NCT01305200

Brief Summary

This randomized phase III trial is studying how well Caphosol rinse works in preventing mucositis in young patients undergoing autologous or donor stem cell transplant. Supersaturated calcium phosphate (Caphosol) rinse may be able to prevent mucositis, or mouth sores, in patients undergoing stem cell transplant.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
226

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Mar 2011

Typical duration for phase_3

Geographic Reach
3 countries

35 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 25, 2011

Completed
3 days until next milestone

First Posted

Study publicly available on registry

February 28, 2011

Completed
1 day until next milestone

Study Start

First participant enrolled

March 1, 2011

Completed
4.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2015

Completed
29 days until next milestone

Study Completion

Last participant's last visit for all outcomes

June 30, 2015

Completed
1.9 years until next milestone

Results Posted

Study results publicly available

May 9, 2017

Completed
Last Updated

September 17, 2019

Status Verified

November 1, 2016

Enrollment Period

4.3 years

First QC Date

February 25, 2011

Results QC Date

November 30, 2016

Last Update Submit

September 9, 2019

Conditions

Outcome Measures

Primary Outcomes (1)

  • Duration of Severe Oral Mucositis (WHO Grade 3 or 4)

    Mean days of severe (WHO Grade 3 or 4) Mucositis.

    Day -1 (day prior to stem cell infusion) to Day 20 following transplantation.

Secondary Outcomes (10)

  • Incidence of Severe Oral Mucositis

    Day -1 (day prior to stem cell infusion) to Day 20 following transplantation.

  • Oral Mucositis Daily Questionnaire (OMDQ)

    Day -1 (day prior to stem cell infusion) to Day 20 following transplantation

  • Incidence of Parenteral Opioid Analgesic Use (Morphine Equivalents).

    Day -1 (day prior to stem cell infusion) to Day 20 following transplantation.

  • Duration of Parenteral Opioid Analgesic Use (Morphine Equivalents).

    Day -1 (day prior to stem cell infusion) to Day 20 following transplantation.

  • Total Dose of Parenteral Opioid Analgesic Used (Morphine Equivalents).

    Day -1 (day prior to stem cell infusion) to Day 20 following transplantation.

  • +5 more secondary outcomes

Other Outcomes (1)

  • Ancillary Validation Study of ChIMES

    Day -1 (day prior to stem cell infusion) to Day 20 following transplantation.

Study Arms (2)

Arm I (placebo)

PLACEBO COMPARATOR

Patients rinse and gargle with placebo over 1 minute QID beginning the first day (about day -7) of the conditioning regimen. Treatment continues until day 20 post-transplantation.

Other: placeboOther: questionnaire administrationProcedure: quality-of-life assessment

Arm II (supersaturated calcium phosphate rinse)

EXPERIMENTAL

Patients rinse and gargle with supersaturated calcium phosphate rinse over 1 minute QID beginning on the first day (about day -7) of the conditioning regimen. Treatment continues until day 20 post-transplantation.

Drug: supersaturated calcium phosphate rinseOther: questionnaire administrationProcedure: quality-of-life assessment

Interventions

Mouth rinse

Also known as: Caphosol
Arm II (supersaturated calcium phosphate rinse)
placeboOTHER

Mouth rinse

Also known as: PLCB
Arm I (placebo)

Ancillary studies

Arm I (placebo)Arm II (supersaturated calcium phosphate rinse)

Ancillary studies

Also known as: quality of life assessment
Arm I (placebo)Arm II (supersaturated calcium phosphate rinse)

Eligibility Criteria

Age4 Years - 21 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Patients undergoing myeloablative autologous or allogeneic hematopoietic stem cell transplantation (HSCT) for any indication
  • One or more of the following donor stem cell sources (autologous or allogeneic):
  • Bone marrow
  • Placental blood (umbilical cord blood)
  • Cytokine-mobilized peripheral blood
  • Patients eligible for allogeneic HSCT must have one of the following types of donor stem cells:
  • Human leukocyte antigen (HLA)-matched sibling or parent
  • Partially matched family donor (mismatched for a single HLA locus \[Class I\])
  • Fully matched unrelated marrow or peripheral blood stem cell donor
  • HLA-matched or partially mismatched (at least 4 of 6 match) cord blood (Class I or II)
  • Patients expecting to receive any type of myeloablative HSCT conditioning regimen are eligible
  • No non-myeloablative or reduced-intensity conditioning regimens
  • Eligible patients must not have received palifermin within 30 days prior to enrollment
  • Eligible patients must not have received prior treatment with Caphosol

You may not qualify if:

  • Females of childbearing potential must have a negative pregnancy test; patients must agree to use an effective birth control method; lactating patients must agree not to nurse a child while on this trial

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (35)

Children's Oncology Group

Arcadia, California, 91006-3776, United States

Location

City of Hope

Duarte, California, 91010, United States

Location

Children's Hospital and Research Center at Oakland

Oakland, California, 94609-1809, United States

Location

Rady Children's Hospital - San Diego

San Diego, California, 92123, United States

Location

University of California San Francisco Medical Center-Parnassus

San Francisco, California, 94143, United States

Location

Alfred I duPont Hospital for Children

Wilmington, Delaware, 19803, United States

Location

Children's National Medical Center

Washington D.C., District of Columbia, 20010, United States

Location

Miami Children's Hospital

Miami, Florida, 33155, United States

Location

All Children's Hospital

St. Petersburg, Florida, 33701, United States

Location

Children's Healthcare of Atlanta - Egleston

Atlanta, Georgia, 30322, United States

Location

Lurie Children's Hospital-Chicago

Chicago, Illinois, 60614, United States

Location

University of Chicago

Chicago, Illinois, 60637, United States

Location

Riley Hospital for Children

Indianapolis, Indiana, 46202, United States

Location

Kosair Children's Hospital

Louisville, Kentucky, 40202, United States

Location

Children's Hospital-Main Campus

New Orleans, Louisiana, 70118, United States

Location

Floating Hospital for Children at Tufts Medical Center

Boston, Massachusetts, 02111, United States

Location

Dana-Farber Cancer Institute

Boston, Massachusetts, 02115, United States

Location

C S Mott Children's Hospital

Ann Arbor, Michigan, 48109, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

University of Mississippi Medical Center

Jackson, Mississippi, 39216, United States

Location

The Childrens Mercy Hospital

Kansas City, Missouri, 64108, United States

Location

University of Nebraska Medical Center

Omaha, Nebraska, 68198, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

Montefiore Medical Center

The Bronx, New York, 10467-2490, United States

Location

Ny Cancer%

Valhalla, New York, 10595, United States

Location

Nationwide Children's Hospital

Columbus, Ohio, 43205, United States

Location

University of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, 73104, United States

Location

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, 19104, United States

Location

Children's Hospital of Pittsburgh of UPMC

Pittsburgh, Pennsylvania, 15224, United States

Location

Methodist Children's Hospital of South Texas

San Antonio, Texas, 78229, United States

Location

Midwest Children's Cancer Center

Milwaukee, Wisconsin, 53226, United States

Location

Royal Childrens Hospital

Herston, Queensland, 4029, Australia

Location

Princess Margaret Hospital for Children

Perth, Western Australia, 6008, Australia

Location

Hospital for Sick Children

Toronto, Ontario, M5G 1X8, Canada

Location

The Montreal Children's Hospital of the MUHC

Montreal, Quebec, H3H 1P3, Canada

Location

Related Publications (1)

  • Treister N, Nieder M, Baggott C, Olson E, Chen L, Dang H, Krailo M, August A, Sung L. Caphosol for prevention of oral mucositis in pediatric myeloablative haematopoietic cell transplantation. Br J Cancer. 2017 Jan 3;116(1):21-27. doi: 10.1038/bjc.2016.380. Epub 2016 Nov 22.

    PMID: 27875526BACKGROUND

Related Links

MeSH Terms

Conditions

Pdgfra-Associated Chronic Eosinophilic LeukemiaLeukemia, Myelomonocytic, ChronicLeukemia, Neutrophilic, ChronicLeukemia, Myelomonocytic, JuvenileMucositisMyeloproliferative DisordersPrecursor Cell Lymphoblastic Leukemia-LymphomaDendritic Cell Sarcoma, InterdigitatingBurkitt LymphomaTesticular NeoplasmsWilms TumorRecurrence

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsMyelodysplastic-Myeloproliferative DiseasesBone Marrow DiseasesHematologic DiseasesHemic and Lymphatic DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and SymptomsGastroenteritisGastrointestinal DiseasesDigestive System DiseasesMouth DiseasesStomatognathic DiseasesLeukemia, LymphoidLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesHistiocytic Disorders, MalignantHistiocytosisEpstein-Barr Virus InfectionsHerpesviridae InfectionsDNA Virus InfectionsVirus DiseasesInfectionsTumor Virus InfectionsLymphoma, B-CellLymphoma, Non-HodgkinLymphomaEndocrine Gland NeoplasmsNeoplasms by SiteGenital Neoplasms, MaleUrogenital NeoplasmsGenital Diseases, MaleGenital DiseasesUrogenital DiseasesMale Urogenital DiseasesEndocrine System DiseasesTesticular DiseasesGonadal DisordersNeoplasms, Complex and MixedKidney NeoplasmsUrologic NeoplasmsNeoplastic Syndromes, HereditaryFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsKidney DiseasesUrologic DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Results Point of Contact

Title
Results Reporting Coordinator
Organization
Children's Oncology Group

Study Officials

  • Nathaniel Treister, MD

    Children's Oncology Group

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, CARE PROVIDER
Purpose
SUPPORTIVE CARE
Intervention Model
PARALLEL
Sponsor Type
NETWORK
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 25, 2011

First Posted

February 28, 2011

Study Start

March 1, 2011

Primary Completion

June 1, 2015

Study Completion

June 30, 2015

Last Updated

September 17, 2019

Results First Posted

May 9, 2017

Record last verified: 2016-11

Locations