NCT02138253

Brief Summary

This is a double-blind, multicenter study involving patients with chronic HCV infection who had a liver transplantation; developed HCV-related liver fibrosis and/or incomplete cirrhosis; achieved a sustained virologic response (SVR) following anti-HCV therapy; but still have fibrosis and/or incomplete cirrhosis on liver biopsy to see if treatment with IDN-6556 is better than placebo in reversing or stopping the progression of the damage to the new liver caused by HCV.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
64

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started May 2014

Typical duration for phase_2

Geographic Reach
1 country

35 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 1, 2014

Completed
11 days until next milestone

First Submitted

Initial submission to the registry

May 12, 2014

Completed
2 days until next milestone

First Posted

Study publicly available on registry

May 14, 2014

Completed
3.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 15, 2018

Completed
22 days until next milestone

Study Completion

Last participant's last visit for all outcomes

March 9, 2018

Completed
1.8 years until next milestone

Results Posted

Study results publicly available

December 11, 2019

Completed
Last Updated

December 11, 2019

Status Verified

November 1, 2019

Enrollment Period

3.8 years

First QC Date

May 12, 2014

Results QC Date

May 2, 2019

Last Update Submit

November 21, 2019

Conditions

Keywords

liver transplanthepatitis Cliver fibrosishepatic fibrosisliver cirrhosishepatic cirrhosis

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With At Least a One Stage Reduction From Baseline in Ishak Fibrosis Score

    At least a one stage reduction from baseline in Ishak Fibrosis Stage. Score F0 No fibrosis F1 Fibrous expansion of some portal areas, with or without short fibrous septa F2 Fibrous expansion of most portal areas, with or without short fibrous septa F3 Fibrous expansion of most portal areas, with occasional portal to portal bridging F4 Fibrous expansion of portal areas, with marked bridging (portal to portal as well as portal to central) F5 Marked bridging (portal to portal and/or portal to central) with occasional nodules (incomplete cirrhosis) F6 Cirrhosis probable or definite Since the primary analysis used multiple imputation methodology, the numerator and denominator varied across 20 imputations.

    24 months

Secondary Outcomes (11)

  • Number of Participants With At Least a One Stage Reduction From Baseline in Ishak Fibrosis Score (Observed Cases Only)

    24 months

  • Number of Participants With At Least a One Stage Reduction From Baseline in Ishak Fibrosis Score

    12 months

  • Alanine Aminotransferase (ALT) - Change From Baseline

    Baseline and 24 months

  • Aspartate Aminotransferase (AST) Change From Baseline

    Baseline and 24 months

  • Caspase 3/7 Change From Baseline

    Baseline and 24 months

  • +6 more secondary outcomes

Study Arms (2)

IDN-6556

EXPERIMENTAL

IDN-6556 25 mg BID

Drug: IDN-6556

Placebo

PLACEBO COMPARATOR

Placebo BID

Drug: Placebo

Interventions

Also known as: emricasan, PF-03491390
IDN-6556

Placebo control

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female subjects of minimum adult legal age (according to local laws for signing the informed consent document), able to provide written informed consent, and able to understand and willing to comply with the requirements of the study
  • History of orthotopic liver transplantation for HCV-induced liver disease
  • Diagnosis of HCV infection (HCV-RNA detectable in serum) and liver fibrosis and/or incomplete cirrhosis status post liver transplantation, and achieved a sustained virologic response (SVR) with anti-viral HCV treatment within 18 months of Day 1
  • Liver fibrosis on liver histology as read by central histopathologist of Ishak F2 to F6 within three months of Day 1 (Up to 15 subjects with an Ishak score of F6 can be enrolled)
  • Willingness to utilize two reliable forms of contraception (for both males and females of childbearing potential) from Screening to one month after the last dose of study drug

You may not qualify if:

  • Known infection with hepatitis B virus (HBV) and/or human immunodeficiency virus (HIV)
  • History of renal transplant and/or severe renal impairment defined as eGFR (estimated glomerular filtration rate) of less than 30 mL/min/1.73 m2
  • Evidence of tumor burden \>Milan criteria, or evidence of micro- or macrovascular invasion in explanted liver
  • Hepatocellular carcinoma (HCC) at entry into the study
  • Concurrent sirolimus (rapamycin) use
  • History or presence of clinically concerning cardiac arrhythmias, or prolongation of Screening (pre-treatment) QT or QTc interval of \> 480 milliseconds (msec)
  • Subjects with diagnosed or suspected systemic lupus erythematosus (SLE) and/or rheumatoid arthritis (RA)
  • If female: known pregnancy, positive urine or serum pregnancy test, or lactating/breastfeeding

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (35)

Southern California Research Center

Coronado, California, 92118, United States

Location

Scripps Clinic

La Jolla, California, 92037, United States

Location

Loma Linda University Medical Center

Loma Linda, California, 92354, United States

Location

UCLA Pfleger Liver Institute

Los Angeles, California, 90095, United States

Location

Georgetown University Hospital

Washington D.C., District of Columbia, 20007, United States

Location

Johns Hopkins Sibley Memorial Hospital

Washington D.C., District of Columbia, 21287, United States

Location

University of Florida

Gainesville, Florida, 32610, United States

Location

University of Miami

Miami, Florida, 33136, United States

Location

Piedmont Atlanta Hospital

Atlanta, Georgia, 30309, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

University of Chicago Medicine

Chicago, Illinois, 60637, United States

Location

Indiana University

Indianapolis, Indiana, 46202, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

University of Louisville

Louisville, Kentucky, 40202, United States

Location

Tulane Health Science Center

New Orleans, Louisiana, 70112, United States

Location

Ochsner Clinic

New Orleans, Louisiana, 70121, United States

Location

John Hopkins Hospital

Baltimore, Maryland, 21287, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

Henery Ford Health System

Detroit, Michigan, 48202, United States

Location

Saint Louis University

St Louis, Missouri, 63104, United States

Location

Rutgers New Jersey Medical School

Newark, New Jersey, 07103, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

University of Cincinnati Physicians Company

Cincinnati, Ohio, 45267, United States

Location

University of Pennsylvania Milton Hershey Hospital

Philadelphia, Pennsylvania, 19104, United States

Location

Temple University Hospital

Philadelphia, Pennsylvania, 19140, United States

Location

Albert Einstein Medical Center

Philadelphia, Pennsylvania, 19141, United States

Location

Baylor All Saints Medical Center

Fort Worth, Texas, 76104, United States

Location

Liver Associates of Texas, PA

Houston, Texas, 77030, United States

Location

University of Texas Health Science Center at Houston

Houston, Texas, 77030, United States

Location

VAMC/Baylor College of Medicine

Houston, Texas, 77030, United States

Location

University of Utah

Salt Lake City, Utah, 84132, United States

Location

Bon Secours Mary Immaculate Hospital

Newport News, Virginia, 23602, United States

Location

Bon Secours St. Mary's Hospital of Richmond

Richmond, Virginia, 23226, United States

Location

McGuire DVAMC

Richmond, Virginia, 23249, United States

Location

University of Washington Harborview Medical Center

Seattle, Washington, 98104, United States

Location

MeSH Terms

Conditions

Liver CirrhosisHepatitis C

Interventions

3-(2-(2-tert-butylphenylaminooxalyl)aminopropionylamino)-4-oxo-5-(2,3,5,6-tetrafluorophenoxy)pentanoic acid

Condition Hierarchy (Ancestors)

Liver DiseasesDigestive System DiseasesFibrosisPathologic ProcessesPathological Conditions, Signs and SymptomsBlood-Borne InfectionsCommunicable DiseasesInfectionsHepatitis, Viral, HumanVirus DiseasesFlaviviridae InfectionsRNA Virus InfectionsHepatitis

Limitations and Caveats

The broad range of fibrosis stages included in the study and the high placebo response rates especially in the F2 and F6 fibrosis stages impacted the primary endpoint of improvement in fibrosis score from baseline.

Results Point of Contact

Title
Steven Mento, Ph.D., CEO
Organization
Conatus Pharmaceuticals, Inc.

Study Officials

  • David Hagerty, MD

    Conatus Pharmaceuticals Inc.

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 12, 2014

First Posted

May 14, 2014

Study Start

May 1, 2014

Primary Completion

February 15, 2018

Study Completion

March 9, 2018

Last Updated

December 11, 2019

Results First Posted

December 11, 2019

Record last verified: 2019-11

Locations