NCT02159573

Brief Summary

The primary objective of the study is to evaluate relapse activity, as measured by the proportion of participants relapsed at 12 months, in participants with relapsing-remitting multiple sclerosis (RRMS) who transition from Tysabri (BG00002) to Tecfidera (BG00012) in the real-world setting. The secondary objective is to further evaluate relapse activity, defined as annualized relapse rate (ARR), hospitalization and intravenous corticosteroid use, during the first year of Tecfidera treatment following transition from Tysabri treatment.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
530

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Jul 2014

Shorter than P25 for all trials

Geographic Reach
1 country

43 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 19, 2014

Completed
22 days until next milestone

First Posted

Study publicly available on registry

June 10, 2014

Completed
21 days until next milestone

Study Start

First participant enrolled

July 1, 2014

Completed
6 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2015

Completed
Last Updated

June 7, 2016

Status Verified

June 1, 2016

Enrollment Period

6 months

First QC Date

May 19, 2014

Last Update Submit

June 4, 2016

Conditions

Outcome Measures

Primary Outcomes (1)

  • Kaplan-Meier Estimates for the Proportion of Participants relapsed at 12 months after initiation of treatment with Tecfidera

    12 months post initiation of treatment with Tecfidera

Secondary Outcomes (3)

  • ARR at 12 months post-initiation of treatment with Tecfidera

    12 months post initiation of treatment with Tecfidera

  • The percent of participants with MS-related hospitalization at 12 months post-initiation of treatment with Tecfidera

    12 months post initiation of treatment with Tecfidera

  • The percent of participants with relapses requiring treatment with intravenous steroids

    12 months post initiation of treatment with Tecfidera

Interventions

natalizumabBIOLOGICAL

Administered as per routine clinical practice

Also known as: BG00002, Tysabri

Administered as per routine clinical practice

Also known as: BG00012, Tecfidera, DMF

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Participants with a diagnosis of RRMS receiving at least 12 months of continuous treatment with Tysabri monotherapy prior to initiation of Tecfidera. Additionally, participants must have initiated treatment with Tecfidera at least 12 months prior to enrollment into the study.

You may qualify if:

  • Diagnosis of RRMS per McDonald criteria
  • Received at least 12 months of continuous treatment with Tysabri monotherapy prior to initiation of Tecfidera. Note: continuous treatment with Tysabri is defined as treatment uninterrupted by other disease-modifying treatment.
  • Initiated treatment with Tecfidera at least 12 months prior to enrollment into the study
  • Patient has sufficient available medical records for data abstraction to meet the objectives of the study

You may not qualify if:

  • Diagnosed with a progressive form of multiple sclerosis (MS) (progressive-relapsing, primary progressive, secondary progressive)
  • Received treatment with any of the following after discontinuation of Tysabri and before initiation of treatment with Tecfidera (i.e., during washout period): interferon-beta, glatiramer acetate, fingolimod, teriflunomide, rituximab, alemtuzumab, ocrelizumab or any investigational compound for the treatment of RRMS
  • Received BG00012, or other formulations of dimethyl fumarate, or Fumaderm® or compounded fumarates at any time prior to initiation of treatment with Tecfidera
  • History of progressive multifocal leukoencephalopathy (PML) while on Tysabri or within 6 months of discontinuing treatment with Tysabri

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (43)

Research Site

Birmingham, Alabama, United States

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Research Site

Cullman, Alabama, United States

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Gilbert, Arizona, United States

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Phoenix, Arizona, United States

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Aurora, Colorado, United States

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Centennial, Colorado, United States

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Washington D.C., District of Columbia, United States

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Jacksonville Beach, Florida, United States

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Palm Bay, Florida, United States

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Tampa, Florida, United States

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Athens, Georgia, United States

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Atlanta, Georgia, United States

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Idaho Falls, Idaho, United States

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Chicago, Illinois, United States

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Peoria, Illinois, United States

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Baton Rouge, Louisiana, United States

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Glen Burnie, Maryland, United States

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Boston, Massachusetts, United States

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Farmington Hills, Michigan, United States

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Golden Valley, Minnesota, United States

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Lincoln, Nebraska, United States

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Teaneck, New Jersey, United States

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Amherst, New York, United States

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East Meadow, New York, United States

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New York, New York, United States

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Charlotte, North Carolina, United States

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Raleigh, North Carolina, United States

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Columbus, Ohio, United States

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Gahanna, Ohio, United States

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Uniontown, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Portland, Oregon, United States

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Altoona, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Nashville, Tennessee, United States

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Dallas, Texas, United States

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Salt Lake City, Utah, United States

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Newport News, Virginia, United States

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Norfolk, Virginia, United States

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Seattle, Washington, United States

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Spokane, Washington, United States

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Madison, Wisconsin, United States

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Milwaukee, Wisconsin, United States

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Related Publications (1)

  • Cohan SL, Moses H, Calkwood J, Tornatore C, LaGanke C, Smoot KE, Meka V, Okwuokenye M, Hotermans C, Mendoza JP, Mann MK, Meltzer LA. Clinical outcomes in patients with relapsing-remitting multiple sclerosis who switch from natalizumab to delayed-release dimethyl fumarate: A multicenter retrospective observational study (STRATEGY). Mult Scler Relat Disord. 2018 May;22:27-34. doi: 10.1016/j.msard.2018.02.028. Epub 2018 Feb 26.

MeSH Terms

Conditions

Multiple Sclerosis, Relapsing-Remitting

Interventions

NatalizumabDimethyl Fumarate

Condition Hierarchy (Ancestors)

Multiple SclerosisDemyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesDemyelinating DiseasesAutoimmune DiseasesImmune System Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsFumaratesDicarboxylic AcidsAcids, AcyclicCarboxylic AcidsOrganic Chemicals

Study Officials

  • Medical Director

    Biogen

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
RETROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 19, 2014

First Posted

June 10, 2014

Study Start

July 1, 2014

Primary Completion

January 1, 2015

Study Completion

January 1, 2015

Last Updated

June 7, 2016

Record last verified: 2016-06

Locations