NCT02551991

Brief Summary

This is an open-label, phase 2 non-comparative study to assess the safety, tolerability, and preliminary efficacy of nal-IRI in combination with other anticancer therapies in patients not previously treated for metastatic pancreatic adenocarcinoma. This study will assess the following regimen: • nal-IRI + 5-fluorouracil (5-FU)/leucovorin (LV) + oxaliplatin The study will be conducted in two parts: Part 1, consisting of an initial dose exploration (Part 1A) followed by dose expansion (Part 1B) of the irinotecan liposome injection +5-FU/LV + oxaliplatin regimen and Part 2, consisting of a comparison of irinotecan liposome injection-containing regimen versus nab-paclitaxel plus gemcitabine. The comparative Part 2 was removed in a protocol amendment, dated 11 April 2018 (Version 6.0), before it was initiated, as this comparative part of the study is being undertaken as a stand-alone phase III study D-US-60010-001. This CSR only pertains to the single-arm dose exploration and dose expansion Part 1 results and no further reference is made to the comparative Part 2.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
56

participants targeted

Target at P50-P75 for phase_2 pancreatic-cancer

Timeline
Completed

Started Oct 2015

Typical duration for phase_2 pancreatic-cancer

Geographic Reach
3 countries

36 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 10, 2015

Completed
6 days until next milestone

First Posted

Study publicly available on registry

September 16, 2015

Completed
1 month until next milestone

Study Start

First participant enrolled

October 19, 2015

Completed
5.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 15, 2021

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 15, 2021

Completed
1.6 years until next milestone

Results Posted

Study results publicly available

October 10, 2022

Completed
Last Updated

October 10, 2022

Status Verified

October 1, 2022

Enrollment Period

5.3 years

First QC Date

September 10, 2015

Results QC Date

May 20, 2022

Last Update Submit

October 7, 2022

Conditions

Keywords

Pancreatic cancerMM-398Metastatic pancreatic cancerFirst line pancreatic cancer treatment

Outcome Measures

Primary Outcomes (1)

  • Part 1A: Number of Participants With Dose-Limiting Toxicities (DLT)

    Adverse events (AEs) were considered to be DLTs if they occurred during the safety evaluation period (i.e, 28 days of Cycle 1; or 14 days after the second dose of study treatment if there was a treatment delay) and were deemed related to the study treatment regimen. Any AE that was related to disease progression was not considered a DLT.

    From the start of the first study treatment (Cycle 1 Day 1) up to 14 days after the second dose of study treatment, maximum of 42 days

Secondary Outcomes (6)

  • Median Progression Free Survival (PFS)

    RECIST assessments performed at baseline (within 28 days before start of study treatment), every 8 weeks after first dose, end of treatment (EoT) visit, then every 2 months thereafter (maximum of 278 weeks).

  • Best Overall Response (BOR)

    RECIST assessments performed at baseline (within 28 days before start of study treatment), every 8 weeks after first dose, EoT visit, then every 2 months thereafter (maximum of 278 weeks).

  • Overall Response Rate (ORR)

    RECIST assessments performed at baseline (within 28 days before start of study treatment), every 8 weeks after first dose, EoT visit, then every 2 months thereafter (maximum of 278 weeks).

  • Disease Control Rate (DCR)

    At Week 16

  • Median Overall Survival (OS)

    RECIST assessments performed at baseline (within 28 days before start of study treatment), every 8 weeks after first dose, EoT visit, then every 2 months thereafter (maximum of 278 weeks).

  • +1 more secondary outcomes

Study Arms (1)

nal-IRI + 5-FU/LV + oxaliplatin

EXPERIMENTAL
Drug: nal-IRIDrug: 5 fluorouracilDrug: LeucovorinDrug: Oxaliplatin

Interventions

Also known as: MM-398
nal-IRI + 5-FU/LV + oxaliplatin
Also known as: 5-FU
nal-IRI + 5-FU/LV + oxaliplatin
Also known as: LV
nal-IRI + 5-FU/LV + oxaliplatin
nal-IRI + 5-FU/LV + oxaliplatin

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically or cytologically confirmed adenocarcinoma of the pancreas that has not been previously treated in the metastatic setting
  • Unresectable, locally advanced or metastatic disease; diagnosed within 6 weeks prior to screening
  • At least one tumor lesion measurable by CT or MRI scan (according to RECIST v1.1)
  • ECOG performance status of 0 or 1 at screening and within 72 hours prior to first dose if first dose occurs more than 72 hours post-screening
  • Adequate hematological, hepatic, renal and cardiac function
  • Recovered from the effects of any prior surgery or radiotherapy
  • Patient has a Karnofsky performance status (KPS) ≥ 70 at Screening, and within 72 hours prior to date of first dose if first dose occurs more than 72 hours after screening (Part 1B only)

You may not qualify if:

  • Prior treatment of pancreatic cancer in the metastatic setting (or locally advanced setting) with surgery (placement of stent is allowed), radiotherapy, chemotherapy or investigational therapy
  • Prior treatment of pancreatic cancer with chemotherapy in adjuvant setting, except those where at least 12 months have elapsed since completion of the last dose and no persistent treatment-related toxicities present
  • Uncontrolled Central Nervous System (CNS) metastases
  • Clinically significant gastrointestinal disorder
  • History of any second malignancy in the last 3 years. Patients with prior history of in-situ cancer or basal or squamous cell skin cancer are eligible
  • Presence of any contraindications for nal-IRI, irinotecan, 5-FU, leucovorin, oxaliplatin
  • Use of strong CYP3A4 or inducers or presence of any other contra indications for irinotecan
  • Pregnant or breast feeding
  • Neuroendocrine or acinar pancreatic carcinoma
  • Serum albumin \< 3 g/dL at screening visit and within 72 hours prior to first dose if first dose occurs more than 72 hours post screening
  • Patients with symptoms and signs of clinically unacceptable deterioration of primary disease at time of screening
  • Previous treatment with irinotecan-based, nab-paclitaxel-based or gemcitabine-based resulting in disease progression

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (36)

University of South Alabama

Mobile, Alabama, 36604, United States

Location

University of South Alabama - Mobile

Mobile, Alabama, 36688, United States

Location

Arizona Center for Cancer Care

Avondale, Arizona, 85392, United States

Location

Mayo Clinic Hospital

Phoenix, Arizona, 85054, United States

Location

UCLA Hematology Oncology - Ventura

Los Angeles, California, 90095, United States

Location

University of California Irvine Medical Center (UCIMC) - Chao Family Comprehensive Cancer Center

Orange, California, 92868, United States

Location

University of Colorado (CU) Cancer Center - Anschutz Cancer Pavilion

Aurora, Colorado, 80045, United States

Location

Mayo Clinic Cancer Center

Jacksonville, Florida, 32224, United States

Location

University of Miami

Miami, Florida, 33136, United States

Location

Eastern Maine Medical Cancer Care

Brewer, Maine, 04412, United States

Location

Maryland Oncology Hematology

Silver Spring, Maryland, 20904, United States

Location

Lahey Hospital & Medical Center

Burlington, Massachusetts, 01805, United States

Location

Mayo Clinic Cancer Center - Rochester

Rochester, Minnesota, 55905, United States

Location

Oncology Hematology West PC dba Nebraska

Omaha, Nebraska, 68130, United States

Location

US Oncology - Comprehensive Cancer Centers of Nevada (CCCN)

Las Vegas, Nevada, 89169, United States

Location

Holy Name Medical Center

Teaneck, New Jersey, 07666, United States

Location

Roswell Park Cancer Institute

Buffalo, New York, 14263, United States

Location

Oncology/Hematology Care Clinical Trials, LLC

Cincinnati, Ohio, 45230, United States

Location

University of Oklahoma Health Sciences Center (OUHSC) Stephenson Cancer Center

Oklahoma City, Oklahoma, 73104, United States

Location

Willamette Valley Cancer Institute & Research Center

Eugene, Oregon, 97401, United States

Location

Gettysburg Cancer Center

Gettysburg, Pennsylvania, 17325, United States

Location

Greenville Health System

Greenville, South Carolina, 29605, United States

Location

Medical Group of the Carolinas - Spartanburg Regional Health Services

Spartanburg, South Carolina, 29303, United States

Location

Texas Oncology Methodist Dallas Cancer Center

Dallas, Texas, 75203, United States

Location

Texas Oncology-Fort Worth 12 Ave

Fort Worth, Texas, 76104, United States

Location

Houston Methodist Cancer Center and Institute of Academic Medicine

Houston, Texas, 77030, United States

Location

Oncology Consultants - Houston

Houston, Texas, 77030, United States

Location

Joe Arrington Cancer Research and Treatment Center - Lubbock

Lubbock, Texas, 79410, United States

Location

Texas Oncology, P.A.

San Antonio, Texas, 78217, United States

Location

St. John of God Health Care - Subiaco

Subiaco, Western Australia, 6008, Australia

Location

Flinders Medical Centre

Bedford Park, 5042, Australia

Location

Box Hill Hospital

Lilydale, 3140, Australia

Location

Hospital General Universitario de Elche

Elche, Alicante, 03203, Spain

Location

Hospital Universitario de Fuenlabrada

Fuenlabrada, Madrid, 28942, Spain

Location

Hospital Universitario Vall d'Hebron

Barcelona, 08035, Spain

Location

Hospital Universitario Madrid Sanchinarro Centro Integral Oncologico Clara Campal (CIOCC)

Madrid, 28050, Spain

Location

Related Publications (3)

  • Brendel K, Bekaii-Saab T, Boland PM, Dayyani F, Dean A, Macarulla T, Maxwell F, Mody K, Pedret-Dunn A, Wainberg ZA, Zhang B. Population pharmacokinetics of liposomal irinotecan in patients with cancer and exposure-safety analyses in patients with metastatic pancreatic cancer. CPT Pharmacometrics Syst Pharmacol. 2021 Dec;10(12):1550-1563. doi: 10.1002/psp4.12725. Epub 2021 Nov 20.

  • Wainberg ZA, Bekaii-Saab T, Boland PM, Dayyani F, Macarulla T, Mody K, Belanger B, Maxwell F, Moore Y, Thiagalingam A, Wang T, Zhang B, Dean A. First-line liposomal irinotecan with oxaliplatin, 5-fluorouracil and leucovorin (NALIRIFOX) in pancreatic ductal adenocarcinoma: A phase I/II study. Eur J Cancer. 2021 Jul;151:14-24. doi: 10.1016/j.ejca.2021.03.028. Epub 2021 May 4.

  • Liu X, Jiang J, Chan R, Ji Y, Lu J, Liao YP, Okene M, Lin J, Lin P, Chang CH, Wang X, Tang I, Zheng E, Qiu W, Wainberg ZA, Nel AE, Meng H. Improved Efficacy and Reduced Toxicity Using a Custom-Designed Irinotecan-Delivering Silicasome for Orthotopic Colon Cancer. ACS Nano. 2019 Jan 22;13(1):38-53. doi: 10.1021/acsnano.8b06164. Epub 2018 Dec 11.

MeSH Terms

Conditions

Pancreatic Neoplasms

Interventions

irinotecan sucrosofateFluorouracilLeucovorinOxaliplatin

Condition Hierarchy (Ancestors)

Digestive System NeoplasmsNeoplasms by SiteNeoplasmsEndocrine Gland NeoplasmsDigestive System DiseasesPancreatic DiseasesEndocrine System Diseases

Intervention Hierarchy (Ancestors)

UracilPyrimidinonesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsFormyltetrahydrofolatesTetrahydrofolatesFolic AcidPterinsPteridinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingCoenzymesEnzymes and CoenzymesCoordination ComplexesOrganic Chemicals

Limitations and Caveats

The comparative Part 2 was removed in a protocol amendment, dated 11 April 2018, before it was initiated, as this comparative part of the study is being undertaken as a stand-alone Phase 3 study D-US-60010-001.

Results Point of Contact

Title
Medical Director
Organization
Ipsen Bioscience, Inc.

Study Officials

  • Ipsen Medical Director

    Ipsen

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 10, 2015

First Posted

September 16, 2015

Study Start

October 19, 2015

Primary Completion

February 15, 2021

Study Completion

February 15, 2021

Last Updated

October 10, 2022

Results First Posted

October 10, 2022

Record last verified: 2022-10

Locations