NCT00720798

Brief Summary

This single-arm study evaluated the long-term efficacy and safety of tocilizumab in participants who had completed treatment in the tocilizumab core studies (NCT00106522 \[Roche protocol WA18062\], NCT00106574 \[Roche protocol WA18063\], and NCT00109408 \[Roche protocol WA17824\]) of adults with rheumatoid arthritis. Participants received tocilizumab alone or in combination with standard anti-rheumatic treatment.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
2,067

participants targeted

Target at P75+ for phase_3 rheumatoid-arthritis

Timeline
Completed

Started Sep 2005

Longer than P75 for phase_3 rheumatoid-arthritis

Geographic Reach
33 countries

293 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 1, 2005

Completed
2.9 years until next milestone

First Submitted

Initial submission to the registry

July 22, 2008

Completed
1 day until next milestone

First Posted

Study publicly available on registry

July 23, 2008

Completed
4.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2013

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2013

Completed
1.5 years until next milestone

Results Posted

Study results publicly available

September 30, 2014

Completed
Last Updated

September 30, 2014

Status Verified

September 1, 2014

Enrollment Period

7.6 years

First QC Date

July 22, 2008

Results QC Date

June 10, 2014

Last Update Submit

September 26, 2014

Conditions

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants With ≥ 1 Adverse Event

    Baseline to the end of the study (up to 7 years, 7 months)

Secondary Outcomes (15)

  • Percentage of Participants Who Withdrew From Treatment

    Baseline to the end of the study (up to 7 years, 7 months)

  • Percentage of Participants With Concomitant Oral Corticosteroid Therapy

    Baseline to the end of the study (up to 7 years, 7 months)

  • Percentage of Participants Who Changed From Monotherapy to Combination Therapy

    Baseline to Week 296

  • Percentage of Participants With an Improvement of at Least 20%, 50%, 70%, or 90% in the American College of Rheumatology (ACR) Score (ACR20/50/70/90) From Baseline at Weeks 24, 48, 108, 156, 204, and 264

    Baseline to Week 264

  • Percentage of Participants Who Achieved a Major Clinical Response at Weeks 48, 96, 144, 192, and 264

    Baseline to Week 264

  • +10 more secondary outcomes

Study Arms (1)

Tocilizumab

EXPERIMENTAL

Participants received tocilizumab 8 mg/kg intravenously every 4 weeks till the end of the study (up to 7 years, 7 months). In addition, participants may have also received disease-modifying anti-rheumatic drugs, non-steroidal anti-inflammatory drugs, and oral corticosteroids at the discretion of the investigator.

Drug: TocilizumabDrug: Disease-modifying anti-rheumatic drugsDrug: Non-steroidal anti-inflammatory drugsDrug: Oral corticosteroids

Interventions

For participants weighing \> 100 kg, the maximum dose of tocilizumab was 800 mg. Tocilizumab was supplied as a sterile solution in vials.

Also known as: RoActemra, Actemra
Tocilizumab

Disease-modifying anti-rheumatic drugs included methotrexate, chloroquine, hydroxychloroquine, parenteral gold, sulfasalazine, azathioprine, and leflunomide. These drugs could be used alone or in combination, except for the combination of methotrexate and leflunomide, which was not allowed.

Tocilizumab

Participants could be treated with non-steroidal anti-inflammatory drugs up to the maximum recommended dose throughout the study. The choice and doses of non-steroidal anti-inflammatory drugs were at the discretion of the investigator.

Tocilizumab

Oral corticosteroids (≤ 10 mg/day) were permitted during the study.

Tocilizumab

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients who have completed participation in 1 of the core studies in adult rheumatoid arthritis.

You may not qualify if:

  • Treatment with any investigational agent since the last administration of study drug in the core studies.
  • Treatment with iv gamma globulin, plasmapheresis, or prosorba column since the last administration of study drug in the core studies.
  • Treatment with an anti-TNF or anti-IL1 agent, a T-cell co-stimulation modulator, or any biologic since the last administration of study drug in the core studies.
  • Immunization with a live/attenuated vaccine since the last administration of study drug in the core studies.
  • Previous treatment with any cell-depleting therapies, including investigational agents.
  • Parenteral, intramuscular, or intra-articular corticosteroids within 6 weeks prior to baseline in this study.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (295)

Unknown Facility

Birmingham, Alabama, 35294-7201, United States

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Huntsville, Alabama, 35801, United States

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Mesa, Arizona, 85208, United States

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Paradise Valley, Arizona, 85253, United States

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Peoria, Arizona, 85381, United States

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Scottsdale, Arizona, 85251, United States

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Scottsdale, Arizona, 85258, United States

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Tucson, Arizona, 85723, United States

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Tucson, Arizona, 85724, United States

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Little Rock, Arkansas, 72205, United States

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Anaheim, California, 92801, United States

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Long Beach, California, 90806, United States

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Long Beach, California, 90808, United States

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Los Angeles, California, 90045, United States

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Los Angeles, California, 90095, United States

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Palm Desert, California, 92260, United States

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Palm Springs, California, 92262, United States

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Palo Alto, California, 94304, United States

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San Diego, California, 92101, United States

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San Diego, California, 92108, United States

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San Jose, California, 95126, United States

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San Leandro, California, 94578, United States

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Santa Maria, California, 93454, United States

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Torrance, California, 90505, United States

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Upland, California, 91786, United States

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Colorado Springs, Colorado, 80910, United States

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Newark, Delaware, 19713, United States

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Aventura, Florida, 33180, United States

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Delray Beach, Florida, 33484, United States

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Fort Lauderdale, Florida, 33334, United States

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Palm Habor, Florida, 34684, United States

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Palm Harbor, Florida, 34684, United States

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Sarasota, Florida, 34239, United States

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Tampa, Florida, 33609, United States

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Tampa, Florida, 33614, United States

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West Palm Beach, Florida, 33407, United States

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Atlanta, Georgia, 30342, United States

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Boise, Idaho, 83702, United States

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Idaho Falls, Idaho, 83404, United States

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Meridian, Idaho, 83642, United States

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Morton Grove, Illinois, 60053, United States

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Springfield, Illinois, 62704, United States

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Vernon Hills, Illinois, 60061, United States

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Indianapolis, Indiana, 46202-5149, United States

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Cedar Rapids, Iowa, 52401, United States

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Des Moines, Iowa, 50322, United States

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Bowling Green, Kentucky, 42102, United States

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Lexington, Kentucky, 40515, United States

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Louisville, Kentucky, 40202, United States

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Baton Rouge, Louisiana, 70808, United States

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Shreverport, Louisiana, 71103, United States

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Slidell, Louisiana, 70458, United States

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Portland, Maine, 04102, United States

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Frederick, Maryland, 21702, United States

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Wheaton, Maryland, 20902, United States

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Boston, Massachusetts, 02111, United States

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Pittsfield, Massachusetts, 01201, United States

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Grand Rapids, Michigan, 49546, United States

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Kalamazoo, Michigan, 49048, United States

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Lansing, Michigan, 48910, United States

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Eagan, Minnesota, 55121, United States

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Saint Cloud, Minnesota, 56303, United States

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Saint Louis Park, Minnesota, 55426, United States

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Flowood, Mississippi, 39232, United States

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Tupelo, Mississippi, 38802, United States

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Springfield, Missouri, 65807, United States

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St Louis, Missouri, 63117, United States

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St Louis, Missouri, 63128, United States

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St Louis, Missouri, 63131, United States

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St Louis, Missouri, 63141, United States

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Billings, Montana, 59107-5100, United States

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Lincoln, Nebraska, 68516, United States

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Reno, Nevada, 89502, United States

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Dover, New Hampshire, 03820, United States

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Haddon Heights, New Jersey, 08035, United States

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New Brunswick, New Jersey, 08903, United States

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Passaic, New Jersey, 07055, United States

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Albuquerque, New Mexico, 87131, United States

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Albany, New York, 12206, United States

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Binghamton, New York, 13905, United States

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Great Neck, New York, 11020, United States

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New York, New York, 10021, United States

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Orchard Park, New York, 14127, United States

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Plainview, New York, 11803, United States

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Rochester, New York, 14642, United States

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Syracuse, New York, 13210, United States

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Asheville, North Carolina, 28803, United States

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Chapel Hill, North Carolina, 27599-7280, United States

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Charlotte, North Carolina, 28210, United States

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Durham, North Carolina, 27704, United States

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Raleigh, North Carolina, 27609, United States

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Bismarck, North Dakota, 58501, United States

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Canton, Ohio, 44718, United States

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Cincinnati, Ohio, 45219, United States

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Cleveland, Ohio, 44109, United States

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Dayton, Ohio, 45408, United States

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Oklahoma City, Oklahoma, 73103, United States

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Oklahoma City, Oklahoma, 73109, United States

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Oklahoma City, Oklahoma, 73112, United States

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Tulsa, Oklahoma, 74104, United States

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Tulsa, Oklahoma, 74135, United States

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Eugene, Oregon, 97401, United States

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Medford, Oregon, 97504, United States

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Allentown, Pennsylvania, 18103, United States

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Bethlehem, Pennsylvania, 18015, United States

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Danville, Pennsylvania, 17822, United States

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Duncansville, Pennsylvania, 16635, United States

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Philadelphia, Pennsylvania, 19152, United States

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Pittsburgh, Pennsylvania, 15261, United States

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Willow Grove, Pennsylvania, 19090, United States

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Willow Grove, Pennsylvania, 80045, United States

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Wyomissing, Pennsylvania, 19610, United States

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Johnston, Rhode Island, 02919, United States

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Charleston, South Carolina, 29406, United States

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Columbia, South Carolina, 29204, United States

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Greenville, South Carolina, 29601, United States

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Hickory Grove, South Carolina, 28602, United States

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Hixson, Tennessee, 37343, United States

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Jackson, Tennessee, 38305, United States

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Nashville, Tennessee, 37203, United States

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Amarillo, Texas, 79124, United States

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Austin, Texas, 78705, United States

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Austin, Texas, 78749, United States

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Dallas, Texas, 75231-4406, United States

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Dallas, Texas, 75231, United States

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Houston, Texas, 77074, United States

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Mesquite, Texas, 75150, United States

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Burlington, Vermont, 05401, United States

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Chesapeake, Virginia, 23320, United States

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Norfolk, Virginia, 23502, United States

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Mountlake Terrace, Washington, 98043, United States

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Olympia, Washington, 98502, United States

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Seattle, Washington, 98104, United States

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Seattle, Washington, 98195, United States

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Spokane, Washington, 99204, United States

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Tacoma, Washington, 98405, United States

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Glendale, Wisconsin, 53217, United States

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La Crosse, Wisconsin, 54601, United States

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Buenos Aires, C1015ABO, Argentina

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Buenos Aires, C1428DQG, Argentina

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Rosario, S2000PBJ, Argentina

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San Juan Bautista, B1878DVB, Argentina

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Hobart, 7000, Australia

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Malvern, 3144, Australia

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Shenton Park, 6008, Australia

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Sydney, 2050, Australia

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Woolloongabba, 4102, Australia

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Hasselt, 3500, Belgium

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Merksem, 2170, Belgium

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Campinas, 13060-803, Brazil

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Goiânia, 74653-050, Brazil

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Rio de Janeiro, 20551030, Brazil

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Calgary, Alberta, T2V 1P9, Canada

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Edmonton, Alberta, T5H 3V9, Canada

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Victoria, British Columbia, V8V 3P9, Canada

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Winnipeg, Manitoba, R3A 1M3, Canada

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St. John's, Newfoundland and Labrador, A1A 5E8, Canada

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Burlington, Ontario, L7R 1E2, Canada

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Hamilton, Ontario, L8N 2B6, Canada

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Kitchener, Ontario, N2M 5N6, Canada

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London, Ontario, N6A 4V2, Canada

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Mississauga, Ontario, L5M 2V8, Canada

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Ottawa, Ontario, K1H 1A2, Canada

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Toronto, Ontario, M5T 3L9, Canada

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Montreal, Quebec, H2L 1S6, Canada

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Québec, Quebec, G1V 3M7, Canada

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Sainte-Foy, Quebec, G1W 4R4, Canada

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Saskatoon, Saskatchewan, S7N 0W8, Canada

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Beijing, 100032, China

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Beijing, 100044, China

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Guangzhou, 510630, China

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Hefei Anhui, 230022, China

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Jinan, 250012, China

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Shanghai, 200127, China

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Shanghai, 200433, China

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San José, 10103, Costa Rica

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Hradec Králové, 500 05, Czechia

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Prague, 128 50, Czechia

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Prague, 140 59, Czechia

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Hellerup, 2900, Denmark

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Helsinki, 00290, Finland

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Jyväskylä, 40620, Finland

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Amiens, 80054, France

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Bordeaux, 33076, France

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Boulogne-Billancourt, 92104, France

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Brest, 29609, France

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Grenoble, 38042, France

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Le Kremlin-Bicêtre, 94270, France

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Lille, 59037, France

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Lyon, 69437, France

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Marseille, 13285, France

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Montpellier, 34295, France

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Nantes, 44035, France

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Nice, 06202, France

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Paris, 75181, France

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Paris, 75679, France

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Pierre-Bénite, 69495, France

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Rennes, 35203, France

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Rouen, 76031, France

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Saint-Priest-en-Jarez, 42277, France

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Strasbourg, 67098, France

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Toulouse, 31059, France

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Aachen, 52064, Germany

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Berlin, 10117, Germany

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Cologne, 50924, Germany

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Dresden, 01067, Germany

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Essen, 45239, Germany

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Gommern, 39245, Germany

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Herne, 44652, Germany

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Hildesheim, 31134, Germany

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München, 80335, Germany

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München, 81541, Germany

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Osnabrück, 49074, Germany

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Sendenhorst, 48324, Germany

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Wiesbaden, 65191, Germany

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Würzburg, 97080, Germany

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Hong Kong, 852, Hong Kong

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Tuenmen, 852, Hong Kong

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Reykjavik, 108, Iceland

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Ashkelon, 78306, Israel

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Haifa, 31048, Israel

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Haifa, 34354, Israel

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Rishon LeZiyyon, 70300, Israel

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Brescia, 25123, Italy

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Genova, 16132, Italy

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Milan, 20157, Italy

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Padua, 35128, Italy

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Pavia, 27100, Italy

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Pisa, 56100, Italy

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Siena, 53100, Italy

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Udine, 33100, Italy

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Kaunas, 50009, Lithuania

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Klaipėda, 92288, Lithuania

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Panevezys, 35144, Lithuania

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Šiauliai, 76231, Lithuania

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Vilnius, LT-08661, Lithuania

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Guadalajara, 44340, Mexico

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Guadalajara, 44620, Mexico

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Guadalajara, 45235, Mexico

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León, 37000, Mexico

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Mexico City, 06700, Mexico

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Mexico City, 07760, Mexico

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Mexico City, 14050, Mexico

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Tijuana, 22320, Mexico

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Nijmegen, 6525 GA, Netherlands

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Levanger, 7600, Norway

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Lillehammer, 2609, Norway

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Panama City, 32400, Panama

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Lima, 11, Peru

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Lima, 13, Peru

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Lisbon, 1349-019, Portugal

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Ponce, 00716, Puerto Rico

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Moscow, 105203, Russia

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Moscow, 115522, Russia

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Moscow, 117049, Russia

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Ryazan, 390026, Russia

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Saint Petersburg, 190068, Russia

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Saint Petersburg, 191015, Russia

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Tula, 300053, Russia

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Belgrade, 11000, Serbia

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Niška Banja, 18250, Serbia

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Ljubljana, 1000, Slovenia

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Maribor, 2000, Slovenia

Location

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Cape Town, 4001, South Africa

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Cape Town, 7500, South Africa

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Diepkloof, 1862, South Africa

Location

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Durban, 4001, South Africa

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Pinelands, 7405, South Africa

Location

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Pretoria, 0002, South Africa

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Radiokop, 2040, South Africa

Location

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Barakaldo, 48903, Spain

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Barcelona, 08035, Spain

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Madrid, 28046, Spain

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Málaga, 29010, Spain

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Pontevedra, 36001, Spain

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Santiago de Compostela, 15706, Spain

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Stockholm, 17176, Sweden

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Umeå, 90185, Sweden

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Lausanne, 1011, Switzerland

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Bangkok, 10330, Thailand

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Bangkok, 10400, Thailand

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Chiang Mai, 50200, Thailand

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Basingstoke, RG24 9NA, United Kingdom

Location

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Birmingham, B29 6JD, United Kingdom

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Cannock, WS11 5XY, United Kingdom

Location

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Derby, DE1 2QY, United Kingdom

Location

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Leeds, LS7 4SA, United Kingdom

Location

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London, SE1 9RT, United Kingdom

Location

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Manchester, M13 9WL, United Kingdom

Location

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Manchester, M41 5SL, United Kingdom

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Middlesbrough, TS4 3BW, United Kingdom

Location

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Newcastle upon Tyne, NE1 4LP, United Kingdom

Location

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Oxford, OX3 7LD, United Kingdom

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Southampton, SO16 6YD, United Kingdom

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Stoke-on-Trent, ST6 7AG, United Kingdom

Location

Related Publications (1)

  • Jones G, Wallace T, McIntosh MJ, Brockwell L, Gomez-Reino JJ, Sebba A. Five-year Efficacy and Safety of Tocilizumab Monotherapy in Patients with Rheumatoid Arthritis Who Were Methotrexate- and Biologic-naive or Free of Methotrexate for 6 Months: the AMBITION Study. J Rheumatol. 2017 Feb;44(2):142-146. doi: 10.3899/jrheum.160287. Epub 2016 Dec 1.

MeSH Terms

Conditions

Arthritis, Rheumatoid

Interventions

tocilizumabAntirheumatic AgentsAdrenal Cortex Hormones

Condition Hierarchy (Ancestors)

ArthritisJoint DiseasesMusculoskeletal DiseasesRheumatic DiseasesConnective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Intervention Hierarchy (Ancestors)

Therapeutic UsesPharmacologic ActionsChemical Actions and UsesHormonesHormones, Hormone Substitutes, and Hormone Antagonists

Results Point of Contact

Title
Medical Communications
Organization
Hoffmann-La Roche

Study Officials

  • Clinical Trials

    Hoffmann-La Roche

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 22, 2008

First Posted

July 23, 2008

Study Start

September 1, 2005

Primary Completion

April 1, 2013

Study Completion

April 1, 2013

Last Updated

September 30, 2014

Results First Posted

September 30, 2014

Record last verified: 2014-09

Locations