NCT01233479

Brief Summary

RATIONALE: Studying samples of blood in the laboratory from patients receiving radiation therapy and chemotherapy may help doctors learn more about the effects of this treatment on cells. It may also help doctors understand how well patients respond to treatment. PURPOSE: This research study is studying biomarkers in blood samples from young patients with newly diagnosed brain tumors undergoing standard radiation therapy and chemotherapy.

Trial Health

30
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Timeline
Completed

Started May 2010

Longer than P75 for not_applicable

Geographic Reach
1 country

11 active sites

Status
withdrawn

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 1, 2010

Completed
6 months until next milestone

First Submitted

Initial submission to the registry

November 2, 2010

Completed
1 day until next milestone

First Posted

Study publicly available on registry

November 3, 2010

Completed
8 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2011

Completed
6.2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

August 24, 2017

Completed
Last Updated

April 1, 2019

Status Verified

March 1, 2019

Enrollment Period

1.2 years

First QC Date

November 2, 2010

Last Update Submit

March 28, 2019

Conditions

Keywords

untreated childhood medulloblastomauntreated childhood cerebellar astrocytomauntreated childhood cerebral astrocytomauntreated childhood brain stem gliomachildhood medulloepitheliomachildhood infratentorial ependymomanewly diagnosed childhood ependymomachildhood atypical teratoid/rhabdoid tumor

Outcome Measures

Primary Outcomes (3)

  • Peripherally circulating T-regulatory (T-reg) cells in patients with medulloblastoma or Chiari malformation

  • Longitudinal side effects of standard radiotherapy and chemotherapy regimens on the overall population of lymphocytes as well as the fraction of circulating T-reg cells

  • Effect of treatment on lymphocytes and T-reg cells

Secondary Outcomes (1)

  • Baseline fraction of circulating T-reg cells

Interventions

Eligibility Criteria

Age4 Years - 21 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)
DISEASE CHARACTERISTICS: * Meets 1 of the following criteria: * Histologically confirmed posterior fossa tumor * Newly diagnosed disease * Medulloblastoma OR non-medulloblastoma (pilocytic astrocytoma, ependymoma, atypical rhabdoid tumor, or others) * Scheduled to undergo craniotomy and tumor resection * Chiari malformation * Requires craniectomy for decompression * No secondary decompression PATIENT CHARACTERISTICS: * No unexplained febrile illness * No active infection * No autoimmune disorders such as inflammatory bowel disease, juvenile rheumatoid arthritis, or systemic lupus erythematosus * No other immunosuppressive disorders (e.g., HIV infection) PRIOR CONCURRENT THERAPY: * See Disease Characteristics

Contact the study team to discuss eligibility requirements. They can help determine if this study is right for you.

Sponsors & Collaborators

Study Sites (11)

Childrens Hospital Los Angeles

Los Angeles, California, 90027-0700, United States

Location

Lucile Packard Children's Hospital at Stanford University Medical Center

Palo Alto, California, 94304, United States

Location

Children's National Medical Center

Washington D.C., District of Columbia, 20010-2970, United States

Location

Children's Memorial Hospital - Chicago

Chicago, Illinois, 60614, United States

Location

NCI - Pediatric Oncology Branch

Bethesda, Maryland, 20892, United States

Location

Memorial Sloan-Kettering Cancer Center

New York, New York, 10065, United States

Location

Duke Cancer Institute

Durham, North Carolina, 27710, United States

Location

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, 45229-3039, United States

Location

Children's Hospital of Pittsburgh of UPMC

Pittsburgh, Pennsylvania, 15213, United States

Location

St. Jude Children's Research Hospital

Memphis, Tennessee, 38105, United States

Location

Texas Children's Cancer Center and Hematology Service at Texas Children's Hospital

Houston, Texas, 77030-2399, United States

Location

MeSH Terms

Conditions

Central Nervous System NeoplasmsRhabdoid Tumor

Interventions

Neoadjuvant TherapyRadiotherapy

Condition Hierarchy (Ancestors)

Nervous System NeoplasmsNeoplasms by SiteNeoplasmsNervous System DiseasesNeoplasms, Complex and MixedNeoplasms by Histologic Type

Intervention Hierarchy (Ancestors)

Combined Modality TherapyTherapeutics

Study Officials

  • Sri Gururangan, MD

    Duke Cancer Institute

    PRINCIPAL INVESTIGATOR
0

Study Design

Study Type
interventional
Phase
not applicable
Masking
NONE
Purpose
BASIC SCIENCE
Sponsor Type
NETWORK

Study Record Dates

First Submitted

November 2, 2010

First Posted

November 3, 2010

Study Start

May 1, 2010

Primary Completion

July 1, 2011

Study Completion

August 24, 2017

Last Updated

April 1, 2019

Record last verified: 2019-03

Locations