location

National Cheng Kung University Hospital

Tainan, 704, Taiwan

Location

National Taiwan University Hospital

Taipei, 100, Taiwan

Location

Taipei Veterans General Hospital

Taipei, 11217, Taiwan

Location

Chang Gung Medical Foundation - Linkou Branch

Taoyuan District, 33305, Taiwan

Location

Cherkasy Regional Oncology Dispensary

Cherkasy, 18009, Ukraine

Location

Poltava Regional Clinical Hospital named after M. V. Sklifosovskoho

Poltava, 36011, Ukraine

Location

Vinnitsa Regional Clinical Hospital im. N.I. Pirogov

Vinnytsia, 21018, Ukraine

Location

Zhitomir Regional Clinical Hospital

Zhytomyr, 10002, Ukraine

Location

Maidstone and Tunbridge Wells NHS Trust - Maidstone Hospital

Maidstone, ME16 9QQ, United Kingdom

Location

Related Publications (4)

  • Levis MJ, Erba HP, Montesinos P, Kim HJ, Vrhovac R, Patkowska E, Zak P, Wang PN, Connolly Rohrbach JE PhD, Chang K, Liu L, Mostafa Kamel Y, Imadalou K, Lesegretain A, Cortes JE, Sekeres MA, Dombret H, Amadori S, Wang J, Schlenk RF, Perl AE. FLT3-ITD measurable residual disease from the QuANTUM-First trial. Blood Adv. 2025 Oct 6:bloodadvances.2025016444. doi: 10.1182/bloodadvances.2025016444. Online ahead of print.

  • Schlenk RF, Montesinos P, Kim HJ, Romero-Aguilar A, Vrhovac R, Patkowska E, Zak P, Wang PN, Hanyok J, Liu L, Kamel YM, Imadalou K, Lesegretain A, Cortes J, Sekeres MA, Dombret H, Amadori S, Wang J, Perl AE, Levis MJ, Erba HP. Impact of hematopoietic cell transplantation and quizartinib in newly diagnosed patients with acute myeloid leukemia and FMS-like tyrosine kinase 3-internal tandem duplications in the QuANTUM-First trial. Haematologica. 2025 Sep 1;110(9):2024-2039. doi: 10.3324/haematol.2024.286623. Epub 2025 Mar 13.

  • Erba HP, Montesinos P, Kim HJ, Patkowska E, Vrhovac R, Zak P, Wang PN, Mitov T, Hanyok J, Kamel YM, Rohrbach JEC, Liu L, Benzohra A, Lesegretain A, Cortes J, Perl AE, Sekeres MA, Dombret H, Amadori S, Wang J, Levis MJ, Schlenk RF; QuANTUM-First Study Group. Quizartinib plus chemotherapy in newly diagnosed patients with FLT3-internal-tandem-duplication-positive acute myeloid leukaemia (QuANTUM-First): a randomised, double-blind, placebo-controlled, phase 3 trial. Lancet. 2023 May 13;401(10388):1571-1583. doi: 10.1016/S0140-6736(23)00464-6. Epub 2023 Apr 25.

  • Cortes J, Perl AE, Dohner H, Kantarjian H, Martinelli G, Kovacsovics T, Rousselot P, Steffen B, Dombret H, Estey E, Strickland S, Altman JK, Baldus CD, Burnett A, Kramer A, Russell N, Shah NP, Smith CC, Wang ES, Ifrah N, Gammon G, Trone D, Lazzaretto D, Levis M. Quizartinib, an FLT3 inhibitor, as monotherapy in patients with relapsed or refractory acute myeloid leukaemia: an open-label, multicentre, single-arm, phase 2 trial. Lancet Oncol. 2018 Jul;19(7):889-903. doi: 10.1016/S1470-2045(18)30240-7. Epub 2018 May 31.

MeSH Terms

Conditions

Leukemia, Myeloid, AcuteLeukemia

Interventions

Drug TherapyCytarabineDaunorubicinIdarubicinquizartinib

Condition Hierarchy (Ancestors)

Leukemia, MyeloidNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

TherapeuticsCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsArabinonucleosidesNucleosidesNucleic Acids, Nucleotides, and NucleosidesAnthracyclinesNaphthacenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsPolycyclic CompoundsAminoglycosidesGlycosidesCarbohydrates

Results Point of Contact

Title
Contact for Clinical Trial Information
Organization
Daiichi Sankyo Inc.

Study Officials

  • Global Clinical Leader

    Daiichi Sankyo

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 22, 2016

First Posted

January 29, 2016

Study Start

September 1, 2016

Primary Completion

August 13, 2021

Study Completion

June 16, 2023

Last Updated

August 6, 2024

Results First Posted

October 5, 2022

Record last verified: 2024-07

Data Sharing

IPD Sharing
Will share

De-identified individual participant data (IPD) and applicable supporting clinical trial documents may be available upon request at https://vivli.org/. In cases where clinical trial data and supporting documents are provided pursuant to our company policies and procedures, Daiichi Sankyo will continue to protect the privacy of our clinical trial participants. Details on data sharing criteria and the procedure for requesting access can be found at this web address: https://vivli.org/ourmember/daiichi-sankyo/

Shared Documents
STUDY PROTOCOL, SAP, ICF
Time Frame
Studies for which the medicine and indication have received European Union (EU) and United States (US), and/or Japan (JP) marketing approval on or after 01 January 2014 or by the US or EU or JP Health Authorities when regulatory submissions in all regions are not planned and after the primary study results have been accepted for publication.
Access Criteria
Formal request from qualified scientific and medical researchers on IPD and clinical study documents from clinical trials supporting products submitted and licensed in the United States, the European Union and/or Japan from 01 January 2014 and beyond for the purpose of conducting legitimate research. This must be consistent with the principle of safeguarding study participants' privacy and consistent with provision of informed consent.
More information

Locations