NCT00876031

Brief Summary

The purpose of this study is to investigate whether the addition of oral maintenance chemotherapy with O-TIE (Etoposide, Idarubicin, Trofosfamide) for 6 months improves the event free survival (EFS) in patients with localised high-risk RMS and RMS-like Soft Tissue Sarcoma.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
195

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Jul 2009

Longer than P75 for phase_3

Geographic Reach
5 countries

87 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 2, 2009

Completed
4 days until next milestone

First Posted

Study publicly available on registry

April 6, 2009

Completed
3 months until next milestone

Study Start

First participant enrolled

July 1, 2009

Completed
13 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 30, 2022

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 30, 2022

Completed
Last Updated

November 8, 2022

Status Verified

November 1, 2022

Enrollment Period

13 years

First QC Date

April 2, 2009

Last Update Submit

November 3, 2022

Conditions

Keywords

pediatric soft tissue sarcomarhabdomyosarcomaextraosseous Ewing family tumourssynovial sarcomaundifferentiated sarcoma

Outcome Measures

Primary Outcomes (1)

  • event free survival (EFS)

    3 years

Secondary Outcomes (1)

  • Overall survival

    5 years

Study Arms (2)

O-TIE

EXPERIMENTAL

oral maintenance therapy with trofosfamide, idarubicin, and etoposide

Drug: trofosfamide, idarubicin, etoposide

control

NO INTERVENTION

Interventions

oral maintenance therapy for 6 months

O-TIE

Eligibility Criteria

Age6 Months - 21 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • written informed consent for registration, randomisation, data collection/transfer, and tumour material asservation available
  • pathologically (including molecular pathology) proven diagnosis of rhabdomyosarcoma (RMS) or RMS-like soft tissue sarcoma (STS) and tumour material available for pathology review
  • Rhabdomyosarcoma of the "High Risk" Group, i.e.:
  • RME, N0, M0, IRS II\&III, \>5 cm or \>10 years in EXT, HN-PM, OTH, UG-BP
  • RME, N1, M0, any IRS-group, any size or age
  • RMA, NO, M0, any IRS-group, any size or age (exception: paratesticular RMA are not eligible) or
  • Rhabdomyosarcoma of the "Very High Risk" Group, i.e.:
  • RMA, N1, MO, IRS II\&III, any size or age or
  • localised high-risk RMS-like Soft Tissue Sarcoma, i.e.:
  • EES, pPNET, UDS: any N, M0, any IRS-group, any size or age
  • SySa, any N, M0, any size or age (exception: SySa IRSI\&II, not T2b, N0, M0 are not eligible)
  • no pre-existing illness preventing treatment (esp. those listed in the medicinal product information, e.g. cardiac, hepatic, metabolic, or renal dysfunction; hypersensitivity)
  • no previous malignant tumours
  • available for long term follow up through the treating centre
  • in remission (according to the CWS-2007-HR definition (see X7.1.8X)) at the time of randomisation after standard multimodal therapy e.g. according to the CWS-guidance

You may not qualify if:

  • pregnant or lactating women
  • other medical condition precluding treatment with protocol therapy (e.g. HIV, psychiatric disorder, etc.)
  • for sexually active females and males in Arm B (O-TIE treatment): refusal to use effective contraception (e.g. oral, IUD)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (87)

Krankenhaus der Stadt Dornbirn

Dornbirn, Austria

Location

Universitätsklinik für Kinder- und Jugendheilkunde

Graz, Austria

Location

Universitätsklinik für Kinder- und Jugendheilkunde

Innsbruck, Austria

Location

Landeskrankenhaus

Klagenfurt, Austria

Location

Landeskrankenhaus

Leoben, Austria

Location

Landesfrauen - und Kinderklinik Linz

Linz, Austria

Location

St. Johanns Spital / Landeskrankenhaus

Salzburg, Austria

Location

St. Anna Kinderspital

Vienna, Austria

Location

Universitätsklinikum

Aachen, Germany

Location

Klinikum Augsburg

Augsburg, Germany

Location

Charité

Berlin, Germany

Location

Helios Klinikum Berlin-Buch

Berlin, Germany

Location

Krankenhaus Bielefeld

Bielefeld, Germany

Location

Universitätskinderklinik

Bonn, Germany

Location

Klinikum Braunschweig

Braunschweig, Germany

Location

Prof. Hess Kinderklinik

Bremen, Germany

Location

Klinikum Chemnitz

Chemnitz, Germany

Location

Kliniken der Stadt Köln

Cologne, Germany

Location

Universitätsklinikum

Cologne, Germany

Location

Vestische Kinderklinik

Datteln, Germany

Location

Westfälisches Kinderzentrum, Klinikum Dortmund

Dortmund, Germany

Location

Universitätsklinikum

Dresden, Germany

Location

Universitätskinderklinik

Düsseldorf, Germany

Location

Helios Klinikum

Erfurt, Germany

Location

Universitätsklinikum

Erlangen, Germany

Location

Universitätsklinikum

Essen, Germany

Location

Universitätsklinikum

Frankfurt, Germany

Location

Universitätsklinikum

Freiburg im Breisgau, Germany

Location

Universitätsklinikum

Giessen, Germany

Location

Universitätsklinikum

Göttingen, Germany

Location

Universitätsklinikum

Greifswald, Germany

Location

Universitätsklinikum

Halle, Germany

Location

Universitätsklinikum

Hamburg, Germany

Location

Medizinische Hochschule

Hanover, Germany

Location

Universitätsklinikum

Heidelberg, Germany

Location

Gemeinschaftskrankenhaus Herdecke

Herdecke, Germany

Location

Universitätsklinikum

Homburg, Germany

Location

Universitätsklinikum

Jena, Germany

Location

Städtisches Klinikum Karlsruhe

Karlsruhe, Germany

Location

Klinikum Kassel

Kassel, Germany

Location

Universitätsklinikum

Kiel, Germany

Location

Gemeinschaftsklinikum Mayen-Koblenz

Koblenz, Germany

Location

Universitätsklinikum

Leipzig, Germany

Location

Universitätsklinikum

Lübeck, Germany

Location

Universitätsklinikum

Magdeburg, Germany

Location

Universitätsklinikum

Mainz, Germany

Location

Universitätsklinikum

Mannheim, Germany

Location

Klinikum Minden

Minden, Germany

Location

Dr. von Haunersches Kinderspital

München, Germany

Location

Krankenhaus München Schwabing

München, Germany

Location

Universitätsklinikum

Münster, Germany

Location

Cnopf'sche Kinderklinik

Nuremberg, Germany

Location

Klinikum Oldenburg

Oldenburg, Germany

Location

Universitätsklinikum

Regensburg, Germany

Location

Universitätsklinikum

Rostock, Germany

Location

Asklepios Kinderklinik

Sankt Augustin, Germany

Location

Helios Kliniken Schwerin

Schwerin, Germany

Location

Olgahospital

Stuttgart, Germany

Location

Mutterhaus der Borromäerinnen

Trier, Germany

Location

Universitätsklinikum

Tübingen, Germany

Location

Universitätsklinikum

Ulm, Germany

Location

Universitätsklinikum

Würzburg, Germany

Location

Medical University

Bialystok, Poland

Location

Collegium Medicum

Bydgoszcz, Poland

Location

Medical Academy

Gdansk, Poland

Location

Silesian Medical Academy

Katowice, Poland

Location

Polish-American Institute of Paediatrics Jagiellonian University Medical College

Krakow, Poland

Location

Medical Academy

Lodz, Poland

Location

Medical Academy

Lublin, Poland

Location

Pian Medical University

Szczecin, Poland

Location

Department of Surgical Oncology for Children and Youth

Warsaw, Poland

Location

Medical University

Wroclaw, Poland

Location

Sahlgrenska University Hospital, The Queen Siliva Childrens Hospital

Gothenburg, Sweden

Location

University Hospital, Dept. of Pediatrics

Linköping, Sweden

Location

University Hospital, Dept. of Pediatric Hematology and Oncology

Lund, Sweden

Location

Karolinska University Hospital, Astrid Lindgrens Children's Hospital

Stockholm, Sweden

Location

Norrland's University Hospital, Dept. of Pediatrics

Umeå, Sweden

Location

Children's University Hospital

Uppsala, Sweden

Location

Kantonsspital

Aarau, Switzerland

Location

Universitätskinderklinik beider Basel

Basel, Switzerland

Location

Ospedale San Giovanni

Bellinzona, Switzerland

Location

Inselspital University hospital

Bern, Switzerland

Location

Hopital Cantonal de Geneve

Geneva, Switzerland

Location

CHUV

Lausanne, Switzerland

Location

Kinderspital

Lucerne, Switzerland

Location

Ostschweizer Kinderspital

Sankt Gallen, Switzerland

Location

University Children's Hospital

Zurich, Switzerland

Location

Related Publications (9)

  • Dantonello TM, Int-Veen C, Harms D, Leuschner I, Schmidt BF, Herbst M, Juergens H, Scheel-Walter HG, Bielack SS, Klingebiel T, Dickerhoff R, Kirsch S, Brecht I, Schmelzle R, Greulich M, Gadner H, Greiner J, Marky I, Treuner J, Koscielniak E. Cooperative trial CWS-91 for localized soft tissue sarcoma in children, adolescents, and young adults. J Clin Oncol. 2009 Mar 20;27(9):1446-55. doi: 10.1200/JCO.2007.15.0466. Epub 2009 Feb 17.

    PMID: 19224858BACKGROUND
  • Mattke AC, Bailey EJ, Schuck A, Dantonello T, Leuschner I, Klingebiel T, Treuner J, Koscielniak E. Does the time-point of relapse influence outcome in pediatric rhabdomyosarcomas? Pediatr Blood Cancer. 2009 Jul;52(7):772-6. doi: 10.1002/pbc.21906.

    PMID: 19165889BACKGROUND
  • Dantonello TM, Int-Veen C, Winkler P, Leuschner I, Schuck A, Schmidt BF, Lochbuehler H, Kirsch S, Hallmen E, Veit-Friedrich I, Bielack SS, Niggli F, Kazanowska B, Ladenstein R, Wiebe T, Klingebiel T, Treuner J, Koscielniak E. Initial patient characteristics can predict pattern and risk of relapse in localized rhabdomyosarcoma. J Clin Oncol. 2008 Jan 20;26(3):406-13. doi: 10.1200/JCO.2007.12.2382.

    PMID: 18202417BACKGROUND
  • Weihkopf T, Blettner M, Dantonello T, Jung I, Klingebiel T, Koscielniak E, Luckel M, Spix C, Kaatsch P. Incidence and time trends of soft tissue sarcomas in German children 1985-2004 - a report from the population-based German Childhood Cancer Registry. Eur J Cancer. 2008 Feb;44(3):432-40. doi: 10.1016/j.ejca.2007.11.013.

    PMID: 18077150BACKGROUND
  • Koscielniak E, Morgan M, Treuner J. Soft tissue sarcoma in children: prognosis and management. Paediatr Drugs. 2002;4(1):21-8. doi: 10.2165/00128072-200204010-00003.

    PMID: 11817983BACKGROUND
  • Dantonello TM, Winkler P, Boelling T, Friedel G, Schmid I, Mattke AC, Ljungman G, Bielack SS, Klingebiel T, Koscielniak E; CWS Study Group. Embryonal rhabdomyosarcoma with metastases confined to the lungs: report from the CWS Study Group. Pediatr Blood Cancer. 2011 May;56(5):725-32. doi: 10.1002/pbc.22862. Epub 2010 Nov 8.

    PMID: 21370403BACKGROUND
  • Siepermann M, Koscielniak E, Dantonello T, Klee D, Boos J, Krefeld B, Borkhardt A, Hoehn T, Asea A, Wessalowski R. Oral low-dose chemotherapy: successful treatment of an alveolar rhabdomyosarcoma during pregnancy. Pediatr Blood Cancer. 2012 Jan;58(1):104-6. doi: 10.1002/pbc.22934. Epub 2011 Jan 16.

    PMID: 22076833BACKGROUND
  • Klingebiel T, Boos J, Beske F, Hallmen E, Int-Veen C, Dantonello T, Treuner J, Gadner H, Marky I, Kazanowska B, Koscielniak E. Treatment of children with metastatic soft tissue sarcoma with oral maintenance compared to high dose chemotherapy: report of the HD CWS-96 trial. Pediatr Blood Cancer. 2008 Apr;50(4):739-45. doi: 10.1002/pbc.21494.

  • Koscielniak E, Ljungman G, Kazanowska B, Niggli F, Sparber-Sauer M, Handgretinger R, Zimmermann M, Boos J, Blank B, Hallmen E, Teichert von Luttichau I, Schmid I, Frohlich B, Muller HL, Behnisch W, Ladenstein R, Scheer M, Vokuhl C, von Kalle T, Blattmann C, Bielack S, Klingebiel T. Maintenance therapy with trofosfamide, idarubicin and etoposide in patients with rhabdomyosarcoma and other high-risk soft tissue sarcomas (CWS-2007-HR): a multicentre, open-label, randomised controlled phase 3 trial. EClinicalMedicine. 2024 Nov 29;78:102957. doi: 10.1016/j.eclinm.2024.102957. eCollection 2024 Dec.

Related Links

MeSH Terms

Conditions

SarcomaRhabdomyosarcomaSarcoma, Synovial

Interventions

trofosfamideIdarubicinEtoposide

Condition Hierarchy (Ancestors)

Neoplasms, Connective and Soft TissueNeoplasms by Histologic TypeNeoplasmsMyosarcomaNeoplasms, Muscle TissueNeoplasms, Connective Tissue

Intervention Hierarchy (Ancestors)

DaunorubicinAnthracyclinesNaphthacenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsPolycyclic CompoundsAminoglycosidesGlycosidesCarbohydratesPodophyllotoxinTetrahydronaphthalenesNaphthalenesGlucosides

Study Officials

  • Ewa Koscielniak, MD

    Olgahospital, CWS

    PRINCIPAL INVESTIGATOR
  • Thomas Klingebiel, MD

    Universitätsklinikum Frankfurt, CWS

    STUDY CHAIR
  • Monika Sparber Sauer, MD

    Olgahospital, CWS

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 2, 2009

First Posted

April 6, 2009

Study Start

July 1, 2009

Primary Completion

June 30, 2022

Study Completion

June 30, 2022

Last Updated

November 8, 2022

Record last verified: 2022-11

Locations