NCT01790594

Brief Summary

The purpose of this study is to find out if the drug NULOJIX® (belatacept) will minimize the amount of other anti-rejection medications necessary and thereby reduce the long-term side effects caused by the other medications. The researchers also want to learn more about the safety of this treatment and long term health of transplanted pancreases and kidneys.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
46

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Feb 2013

Typical duration for phase_2

Geographic Reach
1 country

5 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

February 1, 2013

Completed
10 days until next milestone

First Submitted

Initial submission to the registry

February 11, 2013

Completed
2 days until next milestone

First Posted

Study publicly available on registry

February 13, 2013

Completed
3.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2016

Completed
1.4 years until next milestone

Results Posted

Study results publicly available

December 7, 2017

Completed
Last Updated

July 20, 2021

Status Verified

June 1, 2021

Enrollment Period

3.5 years

First QC Date

February 11, 2013

Results QC Date

October 6, 2017

Last Update Submit

June 30, 2021

Conditions

Keywords

transplantationkidneypancreasimmunosuppressioncalcineurin inhibitor (CNI)

Outcome Measures

Primary Outcomes (1)

  • Mean Estimated Glomerular Filtration Rate (eGFR) Calculated for Each Treatment Group Using the CKD-EPI Equation at Wk 52 Post-Transplant

    eGFR was calculated using the Chronic Kidney Disease Epidemiology Collaboration equation (CKD-EPI): * A score of ≥90 means kidney function is normal. * A score between 60 and 89 indicates mildly reduced kidney function, pointing to kidney disease. * Scores between 30 and 59 indicates moderately reduced kidney function. * Scores between 15 and 29 indicate severely reduced kidney function. * Scores below 15 indicate very severe or end stage kidney failure.

    Week 52 Post-Transplant

Secondary Outcomes (30)

  • Count of Participants With eGFR < 60 mL/Min/1.73 m^2 Measured by CKD-EPI at Wk 52 Post-Transplant

    Week 52 Post-Transplant

  • Count of Participants by CKD Stage at Wk 52 Post-Transplant

    Week 52 Post-Transplant

  • Count of Participants With Defined CKD Stage 4 or 5 at Wk 52 Post-Transplant

    Week 52 Post-Transplant

  • Mean Calculated eGFR Using MDRD 4 Variable Model at Wk 52 Post-Transplant

    Week 52 Post-Transplant

  • The Slope of eGFR by CKD-EPI Over Time Based on Serum Creatinine Post-Transplant

    Day 28 through Week 52 Post-Transplant

  • +25 more secondary outcomes

Study Arms (2)

Immunosuppression without Belatacept

ACTIVE COMPARATOR

* Induction: 5 day course of methylprednisolone or equivalent; * Induction: Anti-thymocyte Globulin (Rabbit); * Maintenance Immunosuppression: Tacrolimus (or generic). The site investigator will identify a starting tacrolimus dose at his or her discretion, in order to achieve the target trough levels, no later than 5 days post-transplantation. Tacrolimus dosing will be initiated on the day of surgery or post-operative day 1 depending upon when during the day the surgery is completed, then adjusted to target trough levels of 8-12 ng/ml during the first 24 weeks post-transplant, then adjusted to target trough levels of 5-8 ng/ml thereafter. * Maintenance Immunosuppression: Mycophenolate mofetil (or Myfortic (mycophenolate sodium), or generic).

Drug: methylprednisoloneBiological: Anti-thymocyte Globulin (Rabbit)Drug: TacrolimusDrug: Mycophenolate mofetil

Immunosuppression Including Belatacept

EXPERIMENTAL

* Induction: 5 day course of methylprednisolone or equivalent; * Induction: Anti-thymocyte Globulin (Rabbit); * Maintenance Immunosuppression: Belatacept * Maintenance Immunosuppression: Tacrolimus (or generic)- The site investigator will identify a starting tacrolimus dose at his or her discretion, in order to achieve the target trough levels no later than 5 days post-transplantation. Tacrolimus dosing will be initiated on the day of surgery or post-operative day 1 depending upon when during the day the surgery is completed. The dosage will be adjusted to achieve the following therapeutic trough levels: 5-8 ng/ml during the first 24 weeks post-transplant and then 3-5 ng/ml until day 280 (week 40). Subjects may be withdrawn if they meet all the criteria defined below. * Maintenance Immunosuppression: Mycophenolate mofetil (or Myfortic (mycophenolate sodium), or generic).

Biological: BelataceptDrug: methylprednisoloneBiological: Anti-thymocyte Globulin (Rabbit)Drug: TacrolimusDrug: Mycophenolate mofetil

Interventions

BelataceptBIOLOGICAL

The first dose of belatacept will be administered approximately 24-48 hours after the last dose of Anti-Thymocyte Globulin (Rabbit).

Also known as: NULOJIX
Immunosuppression Including Belatacept
Also known as: Medrol
Immunosuppression Including BelataceptImmunosuppression without Belatacept
Also known as: Thymoglobulin, ATG (Rabbit)
Immunosuppression Including BelataceptImmunosuppression without Belatacept

There may be an opportunity to withdraw tacrolimus at week 40

Also known as: Prograf
Immunosuppression Including BelataceptImmunosuppression without Belatacept

Mycophenolate mofetil will be administered at a target dose of 1000 mg by mouth twice daily (e.g., BID) beginning on the day of surgery or post-operative day 1 depending upon when during the day the surgery is completed (maximum MMF dosing is 2G per day). MMF will be adjusted based on clinical complications (such as neutropenia). Myfortic® (mycophenolate sodium) may be used as a replacement for MMF. Mycophenolate sodium will be dosed at 720 mg PO BID. Mycophenolate sodium will be adjusted based on clinical complications.

Also known as: MMF, mycophenolate sodium, CellCept
Immunosuppression Including BelataceptImmunosuppression without Belatacept

Eligibility Criteria

Age18 Years - 55 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • Ability to understand and provide written informed consent;
  • Candidate for a primary simultaneous kidney and pancreas allograft with random c-peptide \<0.3 ng/mL;
  • No known contraindications to study therapy using NULOJIX® (belatacept);
  • Female subjects of childbearing potential must have a negative pregnancy test upon study entry;
  • Female and male participants with reproductive potential must agree to use FDA approved methods of birth control during participation in the study and for 4 months following study completion;
  • No donor specific antibodies prior to transplant that are considered to be of clinical significance by the site investigator;
  • Negative crossmatch, actual or virtual, or a Panel Reactive Antibodies (PRA) of 0% on historic and admission sera, as determined by each participating study center;
  • A documented negative Tuberculosis (TB) test within the 12 months prior to transplant. If documentation is not present at the time of transplantation, and the subject does not have any risk factors for TB, a TB-specific interferon gamma release assay (IGRA) may be performed.

You may not qualify if:

  • Need for multi-organ transplantation other than a kidney and pancreas;
  • Recipient of previous organ transplant;
  • Epstein-Barr Virus (EBV) sero-negative recipients or recipients whose EBV serostatus is unknown prior to the time of transplantation;
  • Individuals infected by the hepatitis B or C viruses or HIV;
  • Individuals who have required treatment with systemic prednisone or other immunosuppressive drugs within 1 year prior to transplant;
  • Individuals previously treated with NULOJIX® (belatacept);
  • Any condition that, in the opinion of the investigator, would interfere with the participant's ability to comply with study requirements;
  • Use of investigational drugs within 4 weeks of enrollment;
  • Known hypersensitivity to mycophenolate mofetil (MMF)or any of the drug's components;
  • Administration of live attenuated vaccine(s) within 8 weeks of enrollment.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (5)

University of Alabama at Birmingham

Birmingham, Alabama, 35294, United States

Location

University of California San Francisco Medical Center

San Francisco, California, 94143-0780, United States

Location

Emory University

Atlanta, Georgia, 30322, United States

Location

Indiana University Hospital

Indianapolis, Indiana, 46202, United States

Location

University of Wisconsin

Madison, Wisconsin, 53792, United States

Location

Related Publications (1)

  • Stock PG, Mannon RB, Armstrong B, Watson N, Ikle D, Robien MA, Morrison Y, Odorico J, Fridell J, Mehta AK, Newell KA. Challenges of calcineurin inhibitor withdrawal following combined pancreas and kidney transplantation: Results of a prospective, randomized clinical trial. Am J Transplant. 2020 Jun;20(6):1668-1678. doi: 10.1111/ajt.15817. Epub 2020 Mar 8.

Related Links

MeSH Terms

Interventions

AbataceptMethylprednisoloneAntilymphocyte SerumthymoglobulinTacrolimusMycophenolic Acid

Intervention Hierarchy (Ancestors)

ImmunoconjugatesAntibodiesImmunoglobulinsSerum GlobulinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsGlobulinsPrednisolonePregnadienetriolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic CompoundsImmune SeraImmunoproteinsBiological ProductsComplex MixturesMacrolidesLactonesOrganic ChemicalsCaproatesAcids, AcyclicCarboxylic AcidsFatty AcidsLipids

Results Point of Contact

Title
Director, Clinical Research Operations Program
Organization
DAIT/NIAID

Study Officials

  • Kenneth Newell, MD, PhD

    Emory University

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
NIH
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 11, 2013

First Posted

February 13, 2013

Study Start

February 1, 2013

Primary Completion

August 1, 2016

Study Completion

August 1, 2016

Last Updated

July 20, 2021

Results First Posted

December 7, 2017

Record last verified: 2021-06

Data Sharing

IPD Sharing
Will share

Data is available in: Immunology Database and Analysis Portal (ImmPort), a long-term archive of clinical and mechanistic data from DAIT-funded grants and contracts.

Shared Documents
STUDY PROTOCOL
Time Frame
On average, data is available within 24 months after database lock for a trial.
Access Criteria
Open access. Study's: * Accession ID is SDY1433, and * Digital Object Identifier (DOI) is : 10.21430/M3CEH2A7ZF
More information

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