NCT01590069

Brief Summary

This phase I/II trial studies the side effects and best dose of aerosolized aldesleukin and to see how well it works in treating patients with cancer that has spread from the original tumor to the lungs. Biological therapies, such as aerosolized aldesleukin, may stimulate or suppress the immune system in different ways and stop tumor cells from growing.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
70

participants targeted

Target at P75+ for phase_1

Timeline
0mo left

Started Jun 2012

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 30, 2012

Completed
2 days until next milestone

First Posted

Study publicly available on registry

May 2, 2012

Completed
2 months until next milestone

Study Start

First participant enrolled

June 28, 2012

Completed
13.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 30, 2026

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 30, 2026

Last Updated

April 16, 2026

Status Verified

April 1, 2026

Enrollment Period

13.8 years

First QC Date

April 30, 2012

Last Update Submit

April 13, 2026

Conditions

Outcome Measures

Primary Outcomes (3)

  • Maximum tolerated dose, defined as the highest dose level with six patients with at most one dose limiting toxicity, using the CTCAE v4.0 (Phase I)

    The dose escalation will be conducted via the accelerated titration method for the first 2 dose levels.

    28 days

  • Incidence of adverse events (AE)s, using the CTCAE v4.0 (Phase II)

    AEs will be summarized by severity according to the worst grade experienced over the number of patients at risk.

    Up to 4 years

  • Response of measurable lesions to aerosol aldesleukin using modified RECIST (Phase II)

    Response analysis will be performed on intent-to-treat, that is, any patient who enrolled into the expansion cohort. Patients who withdraw before the end of 2 months without responding will be considered non-responders. The two-sided 95% Clopper-Pearson confidence intervals will be calculated for the proportion of patients with responses.

    Up to 4 years

Secondary Outcomes (2)

  • IL-2 levels in serum

    Day 1 of therapy

  • Changes in biomarker levels

    Baseline to 8 weeks

Study Arms (1)

Treatment (aerosolized aldesleukin)

EXPERIMENTAL

Patients receive aerosolized aldesleukin QD on days 1-21. Courses repeat every 28 days in the absence of disease progression of unacceptable toxicity.

Biological: Aerosolized AldesleukinOther: Laboratory Biomarker Analysis

Interventions

Breathe aerosolized aldesleukin

Also known as: Aerosolized Recombinant IL-2
Treatment (aerosolized aldesleukin)

Optional correlative studies

Treatment (aerosolized aldesleukin)

Eligibility Criteria

Age12 Years - 50 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Patients with diagnosis of advanced cancer with lung metastases; patients with no prior therapy are eligible if there is no known superior alternative medical therapy; for phase Ib expansion cohort diagnosis of osteosarcoma, lung metastases will be required
  • Willing to comply with protocol therapy and required safety monitoring (self-report, pulse oximetry, remote spirometry, labs)
  • Creatinine =\< 2 x upper limit of normal (ULN)
  • Bilirubin =\< 5 x ULN
  • Aspartate aminotransferase (AST) =\< 5 x ULN
  • Forced vital capacity (FVC) \>= 50% predicted
  • Oxygen (O2) saturation at rest \>= 90% (off supplementary oxygen)
  • Eastern Cooperative Oncology Group (ECOG) performance status =\< 1 for ages \>= 16 or Lansky play \>= 80% for ages =\< 15
  • Patients must have recovered to =\< grade 1 toxicity (except alopecia and hearing loss) from any prior chemotherapy, other investigational therapy, hormonal, biological, targeted agents
  • No radiotherapy within 2 weeks: exception: patients may receive palliative low dose radiotherapy (30 Gy or less) for lesions outside the lung at the discretion of the treating physician; palliative radiotherapy could be given before aerosol treatment is started if necessary
  • Subjects have to be able to read and understand English
  • Patients with advanced cancer with resectable lung metastases
  • Patients with sarcoma, renal cell carcinoma, or melanoma or with known disease outside the lungs and/or thorax

You may not qualify if:

  • Currently being treated with bronchodilators or corticosteroids
  • Females: pregnant or breast feeding and if of child bearing potential (e.g. female of childbearing age that has not been amenorrheic for at least 12 consecutive month or surgically sterilized) not willing to use effective contraception
  • Uncontrolled intercurrent illness including, but not limited to, ongoing or active infection, bradycardia, related to cardiac disease, bundle branch block, symptomatic congestive heart failure, unstable angina pectoris, cardiac arrhythmia, or psychiatric illness/social situations that would limit compliance with study requirements
  • Subjects with baseline symptoms of fever and/or cough and/or shortness of breath and/or wheezing and/or fatigue grade \>= 2 (Common Terminology Criteria for Adverse Events \[CTCAE\] version \[v\] 4.0)
  • Patients with unresectable lung metastases
  • Patients without sarcoma, renal cell carcinoma, or melanoma

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

M D Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Related Links

MeSH Terms

Conditions

MelanomaOsteosarcomaCarcinoma, Renal CellSarcoma

Condition Hierarchy (Ancestors)

Neuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Nerve TissueNevi and MelanomasSkin NeoplasmsNeoplasms by SiteSkin DiseasesSkin and Connective Tissue DiseasesNeoplasms, Bone TissueNeoplasms, Connective TissueNeoplasms, Connective and Soft TissueAdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialKidney NeoplasmsUrologic NeoplasmsUrogenital NeoplasmsFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesKidney DiseasesUrologic DiseasesMale Urogenital Diseases

Study Officials

  • Najat Daw

    M.D. Anderson Cancer Center

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 30, 2012

First Posted

May 2, 2012

Study Start

June 28, 2012

Primary Completion (Estimated)

April 30, 2026

Study Completion (Estimated)

April 30, 2026

Last Updated

April 16, 2026

Record last verified: 2026-04

Locations