NCT01937130

Brief Summary

The study will evaluate the pharmacokinetics, pharmacodynamics, safety and preliminary efficacy of IDN-6556 in subjects with cirrhosis of the liver who are hospitalized for more than 24 hours due to acute deterioration of liver function.

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
23

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Sep 2013

Shorter than P25 for phase_2

Geographic Reach
2 countries

26 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 1, 2013

Completed
3 days until next milestone

First Submitted

Initial submission to the registry

September 4, 2013

Completed
5 days until next milestone

First Posted

Study publicly available on registry

September 9, 2013

Completed
1.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2015

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2015

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

April 11, 2016

Completed
Last Updated

April 11, 2016

Status Verified

March 1, 2016

Enrollment Period

1.3 years

First QC Date

September 4, 2013

Results QC Date

February 26, 2016

Last Update Submit

March 28, 2016

Conditions

Keywords

Liver FailureCirrhosisAlcoholic Hepatitis

Outcome Measures

Primary Outcomes (3)

  • Area Under the Curve (AUC)

    Primary endpoints for AUC\_0-8, AUC\_0 last, AUC\_0-inf on Day 1 and Day 4 for the active treatment arms were analyzed.

    28 days

  • Cmax

    Primary endpoints forCmax on Day 1 and Day 4 for the active treatment arms were analyzed.

    28 Days

  • Tmax & t1/2 Parameters

    Primary endpoints for tmax \& t1/2 on Day 1 and Day 4 for the active treatment arms were analyzed.

    28 Days

Secondary Outcomes (3)

  • Levels of CK18/M30

    Baseline, Day 2, Day 4, Day 7, Day 14, Day 21, and Day 28

  • Levels of CK18/M65

    Baseline, Day 2, Day 4, Day 7, Day 14, Day 21, and Day 28

  • Levels of Caspase 3/7 RLU

    Baseline, Day 2, Day 4, Day 7, Day 14, Day 21, and Day 28

Study Arms (4)

IDN-6556 5 mg

EXPERIMENTAL

Dosed twice daily

Drug: IDN-6556

IDN-6556 25 mg

EXPERIMENTAL

Dosed twice daily

Drug: IDN-6556

IDN-6556 50 mg

EXPERIMENTAL

Dosed twice daily

Drug: IDN-6556

Placebo

PLACEBO COMPARATOR

Dosed twice daily

Other: Placebo

Interventions

Also known as: emricasan, PF-03491390
IDN-6556 25 mgIDN-6556 5 mgIDN-6556 50 mg
PlaceboOTHER
Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female subjects of minimum adult legal age (according to local laws for signing the informed consent document), able to provide written informed consent, and understand and comply with the requirements of the study
  • Subjects with a clinical, radiological and/or histological diagnosis of cirrhosis
  • Subjects having not required hospital admission within 4 weeks of screening for a complication of cirrhosis
  • Subjects with an acute deterioration of liver function
  • Subjects who meet one of the following criteria:
  • Subjects with renal failure (defined as creatinine ≥ 2.0 to ≤ 3.4 mg/dL)
  • Subjects with two organ failures
  • If a subject received steroids for alcohol-induced acute liver failure, he/she must be unresponsive to steroid therapy. Responsiveness is based on investigator discretion.
  • Willingness to utilize two reliable forms of contraception (for both males and females of childbearing potential) from screening to one month after the last dose of study drug

You may not qualify if:

  • Known infection with HIV
  • Subjects with cirrhosis who develop decompensation at any time in the postoperative period following partial hepatectomy
  • Subjects with evidence of uncontrolled infection defined as persistent bacterial culture positivity despite adequate antibiotic therapy
  • Subjects with clinical evidence of disseminated intravascular coagulation
  • Subjects with chronic and/or pre-existing kidney disease defined as eGFR (estimated glomerular filtration rate) of less than 30 mL/min for 3 months or longer
  • Subjects who are hypotensive (defined as mean arterial pressure \<70 mmHg) or require the use of inotropic support
  • Subjects with evidence of significant and/or uncontrolled bleeding
  • Subjects requiring mechanical ventilation
  • Subjects with active or history of malignancies other than hepatocellular carcinoma (HCC) within Milan criteria or curatively treated skin cancer (basal cell or squamous cell carcinomas), unless adequately treated or in complete remission for five or more years
  • Subjects previously exposed to IDN-6556
  • History or presence of clinically concerning cardiac arrhythmias, or prolongation of Screening (pre-treatment) QT or QTc interval of \> 480 milliseconds (msec)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (26)

University of Alabama at Birmingham

Birmingham, Alabama, 35294, United States

Location

Scripps Clinic

La Jolla, California, 92037, United States

Location

VA San Diego Healthcare System

San Diego, California, 92161, United States

Location

Sutter Pacific Medical Foundation

San Francisco, California, 94115, United States

Location

Georgetown University Hospital

Washington D.C., District of Columbia, 20007, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

Univerisity of Louisville Liver Research Center

Louisville, Kentucky, 40202, United States

Location

University of Mississippi Medical Center

Jackson, Mississippi, 39216, United States

Location

Montefiore Medical Center

The Bronx, New York, 10467, United States

Location

University of Utah

Salt Lake City, Utah, 84132, United States

Location

University of Washington Harborview Medical Center

Seattle, Washington, 98104, United States

Location

Singleton Hospital

Swansea, Wales, SA2 8QA, United Kingdom

Location

Basildon and Thurrock University Hospital

Basildon, SS16 5NL, United Kingdom

Location

Blackpool Victoria Hospital

Blackpool, FY3 8NR, United Kingdom

Location

Bristol Royal Infirmary

Bristol, BS2 8HW, United Kingdom

Location

Ninewells Hospital

Dundee, DD1 9SY, United Kingdom

Location

Glasgow Royal Infirmary

Glasgow, United Kingdom

Location

Leicester Royal Infirmary

Leicester, LE1 5WW, United Kingdom

Location

Royal Liverpool University Hospital

Liverpool, L7 8XP, United Kingdom

Location

University College London, Royal Free Hospital

London, NW3 2PF, United Kingdom

Location

Royal London Hospital

London, United Kingdom

Location

Central Manchester University Hospitals NHS Trust

Manchester, M13 9WL, United Kingdom

Location

Freeman Hospital

Newcastle upon Tyne, NE7 7DN, United Kingdom

Location

Nottingham University Hospitals NHS Trust

Nottingham, NG7 2UH, United Kingdom

Location

Derriford Hospital

Plymouth, United Kingdom

Location

Queen Alexandra Hospital

Portsmouth, PO6 3LY, United Kingdom

Location

MeSH Terms

Conditions

Liver Failure, AcuteLiver CirrhosisLiver FailureFibrosisHepatitis, Alcoholic

Interventions

3-(2-(2-tert-butylphenylaminooxalyl)aminopropionylamino)-4-oxo-5-(2,3,5,6-tetrafluorophenoxy)pentanoic acid

Condition Hierarchy (Ancestors)

Hepatic InsufficiencyLiver DiseasesDigestive System DiseasesPathologic ProcessesPathological Conditions, Signs and SymptomsHepatitisLiver Diseases, AlcoholicAlcohol-Induced DisordersAlcohol-Related DisordersSubstance-Related DisordersChemically-Induced Disorders

Limitations and Caveats

Study was terminated early.

Results Point of Contact

Title
Jean L. Chan, MD
Organization
Conatus Pharmaceuticals

Study Officials

  • Stephen Ryder, Dr.

    Nottingham University Hospital NHS Trust

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 4, 2013

First Posted

September 9, 2013

Study Start

September 1, 2013

Primary Completion

January 1, 2015

Study Completion

February 1, 2015

Last Updated

April 11, 2016

Results First Posted

April 11, 2016

Record last verified: 2016-03

Locations