NCT01644773

Brief Summary

This is a phase I study to find the highest tolerable dose of crizotinib and dasatinib given in combination to patients with diffuse intrinsic pontine glioma (DIPG) and other types of high grade gliomas (HGG). Participants will receive escalating doses until the highest dose is determined. Participants will be enrolled in two strata: stratum A for recurrent/ progressive tumors and stratum B for recently diagnosed patients who have completed standard radiation therapy without progressive disease. Up to 7 dosage levels will be tested. Both drugs are taken orally daily, once per day. Correlative pharmacokinetic and biology studies are planned, as well as advanced methods of magnetic resonance imaging (MRI).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
36

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Nov 2012

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 17, 2012

Completed
2 days until next milestone

First Posted

Study publicly available on registry

July 19, 2012

Completed
4 months until next milestone

Study Start

First participant enrolled

November 27, 2012

Completed
5.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 7, 2018

Completed
7 months until next milestone

Study Completion

Last participant's last visit for all outcomes

September 28, 2018

Completed
Last Updated

March 22, 2019

Status Verified

March 1, 2019

Enrollment Period

5.3 years

First QC Date

July 17, 2012

Last Update Submit

March 20, 2019

Conditions

Outcome Measures

Primary Outcomes (2)

  • Maximum tolerated dose of combination crizotinib and dasatinib in stratum A patients

    6 weeks after start of therapy for last enrolled participant

  • Maximum tolerated dose of combination crizotinib and dasatinib in stratum B patients

    6 weeks after start of therapy for last enrolled participant

Study Arms (1)

Chemotherapy

EXPERIMENTAL

Research participants with high grade glioma or diffuse intrinsic pontine glioma will receive crizotinib and dasatinib.

Drug: CrizotinibDrug: Dasatinib

Interventions

Starting dose level: * Initial Treatment Plan: 130 mg/m\^2 per dose * Modified Treatment Plan per Amendment 1.0: 165 mg/m\^2 per dose The dose of a single agent will be increased by approximately 30% in each subsequent cohort until the MTD of this combination is reached. The doses of each agent will not exceed their single-agent MTD already determined for children with recurrent solid tumors. Cycle 1 (28 days): once a day for 28 days Cycles 2-26 (28 days each): once a day

Also known as: PF-02341066, Xalkori®
Chemotherapy

Starting dose level: 50 mg/m\^2 per dose The dose of a single agent will be increased by approximately 30% in each subsequent cohort until the MTD of this combination is reached. The doses of each agent will not exceed their single-agent MTD already determined for children with recurrent solid tumors. Cycle 1 (28 days): starting on day 3, once a day for 28 days Cycles 2-26 (28 days each): once a day

Also known as: BMS-354825, Sprycel®
Chemotherapy

Eligibility Criteria

Age2 Years - 21 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Diagnosis of high-grade glioma (HGG) or diffuse intrinsic pontine glioma (DIPG). If histologic confirmation was obtained, diagnosis must be one of the following: anaplastic astrocytoma (WHO grade 3), anaplastic oligodendroglioma (WHO grade 3), anaplastic oligoastrocytoma (WHO grade 3), anaplastic ganglioglioma (WHO grade 3), pleomorphic xanthoastrocytoma with anaplastic features (WHO grade 3), malignant glioneuronal tumor, glioblastoma, or gliosarcoma (WHO grade 4)
  • Age \> or = 2 years and \< or = 21 years
  • Performance score \> or = 50 (Lansky for research participants \< or = 16 years and Karnofsky for those \> 16 years).
  • Adequate organ function at the time of enrollment as follows:
  • Bone marrow: Hemoglobin \> or = 8g/dL \[may have received packed red blood cell transfusion\], absolute neutrophil count (ANC) \> or = 1000/mm\^3, platelets \> or = 100,000/mm\^3 \[transfusion independent\])
  • Renal: Normal serum creatinine based on age as shown below or GFR \> 70ml/min/1.73m\^2:
  • Age \< or = 5 years: 0.8 mg/dL maximum
  • Age 5 to 10 years: 1.0 mg/dL maximum
  • Age 10 to 15 years: 1.2 mg/dL maximum
  • Age \> 15 years: 1.5 mg/dL maximum
  • Hepatic: SGPT and SGOT \< 3x the institutional upper limit of normal (ULN), total bilirubin concentration \< 1.5x the institutional ULN, albumin \> or = 2g/dL
  • Female research participants \> or = 10 years of age or post-menarchal must not be pregnant (confirmed by serum or urine pregnancy test within 1 week of study enrollment) or breastfeeding
  • Female research participants of childbearing age or males research participants of child fathering potential must agree to use safe contraceptive methods for the duration of the study and for 3 months thereafter
  • Diagnosis of recurrent or progressive HGG or DIPG.
  • Neurological deficits must be stable on a fixed or decreasing dose of dexamethasone for ≥7 days before study enrollment.
  • +10 more criteria

You may not qualify if:

  • Metastatic disease for stratum B only
  • Concomitant use of other anticancer (except for corticosteroids) or experimental agents
  • Use of enzyme-inducing anticonvulsants (EIACs). A minimum interval of 10 days between the last dose of EIAC and start of this therapy will be required for research participants who were previously receiving such medications.
  • Pregnant or lactating patients
  • Research participants with other clinically significant medical disorders that could compromise their ability to tolerate protocol therapy or would interfere with the study procedures or results
  • Prior therapy with a PDGFR or c-Met inhibitor
  • Original treatment design: Body surface area ≥ 1.8m2on dosage levels 3b, 4, and 5
  • Modified treatment design: Body surface area \< 0.55 m\^2 for all dosage levels

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

St. Jude Children's Research Hospital

Memphis, Tennessee, 38105, United States

Location

Related Publications (1)

  • Gibson EG, Campagne O, Selvo NS, Gajjar A, Stewart CF. Population pharmacokinetic analysis of crizotinib in children with progressive/recurrent high-grade and diffuse intrinsic pontine gliomas. Cancer Chemother Pharmacol. 2021 Dec;88(6):1009-1020. doi: 10.1007/s00280-021-04357-4. Epub 2021 Sep 29.

Related Links

MeSH Terms

Conditions

Diffuse Intrinsic Pontine GliomaGlioma

Interventions

CrizotinibDasatinib

Condition Hierarchy (Ancestors)

Neoplasms, NeuroepithelialNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Glandular and EpithelialNeoplasms, Nerve TissueBrain Stem NeoplasmsInfratentorial NeoplasmsBrain NeoplasmsCentral Nervous System NeoplasmsNervous System NeoplasmsNeoplasms by SiteBrain DiseasesCentral Nervous System DiseasesNervous System Diseases

Intervention Hierarchy (Ancestors)

PiperidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsAminopyridinesPyridinesThiazolesSulfur CompoundsOrganic ChemicalsAzolesPyrimidines

Study Officials

  • Anna Vinitsky, MD

    St. Jude Children's Research Hospital

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 17, 2012

First Posted

July 19, 2012

Study Start

November 27, 2012

Primary Completion

March 7, 2018

Study Completion

September 28, 2018

Last Updated

March 22, 2019

Record last verified: 2019-03

Locations