NCT00393029

Brief Summary

Background: The p53 gene normally suppresses tumor growth, but when it is mutated, or damaged, tumors can grow unchecked. In cancers where the p53 gene has mutated, an increased level of p53(overexpression of p53) can be measured in the tumor. Objectives To determine whether advanced cancers that overexpress p53 can be treated effectively with lymphocytes (white blood cells) that have been genetically engineered to contain an anti-p53 protein. Eligibility Patients 18 years of age and older with metastatic cancer (cancer that has spread beyond the original site) Patient's tumor overexpresses p53 Patient's leukocyte antigen type is HLA-A 0201 Design Patients undergo the following procedures: Leukapheresis (on two occasions). This is a method of collecting large numbers of white blood cells. The cells obtained in the first leukapheresis procedure are grown in the laboratory, and the anti-p53 protein is inserted into the cells using an inactivated (harmless)virus in a process called transduction. Cells collected in the second leukapheresis procedure are used to evaluate the effectiveness of the study treatment. Chemotherapy. Patients are given chemotherapy through a vein (intravenously, IV) for 1 week to suppress the immune system so that the patients immune cells do not interfere with the treatment. Treatment with anti-p53 cells. Patients receive an IV infusion of the transduced cells containing anti-p53 protein, followed by infusions of a drug called IL-2, which helps boost the effectiveness of the transduced white cells. Patients may undergo a tumor biopsy (removal of a small piece of tumor tissue). Patients are evaluated with laboratory tests and imaging tests, such as computed tomography (CT) scans 4 to 6 weeks after treatment and then once a month 3 to 4 months to determine the response to treatment. Patients have blood tests at 1, 3, 6 and 12 months and then annually for the next 10 years.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
12

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Oct 2006

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 1, 2006

Completed
24 days until next milestone

First Submitted

Initial submission to the registry

October 25, 2006

Completed
1 day until next milestone

First Posted

Study publicly available on registry

October 26, 2006

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2008

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2008

Completed
2.8 years until next milestone

Results Posted

Study results publicly available

August 5, 2011

Completed
Last Updated

August 15, 2011

Status Verified

August 1, 2011

Enrollment Period

2.1 years

First QC Date

October 25, 2006

Results QC Date

June 1, 2011

Last Update Submit

August 10, 2011

Conditions

Keywords

Tumor RegressionIn Vivo Cell SurvivalToxicity ProfileMetastatic Renal Cell CancerCancerMetastatic Cancer

Outcome Measures

Primary Outcomes (2)

  • Clinical Tumor Regression

    Response Evaluation Criteria In Solid Tumors (RECIST). See the protocol Link module for full criteria if desired.

    1-11 months

  • The Number of Participants With Adverse Events

    Here are the total number of participants with adverse events. Adverse events were described using the Common Terminology Criteria for Adverse Events (CTCAE) version 3. For the detailed list of adverse events see the adverse event module.

    events related to all components of the treatment regimen were reported from the start of the non-myeloablative conditioning regiment through 30 days following treatment or resolution.

Secondary Outcomes (1)

  • In Vivo Survival of T-cell Receptor (TCR) Gene-engineered Cells in Participants

    3-12 months

Study Arms (2)

Patients with metastatic melanoma

EXPERIMENTAL

Melanoma is a serious form of skin cancer that develops in the skin cells that make our skin color (melanocytes).

Biological: anti-protein 53 or tumor protein 53 (p53) T-cell receptor transduced peripheral blood lymphocytesBiological: aldesleukinBiological: filgrastimDrug: cyclophosphamideDrug: fludarabine phosphate

Patients with other metastatic cancers

EXPERIMENTAL
Biological: anti-protein 53 or tumor protein 53 (p53) T-cell receptor transduced peripheral blood lymphocytesBiological: aldesleukinBiological: filgrastimDrug: cyclophosphamideDrug: fludarabine phosphate

Interventions

Peripheral blood lymphocytes are harvested by lymphapheresis and engineered to express a T cell receptor that binds to P53.

Also known as: Tumor protein 53, Anti-protein 53
Patients with metastatic melanomaPatients with other metastatic cancers
aldesleukinBIOLOGICAL

720,000 IU/kg intravenously over 15 minutes every 8 hours for up to 5 days

Also known as: Interleukin-2 (IL-2), Proleukin, Recombinant human interleukin-2
Patients with metastatic melanomaPatients with other metastatic cancers
filgrastimBIOLOGICAL

Beginning on day 1 or 2, administered subcutaneously at a dose of 5 mcg/kg/day (not to exceed 300 mcg/day); continue daily until neutrophil count \> 1.0 x 10\^9/L x 3 days or \> 5.0 x 10\^9/L.

Also known as: Granulocyte colony stimulating factor (GCSF), Neupogen
Patients with metastatic melanomaPatients with other metastatic cancers

60 mg/kg/day x 2 days intravenously in 250ml dextrose 5% in water (D5W) with mesna 15 mg/kg/day x 2 days over 1 hour.

Also known as: Cytoxan, Endoxan, Neosar, Procytox, Revimmune
Patients with metastatic melanomaPatients with other metastatic cancers

25 mg/m2/day intravenously piggyback (IVPB) daily over 30 minutes for 5 days.

Also known as: Fludara
Patients with metastatic melanomaPatients with other metastatic cancers

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients must have metastatic cancer that overexpresses p53 as assessed by immunohistochemistry, as determined by positive staining of tumor sample. when compared to negative controls per procedure in Appendix 1. The immunohistochemical staining will be performed in the Pathology Laboratory Center for Cancer Research (CCR), National Cancer Institute (NCI) on fresh or archival tissue and will be supervised by Dr. Maria Merino. The criteria used to determine overexpression will be that used in the Laboratory of Dr. Curt Harris. Ten fields will be evaluated at 40 X magnification and if greater than 5% of cells stain positive, the tumor will be categorized as an overexpressor.
  • Patients with melanoma or renal cell cancer must have previously received interleukin-2 (IL-2) and have been either non-responders (progressive disease) or have recurred. Patients with other histologies,not including hematologic malignancies, must have previously received first line and second line or higher systemic standard care(or effective salvage chemotherapy regimens) for metastatic disease,if known to be effective for that disease and have been either non-responders (progressive disease) or have recurred.
  • Age greater than or equal to 18 years.
  • Clinical performance status of Eastern Cooperative Oncology Group (ECOG) 0 to 1.
  • Life expectancy of greater than three months.
  • Seronegative for human immunodeficiency virus (HIV) antibody. (The experimental treatment being evaluated in this protocol depends on an intact immune system. Patients who are HIV seropositive can have decreased immune competence and thus be less responsive to the experimental and more susceptible to its toxicities).
  • Seronegative for hepatitis B antigen and hepatitis C antibody unless antigen negative.
  • Patients must be human leukocyte antigen A(HLA-A) 0201 positive.
  • Patients of both genders must be willing to practice birth control for four months after receiving the preparative regimen.
  • Absolute neutrophil count greater than 1000/mm\^3, and normal white blood cells (WBC) (greater than 3000/mm\^3).
  • Platelet count greater than 100,000/mm\^3.
  • Hemoglobin greater than 8.0 g/dl.
  • Serum alanine aminotransferase (ALT)/aspartate aminotransferase (AST) less than the upper limit of normal.
  • Serum creatinine less than or equal to 1.6 mg/dl.
  • Total bilirubin less than or equal to 1.5 mg/dl, except in patients with Gilbert's Syndrome who must have a total bilirubin less than 3.0 mg/dl.
  • +3 more criteria

You may not qualify if:

  • Patients requiring systemic steroid therapy
  • Patients with active systemic infections, coagulation disorders or other major medical illnesses of the cardiovascular, respiratory or immune system, myocardial infarction, cardiac arrhythmias, obstructive or restrictive pulmonary disease.
  • Patients with any form of primary immunodeficiency (such as Severe Combined Immunodeficiency Disease and acquired immune deficiency syndrome (AIDS)). Patients with opportunistic infections will be excluded. (The experimental treatment being evaluated in this protocol depends on an intact immune system. Patients who have decreased immune competence may be less responsive to the experimental treatment and more susceptible to its toxicities).
  • Patients with history of severe immediate hypersensitivity reaction to any of the agents used in this study.
  • Patient is not willing to sign a durable power of attorney.
  • Patient is not able to understand and sign the Informed Consent Document.
  • Since aldesleukin will be excluded if they have a history of electrocardio- gram (EKG) abnormalities, symptoms of cardiac ischemia or arrhythmias and have a left ventricular ejection fraction (LVEF) less than 45% on a cardiac stress test (stress thallium, stress multi-gated acquisition scan (MUGA), dobutamine echocardiogram, or other stress test).
  • Similarly, patients who are greater than or equal to 50 years old with a LVEF less than 45% will be excluded.
  • Patients with a prolonged history of cigarette smoking (greater than 20 pack/year within the past 2 years) or symptoms of respiratory dysfunction (e.g. grade 2 dyspnea or hypoxia) who do not have a normal pulmonary function test as evidenced by a FEV(1) less than 60% predicted will be excluded.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

National Institutes of Health

Bethesda, Maryland, 20892, United States

Location

Related Publications (3)

  • Kawakami Y, Eliyahu S, Delgado CH, Robbins PF, Rivoltini L, Topalian SL, Miki T, Rosenberg SA. Cloning of the gene coding for a shared human melanoma antigen recognized by autologous T cells infiltrating into tumor. Proc Natl Acad Sci U S A. 1994 Apr 26;91(9):3515-9. doi: 10.1073/pnas.91.9.3515.

    PMID: 8170938BACKGROUND
  • Kawakami Y, Eliyahu S, Sakaguchi K, Robbins PF, Rivoltini L, Yannelli JR, Appella E, Rosenberg SA. Identification of the immunodominant peptides of the MART-1 human melanoma antigen recognized by the majority of HLA-A2-restricted tumor infiltrating lymphocytes. J Exp Med. 1994 Jul 1;180(1):347-52. doi: 10.1084/jem.180.1.347.

    PMID: 7516411BACKGROUND
  • Kawakami Y, Eliyahu S, Delgado CH, Robbins PF, Sakaguchi K, Appella E, Yannelli JR, Adema GJ, Miki T, Rosenberg SA. Identification of a human melanoma antigen recognized by tumor-infiltrating lymphocytes associated with in vivo tumor rejection. Proc Natl Acad Sci U S A. 1994 Jul 5;91(14):6458-62. doi: 10.1073/pnas.91.14.6458.

    PMID: 8022805BACKGROUND

Related Links

MeSH Terms

Conditions

Carcinoma, Renal CellNeoplasmsNeoplasm Metastasis

Interventions

Genes, p53tumor protein 53-induced nuclear protein 1, mousealdesleukinInterleukin-2FilgrastimGranulocyte Colony-Stimulating FactorCyclophosphamidefludarabine phosphate

Condition Hierarchy (Ancestors)

AdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeKidney NeoplasmsUrologic NeoplasmsUrogenital NeoplasmsNeoplasms by SiteFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesKidney DiseasesUrologic DiseasesMale Urogenital DiseasesNeoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

Genes, Tumor SuppressorGenes, NeoplasmGenesGenome ComponentsGenomeGenetic StructuresGenetic PhenomenaGenes, RecessiveInterleukinsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsLymphokinesProteinsBiological FactorsColony-Stimulating FactorsGlycoproteinsGlycoconjugatesCarbohydratesHematopoietic Cell Growth FactorsPhosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhosphoramidesOrganophosphorus Compounds

Results Point of Contact

Title
Steven Rosenberg, M.D., Ph.D.
Organization
National Cancer Institute (NCI), National Institutes of Health (NIH)

Study Officials

  • Steven A Rosenberg, M.D., Ph.D

    NCI, NIH

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
NIH

Study Record Dates

First Submitted

October 25, 2006

First Posted

October 26, 2006

Study Start

October 1, 2006

Primary Completion

November 1, 2008

Study Completion

November 1, 2008

Last Updated

August 15, 2011

Results First Posted

August 5, 2011

Record last verified: 2011-08

Locations