NCT02562443

Brief Summary

The study's primary objective \[in a population of patients with MDS after failure of treatment with azacitidine (AZA) or decitabine (DAC)\], is to compare the overall survival (OS) of patients in the rigosertib group vs the Physician's Choice group, in all patients and in a subgroup of patients with IPSS-R very high risk.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
372

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Dec 2015

Longer than P75 for phase_3

Geographic Reach
20 countries

153 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 25, 2015

Completed
4 days until next milestone

First Posted

Study publicly available on registry

September 29, 2015

Completed
2 months until next milestone

Study Start

First participant enrolled

December 2, 2015

Completed
4.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 26, 2020

Completed
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

July 26, 2021

Completed
Last Updated

September 26, 2022

Status Verified

September 1, 2022

Enrollment Period

4.7 years

First QC Date

September 25, 2015

Last Update Submit

September 22, 2022

Conditions

Keywords

Myelodysplastic SyndromeMDS

Outcome Measures

Primary Outcomes (1)

  • Overall survival of all randomized patients and overall survival of patients scored as IPSS-R very high risk.

    The overall survival (OS) of all randomized patients (ITT population), and the overall survival of patients scored as IPSS-R very high risk.

    Up to 30 Months

Secondary Outcomes (6)

  • Overall survival of patients with monosomy 7 chromosomal aberrations.

    Up to 30 Months

  • Overall survival of patients with trisomy 8 chromosomal aberrations.

    Up to 30 Months

  • Percent of patients with response according to 2006 IWG criteria.

    Up to 30 Months

  • Scores of Quality of Life Questionnaire.

    At Baseline, at Week 4, Every 4 Weeks thereafter, and at the End-of-treatment.

  • Percent of patients with bone marrow blast response rate according to 2006 IWG criteria.

    Up to 30 Months

  • +1 more secondary outcomes

Other Outcomes (4)

  • Exploratory Objective: Bone Marrow Genomic Mutational Status

    At screening, every 8 week during study treatment, and at the end of study treatment

  • Exploratory Objective: Transition to Acute Myelogenous Leukemia (AML)

    Through study completion, an average of 8 months

  • Safety Objective: Number of Patients with AEs.

    Monthly, through study completion

  • +1 more other outcomes

Study Arms (2)

rigosertib + best supportive care (BSC)

EXPERIMENTAL
Drug: rigosertibDrug: best supportive care (BSC)

Physician's Choice (PC) + best supportive care (BSC)

ACTIVE COMPARATOR
Drug: Any approved or standard-of-care therapyDrug: best supportive care (BSC)

Interventions

Patients will receive intravenous rigosertib 1800 mg/24 hr for 3 days every 2 weeks for first 8 cycles, then every 4 weeks thereafter + best supportive care (BSC).

Also known as: ON 01910.Na
rigosertib + best supportive care (BSC)

Patients will receive Physician's Choice of Treatment or alternative treatment which may include any approved or standard-of-care therapy, based on frequently used treatment for MDS (no experimental therapy) + best supportive care.

Physician's Choice (PC) + best supportive care (BSC)

Patients will receive best supportive care (BSC): azacitidine (AZA) and/or decitabine (DAC) are permitted.

Physician's Choice (PC) + best supportive care (BSC)

Eligibility Criteria

Age18 Years - 81 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • MDS classified as follows:
  • RAEB-1 per World Health Organization (WHO) MDS criteria (5% to \<10% BM blasts)
  • RAEB-2 per WHO MDS criteria (10% to \<20% BM blasts)
  • RAEB-t per French-American-British (FAB) classification (20% to 30% BM blasts)
  • At least one cytopenia (ANC \< 1800/µL or platelet count \< 100,000/µL or hemoglobin \[Hgb\] \< 10 g/dL)
  • Progression (according to 2006 IWG criteria) at any time after initiation of AZA or DAC treatment or Failure to achieve complete or partial response or hematological improvement (HI) (according to 2006 IWG) after at least six 4-week cycles of AZA or either four 4-week or four 6-week cycles of DAC administered or Relapse after initial complete or partial response or HI (according to 2006 IWG criteria)
  • Duration of prior HMA therapy ≤ 9 months and/or total ≤ 9 cycles of prior HMA therapy in ≤ 12 months
  • Last dose of AZA or DAC within 6 months before the planned date of randomization; however, must be off these treatments for ≥ 4 weeks before randomization
  • Has failed to respond to, relapsed following, not eligible for, or opted not to participate in allogeneic stem cell transplantation
  • Off all treatments for MDS (including AZA and DAC) for ≥ 4 weeks before randomization; growth factors (G-CSF, erythropoietin and thrombopoietin) and transfusions are allowed before and during the study as clinically indicated
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0, 1 or 2
  • Willing to adhere to protocol prohibitions and restrictions
  • Patient must sign informed consent form to indicate patient's understanding study's purpose and procedures and willingness to participate. Should patient be incapable of giving consent, the patient's legally authorized representative (as defined by local regulation) must give consent. However, should patient, in any manner, choose not to participate this takes precedence and will be respected.
  • Patients with 5q- syndrome should have failed to respond to or progressed on treatment with lenalidomide, where available and indicated

You may not qualify if:

  • Previous participation in a clinical study of IV or oral rigosertib; patients who failed screening for other rigosertib studies may be screened for participation
  • Eligible to receive induction chemotherapy, such as 7-10 days of cytosine arabinoside plus 2-3 days of an anthracycline, or high-dose cytarabine
  • Suitable candidate to receive allogeneic stem cell transplantation; patient is eligible for study if a suitable candidate refuses to undergo an allogeneic stem cell transplant or a suitable donor cannot be found
  • Any active malignancy within the past year, except basal cell or squamous cell skin cancer or carcinoma in situ that is unlikely to progress in two years
  • Uncontrolled intercurrent illness including, but not limited to, symptomatic congestive heart failure or unstable angina pectoris
  • Active infection not adequately responding to appropriate therapy
  • Total bilirubin ≥1.5 mg/dL not related to hemolysis or Gilbert's disease
  • Alanine transaminase (ALT)/aspartate transaminase (AST) ≥2.5 x upper limit of normal (ULN)
  • Serum creatinine ≥2.0 mg/dL or eGFR (estimated Glomerular Filtration Rate) \< 40 mL/min.
  • Known active HIV, hepatitis B or hepatitis C, where active is defined as follows:
  • HIV or hepatitis C - presence of viral load
  • Hepatitis B - antigen positive
  • Uncorrected hyponatremia (defined as serum sodium value of \<130 mEq/L)
  • Female patients of child-bearing potential and male patients with sexual partners of child-bearing potential who are unwilling to follow strict contraception requirements before entry and throughout the study, up to and including the 30-day non-treatment follow-up period. Examples of acceptable contraception methods include:
  • estrogen-gestagen based contraceptives associated with inhibition of ovulation (oral, intravaginal, transdermal),
  • +15 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (158)

UC San Diego Moores Cancer Center

La Jolla, California, 92093, United States

Location

USC Norris Comprehensive Cancer Center

Los Angeles, California, 90033, United States

Location

UCLA Medical Center

Los Angeles, California, 90095, United States

Location

Cancer Specialists of North Florida

Fleming Island, Florida, 32003, United States

Location

UF Health Shands Cancer Hospital

Gainesville, Florida, 32608, United States

Location

Mid Florida Hematology and Oncology Centers

Orange City, Florida, 32763, United States

Location

Advanced Research Institute, Inc

St. Petersburg, Florida, 33710, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

University of Illinois Cancer Center

Chicago, Illinois, 60612, United States

Location

Loyola University Chicago at Loyola University Medical Center

Maywood, Illinois, 60153, United States

Location

Indiana University Health Hospital

Indianapolis, Indiana, 46202, United States

Location

The University of Kansas Cancer Center

Westwood, Kansas, 66205, United States

Location

Tulane Medical Center

New Orleans, Louisiana, 70112, United States

Location

University of Maryland Greenebaum Cancer Center

Baltimore, Maryland, 21201, United States

Location

Tufts Medical Center

Boston, Massachusetts, 02111, United States

Location

University of Minnesota Physicians Bone Marrow Transplant Clinic

Minneapolis, Minnesota, 55455, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

John Theurer Cancer Center at Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

Rutgers Cancer Institute of New Jersey

New Brunswick, New Jersey, 08903, United States

Location

The Valley Hospital

Ridgewood, New Jersey, 07450, United States

Location

Mount Sinai School of Medicine

New York, New York, 10029, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

New York Medical College

Valhalla, New York, 10595, United States

Location

Hospital of the University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Albert Einstein Medical Center, Cancer Center

Philadelphia, Pennsylvania, 19141, United States

Location

Greenville Health System (GHS) Cancer Institute

Greenville, South Carolina, 29605, United States

Location

UT Southwestern Medical Center

Dallas, Texas, 75390-9015, United States

Location

MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Emily Couric Clinical Cancer Center

Charlottesville, Virginia, 22903, United States

Location

Seattle Cancer Care Alliance (SCCA)

Seattle, Washington, 98109, United States

Location

University of Wisconsin Clinical Science Center

Madison, Wisconsin, 53792, United States

Location

Marshfield Clinic - Marshfield Center

Marshfield, Wisconsin, 54449, United States

Location

Icon Cancer Care Icon South Brisbane

South Brisbane, Queensland, 4101, Australia

Location

Royal Hobart Hospital

Hobart, Tasmania, 7000, Australia

Location

Monash Health, Monash Medical Centre

Melbourne, Victoria, 3168, Australia

Location

Hospital of the Elisabethinen Linz GmbH

Linz, 4020, Austria

Location

Salzburg University Hospital

Salzburg, 5020, Austria

Location

Hanusch Hospital

Vienna, 1140, Austria

Location

Antwerp Hospital Network Stuivenberg

Antwerp, 2060, Belgium

Location

University Hospital Ghent

Ghent, 9000, Belgium

Location

University Hospital Leuven, Campus Gasthuisberg

Leuven, 3000, Belgium

Location

CHU UCL Namur - Site Godinne

Yvoir, B-5530, Belgium

Location

CancerCare Manitoba

Winnipeg, Manitoba, R3E 0V9, Canada

Location

Sunnybrook Research Institute

Toronto, Ontario, M4N 3M5, Canada

Location

Princess Margaret Cancer Centre

Toronto, Ontario, M5G 2M9, Canada

Location

Jewish General Hospital

Montreal, Quebec, H3T 1E2, Canada

Location

Klinički bolnički centar Osijek

Osijek, 31000, Croatia

Location

Clinical Hospital Merkur

Zagreb, 10000, Croatia

Location

Klinički bolnicki centar Sestre milosrdnice

Zagreb, 10000, Croatia

Location

Klinički bolnički centar Zagreb

Zagreb, 10000, Croatia

Location

University Hospital Brno

Brno, 625 00, Czechia

Location

University Hospital Hradec Kralove

Hradec Králové, 500 05, Czechia

Location

University Hospital Ostrava, Department of Hematooncology

Ostrava Poruba, 708 52, Czechia

Location

General University Hospital

Prague, 128 00, Czechia

Location

Institute of Hematology and Blood Transfusion

Prague, 128 20, Czechia

Location

North Estonia Medical Centre

Tallinn, 13419, Estonia

Location

Tartu University Hospital

Tartu, 51014, Estonia

Location

CHD Vendée

La Roche-sur-Yon, 85925, France

Location

Hôpital Claude Huriez, CHRU Lille

Lille, 59037, France

Location

Institut Paoli-Calmettes

Marseille, 13009, France

Location

Hôpital l'Archet 1

Nice, 06202, France

Location

Institut de Cancérologie du Gard

Nîmes, 30029, France

Location

Hôpital Saint Louis

Paris, 75475, France

Location

Centre Hospitalier Lyon-Sud

Pierre-Bénite, 69495, France

Location

Hôpital civil, Strasbourg

Strasbourg, 67091, France

Location

CHRU Tours Hôspital Bretonneau

Tours, 37044, France

Location

Universitätsklinikum Carl Gustav Carus

Dresden, 01307, Germany

Location

Marien Hospital Düsseldorf

Düsseldorf, 40479, Germany

Location

Universitätsklinikum Frankfurt am Main

Frankfurt, 60590, Germany

Location

Semmelweis University Medical School

Budapest, 1083, Hungary

Location

Somogy County Kaposi Mór Teaching Hospital

Kaposvár, 7400, Hungary

Location

Jósa András Teaching Hospital

Nyíregyháza, 4400, Hungary

Location

University of Pécs 1st Department of Internal Medicine

Pécs, 7624, Hungary

Location

Hemato Oncology Clinic Pvt. Ltd

Ahmedabad, Gujarat, 380009, India

Location

St. John's Medical College Hospital

Bangalore, Karnataka, 560034, India

Location

Tata Memorial Hospital

Mumbai, Maharashtra, 400012, India

Location

Jaslok Hospital and Research Center

Mumbai, Maharashtra, 400026, India

Location

Sahyadri Clinical Research and Development Center

Pune, Maharashtra, 411004, India

Location

Christian Medical College

Vellore, Tamil Nadu, 632004, India

Location

Institute Of Hematology And Transfusion Medicine

Kolkata, West Bengal, 700073, India

Location

Cork University Hospital

Cork, Ireland

Location

Adelaide and Meath Hospital, Incorporating the National Children's Hospital

Dublin, Dublin 24, Ireland

Location

University Hospital Waterford

Waterford, Ireland

Location

Ha'Emek Medical Center

Afula, 1834111, Israel

Location

Soroka University Medical Center

Beersheba, 84101, Israel

Location

Rambam Medical Center

Haifa, 31096, Israel

Location

Hadassah Medical Center

Jerusalem, 91120, Israel

Location

Kaplan Medical Center

Rehovot, 76100, Israel

Location

Sourasky Medical Center

Tel Aviv, 64239, Israel

Location

The Chaim Sheba Medical Center

Tel Litwinsky, 52621, Israel

Location

Polyclinic S. Orsola-Malpighi

Bologna, 40138, Italy

Location

Azienda Ospedaliera Spedali Civili

Brescia, 25123, Italy

Location

Azienda Ospedaliero Universitaria Careggi

Florence, 50134, Italy

Location

Azienda Ospedaliero-Universitaria Maggiore della Carità

Novara, 28100, Italy

Location

A.O.U. Pisana, Divisione di Ematologia - University Hospital of Pisa

Pisa, 56126, Italy

Location

Policlinico Universitario Tor Vergata

Roma, 00133, Italy

Location

Ospedale S. Eugenio - S. Eugenio Hospital

Roma, 00144, Italy

Location

Azienda Ospedaliera Santa Maria di Terni

Terni, 05100, Italy

Location

Cittá della Salute e della Scienza di Torino

Torino, 10126, Italy

Location

Kokura Memorial Hospital

Kitakyushu, Fukuoka, 802-8555, Japan

Location

Chugoku Central Hospital of the Mutual Aid Association of Public School Teachers

Fukuyama, Hiroshima, 720-0001, Japan

Location

Sapporo Medical University Hospital

Sapporo, Hokkaido, 060-8556, Japan

Location

Kanazawa University Hospital

Kanazawa, Ishikawa-ken, 920-8641, Japan

Location

Yokohama City University Hospital

Yokohama, Kanagawa, 236-0004, Japan

Location

Shimane University Hospital

Izumo, Shimane, 693-8501, Japan

Location

Japanese Red Cross Medical Center

Shibuya City, Tokyo, 150-8935, Japan

Location

Akita University Hospital

Akita, 010-8543, Japan

Location

Tokyo Metropolitan Cancer and Infectious Diseases Center Komagome Hospital

Bunkyō City, 113-8677, Japan

Location

National Hospital Organization Kyushu Cancer Center

Fukuoka, 811-1395, Japan

Location

Kagoshima University Hospital

Kagoshima, 890-8544, Japan

Location

Tokai Central Hospital of the Mutual Aid Association of Public School Teachers

Kakamigahara, 504-8601, Japan

Location

Saitama Medical Center

Kawagoe, 350-8550, Japan

Location

Kobe City Hospital Organization Kobe City Medical Center General Hospital

Kobe, 650-0047, Japan

Location

National Hospital Organization Kumamoto Medical Center

Kumamoto, 860-008,, Japan

Location

Japanese Red Cross Kyoto Daini Hospital

Kyoto, 602-8026, Japan

Location

Nagasaki University Hospital

Nagasaki, 852-8102, Japan

Location

Japanese Red Cross Nagoya Daini Hospital

Nagoya, 466-8650, Japan

Location

Niigata University Medical and Dental Hospital

Niigata, 951-8510,, Japan

Location

National Hospital Organization Okayama Medical Center

Okayama, 701-1192, Japan

Location

Kindai University Hospital

Osakasayama-shi, 589-8511, Japan

Location

Oita Prefectural Hospital

Ōita, 870-8511, Japan

Location

Hokkaido University Hospital

Sapporo, 060-8648, Japan

Location

Tohoku University Hospital

Sendai, 980-8574, Japan

Location

NTT Medical Center Tokyo

Shinagawa-ku, 141-8625, Japan

Location

Tokyo Medical University Hospital

Shinjuku-ku, 160-0023, Japan

Location

Dokkyo Medical University Hospital

Tochigi, 321-0293, Japan

Location

Tokushima University Hospital

Tokushima, 770-8503, Japan

Location

Yamagata University Hospital

Yamagata, 990-9585, Japan

Location

Saiseikai Yokohamashi Nanbu Hospital

Yokohama, 234-8503, Japan

Location

University of Fukui Hospital

Yoshida, 910-1193, Japan

Location

Independent Public Healthcare Facility University Hospital in Cracow, Clinical Department of Hematology

Krakow, 31-501, Poland

Location

Independent Public Health Care Facility of the Ministry of Internal Affairs with Warmia and Mazury Oncology Centre in Olsztyn

Olsztyn, 10-228, Poland

Location

Ludwik Rydygier Provinicial Hospital in Suwalki, Department of Clinical Oncology and Hematology

Suwałki, 16-400, Poland

Location

MTZ Clinical Research Sp. z o.o.

Warsaw, 02-106, Poland

Location

Independent Public University Hospital No. 1 in Wroclaw, Department of Hematology, Blood Cancers and Bone Marrow

Wroclaw, 50-367, Poland

Location

State Autonomous Healthcare Institution of Kemerovo region "Kemerovo Regional Clinical Hospital n.a. S.V. Belyaev",

Kemerovo, 650066, Russia

Location

State Budgetary Healthcare Institution of Moscow City

Moscow, 129301, Russia

Location

FSBI "Russian Scientific Research Hematology and Tranfusiology Institute of the Federal Biomedical Agency"

Saint Petersburg, 191024, Russia

Location

Hospital Son Llàtzer

Palma de Mallorca, Balearic Islands, 07198, Spain

Location

Hospital Duran i Reynals - Instituto Catalán de Oncología

L'Hospitalet de Llobregat, Barcelona, 08908, Spain

Location

Hospital Universitario Vall d'Hebron

Barcelona, 08035, Spain

Location

Hospital Universitari Germans Trias i Pujol

Barcelona, 08916, Spain

Location

Hospital Universitario Gregorio Marañón

Madrid, 28007, Spain

Location

Fundación Jiménez Díaz

Madrid, 28040, Spain

Location

Hospital Universitario Virgen de la Victoria

Málaga, 29010, Spain

Location

Hospital Universitario Salamanca

Salamanca, 37007, Spain

Location

Hospital Universitari i Politècnic La Fe

Valencia, 46026, Spain

Location

Karolinska University Hospital

Stockholm, Huddinge, 141 57, Sweden

Location

Skåne University Hospital, Department of Hematology

Lund, 222 82, Sweden

Location

Uppsala University Hospital

Uppsala, 751 81, Sweden

Location

Linköping University Hospital

Linköping, Östergötland County, 581 85, Sweden

Location

University Hospital and University of Bern; Inselspital Bern

Bern, 3010, Switzerland

Location

University Hospital Zurich

Zurich, 8091, Switzerland

Location

Royal Bournemouth Hospital

Bournemouth, Dorset, BH7 7DW, United Kingdom

Location

Aberdeen Royal Infirmary

Aberdeen, Scotland, AB25 2ZN, United Kingdom

Location

The Royal Liverpool University Hospital

Liverpool, L7 8XP, United Kingdom

Location

St Bartholomew's Hospital, Barts Health NHS Trust

London, EC1A 7BE, United Kingdom

Location

King's College Hospital NHS Foundation Trust

London, SE5 9RS, United Kingdom

Location

Related Publications (4)

  • Garcia-Manero G, Fenaux P, Al-Kali A, Baer MR, Sekeres MA, Roboz GJ, Gaidano G, Scott BL, Greenberg P, Platzbecker U, Steensma DP, Kambhampati S, Kreuzer KA, Godley LA, Atallah E, Collins R Jr, Kantarjian H, Jabbour E, Wilhelm FE, Azarnia N, Silverman LR; ONTIME study investigators. Rigosertib versus best supportive care for patients with high-risk myelodysplastic syndromes after failure of hypomethylating drugs (ONTIME): a randomised, controlled, phase 3 trial. Lancet Oncol. 2016 Apr;17(4):496-508. doi: 10.1016/S1470-2045(16)00009-7. Epub 2016 Mar 9.

    PMID: 26968357BACKGROUND
  • Athuluri-Divakar SK, Vasquez-Del Carpio R, Dutta K, Baker SJ, Cosenza SC, Basu I, Gupta YK, Reddy MV, Ueno L, Hart JR, Vogt PK, Mulholland D, Guha C, Aggarwal AK, Reddy EP. A Small Molecule RAS-Mimetic Disrupts RAS Association with Effector Proteins to Block Signaling. Cell. 2016 Apr 21;165(3):643-55. doi: 10.1016/j.cell.2016.03.045.

    PMID: 27104980BACKGROUND
  • Navada SC, Silverman LR. The safety and efficacy of rigosertib in the treatment of myelodysplastic syndromes. Expert Rev Anticancer Ther. 2016 Aug;16(8):805-10. doi: 10.1080/14737140.2016.1209413. Epub 2016 Jul 15.

    PMID: 27400247BACKGROUND
  • Garcia-Manero G, Fenaux P. Comprehensive Analysis of Safety: Rigosertib in 557 Patients with Myelodysplastic Syndromes (MDS) and Acute Myeloid Leukemia (AML). Blood Dec 2016, 128 (22) 2011; ASH 2016.

    RESULT

MeSH Terms

Conditions

Myelodysplastic SyndromesAnemia, Refractory, with Excess of Blasts

Interventions

ON 01910

Condition Hierarchy (Ancestors)

Bone Marrow DiseasesHematologic DiseasesHemic and Lymphatic DiseasesAnemia, RefractoryAnemia

Study Officials

  • Steven M. Fruchtman, MD

    Traws Pharma, Inc.

    STUDY CHAIR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 25, 2015

First Posted

September 29, 2015

Study Start

December 2, 2015

Primary Completion

July 26, 2020

Study Completion

July 26, 2021

Last Updated

September 26, 2022

Record last verified: 2022-09

Locations