NCT01632904

Brief Summary

The purpose of the RELIEF study is to compare symptoms in polycythemia vera (PV) subjects treated with ruxolitinib versus subjects treated with hydroxyurea (HU) as measured by the percent of subjects who achieve a clinically meaningful symptom improvement (ie, total symptom score reduction of ≥ 50% reduction) at Week 16 compared to Baseline. The study is also designed to demonstrate that these responses are durable with continued treatment.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
110

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Jun 2012

Typical duration for phase_3

Geographic Reach
7 countries

70 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2012

Completed
28 days until next milestone

First Submitted

Initial submission to the registry

June 29, 2012

Completed
4 days until next milestone

First Posted

Study publicly available on registry

July 3, 2012

Completed
1.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2014

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

April 7, 2015

Completed
1.1 years until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2016

Completed
Last Updated

November 14, 2017

Status Verified

October 1, 2017

Enrollment Period

1.7 years

First QC Date

June 29, 2012

Results QC Date

March 26, 2015

Last Update Submit

October 12, 2017

Conditions

Keywords

Polycythemia VeraPV

Outcome Measures

Primary Outcomes (1)

  • Percentage of Subjects Achieving a ≥ 50% Improvement From Baseline in Total Symptom Score-Cytokine (TSS-C) at Week 16, as Measured by the Modified Myeloproliferative Neoplasm Symptom Assessment Form (MPN-SAF) Diary

    Symptoms of polycythemia vera were assessed using a modified Myeloproliferative Neoplasm Symptom Assessment Form (MPN-SAF) electronic diary. Using the diary, patients rated the following symptoms on a scale from 0 (absent) to 10 (worst imaginable): tiredness, itching, muscle aches, night sweats, and sweats while awake. The total symptom score ranged from 0-50 and was calculated as the sum of the 5 symptom scores. A higher score indicates worse symptoms.

    From Baseline to Week 16

Secondary Outcomes (2)

  • Percentage of Subjects Achieving ≥ 50% Improvement From Baseline in the Individual Symptom Scores for TSS-C at Week 16

    From Baseline to Week 16

  • Proportion of Subjects Randomized to Ruxolitinib Who Achieved ≥ 50% Improvement From Baseline in Total Symptom Score-Cytokine and the Individual Symptom Scores at Week 16 That Were Maintained at Week 48

    Week 48

Study Arms (2)

ruxolitinib and hydroxyurea (HU)-placebo

EXPERIMENTAL
Drug: RuxolitinibDrug: HU-placebo

HU and ruxolitinib-placebo

ACTIVE COMPARATOR
Drug: Hydroxyurea (HU)Drug: Ruxolitinib-placebo

Interventions

Ruxolitinib will be orally self-administered at a starting dose of 10 mg (two 5 mg tablets) twice a day. Dose increases of 5 mg (1 tablet) in twice-daily increments are permitted after 4 weeks and again after 8 weeks of therapy for subjects who meet prespecified criteria for inadequate efficacy.

ruxolitinib and hydroxyurea (HU)-placebo

Hydroxyurea (500 mg capsules) will be orally self-administered at the dose that the subject was receiving previously. The dose may be increased after 4 weeks and again after 8 weeks of therapy to optimize efficacy for subjects meeting prespecified criteria.

HU and ruxolitinib-placebo

All placebo will be self-administered, and dosing will be the same as with the blinded dose. When adjustments are made to the ruxolitinib dose, the dose of HU-placebo will be adjusted concurrently.

ruxolitinib and hydroxyurea (HU)-placebo

All placebo will be self-administered, and dosing will be the same as with the blinded dose. When adjustments are made to the HU dose, the dose of ruxolitinib-placebo will be adjusted concurrently.

HU and ruxolitinib-placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Subjects must currently be reporting symptoms while on a stable dose of HU monotherapy and be eligible to continue HU on study after randomization.
  • Before screening, the subject must have been receiving HU for at least 12 weeks AND be receiving a stable dose.
  • Subjects must meet baseline symptom criteria
  • Subjects should meet at least 1 of the following criteria:
  • No more than 2 phlebotomies within the 6 months before screening OR
  • No palpable splenomegaly.
  • Subjects must have a hematocrit that can be controlled within 35% to 48% (inclusive) before randomization.

You may not qualify if:

  • Subjects with inadequate liver or renal function at screening.
  • Subjects with clinically significant infection that requires therapy
  • Subjects with known active hepatitis A, B, or C at screening or with known HIV positivity.
  • Subjects with an active malignancy over the previous 2 years
  • Subjects with clinically significant cardiac disease (Class III or IV).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (70)

Unknown Facility

Scottsdale, Arizona, United States

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Fayetteville, Arkansas, United States

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Burbank, California, United States

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Glendale, California, United States

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La Jolla, California, United States

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Los Angeles, California, United States

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San Diego, California, United States

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Aurora, Colorado, United States

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Stamford, Connecticut, United States

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Washington D.C., District of Columbia, United States

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Boynton Beach, Florida, United States

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Orlando, Florida, United States

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Atlanta, Georgia, United States

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Chicago, Illinois, United States

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Niles, Illinois, United States

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Springfield, Illinois, United States

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Ames, Iowa, United States

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Westwood, Kansas, United States

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Alexandria, Louisiana, United States

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Baltimore, Maryland, United States

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Southfield, Michigan, United States

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Minneapolis, Minnesota, United States

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Columbia, Missouri, United States

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St Louis, Missouri, United States

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Henderson, Nevada, United States

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Las Vegas, Nevada, United States

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East Orange, New Jersey, United States

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Morristown, New Jersey, United States

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Somerville, New Jersey, United States

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Albany, New York, United States

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Armonk, New York, United States

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Mineola, New York, United States

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New York, New York, United States

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Canton, Ohio, United States

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Bethlehem, Pennsylvania, USA, United States

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Charleston, South Carolina, United States

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Chattanooga, Tennessee, United States

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Amarillo, Texas, United States

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Bedford, Texas, United States

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Dallas, Texas, United States

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Garland, Texas, United States

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Houston, Texas, United States

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Longview, Texas, United States

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Midland, Texas, United States

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San Antonio, Texas, United States

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Temple, Texas, United States

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Tyler, Texas, United States

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Salt Lake City, Utah, United States

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Alexandria, Virginia, United States

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Seattle, Washington, United States

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Milwaukee, Wisconsin, United States

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Antwerp, Belgium

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Bruges, Belgium

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Aachen, Germany

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Berlin, Germany

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Freiburg im Breisgau, Germany

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Hamburg, Germany

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Stuttgart, Germany

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Ulm, Germany

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Galway, Ireland

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Florence, Italy

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Reggio Calabria, Italy

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Varese, Italy

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Barcelona, Spain

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Pamplona, Spain

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Salamanca, Spain

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Boston, United Kingdom

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Leicester, United Kingdom

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Nottingham, United Kingdom

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West Bromwich, United Kingdom

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MeSH Terms

Conditions

Polycythemia Vera

Interventions

ruxolitinibHydroxyurea

Condition Hierarchy (Ancestors)

Bone Marrow NeoplasmsHematologic NeoplasmsNeoplasms by SiteNeoplasmsBone Marrow DiseasesHematologic DiseasesHemic and Lymphatic DiseasesMyeloproliferative Disorders

Intervention Hierarchy (Ancestors)

UreaAmidesOrganic Chemicals

Results Point of Contact

Title
Study Director
Organization
Incyte Corporation

Study Officials

  • Mark Jones, M.D.

    Incyte Corporation

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 29, 2012

First Posted

July 3, 2012

Study Start

June 1, 2012

Primary Completion

March 1, 2014

Study Completion

May 1, 2016

Last Updated

November 14, 2017

Results First Posted

April 7, 2015

Record last verified: 2017-10

Locations