NCT01394939

Brief Summary

The purpose of this study is to evaluate the safety, tolerability, and efficacy of JX-594 (Pexa-Vec) administered intravenously either alone or in combination with Irinotecan in colorectal carcinoma patients who are refractory to or intolerant to standard therapy.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
52

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Jan 2012

Typical duration for phase_1

Geographic Reach
3 countries

11 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 13, 2011

Completed
2 days until next milestone

First Posted

Study publicly available on registry

July 15, 2011

Completed
6 months until next milestone

Study Start

First participant enrolled

January 1, 2012

Completed
3.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2015

Completed
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2015

Completed
5.3 years until next milestone

Results Posted

Study results publicly available

January 8, 2021

Completed
Last Updated

January 8, 2021

Status Verified

December 1, 2020

Enrollment Period

3.4 years

First QC Date

July 13, 2011

Results QC Date

September 14, 2020

Last Update Submit

December 11, 2020

Conditions

Keywords

VacciniaVaccinia VirusJX-594JennerexColorectal CarcinomaColorectal cancerColon CancerRectal Canceroncolytic virusviral therapyRAS mutantErbitux failureOxaliplatin failureFOLFOX failureFOLFIRI failureIrinotecan failurePexa-Vec

Outcome Measures

Primary Outcomes (1)

  • Determine Radiographic Response Rate of Patients Enrolled in the Phase 2a Portion of the Study

    Percentage of participants who showed overall response during their participation in the study. Per Modified Response Evaluation Criteria In Solid Tumors Criteria (mRECIST) and assessed by tri-phasic contrast enhanced CT: Complete Response (CR), Disappearance of intratumoral enhancing area; Partial Response (PR), \>=30% decrease in the sum of the diameters of enhancing area; Overall Response (OR) = CR + PR.

    Scans Every 8 weeks until radiographic progression was confirmed by the site.

Study Arms (4)

Single Agent_ Cohort 1

EXPERIMENTAL

JX-594 administered intravenously weekly for 5 weeks followed by up to 3 additional intravenous infusion boosts. JX-594: Recombinant Vaccinia Granulocyte-Macrophage Colony-Stimulating Factor (RAC VAC GM-CSF) Cohort 1: JX-594 3 x 10\^8 plaque forming unit (pfu), Days 1, 8,15, 22, and 29

Biological: JX-594

Single Agent_Cohort 2

EXPERIMENTAL

JX-594 administered intravenously weekly for 5 weeks followed by up to 3 additional intravenous infusion boosts. JX-594: RAC VAC GM-CSF Cohort 2: JX-594 1 x 10\^9 pfu, Days 1, 8,15, 22, and 29

Biological: JX-594

Combination_Cohort 3

EXPERIMENTAL

JX-594 administered intravenously weekly for 5 weeks followed by up to three additional intravenous infusion boosts in combination with Irinotecan administered every 14 days beginning at Day 9. JX-594: RAC VAC GM-CSF Irinotecan: 180 mg/m2 IV every 2 weeks. JX-594 3 x 10\^8 pfu Day 1,8, 15, 22, 29 + irinotecan 180 mg/m2 biweekly starts on Day 9.

Biological: JX-594Drug: Irinotecan

Combination_Cohort 4

EXPERIMENTAL

JX-594 administered intravenously weekly for 5 weeks followed by up to three additional intravenous infusion boosts in combination with Irinotecan administered every 14 days beginning at Day 9. JX-594: RAC VAC GM-CSF JX-594 1 x 10\^9 pfu Day1, 8, 15, 22, 29 + irinotecan 180 mg/m2 biweekly starts on Day 9.

Biological: JX-594Drug: Irinotecan

Interventions

JX-594BIOLOGICAL

Recombinant Vaccinia GM-CSF; RAC VAC GM-CSF (JX-594)

Combination_Cohort 3Combination_Cohort 4Single Agent_ Cohort 1Single Agent_Cohort 2

180 mg/m2 IV every 2 weeks.

Combination_Cohort 3Combination_Cohort 4

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically-confirmed, advanced metastatic colorectal cancer failed treatment with fluoropyrimidine (fluoruracil or capecitabine) and oxaliplatin based therapies or had contradictions to treatment with these drugs as determined by the investigator
  • Failed treatment with irinotecan
  • Kras mutant tumor or Kras wild-type having failed cetuximab (Erbitux) or panitumumab (Vectibix) or had contradictions to treatment
  • Regorafenib-naïve (have not received regorafenib)
  • Eastern Cooperative Oncology Group (ECOG) Performance Status 0, 1 or 2
  • Measurable tumor (≥1 cm longest diameter)
  • Acceptable health status as determined by the investigator and blood work (Chemistry, Complete Blood Count, Coagulation)

You may not qualify if:

  • Intolerant to Irinotecan (if assigned to the combination arm: Cohort 3, Cohort 4 or Combination Expansion Arm)
  • Treatment with ketoconazole, enzyme-inducing anticonvulsants and St. John's Wort (if assigned to combination arm)
  • Significant immunodeficiency due to underlying illness and/or medication
  • History of severe exfoliative skin condition requiring systemic therapy within the past 2 years
  • Clinically significant and/or rapidly accumulating ascites, pericardial and/or pleural effusions
  • Active cardiovascular disease, including but not limited to significant coronary artery disease (e.g., requiring angioplasty or stenting) or congestive heart failure within the preceding 12 months
  • Viable Centrual Nervous System (CNS) malignancy associated with clinical symptoms
  • Received anti-cancer therapy within 4 weeks prior to first treatment (6 weeks for mitomycin c or nitrosoureas)
  • Prior participation in any other research protocol involving an investigational medicinal product within 4 weeks prior to first treatment
  • Use of prohibited anti-viral medication, interferon/pegylated interferon (PEG-IFN) or ribavirin that cannot be discontinued within 14 days prior to any JX 594 dose
  • Inability to suspend treatment with anti-hypertensive medication for 48 hours prior to and 48 hours after all JX-594 treatments.
  • Pregnant or nursing an infant
  • Diagnosis of chronic inflammatory bowel disease and/or bowel obstruction.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (11)

Mayo Clinic

Scottsdale, Arizona, 85259-5499, United States

Location

UCSD Moores Cancer Center

La Jolla, California, 92093, United States

Location

Billings Clinic Cancer Center

Billings, Montana, 59101, United States

Location

University of North Carolina

Chapel Hill, North Carolina, 27599-1651, United States

Location

Gabrail Cancer Center

Canton, Ohio, 44718, United States

Location

The Ohio State University

Columbus, Ohio, 43210, United States

Location

Juravinski Cancer Centre

Hamilton, Ontario, L8V 5C2, Canada

Location

Ottawa Hospital and Research Institute (OHRI)

Ottawa, Ontario, K1H 8L6, Canada

Location

Hôpital Saint Antoine

Paris, 75012, France

Location

Hôpital Hautepierre

Strasbourg, 67200, France

Location

Institut Claudius Regaud

Toulouse, 31052, France

Location

MeSH Terms

Conditions

Colorectal NeoplasmsVacciniaColonic NeoplasmsRectal Neoplasms

Interventions

Irinotecan

Condition Hierarchy (Ancestors)

Intestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal DiseasesPoxviridae InfectionsDNA Virus InfectionsVirus DiseasesInfections

Intervention Hierarchy (Ancestors)

CamptothecinAlkaloidsHeterocyclic Compounds

Results Point of Contact

Title
Kyoung Soo Ha, Head of Clinical Development
Organization
Sillajen Biotherapeutics Inc.

Study Officials

  • James Burke, MD

    Jennerex Biotherapeutics

    STUDY DIRECTOR
  • Derek Jonker, MD

    Ottawa Hospital and Research Institute

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 13, 2011

First Posted

July 15, 2011

Study Start

January 1, 2012

Primary Completion

June 1, 2015

Study Completion

October 1, 2015

Last Updated

January 8, 2021

Results First Posted

January 8, 2021

Record last verified: 2020-12

Locations