NCT01569438

Brief Summary

The purpose of this study is to assess the efficacy of gefapixant (AF-219/MK-7264) in female participants with moderate to severe pain associated with interstitial cystitis/bladder pain syndrome (IC/BPS) after 4 weeks of treatment.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
107

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Apr 2012

Geographic Reach
1 country

41 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 30, 2012

Completed
4 days until next milestone

First Posted

Study publicly available on registry

April 3, 2012

Completed
10 days until next milestone

Study Start

First participant enrolled

April 13, 2012

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2014

Completed
13 days until next milestone

Study Completion

Last participant's last visit for all outcomes

May 14, 2014

Completed
2.7 years until next milestone

Results Posted

Study results publicly available

January 12, 2017

Completed
Last Updated

August 17, 2020

Status Verified

August 1, 2020

Enrollment Period

2 years

First QC Date

March 30, 2012

Results QC Date

September 23, 2016

Last Update Submit

August 6, 2020

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change From Baseline in the Average Mean Numeric Pain Rating Scale (NPRS) Score at Week 4

    The bladder pain severity was measured using 0-10 NPRS, with 0 representing 'no pain' and 10 representing 'the worst pain possible'. Participants were asked to select a number on the scale that best described the severity of bladder pain during past 24 hours over telephone using an interactive voice response system (IVRS) every evening at bedtime during the baseline assessment phase and treatment phase (up to 4 weeks). The primary analysis was conducted using a Mixed Model with Repeated Measures (MMRM) approach to calculate the Least Squares (LS) mean change from baseline in NPRS score and associated Standard Error (SE) at Week 4 for each treatment arm. Negative values indicate decrease in bladder pain severity.

    Baseline and Week 4

Secondary Outcomes (3)

  • Change From Baseline in Painful Bladder/Interstitial Cystitis Symptom Diary (PBIC-SD) Score at Week 4

    Baseline and Week 4

  • Change From Baseline in O'Leary-Sant Interstitial Cystitis Symptom Index (ICSI) Score at Week 4

    Baseline and Week 4

  • Change From Baseline in Genitourinary Pain Index (GUPI) Score at Week 4

    Baseline and Week 4

Study Arms (2)

Gefapixant

EXPERIMENTAL

Female participants receive gefapixant, a total dose titrated from 50 mg to highest tolerated dose (maximum of 300 mg) twice daily (BID), orally over a period of 6 days with food depending on safety and tolerability, and then maintain that dose for the course of a 4-week treatment period. Participants were allowed to decrease the dose if tolerability issues occurred.

Drug: Gefapixant

Placebo

PLACEBO COMPARATOR

Female participants receive dose matched placebo tablets, BID, orally, with food for 4 weeks.

Drug: Placebo

Interventions

50 or 300 mg tablets for a total daily dose of 50, 100, 150, 200, 250 or 300 mg BID, orally with food for 4 weeks

Also known as: AF-219, MK-7264
Gefapixant

Dose matched placebo tablets, BID, orally, with food for 4 weeks

Placebo

Eligibility Criteria

Age18 Years - 80 Years
Sexfemale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Women
  • Women of child bearing potential must not be pregnant during the study and must use two forms of birth control
  • Clinical evidence of Interstitial Cystitis /Bladder Pain Syndrome (IC/BPS)
  • Have provided written informed consent

You may not qualify if:

  • History of diseases that can be confused for IC/BPS
  • Unable to void spontaneously
  • Immunosuppressant, intravesicular, nerve stimulator or opioid treatment for certain periods prior to start of the study
  • Changes to doses of Elmiron®, antidepressant, alpha-adrenergic antagonist, H1 antagonist, or anti-muscarinic treatment within a certain period prior to the start of the study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (41)

Afferent Investigative Site

Glendale, Alabama, 85306, United States

Location

Afferent Investigative Site

Homewood, Alabama, 35209, United States

Location

Afferent Investigative Site

Mobile, Alabama, 36608, United States

Location

Afferent Investigative Site

Phoenix, Arizona, 85018, United States

Location

Afferent Investigative Site

Glendora, California, 91741, United States

Location

Afferent Investigative Site

Murrieta, California, 91741, United States

Location

Afferent Investigative Site

San Diego, California, 92120, United States

Location

Afferent Investigative Site

San Diego, California, 92123, United States

Location

Afferent Investigative Site

Farmington, Connecticut, 06032, United States

Location

Afferent Investigative Site

New Britain, Connecticut, 06052, United States

Location

Afferent Investigative Site

Boynton Beach, Florida, 33472, United States

Location

Afferent Investigative Site

Plantation, Florida, 33317, United States

Location

Afferent Investigative Site

Coeur d'Alene, Idaho, 83814, United States

Location

Afferent Investigative Site

Idaho Falls, Idaho, 83404, United States

Location

Afferent Investigative Site

Meridian, Idaho, 83642, United States

Location

Afferent Investigative Site

Shreveport, Louisiana, 71106, United States

Location

Afferent Investigative Site

Annapolis, Maryland, 21401, United States

Location

Afferent Investigative Site

Ann Arbor, Michigan, 48109, United States

Location

Afferent Investigative Site

Grand Rapids, Michigan, 49503, United States

Location

Afferent Investigative Site

Kalamazoo, Michigan, 49009, United States

Location

Afferent Investigative Site

Royal Oak, Michigan, 48073, United States

Location

Afferent Investigative Site

Voorhees Township, New Jersey, 08043, United States

Location

Afferent Investigative Site

Albuquerque, New Mexico, 87109, United States

Location

Afferent Investigative Site

Brooklyn, New York, 11215, United States

Location

Afferent Investigative Site

Hyde Park, New York, 11040, United States

Location

Afferent Investigative Site

Greenville, North Carolina, 27834, United States

Location

Afferent Investigative Site

Salisbury, North Carolina, 28144, United States

Location

Afferent Investigative Site

Winston-Salem, North Carolina, 27103, United States

Location

Afferent Investigative Site

Cincinnati, Ohio, 45212, United States

Location

Afferent Investigative Site

Cleveland, Ohio, 44109, United States

Location

Afferent Investigative Site

Tiffin, Ohio, 43351, United States

Location

Afferent Investigative Site

Zanesville, Ohio, 43701, United States

Location

Afferent Investigative Site

Bala-Cynwyd, Pennsylvania, 19004, United States

Location

Afferent Investigative Site

Lancaster, Pennsylvania, 17604, United States

Location

Afferent Investigative Site

Myrtle Beach, South Carolina, 29572, United States

Location

Afferent Investigative Site

Dallas, Texas, 75390, United States

Location

Afferent Investigative Site

Fort Worth, Texas, 76104, United States

Location

Afferent Investigative Site

Houston, Texas, 77062, United States

Location

Afferent Investigative Site

Irving, Texas, 75062, United States

Location

Afferent Investigative Site

Salt Lake City, Utah, 84124, United States

Location

Afferent Investigative Site

Virginia Beach, Virginia, 23462, United States

Location

Related Publications (1)

  • Imamura M, Scott NW, Wallace SA, Ogah JA, Ford AA, Dubos YA, Brazzelli M. Interventions for treating people with symptoms of bladder pain syndrome: a network meta-analysis. Cochrane Database Syst Rev. 2020 Jul 30;7(7):CD013325. doi: 10.1002/14651858.CD013325.pub2.

MeSH Terms

Conditions

Cystitis, Interstitial

Interventions

Gefapixant

Condition Hierarchy (Ancestors)

CystitisUrinary Bladder DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital Diseases

Results Point of Contact

Title
Senior Vice President, Global Clinical Development
Organization
Merck Sharp & Dohme Corp.

Study Officials

  • Medical Director

    Afferent Pharmaceuticals, Inc., a subsidiary of Merck & Co., Inc. (Rahway, New Jersey USA)

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Masking Details
Double Blind
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 30, 2012

First Posted

April 3, 2012

Study Start

April 13, 2012

Primary Completion

May 1, 2014

Study Completion

May 14, 2014

Last Updated

August 17, 2020

Results First Posted

January 12, 2017

Record last verified: 2020-08

Data Sharing

IPD Sharing
Will share

http://engagezone.msd.com/doc/ProcedureAccessClinicalTrialData.pdf

More information

Locations