NCT01327885

Brief Summary

This is a randomized, open-label, multicenter, Phase 3 study comparing the efficacy and safety of eribulin with dacarbazine in subjects with advanced soft tissue sarcoma who have disease progression within 6 months prior to study enrolment following standard therapies which must have included an anthracycline, unless contraindicated and then at least one additional regimen after failure of the anthracycline.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
452

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Mar 2011

Longer than P75 for phase_3

Geographic Reach
22 countries

116 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

March 10, 2011

Completed
21 days until next milestone

First Submitted

Initial submission to the registry

March 31, 2011

Completed
4 days until next milestone

First Posted

Study publicly available on registry

April 4, 2011

Completed
3.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 2, 2015

Completed
1.6 years until next milestone

Study Completion

Last participant's last visit for all outcomes

August 10, 2016

Completed
7 months until next milestone

Results Posted

Study results publicly available

February 28, 2017

Completed
Last Updated

June 22, 2023

Status Verified

February 1, 2018

Enrollment Period

3.8 years

First QC Date

March 31, 2011

Results QC Date

January 6, 2017

Last Update Submit

June 16, 2023

Conditions

Outcome Measures

Primary Outcomes (1)

  • Overall Survival (OS)

    OS was defined as the time in months from the date of treatment start until death, regardless of cause. In the absence of confirmation of death, participants were censored either at the date that participant was last known to be alive or the date of study cut-off, whichever was earlier. Participants who died on the date of randomization had a survival time of 0.5 day. Allocation of randomization numbers were performed based upon the following stratification factors: (a) Histology (adipocytic \[ADI\] or leiomyosarcoma \[LMS\]), (b) Region (Region 1: USA and Canada; or Region 2: Western Europe, Australia, Israel; or Region 3: Eastern Europe, Latin America, and Asia), and (c) Number of prior regimens for advanced soft tissue sarcoma (STS) (2 or greater than \[\>\] 2 prior regimens).

    From date of treatment start until date of death from any cause, up to 5 years 5 months

Secondary Outcomes (3)

  • Progression-Free Survival (PFS)

    Randomization (day 1) to the date of first documentation of disease progression, or date of death (whichever occurred first), up to 5 years 5 months

  • Progression-Free Rate at 12 Weeks (PFR12wks)

    From date of randomization start until Week 12

  • Clinical Benefit Rate (CBR)

    From date of treatment start (Day 1) until disease progression, development of unacceptable toxicity, withdrawal of consent, participant's choice to stop study treatment, up to 5 years 5 months

Study Arms (2)

Arm A

EXPERIMENTAL
Drug: Eribulin mesylate 1.4 mg/m^2 intravenous

Arm B

ACTIVE COMPARATOR
Drug: Dacarbazine of 850 mg/m^2, or 1,000 mg/m^2, or 1,200 mg/m^2 IV

Interventions

Administration of eribulin mesylate at a dose of 1.4 mg/m\^2 as an intravenous (IV) bolus infusion over 2-5 minutes on Days 1 and 8 of every cycle, where the duration of each cycle is 21 days.

Arm A

Administration of dacarbazine at a dose of 850 mg/m\^2, or 1,000 mg/m\^2, or 1,200 mg/m\^2 selected by the Principal Investigator \[PI\] or designee according to the subject's clinical status as an IV infusion over 15-30 minutes on Day 1 of every cycle, where the duration of each cycle is 21 days.

Arm B

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically confirmed diagnosis of soft tissue sarcoma of high or intermediate grade with one of the following histological subtypes:
  • Adipocytic sarcoma, including:
  • Dedifferentiated
  • Myxoid
  • Round Cell
  • Pleomorphic - Leiomyosarcoma
  • Subjects should have received at least two standard systematic regimens for advanced soft tissue sarcoma one of which must have included an anthracycline (unless contraindicated).
  • Radiographic evidence of disease progression by RECIST criteria on or after the last anti-cancer therapy within the 6 months prior to randomization.
  • Presence of measurable disease meeting the following criteria:
  • At least one lesion of greater than or equal to 1.0 cm in long-axis diameter for non lymph nodes or greater than or equal to 1.5 cm in short-axis diameter for lymph nodes which is serially measurable according to RECIST 1.1 using either computerized tomography or magnetic resonance imaging or panoramic and close-up color photography.
  • Lesions that have had radiotherapy must show evidence of progressive disease based on RECIST 1.1 to be deemed a target lesion.
  • Eastern Cooperative Oncology Group, performance status of 0, 1 or 2.
  • Adequate renal function defined as calculated creatinine clearance greater than 50 mL/min per the Cockroft and Gault formula.
  • Adequate bone marrow function, defined as:
  • Absolute neutrophil count (ANC) greater than or equal to 1,500/mm3 or greater than or equal to 1.5 x 10\^9/L.
  • +13 more criteria

You may not qualify if:

  • Subjects who have received any anti-cancer therapy, including radiotherapy, cytotoxic, hormonal, biological (including humanized antibodies) and targeted agents within 21 days, or five half-lives of the drug (whichever is longer) prior to randomization.
  • Subjects that have previously been treated with dacarbazine or its analogue temozolomide or eribulin.
  • Major surgery within 21 days prior to randomization.
  • Pre-existing peripheral neuropathy greater than CTCAE Grade 2.
  • Significant cardiovascular impairment, defined as:
  • Cardiac failure, New York Heart Association (NYHA) Class II according to the NYHA Functional Classification,
  • Unstable angina or myocardial infarction within 6 months of enrolment,
  • Serious and potentially life-threatening arrhythmia.
  • Subjects with a high probability of Long QT Syndrome or QTc interval prolongation of more than or equal to 501 msec on at least two separate ECGs, following correction of any electrolyte imbalance.
  • Subjects with known central nervous system metastases.
  • Any serious concomitant illness or infectious disease requiring treatment, or infectious disease not requiring treatment, but with significant risks for myelosuppressive complications associated with chemotherapy.
  • Any malignancy that required treatment, or has shown evidence of recurrence (except for soft tissue sarcoma, non-melanoma skin cancer, or histologically confirmed complete excision of carcinoma in situ) during the 5 years prior to randomization.
  • Female subjects must not be pregnant as documented by a negative beta-human chorionic gonadotropin (beta-hCG) test with a minimum sensitivity 25 IU/L or equivalent unit of beta-hCG at Screening and Baseline, or breastfeeding.
  • Hypersensitivity to the active substance, or any of the excipients of the eribulin drug product, or dacarbazine, (please refer to the dacarbazine prescribing information).
  • Any medical or other condition which, in the opinion of the PI or designee, will preclude participation in a clinical trial.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (119)

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Tucson, Arizona, United States

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Los Angeles, California, United States

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Orange, California, United States

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Santa Monica, California, United States

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Stanford, California, United States

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Aurora, Colorado, United States

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Denver, Colorado, United States

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Newark, Delaware, United States

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Washington D.C., District of Columbia, United States

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Tampa, Florida, United States

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Atlanta, Georgia, United States

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Post Falls, Idaho, United States

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Chicago, Illinois, United States

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Park Ridge, Illinois, United States

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Urbana, Illinois, United States

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Iowa City, Iowa, United States

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Boston, Massachusetts, United States

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St Louis, Missouri, United States

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Newark, New Jersey, United States

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Buffalo, New York, United States

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New York, New York, United States

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Rochester, New York, United States

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Durham, North Carolina, United States

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Cleveland, Ohio, United States

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Portland, Oregon, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Houston, Texas, United States

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Burlington, Vermont, United States

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Seattle, Washington, United States

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Ciudad de Buenos Aires, Argentina

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San Miguel de Tucumán, Argentina

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San Salvador de Jujuy, Argentina

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Camperdown, New South Wales, Australia

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St Leonards, New South Wales, Australia

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Woolloongabba, Queensland, Australia

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Woodville South, South Australia, Australia

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Nedlands, Western Australia, Australia

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Graz, Austria

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Salzburg, Austria

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Vienna, Austria

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Brussels, Belgium

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Leuven, Belgium

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Liège, Belgium

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Porto Alegre, Rio Grande do Sul, Brazil

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Florianópolis, Santa Catarina, Brazil

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Barretos, Brazil

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Curitiba, Brazil

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Jaú, Brazil

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Porto Alegre, Brazil

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Salvador, Brazil

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São Paulo, Brazil

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Ottawa, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Brno, Czechia

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Hradec Králové, Czechia

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Nový Jičín, Czechia

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Prague, Czechia

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Herlev, Denmark

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Angers, France

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Bordeaux, France

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Lyon, France

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Marseille, France

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Nantes, France

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Paris, France

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Poitiers, France

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Saint-Priest-en-Jarez, France

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Villejuif, France

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Berlin, Germany

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Cologne, Germany

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Dresden, Germany

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Essen, Germany

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Hanover, Germany

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Mannheim, Germany

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Tübingen, Germany

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Haifa, Israel

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Jerusalem, Israel

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Ramat Gan, Israel

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Tel Aviv, Israel

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Aviano, Pordenone, Italy

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Candiolo, Italy

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Milan, Italy

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Monza, Italy

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Padua, Italy

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Rozzano (MI), Italy

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Torino, Italy

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Amsterdam, Netherlands

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Leiden, Netherlands

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Christchurch, New Zealand

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Gdansk, Poland

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Gliwice, Poland

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Warsaw, Poland

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Cluj-Napoca, Romania

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Craiova, Romania

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Iași, Romania

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Sibiu, Romania

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Chelyabinsk, Russia

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Kazan', Russia

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Moscow, Russia

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Obninsk, Russia

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Singapore, Singapore

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Daejeon, South Korea

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Seongnam, South Korea

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Seoul, South Korea

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Palma de Mallorca, Balearic Islands, Spain

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Badalona, Catalonia, Spain

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L'Hospitalet de Llobregat, Catalonia, Spain

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Madrid, Madrid, Spain

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Barcelona, Spain

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Valencia, Spain

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Hat Yai, Changwat Songkhla, Thailand

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Bangkok, Thailand

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Chiang Mai, Thailand

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Pathum Wan, Thailand

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Glasgow, United Kingdom

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London, United Kingdom

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Manchester, United Kingdom

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Swansea, United Kingdom

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Related Publications (1)

  • Schoffski P, Chawla S, Maki RG, Italiano A, Gelderblom H, Choy E, Grignani G, Camargo V, Bauer S, Rha SY, Blay JY, Hohenberger P, D'Adamo D, Guo M, Chmielowski B, Le Cesne A, Demetri GD, Patel SR. Eribulin versus dacarbazine in previously treated patients with advanced liposarcoma or leiomyosarcoma: a randomised, open-label, multicentre, phase 3 trial. Lancet. 2016 Apr 16;387(10028):1629-37. doi: 10.1016/S0140-6736(15)01283-0. Epub 2016 Feb 10.

MeSH Terms

Conditions

Sarcoma

Interventions

eribulin

Condition Hierarchy (Ancestors)

Neoplasms, Connective and Soft TissueNeoplasms by Histologic TypeNeoplasms

Results Point of Contact

Title
Eisai Medical Information
Organization
Eisai Inc.

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 31, 2011

First Posted

April 4, 2011

Study Start

March 10, 2011

Primary Completion

January 2, 2015

Study Completion

August 10, 2016

Last Updated

June 22, 2023

Results First Posted

February 28, 2017

Record last verified: 2018-02

Locations