NCT00401843

Brief Summary

The purpose of Part 1 of the study is to determine the safety of the combination of Siltuximab (CNTO 328) and bortezomib (Velcade). The purpose of Part 2 of the study is to compare the length of progression free survival for those patients given CNTO 328 and bortezomib to those patients given bortezomib alone.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
307

participants targeted

Target at P75+ for phase_2 multiple-myeloma

Timeline
Completed

Started Nov 2006

Longer than P75 for phase_2 multiple-myeloma

Geographic Reach
18 countries

80 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 17, 2006

Completed
5 days until next milestone

First Posted

Study publicly available on registry

November 22, 2006

Completed
6 days until next milestone

Study Start

First participant enrolled

November 28, 2006

Completed
4.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 16, 2011

Completed
4 years until next milestone

Results Posted

Study results publicly available

August 4, 2015

Completed
4.1 years until next milestone

Study Completion

Last participant's last visit for all outcomes

September 24, 2019

Completed
Last Updated

November 19, 2019

Status Verified

November 1, 2019

Enrollment Period

4.7 years

First QC Date

November 17, 2006

Results QC Date

July 7, 2015

Last Update Submit

November 7, 2019

Conditions

Keywords

multiple myelomaMonoclonal AntibodyIntravenousrefractory or relapsed multiple myelomavelcadebortezomib

Outcome Measures

Primary Outcomes (2)

  • Progression-free Survival

    Progression-free survival was defined as the time interval between randomization and the first documented sign of disease progression (including relapse from complete response \[CR\]) by the European Bone Marrow Transplant (EBMT) criteria or death, whichever occurred first. Relapse from CR requires at least 1 of the following: Reappearance of serum or urinary M-protein on immunofixation or routine electrophoresis, confirmed by at least 1 further investigation and excluding oligoclonal immune reconstitution; Greater than or equal to (\>=) 5 percent (%) plasma cells either in a bone marrow aspirate or on trephine bone biopsy; Development of new lytic bone lesions or soft tissue plasmacytomas or definite increase in the size of residual bone lesions (development of a compression fracture does not exclude continued response and may not indicate progression); Development of hypercalcemia not attributable to any other cause.

    Randomization until disease progression or death, which ever occured first (maximum up to 5 years)

  • Number of Participants With Adverse Events (AEs) or Serious Adverse Events (SAEs)

    An AE is any untoward medical occurrence in a participant who received study drug without regard to possibility of causal relationship. An SAE is an AE resulting in any of the following outcomes or deemed significant for any other reason: death; initial or prolonged inpatient hospitalization; lifethreatening experience (immediate risk of dying); persistent or significant disability/incapacity; congenital anomaly.

    up to 5 years

Secondary Outcomes (3)

  • Percentage of Participants With Best Confirmed Response of Complete Response (CR) or Partial Response (PR) (Overall Response Rate)

    Randomization until disease progression (maximum up to 5 years)

  • Percentage of Participants With Confirmed Complete Response (CR Rate)

    Randomization until disease progression (maximum up to 5 years)

  • Overall Survival

    up to 5 years

Study Arms (3)

Part 1: Siltuximab Plus Bortezomib

EXPERIMENTAL

Siltuximab 6 milligram per kilogram (mg/kg) will be administered as intravenous infusion once every 2 weeks along with bortezomib 1.3 milligram per square meter (mg/m\^2) during cycle 1.

Biological: SiltuximabDrug: Bortezomib

Part 2: Bortezomib + Placebo

EXPERIMENTAL

Bortezomib 1.3 mg/m\^2 will be administered as intravenous bolus on Days 1, 4, 8, 11, followed by a 10-day rest period; and on Days 22, 25, 29, and 32 followed by a 10-day rest period along with matching placebo administered as intravenous infusion once every 2 weeks during 42-day treatment phase. Bortezomib 1.3 mg/m\^2 will be administered as intravenous bolus on Days 1, 8, 15, 22 followed by a 13-day rest period (cycle Days 23 to 35) along with matching placebo once every 2 weeks during 35-day Maintenance Phase. Dexamethasone tablet will be administered at first occurrence of documented disease progression or if bortezomib was discontinued due to intolerable toxicity. Dexamethasone 40 milligram per day (mg/day) will be administered on days 1-4, 9-12, and 17-20 for four 28-day cycles then 40 mg/day for Days 1-4 for all subsequent cycles.

Drug: BortezomibDrug: PlaceboDrug: Dexamethasone

Part 2: Bortezomib + Siltuximab

EXPERIMENTAL

Bortezomib 1.3 mg/m\^2 will be administered as intravenous bolus on Days 1, 4, 8, 11, followed by a 10-day rest period; and on Days 22, 25, 29, and 32 followed by a 10-day rest period along with Siltuximab administered as intravenous infusion once every 2 weeks during 42-day treatment phase. Bortezomib 1.3 mg/m\^2 will be administered as intravenous bolus on Days 1, 8, 15, 22 followed by a 13-day rest period (cycle Days 23 to 35) along with Siltuximab administered as intravenous infusion once every 2 weeks for 35-day Maintenance Phase. Dexamethasone tablet will be administered at first occurrence of documented disease progression or if bortezomib was discontinued due to intolerable toxicity. Dexamethasone 40 mg/day will be administered on days 1-4, 9-12, and 17-20 for four 28-day cycles then 40 mg/day for Days 1-4 for all subsequent cycles.

Biological: SiltuximabDrug: BortezomibDrug: Dexamethasone

Interventions

SiltuximabBIOLOGICAL

Siltuximab 6 mg/kg will be administered as intravenous infusion once every 2 weeks during cycle 1 in Part 1. Siltuximab 6 mg/kg will be administered as intravenous infusion once every 2 weeks during 42-day Treatment Phase and 35-day Maintenance Phase in Part 2.

Also known as: CNTO 328
Part 1: Siltuximab Plus BortezomibPart 2: Bortezomib + Siltuximab

Bortezomib 1.3 mg/m\^2 will be administered as intravenous bolus once every 2 weeks during cycle 1 in Part 1. Bortezomib 1.3 mg/m\^2 will be administered as intravenous bolus on Days 1, 4, 8, 11, followed by a 10-day rest period; and on Days 22, 25, 29, and 32 followed by a 10-day rest period during 42-day treatment phase in Part 2. Bortezomib 1.3 mg/m2 will be administered as intravenous bolus on Days 1, 8, 15, 22 followed by a 13-day rest period (cycle Days 23 to 35) during 35-day Maintenance Phase in Part 2.

Also known as: VELCADE
Part 1: Siltuximab Plus BortezomibPart 2: Bortezomib + PlaceboPart 2: Bortezomib + Siltuximab

Matching placebo will be administered as intravenous infusion once every 2 weeks during 42-day treatment phase and 35-day maintenance phase in Part 2.

Part 2: Bortezomib + Placebo

Dexamethasone tablet will be administered in this study at the first occurrence of documented disease progression or if bortezomib was discontinued due to intolerable toxicity. Dexamethasone 40 mg/day will be administered on days 1-4, 9-12, and 17-20 for four 28-day cycles then 40 mg/day for Days 1-4 for all subsequent cycles in treatment phase and maintenance phase of Part 2.

Part 2: Bortezomib + PlaceboPart 2: Bortezomib + Siltuximab

Eligibility Criteria

Age18 Years - 99 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Measurable secretory disease defined as either serum monoclonal paraprotein, (M-protein) greater than or equal to (\>=)1 gram per deciliter (g/dL) or urine monoclonal (light chain) protein (\> 200 mg/24 hours)
  • Documented disease progression after at least 1 prior line of therapy but no more than 3 or have had no response to previous treatment (primary refractory disease)
  • ECOG performance status score of less than or equal to (\<=) 2
  • Adequate bone marrow, liver, and renal function

You may not qualify if:

  • No prior treatment with bortezomib
  • Not Refractory to high-dose dexamethasone
  • Not \>= Grade 2 peripheral neuropathy
  • Have not received an allogeneic bone marrow or allogeneic peripheral blood stem cell transplant
  • No prior or concomitant malignancy (other than multiple myeloma) except adequately treated basal cell or squamous cell carcinoma of the skin, carcinoma in situ of the cervix, or other cancer for which the patient has been disease-free for \<= 3 years

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (80)

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Greenbrae, California, United States

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Los Angeles, California, United States

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Indianapolis, Indiana, United States

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Albuquerque, New Mexico, United States

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New York, New York, United States

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Syracuse, New York, United States

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Chapel Hill, North Carolina, United States

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North Charleston, South Carolina, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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Madison, Wisconsin, United States

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Antwerp, Belgium

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B-8000 Brugge, Belgium

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Brussels, Belgium

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Edegem, Belgium

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Leuven, Belgium

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Rio de Janeiro, Brazil

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Bulgaria, Bulgaria

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Pleven, Bulgaria

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Plovdiv, Bulgaria

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Vancouver, British Columbia, Canada

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Québec, Quebec, Canada

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Calgary, Canada

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Brno, Czechia

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Hradec Králové, Czechia

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Prague, Czechia

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Grenoble, France

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Lille Cedex N/a, France

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Montpellier, France

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Pierre-Bénite, France

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Vandœuvre-lès-Nancy, France

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Aschaffenburg, Germany

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Essen, Germany

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Mainz, Germany

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Münster, Germany

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Stuttgart, Germany

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Ulm, Germany

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Athens, Greece

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Budapest, Hungary

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Debrecen, Hungary

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Gyõr, Hungary

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Nyíregyháza, Hungary

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Szeged, Hungary

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Amersfoort, Netherlands

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Amsterdam, Netherlands

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Rotterdam, Netherlands

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The Hague, Netherlands

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Bialystok, Poland

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Gdansk, Poland

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Katowice, Poland

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Lodz, Poland

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Lublin, Poland

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Poznan, Poland

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Wroclaw, Poland

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Coimbra, Portugal

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Lisbon, Portugal

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Porto, Portugal

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Baia Mare, Romania

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Brasov, Romania

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Bucharest, Romania

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Iași, Romania

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Tg Mures, Romania

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Arkhangelsk, Russia

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Izhevsk, Russia

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Moscow, Russia

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Nizhny Novgorod, Russia

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Novosibirsk, Russia

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Saint Petersburg, Russia

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Ufa, Russia

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Bratislava, Slovakia

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Martin, Slovakia

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Badalona, Spain

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Barcelona, Spain

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Madrid, Spain

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Salamanca, Spain

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Valencia, Spain

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London, United Kingdom

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Nottingham, United Kingdom

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Plymouth, United Kingdom

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Sutton, United Kingdom

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Related Publications (1)

  • Orlowski RZ, Gercheva L, Williams C, Sutherland H, Robak T, Masszi T, Goranova-Marinova V, Dimopoulos MA, Cavenagh JD, Spicka I, Maiolino A, Suvorov A, Blade J, Samoylova O, Puchalski TA, Reddy M, Bandekar R, van de Velde H, Xie H, Rossi JF. A phase 2, randomized, double-blind, placebo-controlled study of siltuximab (anti-IL-6 mAb) and bortezomib versus bortezomib alone in patients with relapsed or refractory multiple myeloma. Am J Hematol. 2015 Jan;90(1):42-9. doi: 10.1002/ajh.23868.

MeSH Terms

Conditions

Multiple Myeloma

Interventions

siltuximabBortezomibDexamethasone

Condition Hierarchy (Ancestors)

Neoplasms, Plasma CellNeoplasms by Histologic TypeNeoplasmsHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHematologic DiseasesHemic and Lymphatic DiseasesHemorrhagic DisordersLymphoproliferative DisordersImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

Boronic AcidsAcids, NoncarboxylicAcidsInorganic ChemicalsBoron CompoundsOrganic ChemicalsPyrazinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsPregnadienetriolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic CompoundsSteroids, Fluorinated

Results Point of Contact

Title
Project Physician
Organization
Janssen R&D UK

Study Officials

  • Janssen Research & Development, LLC Clinical Trial

    Janssen Research & Development, LLC

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, CARE PROVIDER
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 17, 2006

First Posted

November 22, 2006

Study Start

November 28, 2006

Primary Completion

August 16, 2011

Study Completion

September 24, 2019

Last Updated

November 19, 2019

Results First Posted

August 4, 2015

Record last verified: 2019-11

Locations