NCT00893867

Brief Summary

The purpose of this trial is to determine if intravenous administration of the metal ion trapping agent DP-b99 up to 9 hours following acute ischemic stroke onset, and then for 3 additional days (4 consecutive days in total) is effective in improving long term outcome. Patients will be followed up for 3 months after the stroke.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
446

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Dec 2009

Geographic Reach
18 countries

154 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 4, 2009

Completed
2 days until next milestone

First Posted

Study publicly available on registry

May 6, 2009

Completed
7 months until next milestone

Study Start

First participant enrolled

December 1, 2009

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2012

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2012

Completed
Last Updated

October 24, 2012

Status Verified

October 1, 2012

Enrollment Period

2.3 years

First QC Date

May 4, 2009

Last Update Submit

October 23, 2012

Conditions

Keywords

acute ischemic strokeneuroprotective agent

Outcome Measures

Primary Outcomes (1)

  • Modified Rankin Scale (mRS) categorical analysis ("shift")

    90 days

Secondary Outcomes (4)

  • Recovery, defined as a score of ≤ 1 on modified Rankin Score

    90 days

  • Safety and tolerability

    throughout study - baseline until day 90

  • recovery as assessed by an NIHSS of not more than 1

    90 days

  • 'home time'

    90 days

Study Arms (2)

DP-b99

EXPERIMENTAL
Drug: DP-b99

Mannitol

PLACEBO COMPARATOR
Drug: Placebo

Interventions

DP-b99DRUG

1mg/kg/day over 4 consecutive days given intravenously and initiated up to 9 hours following acute stroke onset.

DP-b99

1mg/kg/day over 4 consecutive days given intravenously and initiated up to 9 hours following acute stroke onset.

Mannitol

Eligibility Criteria

Age18 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • M or F age 18 - 85, inclusive
  • Suffered an acute, likely hemispheric, ischemic stroke, defined as acute, focal, neurological deficit(s), secondary to a presumed vascular event, which must include at least one of the following components (as reflected by at least 1 point on any of the corresponding items of the NIHSS: 3, 9 or 11):
  • Visual
  • Best Language
  • Extinction and Inattention (formerly Neglect)
  • Suffered the onset of an acute ischemic stroke that can be evaluated and treatment initiated within 9 hours after the onset of acute ischemic stroke symptoms.
  • Screening NIHSS score of 10 to 16, inclusive
  • Readily accessible peripheral venous access for clinical trial material (CTM) administration and blood sampling
  • Ability to understand the requirements of the study and be willing to provide written informed consent as evidenced by signature on an informed consent document approved by an institutional review board or independent ethics committee, and agree to abide by the study restrictions and return for the required assessments.
  • Provided written authorization for use and disclosure of protected health information in accordance with the Health Insurance Portability and Accountability Act in the United States and the Personal Information Protection and Electronic Documents Act in Canada

You may not qualify if:

  • An intracerebral or subarachnoid hemorrhage per screening/baseline computerized tomography scan or susceptibility-weighted magnetic resonance imaging
  • A candidate for either:
  • thrombolytic therapy, or have been treated with thrombolytic therapy for the current stroke
  • mechanical thromboembolectomy, or have been treated with mechanical thromboembolectomy for the current stroke
  • Delirious, comatose or stuporous or demented, or having a mental impairment that in the investigator's opinion renders the subject incapable to participate in the study
  • Have seizure(s) anytime from stroke onset to screening/baseline NIHSS evaluation
  • Neurological or non-neurological comorbidities that in the investigator's opinion may lead, independent of the current stroke, to further deterioration in the subject's neurological status during the trial period, or may render the study's neurological assessments inconclusive for the purpose of evaluating solely the stroke's effects
  • Likely to undergo a procedure involving cardiopulmonary bypass during the study period
  • Suffered a myocardial infarction in the last 90 days
  • Any medical condition that in the investigator's opinion may threaten the subject's ability to complete the study (e.g., concurrent significant or life-threatening diseases, such as malignancies or end stage organ failure)
  • Rapid spontaneous improvement of neurological signs during screening/baseline assessments
  • Premorbid neurological deficits and functional limitations assessed by a pre-stroke Modified Rankin Scale score of \> 1
  • Suffered a stroke within 90 days of the screening/baseline assessments that is either diagnostically confirmed or assumed to be in the same cerebral territory as is the current acute stroke
  • Either severe hypertension or hypotension, as measured by at least 2 consecutive supine measurements taken 10 minutes apart prior to randomization.
  • Significant current renal or hepatic disease(s): a serum creatinine concentration of \>2.5 mg/dL; alanine aminotransferase, aspartate aminotransferase, or gamma-glutamyl transferase values that are three times greater than the upper limit of normal.
  • +8 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (154)

Research Center of Southern California

Oceanside, California, United States

Location

Associated Neurologists, P.C.

Danbury, Connecticut, United States

Location

Memorial Health University Medical Center

Savannah, Georgia, United States

Location

The University of Kentucky The Methodist Hospital

Lexington, Kentucky, United States

Location

University of Louisville, Kentucky Neuroscience Research

Louisville, Kentucky, United States

Location

Tufts Medical Center

Boston, Massachusetts, United States

Location

Capital Health Regional Medical Center Neuroscience Institute

Trenton, New Jersey, United States

Location

Presbitarian Hospital

Charlotte, North Carolina, United States

Location

St. Elizabeth's Medical Center

Youngstown, Ohio, United States

Location

Legacy Meridian Park Medical Center

Tualatin, Oregon, United States

Location

Thomas Jefferson University

Philadelphia, Pennsylvania, United States

Location

The Methodist Hospital

Houston, Texas, United States

Location

Carilion Clinic

Roanoke, Virginia, United States

Location

Medizinische Universität Innsbruck

Innsbruck, Austria

Location

Landeskrankenhaus Klagenfurt

Klagenfurt, Austria

Location

Abt. Neurologie und Psychiatrie

Linz, Austria

Location

LKH St. Pölten Department of Neurology

Sankt Pölten, Austria

Location

Santa Casa de Misericordia de Belo Horizonte Departamento de Neurologia

Belo Horizonte, Brazil

Location

Hospital de Clinicas de Porto Alegre

Porto Alegre, Brazil

Location

Hospital Moinhos de Vento

Porto Alegre, Brazil

Location

Hospital Mãe de Deus

Porto Alegre, Brazil

Location

Santa Casa de Misericórdia de Porto Alegre Policlinica Santa Clara Sala de Neurologia

Porto Alegre, Brazil

Location

Hospital das Clínicas da Faculdade de Medicina de Ribeirão Preto Unidade de Emergência Centro de Estudos

Ribeirão Preto, Brazil

Location

Hospital São José de Joinville

Santa Catarina, Brazil

Location

Hospital Santa Marcelina

São Paulo, Brazil

Location

UNIFESP

São Paulo, Brazil

Location

Hamilton Health Sciences Centre

Hamilton, Ontario, Canada

Location

Grey Nun's Community Hospital

Edmonton, Canada

Location

University of Alberta Hospital

Edmonton, Canada

Location

Hamilton Health Sciences Centre

Hamilton, Canada

Location

Kingston General Hospital

Kingston, Canada

Location

Chinook Regional Hospital

Lethbridge, Canada

Location

CHA- Hôpital de l'Enfant-Jésus

Québec, Canada

Location

University Hospital Brno

Brno, Czechia

Location

University Hospital Hradec Kralove, Clinic of Neurology

Hradec Králové, Czechia

Location

Hospital Jihlava Clinic of Neurology

Jihlava, Czechia

Location

Hospital Vítkovice Clinic of Neurology

Ostrava, Czechia

Location

County Hospital Pardubice Clinic of Neurology

Pardubice, Czechia

Location

Clinic of Neurology, Stroke Center, Charles University

Prague, Czechia

Location

University Hospital Kralovske Vinohrady

Prague, Czechia

Location

University Hospital Motol Clinic of Neurology

Prague, Czechia

Location

CHU Jean Minjoz Besançon

Besançon, France

Location

Hopital Pellegrin-Tripode

Bordeaux, France

Location

CHU Henri Mondor

Créteil, France

Location

Hopital Gui de Chauliac

Montpellier, France

Location

Hôpital Bichat

Paris, France

Location

Hôpital Lariboisière - Service Neurologie

Paris, France

Location

Hôpital Saint Jean

Perpignan, France

Location

Ärztlicher Direktor Neurologische Klinik, Neurologische Klink GmbH der Rhoen-Klinikum AG

Bad Neustadt / Saale, Germany

Location

Marien-Krankenhaus gGmbH, Abteilung für Neurologie

Bergisch Gladbach, Germany

Location

DRK Kliniken Berlin, Klinik fuer Neurologie

Berlin, Germany

Location

Vivantes Klinikum Neukölln, Klinik für Neurologie, Stroke Unit

Berlin, Germany

Location

Klinikum Bremen-Mitte

Bremen, Germany

Location

Klinikum Bremerhaven-Reinkenheide gGmbH, Neurologische Klinik

Bremerhaven, Germany

Location

Klinikum Chemnitz GmbH Chefarzt Klinik für Neurologie

Chemnitz, Germany

Location

Klinikum Köln Merheim, Department of Neurology

Cologne, Germany

Location

Helios Klinikum Erfurt GmbH

Erfurt, Germany

Location

Universitätsklinikum Erlangen, Neurologische klinik

Erlangen, Germany

Location

Universitätsklinikum Essen, Klinik und Poliklinik für Neurologie

Essen, Germany

Location

Neurologische Universitätsklinik Freiburg, Neurozentrum

Freiburg im Breisgau, 79106, Germany

Location

Klinikum Fulda, Neurologische Klinik

Fulda, Germany

Location

Evangelische Kliniken Gelsenkirchen GmbH Klinik für Neurologie und Klinische Neurophysiologie

Gelsenkirchen, Germany

Location

Georg-August-Universitat Gottingen Neurologische Klinik

Göttingen, Germany

Location

Ernst Moritz Arndt University

Grifswald, Germany

Location

Askepios Klinik Altona

Hamburg, Germany

Location

Askepios Klinik Heidberg

Hamburg, Germany

Location

Universitätsklinikum Leipzig AöR, Klinik und Poliklinik für Neurologie

Leipzig, Germany

Location

Klinikum der Otto-von-Guericke-Universität Magdeburg, Neurologische Universitätsklinik

Magdeburg, Germany

Location

Johannes Gutenberg Universitat, Klinik und Poliklinik fur Neurologie

Mainz, Germany

Location

Klinikum 1 Minden, Neurologische Klinik

Minden, Germany

Location

Universität Rostock Chefarzt Abteilung Neurologie

Rostock, Germany

Location

ASKLEPIOS Fachklinikum Teupitz

Teupitz, Germany

Location

Krankenhaus der Bramherzigen Brüder

Trier, Germany

Location

Universitätsklinikum Ulm, Abteilung für Neurologie im RKU

Ulm, Germany

Location

Heinrich Braun Klinikum Zwickau

Zwickau, Germany

Location

Fővárosi Önkormányzat Péterfy Sándor utcai Kórház- Rendelőintézet és Baleseti Központ

Budapest, Hungary

Location

Állami Egészségügyi Központ

Budapest, Hungary

Location

Kenezy Korhaz Rendelointezet Egezsegugyi Szolgaltato Nonprofit Kft.

Debrecen, Hungary

Location

University of Debrecen, Medical and Health Science Center

Debrecen, Hungary

Location

Aladár Petz County Teaching Hospital

Győr, Hungary

Location

PM Flór Ferenc County Hospital

Kistarcsa, Hungary

Location

Borsod-Abaúj-Zemplén County Hospital Miskolc

Miskolc, Hungary

Location

Pécsi Tudományegyetem Klinikai Központ

Pécs, Hungary

Location

Zala Megyei Kórház

Zalaegerszeg, Hungary

Location

Bnai Zion Medical Center

Haifa, Israel

Location

Neurological Dept. Edith Wolfson Medical Center

Holon, 58100, Israel

Location

Meir Medical Center

Kfar Saba, Israel

Location

Sourasky Medical Center

Tel Aviv, Israel

Location

Chaim Sheba Medical Center

Tel Litwinsky, Israel

Location

Ospedale Regionale Valle d'Aosta

Aosta, Italy

Location

Dipartimento di Neuroscienze, Ospedale di Brotzu

Cagliari, Italy

Location

Ospedale di Circolo di Varese

Lombardia, Italy

Location

Istituto Scientifico San Raffaele - Stroke Unit

Milan, Italy

Location

Istituto Neurologico C. Mondino

Pavia, Italy

Location

Università di Perugia, Division of Internal and Cardiovascular Medicine - Stroke Unit

Perugia, Italy

Location

Presidio Ospedaliero di Piacenza

Piacenza, Italy

Location

Azienda Ospedaliera Sant'Andrea, Stroke Unit

Rome, Italy

Location

Istituto Patologia Generale U.C.S.C

Rome, Italy

Location

U.O.C. Stroke Unit

Rome, Italy

Location

Università di Roma "La Sapienza" - Stroke Unit

Rome, Italy

Location

Azienda Ospedaliera Universitaria "Santa Maria della Misericordia" Stroke Unit

Udine, Italy

Location

Catharina Ziekenhuis Neurologie

Eindhoven, Netherlands

Location

Medisch Spectrum Twente Hoofd Afdeling Vasculaire Neurologie

Enschede, Netherlands

Location

Atrium MC Parkstad

Heerlen, Netherlands

Location

Isala Klinieken Ploikliniek Neurologie

Zwolle, Netherlands

Location

Pomerania Traumatology Center, Regional Specialist Hospital im. Nicolaus Copernicus

Gdansk, Poland

Location

Medical University of Lublin, Department of Neurology, Stroke Unit

Lublin, Poland

Location

Samodzielny Publiczny Zespol Zakladow Opieki Zdrowotnej w Sandomierzu

Sandomierz, Poland

Location

Szpital Powiatowy im. Marii Curie - Skłodowskiej w Skarżysku-Kamiennej

Skarżysko-Kamienna, Poland

Location

Wojewodzki Szpital Specjalistyczny Nr 1 im. Prof. Jozefa Gasinskiego

Tychy, Poland

Location

Instytut Psychiatrii i Neurologii Oddział Neurologiczny z Pododdziałem Udarowym

Warsaw, Poland

Location

Medical University of Warsaw, Department of Neurology

Warsaw, Poland

Location

Szpital Wolski im. dr Anny Gostyńskiej Samodzielny Publiczny Zakład Opieki Zdrowotnej, Oddział Neurologii

Warsaw, Poland

Location

Wojskowy Instytut Medyczny, Oddział Neurologii

Warsaw, Poland

Location

Hospital Professor Doutor Fernando Fonseca, EPE

Amadora, Portugal

Location

Centro Hospitalar de Coimbra EPE

Coimbra, Portugal

Location

Hospitais da Universidadde de Coimbra, EPE

Coimbra, Portugal

Location

Centro de Estudos Egas Moniz - Hospital de Santa Maria

Lisbon, Portugal

Location

Hospital de São Sebastião, EPE

Santa Maria da Feira, Portugal

Location

Neurology Clinic, Faculty Hospital in Martin

Martin, Slovakia

Location

University Hospital Nitra

Nitra, Slovakia

Location

Hospital un Poliklinic

Spišská Nová Ves, Slovakia

Location

Faculty Hospital Trnava

Trnava, Slovakia

Location

Neurology dept.,Hospital Zilina

Žilina, Slovakia

Location

Fichmed

Bloemfontein, South Africa

Location

Constantiaberg Medi-clinic

Cape Town, South Africa

Location

Union Hospital

Gauteng, South Africa

Location

Helderberg Research Institute

Western Cape, South Africa

Location

Triervlei Trial Centre

Western Cape, South Africa

Location

Clinical Projects Research

Worcester, South Africa

Location

Dong-A Medical Center

Busan, South Korea

Location

Inje University BUSAN Paik Hospital

Busan, South Korea

Location

Inje University ILSAN Paik Hospital

Goyang, South Korea

Location

Chonnam National University Hospital

Gwangju, South Korea

Location

Inha University Hospital

Incheon, South Korea

Location

Seoul National University Bundang Hospital

Seongnam, South Korea

Location

ASAN Medical Center

Seoul, South Korea

Location

Severance Hospital

Seoul, South Korea

Location

The Catholic University of Korea Seoul St. Mary's hospital

Seoul, South Korea

Location

Hospital Universitario de Albacete

Albacete, Spain

Location

Hospital De La Santa Ta Creu i Sant Pau

Barcelona, Spain

Location

Hospital del Mar

Barcelona, Spain

Location

Hospital Germans Triasy Pujol

Barcelona, Spain

Location

Hospital Vall D'hebron

Barcelona, Spain

Location

Hospital Gregorio Maranon

Madrid, Spain

Location

Hospital La Princesa

Madrid, Spain

Location

Hospital Ramon y Cajal

Madrid, Spain

Location

Hospital Universitario Clinico San Carlos

Madrid, Spain

Location

Hospital Universitario La Paz

Madrid, Spain

Location

Hospital Clinico Universitario de Santiago

Santiago de Compostela, Spain

Location

Consorcio Hospital General Universitario Valencia

Valencia, Spain

Location

Hospital Clinico Universitario De Valladolid

Valladolid, Spain

Location

Universitätsspital Basel, Neurologie

Basel, Switzerland

Location

Universitätsspital Zürich, Klinik für Neurologie

Zurich, Switzerland

Location

Related Publications (5)

  • Diener HC, Schneider D, Lampl Y, Bornstein NM, Kozak A, Rosenberg G. DP-b99, a membrane-activated metal ion chelator, as neuroprotective therapy in ischemic stroke. Stroke. 2008 Jun;39(6):1774-8. doi: 10.1161/STROKEAHA.107.506378. Epub 2008 Apr 10.

    PMID: 18403736BACKGROUND
  • Rosenberg G, Angel I, Kozak A. Clinical pharmacology of DP-b99 in healthy volunteers: first administration to humans. Br J Clin Pharmacol. 2005 Jul;60(1):7-16. doi: 10.1111/j.1365-2125.2005.02378.x.

    PMID: 15963088BACKGROUND
  • Barkalifa R, Hershfinkel M, Friedman JE, Kozak A, Sekler I. The lipophilic zinc chelator DP-b99 prevents zinc induced neuronal death. Eur J Pharmacol. 2009 Sep 15;618(1-3):15-21. doi: 10.1016/j.ejphar.2009.07.019. Epub 2009 Jul 19.

    PMID: 19622352BACKGROUND
  • Rosenberg G, Bornstein N, Diener HC, Gorelick PB, Shuaib A, Lees K; MACSI investigators. The Membrane-Activated Chelator Stroke Intervention (MACSI) Trial of DP-b99 in acute ischemic stroke: a randomized, double-blind, placebo-controlled, multinational pivotal phase III study. Int J Stroke. 2011 Aug;6(4):362-7. doi: 10.1111/j.1747-4949.2011.00608.x. Epub 2011 Jun 6.

    PMID: 21645269BACKGROUND
  • Rosenberg G, Marshall LS, Caraco Y. The neuroprotective agent DP-b99 does not interact with s-warfarin in vivo despite significant CYP2C9 inhibition in vitro. Basic Clin Pharmacol Toxicol. 2011 Apr;108(4):289-92. doi: 10.1111/j.1742-7843.2010.00654.x. Epub 2010 Dec 16. No abstract available.

    PMID: 21414144BACKGROUND

MeSH Terms

Conditions

Ischemic Stroke

Interventions

DP-b99

Condition Hierarchy (Ancestors)

StrokeCerebrovascular DisordersBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesVascular DiseasesCardiovascular Diseases

Study Officials

  • Ashfaq Shuaib, MD

    University of Alberta Hospital, Edmonton, Canada

    PRINCIPAL INVESTIGATOR
  • Vasco Salgado, MD

    Hospital Professor Doutor Fernando Fonseca, EPE, Amadora, Portugal

    PRINCIPAL INVESTIGATOR
  • Philippe Lyrer, Prof. Dr.

    Universitätsspital Basel, Neurologie, Basel, Switzerland

    PRINCIPAL INVESTIGATOR
  • Tobien Schreuder, MD

    Atrium MC Parkstad, Heerlen, Netherlands

    PRINCIPAL INVESTIGATOR
  • Maria S Rocha, MD

    Hospital Santa Marcelina, Sao Paulo, Brasil

    PRINCIPAL INVESTIGATOR
  • Hugues Chabriat, Prof.

    Hôpital Lariboisière - Service Neurologie, Paris, France

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 4, 2009

First Posted

May 6, 2009

Study Start

December 1, 2009

Primary Completion

April 1, 2012

Study Completion

April 1, 2012

Last Updated

October 24, 2012

Record last verified: 2012-10

Locations