NCT02077374

Brief Summary

The purpose of this study is to determine the safety and efficacy of IDN-6556 compared to placebo in patients with diagnosed fat deposits in their liver (not caused by alcohol) and with abnormal liver tests

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
38

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Mar 2014

Shorter than P25 for phase_2

Geographic Reach
1 country

7 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 28, 2014

Completed
1 day until next milestone

Study Start

First participant enrolled

March 1, 2014

Completed
3 days until next milestone

First Posted

Study publicly available on registry

March 4, 2014

Completed
12 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2015

Completed
1.4 years until next milestone

Results Posted

Study results publicly available

July 21, 2016

Completed
Last Updated

August 30, 2016

Status Verified

July 1, 2016

Enrollment Period

1 year

First QC Date

February 28, 2014

Results QC Date

March 30, 2016

Last Update Submit

July 25, 2016

Conditions

Keywords

NAFLDNASH

Outcome Measures

Primary Outcomes (2)

  • Change in Alanine Aminotransferase (ALT)

    Mean change in alanine aminotransferase (ALT) from Baseline to Day 28/ET between IDN-6556 vs Placebo

    Day 28/ET

  • Relative Percent Change in Alanine Aminotransferase (ALT)

    Back transformation from log-transformed analysis results to original scale in alanine aminotransferase (ALT) from Baseline to Day 28/ET between IDN-6556 vs Placebo

    Baseline to Day 28/ET

Secondary Outcomes (4)

  • Change in Aspartate Aminotransferase (AST)

    Day 28/ET

  • Levels of cCK18/M30

    Day 28/ET

  • Levels of Caspase 3/7 RLU

    Day 28/ET

  • Levels of flCK18/M65

    Day 28/ET

Study Arms (2)

IDN-6556

EXPERIMENTAL

IDN-6556 capsules, 25 mg BID

Drug: IDN-6556

Placebo

PLACEBO COMPARATOR

Placebo BID

Other: Placebo

Interventions

25 mg BID for 28 days

Also known as: emricasan, PF-03491390
IDN-6556
PlaceboOTHER

Placebo BID for 28 Days

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female subjects of minimum adult legal age (according to local laws for signing the informed consent document), able to provide written informed consent, and understand and comply with the requirements of the study
  • Diagnosis of non-alcoholic fatty liver disease (NAFLD) as evidenced by imaging or other diagnostic assessments
  • Alanine aminotransferase (ALT) levels ≥1.5 x ULN on at least two occasions, seven or more days apart, during the Screening period
  • alpha-fetoprotein (AFP) ≤ 100 ng/mL
  • Hemoglobin ≥10 g/dL, a platelet count ≥ 100 x 10\^9/L, and a white blood cell count ≥ 3.0 x 10\^9/L
  • If on metformin, sulfonylureas, statins, or fibrates, subjects must be on a stable dose of these drugs for at least three months prior to Screening and during the study

You may not qualify if:

  • Known infection with HIV, HCV, or HBV
  • Decompensated or severe liver disease as evidenced by one or more of the following:
  • Confirmed cirrhosis or suspicion of cirrhosis
  • Esophageal varices
  • Ascites
  • Suspicion of portal hypertension
  • Hospitalization for liver disease within 60 days of screening
  • Bilirubin \>2 x ULN, or ALT or AST \> 10 x ULN
  • Inflammatory bowel disease
  • Diagnosed or suspected systemic lupus erythematosus (SLE) and/or rheumatoid arthritis (RA)
  • Hepatocellular carcinoma (HCC) at entry into the study
  • History of or active non-liver malignancies other than curatively treated skin cancer (basal cell or squamous cell carcinomas)
  • Significant systemic or major illness other than liver disease, including coronary artery disease, cerebrovascular disease, pulmonary disease, renal insufficiency, and/or serious psychiatric disease, that, in the opinion of the Investigator would preclude the subject from participating in and completing the study
  • History or presence of alcohol abuse, defined as consumption of more than 210 mL of alcohol per week (the equivalent of 14 4-ounce glasses of wine or 14 12-ounce cans/bottles of beer or wine coolers), or other substance abuse within the prior two years

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (7)

University of Miami

Miami, Florida, 33136, United States

Location

Indiana University

Indianapolis, Indiana, 46202, United States

Location

Henry Ford Hospital

Detroit, Michigan, 48202, United States

Location

Mayo Clinic Rochester

Rochester, Minnesota, 55905, United States

Location

Kansas City Research Institute

Kansas City, Missouri, 64131, United States

Location

Mary Immaculate Hospital

Newport News, Virginia, 23602, United States

Location

Bon Secours St. Mary's Hospital

Richmond, Virginia, 23226, United States

Location

Related Publications (1)

  • Shiffman M, Freilich B, Vuppalanchi R, Watt K, Chan JL, Spada A, Hagerty DT, Schiff E. Randomised clinical trial: emricasan versus placebo significantly decreases ALT and caspase 3/7 activation in subjects with non-alcoholic fatty liver disease. Aliment Pharmacol Ther. 2019 Jan;49(1):64-73. doi: 10.1111/apt.15030. Epub 2018 Nov 14.

MeSH Terms

Conditions

Non-alcoholic Fatty Liver Disease

Interventions

3-(2-(2-tert-butylphenylaminooxalyl)aminopropionylamino)-4-oxo-5-(2,3,5,6-tetrafluorophenoxy)pentanoic acid

Condition Hierarchy (Ancestors)

Fatty LiverLiver DiseasesDigestive System Diseases

Results Point of Contact

Title
Jean L. Chan, MD
Organization
Conatus Pharmaceuticals Inc.

Study Officials

  • Jean L. Chan, MD

    Conatus Pharmaceuticals Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 28, 2014

First Posted

March 4, 2014

Study Start

March 1, 2014

Primary Completion

March 1, 2015

Study Completion

March 1, 2015

Last Updated

August 30, 2016

Results First Posted

July 21, 2016

Record last verified: 2016-07

Locations