NCT01465347

Brief Summary

This open-label study evaluated the safety and efficacy of TSC when dosed concomitantly with the standard of care (radiation therapy and temozolomide) for newly diagnosed glioblastoma in adults. All patients received TSC in the study. The objective of the study was to evaluate the effect of TSC on survival and tumor response in patients with GBM while establishing an acceptable patient risk profile.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
59

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Feb 2012

Longer than P75 for phase_1

Geographic Reach
1 country

18 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 2, 2011

Completed
2 days until next milestone

First Posted

Study publicly available on registry

November 4, 2011

Completed
3 months until next milestone

Study Start

First participant enrolled

February 1, 2012

Completed
3.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2015

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2016

Completed
1.4 years until next milestone

Results Posted

Study results publicly available

July 14, 2017

Completed
Last Updated

July 14, 2017

Status Verified

June 1, 2017

Enrollment Period

3.8 years

First QC Date

November 2, 2011

Results QC Date

October 4, 2016

Last Update Submit

June 16, 2017

Conditions

Keywords

Primary brain tumorGlioblastomaGliomaGBMRadiation therapy

Outcome Measures

Primary Outcomes (2)

  • Dose Limiting Toxicities (DLTs)

    Number of Participants in Phase 1 with Dose Limiting Toxicities (DLTs)

    During phase 1

  • Overall Survival

    Participants in phase 2 (18 dose group, 6 weeks treatment with TSC) were monitored for up to 3 years (last follow-up - February 16, 2016). Overall Survival (OS) was defined as the length of time from the date of tumor resection surgery or definitive biopsy to the date of death. The OS analyses were performed using the Kaplan-Meier estimate method. The OS rates at 6, 12, 18 and 24 months were estimated. Median OS values were calculated; a corresponding 95% confidence interval for each median value was determined using a log rank analysis. The length of OS (in months) was calculated as follows: date of death or censored - date of surgery or definitive biopsy / 30.4375.

    6, 12, 18, 24 months

Secondary Outcomes (2)

  • Progression-Free Survival (PFS)

    6,12,18, 24 months

  • Number of Participants With Reduction in Tumor Size, According to Percentage of Tumor Reduction

    From Baseline to Week 110

Study Arms (1)

TSC 0.25 mg/kg for 9 or 18 doses

EXPERIMENTAL

This was an open-label, sequential-cohort, dose-escalation study in two phases. Phase 1 was a safety run-in evaluating Trans Sodium Crocetinate (TSC) in 3 subjects who received 3 doses per week for 3 weeks (9 doses in total). Phase 2 engaged 56 subjects who received 3 doses per week for 6 weeks (18 doses in total). TSC was consistently dosed at 0.25mg/kg in both phases.

Drug: Trans Sodium Crocetinate (TSC)

Interventions

TSC administered intravenously as a bolus injection prior to radiation therapy sessions during 6 weeks of radiotherapy.

Also known as: TSC
TSC 0.25 mg/kg for 9 or 18 doses

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Aged at least 18 years of age; male or female. A patient who is 70 years of age or older may be considered for enrollment after review of patient clinical and laboratory data by the Protocol Medical Monitor.
  • Histologically confirmed diagnosis of GBM.
  • Contrast enhancing disease on MRI within 21 days prior to screening.
  • Karnofsky score (KPS) of ≥ 60 at Screening.
  • No prior RT, chemotherapy (including Gliadel wafer), immunotherapy or therapy with a biologic agent, or hormonal therapy. Glucocorticoid therapy is allowed.
  • Within 2 weeks of baseline visit, hematologic and renal functions as specified: Absolute neutrophil count ≥ 1500/mm3, platelets ≥ 100,000/mm3, Hgb ≥ 9.0g/dL, creatinine ≤ 1.7mg/dl, total bilirubin ≤ 1.5mg/dL, blood urea nitrogen (BUN) within 2 times the upper limit of normal, transaminases ≤ 4 times above the upper limits of the institutional norm.
  • Sexually active patients must use an acceptable method of contraception while receiving doses of study medication.
  • Females of childbearing potential must have a negative serum or urine pregnancy test at screening and have additional pregnancy tests during study.

You may not qualify if:

  • Patient who cannot undergo MRI.
  • Pregnant or lactating.
  • Serious concurrent infection or medical illness that would jeopardize the ability of the patient to receive study treatment with reasonable safety.
  • Patient receiving concurrent chemotherapeutics or investigational agents within 30 days of baseline assessments, including gliadel wafers or gliasite application.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (18)

St. Joseph's Medical Center Barrow Neurology Clinics

Phoenix, Arizona, 85013, United States

Location

University of Arkansas Winthrop P. Rockefeller Cancer Institute

Little Rock, Arkansas, 72205, United States

Location

USC/Norris Comprehensive Cancer Center

Los Angeles, California, 90033, United States

Location

Cedars-Sinai Medical Center

Los Angeles, California, 90048, United States

Location

The George Washington University Medical Center

Washington D.C., District of Columbia, 20037, United States

Location

University of Florida McKnight Brain Institute

Gainesville, Florida, 32611, United States

Location

Emory University Winship Cancer Institute

Atlanta, Georgia, 30322, United States

Location

Northwestern University Robert H. Lurie Comprehensive Cancer Center

Chicago, Illinois, 60611, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

University of Kentucky Markey Cancer Center

Lexington, Kentucky, 40536, United States

Location

North Shore University Hospital

Manhasset, New York, 11030, United States

Location

Forsyth Regional Cancer Center

Winston-Salem, North Carolina, 27103, United States

Location

Penn State University Milton S. Hershey Medical Center

Hershey, Pennsylvania, 17033, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

Baylor University Medical Center

Dallas, Texas, 75246, United States

Location

University of Texas Health Science Center Memorial Hermann Medical Center

Houston, Texas, 77030, United States

Location

UVA Health Sciences Center Emily Couric Clinical Cancer Center

Charlottesville, Virginia, 22908, United States

Location

Froedtert & Medical College of Wisconsin Cancer Center

Milwaukee, Wisconsin, 53226, United States

Location

Related Publications (2)

  • Stupp R, Mason WP, van den Bent MJ, Weller M, Fisher B, Taphoorn MJ, Belanger K, Brandes AA, Marosi C, Bogdahn U, Curschmann J, Janzer RC, Ludwin SK, Gorlia T, Allgeier A, Lacombe D, Cairncross JG, Eisenhauer E, Mirimanoff RO; European Organisation for Research and Treatment of Cancer Brain Tumor and Radiotherapy Groups; National Cancer Institute of Canada Clinical Trials Group. Radiotherapy plus concomitant and adjuvant temozolomide for glioblastoma. N Engl J Med. 2005 Mar 10;352(10):987-96. doi: 10.1056/NEJMoa043330.

  • Gainer JL, Sheehan JP, Larner JM, Jones DR. Trans sodium crocetinate with temozolomide and radiation therapy for glioblastoma multiforme. J Neurosurg. 2017 Feb;126(2):460-466. doi: 10.3171/2016.3.JNS152693. Epub 2016 May 13.

MeSH Terms

Conditions

GlioblastomaGliomaBrain Neoplasms

Interventions

trans-sodium crocetinate

Condition Hierarchy (Ancestors)

AstrocytomaNeoplasms, NeuroepithelialNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Glandular and EpithelialNeoplasms, Nerve TissueCentral Nervous System NeoplasmsNervous System NeoplasmsNeoplasms by SiteBrain DiseasesCentral Nervous System DiseasesNervous System Diseases

Results Point of Contact

Title
Chief Executive Officer
Organization
Diffusion Pharmaceuticals Inc

Study Officials

  • David R. Jones, M.D.

    Diffusion Pharmaceuticals Inc

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 2, 2011

First Posted

November 4, 2011

Study Start

February 1, 2012

Primary Completion

November 1, 2015

Study Completion

February 1, 2016

Last Updated

July 14, 2017

Results First Posted

July 14, 2017

Record last verified: 2017-06

Data Sharing

IPD Sharing
Will not share

Locations