NCT00514722

Brief Summary

This is a pilot study designed to evaluate the safety and feasibility of performing umbilical cord blood transplants in adults with high-risk hematopoietic malignancies. A novel myeloablative preparative regimen will be used. One, up to a maximum of three cord blood units will be administered to facilitate engraftment.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
4

participants targeted

Target at below P25 for not_applicable

Timeline
Completed

Started Oct 2002

Longer than P75 for not_applicable

Geographic Reach
1 country

1 active site

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 1, 2002

Completed
4.9 years until next milestone

First Submitted

Initial submission to the registry

August 8, 2007

Completed
2 days until next milestone

First Posted

Study publicly available on registry

August 10, 2007

Completed
1.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2009

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2009

Completed
Last Updated

August 14, 2013

Status Verified

August 1, 2013

Enrollment Period

6.4 years

First QC Date

August 8, 2007

Last Update Submit

August 13, 2013

Conditions

Keywords

Hematopoietic malignanciesUmbilical cord blood transplantationLymphoma: diffuse large cell, mantle cell, peripheral T-cell, T-NK cell, or Hodgkin's

Outcome Measures

Primary Outcomes (2)

  • efficacy

    5 years

  • safety of umbilical cord transplant

    5 years

Secondary Outcomes (1)

  • safety of umbilical cord stem cell transplant

    5 years

Interventions

umbilical cord stem cell allogeneic transplantation

Eligibility Criteria

Age18 Years - 55 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • Age \< or equal to 55
  • Availability of donor cord blood (one to three units) matching at least 4 of 6 HLA antigens (A, B, and DR). HLA class I antigens will be determined by serologic methods, and Class II antigens will be determined by high-resolution DNA typing. Typing will be confirmed by UCSF Immunogenetics Department following infusion. The UCB units must contain \>2.5 x 10(7) TNC per kilogram recipient body weight. Cord blood units will be obtained from all available international banks.
  • HLA identical or 1 antigen mismatched related donors or potential HLA-matched unrelated donors (MUD) matching at \>6/8 (A, B,C, DR) alleles must NOT be available.
  • Disease types:
  • Acute myeloid leukemia not expected to be curable with chemotherapy. This will include patients with high-risk cytogenetics (-7, -7q, -5, -5q, t(6,9), t(9,11), complex, Ph+), evolution from prior myelodysplasia or AML secondary to prior chemotherapy, failure to achieve remission, or second or subsequent remission. To ensure adequate time until disease progression, marrow blasts must be \< or equal to 10%. This may be achieved using chemotherapy treatment.
  • Myelodysplasia with high-risk features. This will include patients with IPSS category INT2 or HI-risk MDS. Marrow blasts must be \< or equal to 20%. If required, chemotherapy may be given to achieve target levels of blasts.
  • Acute lymphoblastic leukemia not expected to be curable with chemotherapy. This will include patients with high-risk cytogenetics (Ph+, t(4,11), 11q23 abnormalities, and monosomy 7), patients requiring more than one induction course to achieve remission, as well as patients failing to enter remission or in second or subsequent remission. To ensure adequate time until disease progression, marrow blasts must be \< or equal to 10%. If required, chemotherapy may be given to achieve target levels of blasts.
  • Chronic myelogenous leukemia with advanced disease. This will include patients with accelerated or blastic phase or patients with chronic phase refractory to STI-5741. To ensure adequate time until disease progression, patients with blast crisis must show marrow blasts \< or equal to 10%. If required, chemotherapy may be given to achieve target levels of blasts.
  • Multiple myeloma, stage II-III with \>1st relapse or refractory disease or newly diagnosed with chromosome 13 abnormalities.
  • Lymphoma: diffuse large cell, mantle cell, peripheral T-cell, T-NK cell, or Hodgkin's disease which has failed to respond to primary therapy, progressed or recurred after prior therapy. Patients who have failed autologous transplant are eligible if they are \>1 year post-transplant.
  • Patients must have an ECOG PS\< or equal to 2
  • Laboratory requirements:
  • Creatinine \<2.0mg/dL and creatinine clearance \>40/m/min (calculated or based on 24 hour urine collection)
  • Bilirubin \<2.0 mg/dL, AST/alkaline phosphatase \<3x upper limit of normal
  • Patients with hepatitis C and active Hepatitis B are eligible only if a liver biopsy is performed and there is a \< or equal to grade 2 inflammation or fibrosis.
  • +3 more criteria

You may not qualify if:

  • Active infection requiring ongoing antibiotic treatment
  • HIV infection
  • Poor performance status (ECOG \>2)
  • Rapid progression of malignant disease
  • Opinion of BMT Committee that autologous transplant would be a preferable form of treatment
  • Organ function is below requirements
  • Pregnancy or breast-feeding

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

University of California, San Francisco

San Francisco, California, 94143, United States

Location

MeSH Terms

Conditions

Leukemia, Myeloid, AcuteAnemia, Refractory, with Excess of BlastsPrecursor Cell Lymphoblastic Leukemia-LymphomaLeukemia, Myelogenous, Chronic, BCR-ABL PositiveMultiple MyelomaLymphoma, Large B-Cell, DiffuseLymphoma, Mantle-CellLymphoma, T-Cell, PeripheralLymphoma, Extranodal NK-T-CellHodgkin DiseaseHematologic NeoplasmsDendritic Cell Sarcoma, Interdigitating

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesAnemia, RefractoryAnemiaMyelodysplastic SyndromesBone Marrow DiseasesLeukemia, LymphoidLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesMyeloproliferative DisordersChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and SymptomsNeoplasms, Plasma CellHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHemorrhagic DisordersLymphoma, B-CellLymphoma, Non-HodgkinLymphomaLymphoma, T-CellNeoplasms by SiteHistiocytic Disorders, MalignantHistiocytosis

Study Officials

  • Thomas G. Martin, M.D.

    University of California, San Francisco

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
not applicable
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 8, 2007

First Posted

August 10, 2007

Study Start

October 1, 2002

Primary Completion

March 1, 2009

Study Completion

March 1, 2009

Last Updated

August 14, 2013

Record last verified: 2013-08

Locations