NCT02289898

Brief Summary

This is a randomized, double blind, 3 arm (1:1:1) study in subjects with 1st-line metastatic pancreatic ductal adenocarcinoma. The purpose is to test the efficacy and safety of demcizumab, when given in combination with gemcitabine and Abraxane® compared to placebo. The administration of gemcitabine and Abraxane® is a standard treatment for patients with metastatic pancreatic ductal adenocarcinoma.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
207

participants targeted

Target at P75+ for phase_2 pancreatic-cancer

Timeline
Completed

Started Apr 2015

Shorter than P25 for phase_2 pancreatic-cancer

Geographic Reach
6 countries

42 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 10, 2014

Completed
3 days until next milestone

First Posted

Study publicly available on registry

November 13, 2014

Completed
5 months until next milestone

Study Start

First participant enrolled

April 20, 2015

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2017

Completed
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2017

Completed
11 months until next milestone

Results Posted

Study results publicly available

August 8, 2018

Completed
Last Updated

September 28, 2020

Status Verified

September 1, 2020

Enrollment Period

2 years

First QC Date

November 10, 2014

Results QC Date

May 21, 2018

Last Update Submit

September 7, 2020

Conditions

Keywords

1st-line metastatic pancreatic ductal adenocarcinoma

Outcome Measures

Primary Outcomes (1)

  • Hazard of Progression in the Placebo/Placebo Arm and the Pooled Demcizumab Arms

    Investigator assessed Kaplan-Meier estimates of progression-free survival for placebo/placebo arm and pooled demcizumab arm.

    Investigator-assessed progression-free survival time through duration of the study (2 years, 23 days).

Study Arms (3)

Abraxane® and gemcitabine plus placebo

EXPERIMENTAL

Abraxane® and gemcitabine plus placebo (3 cycles), Abraxane® and gemcitabine (3 cycles), Abraxane® and gemcitabine plus placebo (3 cycles) and then Abraxane® and gemcitabine until disease progression

Drug: DemcizumabDrug: Abraxane®Drug: gemcitabineDrug: Placebo

Abraxane® and gemcitabine plus demcizumab plus placebo

EXPERIMENTAL

Abraxane® and gemcitabine plus demcizumab (3 cycles), Abraxane® and gemcitabine (3 cycles), Abraxane® and gemcitabine plus placebo (3 cycles) and then Abraxane® and gemcitabine until disease progression

Drug: DemcizumabDrug: Abraxane®Drug: gemcitabine

Abraxane® and gemcitabine plus demcizumab

EXPERIMENTAL

Abraxane® and gemcitabine plus demcizumab (3 cycles), Abraxane® and gemcitabine (3 cycles), Abraxane® and gemcitabine plus demcizumab (3 cycles) and then Abraxane® and gemcitabine until disease progression

Drug: DemcizumabDrug: Abraxane®Drug: gemcitabine

Interventions

administered intravenously

Abraxane® and gemcitabine plus demcizumabAbraxane® and gemcitabine plus demcizumab plus placeboAbraxane® and gemcitabine plus placebo

administered intravenously

Abraxane® and gemcitabine plus demcizumabAbraxane® and gemcitabine plus demcizumab plus placeboAbraxane® and gemcitabine plus placebo

administered intravenously

Abraxane® and gemcitabine plus demcizumabAbraxane® and gemcitabine plus demcizumab plus placeboAbraxane® and gemcitabine plus placebo
Abraxane® and gemcitabine plus placebo

Eligibility Criteria

Age21 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Subjects must have histologically confirmed metastatic pancreatic ductal adenocarcinoma.. Prior chemotherapy and/or radiotherapy either in the adjuvant or neoadjuvant setting or for metastatic disease is not allowed.
  • Availability of formalin-fixed paraffin-embedded (FFPE) tumor tissue (from either the primary tumor, locoregional disease or a metastatic site), either fresh core-needle-biopsied or archived (two FFPE cores preferred whenever possible). If fresh tissue is obtained, the core biopsy must be done at least 7 days prior to randomization.
  • Age ≥21 years
  • Eastern Cooperative Oncology Group (ECOG) performance status 0 or 1 5. Measurable disease per RECIST v1.1
  • Adequate organ and marrow function
  • Signed Informed Consent Form
  • For women of childbearing potential, agreement to use two effective forms of contraception

You may not qualify if:

  • Subjects with a neuroendocrine tumor of the pancreas, an acinar tumor of the pancreas or a pancreatic tumor with mixed histologies.
  • Subjects receiving heparin, warfarin, factor Xa inhibitors or other similar anticoagulants. Note: Subjects may be receiving low-dose aspirin and/or non-steroidal anti-inflammatory agents.
  • Subjects with brain metastases, leptomeningeal disease, uncontrolled seizure disorder, or active neurologic disease
  • Subjects with Grade \>2 peripheral neuropathy
  • Subjects with clinically significant ascites
  • Malignancies other than pancreatic cancer successfully treated within 3 years prior to randomization, except for adequately treated carcinoma in situ of the cervix, basal or squamous cell skin cancer, treated superficial bladder cancer, localized prostate cancer treated surgically with curative intent, ductal carcinoma in situ treated surgically with curative intent
  • Significant intercurrent illness that will limit the patient's ability to participate in the study or may result in their death over the next 18 months
  • History of a significant allergic reaction attributed to humanized or human monoclonal antibody therapy
  • Subjects with known clinically significant gastrointestinal disease including, but not limited to, inflammatory bowel disease
  • Pregnant women or nursing women
  • Subjects with known HIV infection
  • Known bleeding disorder or coagulopathy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (42)

Banner MD Anderson Cancer Center

Gilbert, Arizona, 85234, United States

Location

Providence Saint Joseph Medical Center

Burbank, California, 91505, United States

Location

City of Hope

Duarte, California, 91010, United States

Location

Scripps Cancer Center

La Jolla, California, 92037, United States

Location

University of California, Davis Comprehensive Cancer Center

Sacramento, California, 95817, United States

Location

Soulhern California Permanente Medical Group

San Marcos, California, 92078, United States

Location

Kaiser Permanente Medical Center

Vallejo, California, 94589, United States

Location

Rocky Mountain Cancer Centers

Denver, Colorado, 80218, United States

Location

Lynn Cancer Institute

Boca Raton, Florida, 33486, United States

Location

University of Iowa Hospitals and Clinics

Iowa City, Iowa, 52242, United States

Location

University of Kansas Cancer Center

Westwood, Kansas, 66205, United States

Location

Ochsner Clinic Foundation

New Orleans, Louisiana, 70121, United States

Location

University of Michigan

Ann Arbor, Michigan, 48109, United States

Location

Dartmouth Hitchcock Medical Center, Norris Cotton Cancer Center

Lebanon, New Hampshire, 03756, United States

Location

University of Rochester

Rochester, New York, 14642, United States

Location

SUNY Upstate Medical University

Syracuse, New York, 13210, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

Kaiser Permanente NW Oncology Research

Portland, Oregon, 97227, United States

Location

Thomas Jefferson University, Sydney Kimmel Cancer Center

Philadelphia, Pennsylvania, 19107, United States

Location

Baylor College of Medicine

Houston, Texas, 77030, United States

Location

Joe Arrington Cancer Research Treatment Center

Lubbock, Texas, 79410, United States

Location

Huntsman Cancer Institute at The University of Utah

Salt Lake City, Utah, 84112, United States

Location

Prince of Wales Hospital

Randwick, New South Wales, 2031, Australia

Location

Monash Medical Centre, Moorabbin

Bentleigh East, Victoria, 3165, Australia

Location

Western Health (Sunshine Hospitals)

St Albans, Victoria, 3021, Australia

Location

St John of God Murdoch Hospital

Murdoch, Western Australia, 6150, Australia

Location

St. John of God Subiaco Hospital

Subiaco, Western Australia, 6008, Australia

Location

Hopital Erasme

Brussels, Brussels Capital, 1070, Belgium

Location

Tom Baker Cancer Centre

Calgary, Alberta, T2N 4N2, Canada

Location

British Columbia Cancer Agency

Vancouver, British Columbia, V5Z 4E6, Canada

Location

QEII Health Sciences Centre

Halifax, Nova Scotia, B3H 2Y9, Canada

Location

London Regional Cancer Program

London, Ontario, N6A 4L6, Canada

Location

Sunnybrook Health Sciences Centre, Odette Cancer Centre

Toronto, Ontario, M4N 3M5, Canada

Location

Princess Margaret Hospital

Toronto, Ontario, M5G 2M9, Canada

Location

St Josephs Health Centre

Toronto, Ontario, M6R 1B5, Canada

Location

Hospital Universitario de Fuenlabrada

Fuenlabrada, Madrid, 28492, Spain

Location

Hospital Universitari Germans Trias i Pujol - lnstituto Catalan d'Oncologia (!CO)

Barcelona, 08916, Spain

Location

Hospital General Universitario Gregorio Marafi6n

Madrid, 28007, Spain

Location

Hospital Universitario de Fuenlabrada

Madrid, 28942, Spain

Location

Hospital Universitario Miguel Servet

Zaragoza, 50009, Spain

Location

Bristol Haematology & Oncology Centre

Bristol, BS2 8ED, United Kingdom

Location

Sarah Cannon Research Institute UK

London, W1G 6AD, United Kingdom

Location

MeSH Terms

Conditions

Pancreatic Neoplasms

Interventions

demcizumabAlbumin-Bound PaclitaxelGemcitabine

Condition Hierarchy (Ancestors)

Digestive System NeoplasmsNeoplasms by SiteNeoplasmsEndocrine Gland NeoplasmsDigestive System DiseasesPancreatic DiseasesEndocrine System Diseases

Intervention Hierarchy (Ancestors)

PaclitaxelTaxoidsCyclodecanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsDiterpenesTerpenesAlbuminsProteinsAmino Acids, Peptides, and ProteinsHeterocyclic CompoundsDeoxycytidineCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-Ring

Results Point of Contact

Title
John, Lewicki, Chief Scientific Officer
Organization
Mereo BioPharma Group Plc.

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 10, 2014

First Posted

November 13, 2014

Study Start

April 20, 2015

Primary Completion

May 1, 2017

Study Completion

September 1, 2017

Last Updated

September 28, 2020

Results First Posted

August 8, 2018

Record last verified: 2020-09

Locations