NCT00131989

Brief Summary

This phase I trial is studying the side effects and best dose of sorafenib in treating patients with relapsed or refractory acute myeloid leukemia, acute lymphoblastic leukemia, or chronic myelogenous leukemia. Sorafenib may stop the growth of cancer cells by blocking some of the enzymes needed for cell growth and by blocking blood flow to the cancer

Trial Health

80
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
48

participants targeted

Target at P50-P75 for phase_1

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2005

Completed
3 months until next milestone

First Submitted

Initial submission to the registry

August 16, 2005

Completed
3 days until next milestone

First Posted

Study publicly available on registry

August 19, 2005

Completed
1.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2007

Completed
Last Updated

January 9, 2013

Status Verified

January 1, 2013

Enrollment Period

1.8 years

First QC Date

August 16, 2005

Last Update Submit

January 8, 2013

Conditions

Outcome Measures

Primary Outcomes (2)

  • DLT defined as non-hematologic > grade 3 or hematologic grade 4 marrow aplasia > 28 days (without leukemia clearance) as assessed by NCI-CTC version 3.0

    Observed toxicities will be reported and summarized s with frequencies, type and grade in a descriptive manner. No formal statistical inference will be made on this dose-finding study.

    28 days

  • MDT based on the incidence of DTL as assessed by NCI-CTC version 3.0

    Observed toxicities will be reported and summarized s with frequencies, type and grade in a descriptive manner. No formal statistical inference will be made on this dose-finding study.

    28 days

Secondary Outcomes (4)

  • Response (CR and/or PR)

    Up to 1 year

  • Pharmacokinetic parameters

    At baseline, at 0.25, 0.5, 1, 2, 4, 6, 8, 24, and 48 hours (days 1, 2, and 3) at days 8, 15, and 29

  • Sorafenib tosylate related adverse events as assessed by NCI-CTC version 3.0

    Up to 1 year after completion of treatment

  • Impact of sorafenib tosylate on the Raf kinase/MEK/ERK signaling pathway

    At baseline and at 28 days (course 1)

Study Arms (1)

Treatment (sorafenib tosylate)

EXPERIMENTAL

Patients receive oral sorafenib twice daily on days 1-14 or 1-21. Treatment repeats every 28 days for up to 6 courses in the absence of disease progression or unacceptable toxicity. Patients achieving a CR may be considered for retreatment with sorafenib for up to an additional 6 courses upon disease recurrence provided the duration of CR is longer than 1 month.

Drug: sorafenib tosylateOther: pharmacological studyOther: laboratory biomarker analysis

Interventions

Given orally

Also known as: BAY 43-9006, BAY 43-9006 Tosylate Salt, BAY 54-9085, Nexavar, SFN
Treatment (sorafenib tosylate)

Correlative studies

Also known as: pharmacological studies
Treatment (sorafenib tosylate)

Correlative studies

Treatment (sorafenib tosylate)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients must have pathological confirmation (histologically or cytologically) of relapsed or refractory acute myeloid leukemia (other than acute promyelocytic leukemia), acute lymphocytic leukemia, or chronic myeloid leukemia in blast crisis
  • The morphologic diagnosis of AML (non-APL), ALL, and CML in blast crisis will be made independently by members of the hematologic pathology division; routine staining and standard criteria as outlined by the Report of the NCI-Sponsored Workshop will be followed
  • All patients must have been refractory to or relapsed from their most recent therapy AND are considered ineligible for potential curative approaches including allogeneic stem cell transplant; in addition, patients must be at least:
  • weeks from last cytotoxic chemotherapy (excluding hydroxyurea)
  • Hydroxyurea may be used for blast count control but must be discontinued within 48 hours of the initiation of BAY 43-9006
  • weeks from last radiation therapy
  • week from last biologic therapy (including myeloid growth factors)
  • ECOG performance status =\< 2 (Karnofsky \>= 60%)
  • Life expectancy of greater than 2 months
  • Multilineage bone marrow failure due to the subject's underlying leukemia
  • Total blast count in the peripheral blood \< 30,000
  • Total bilirubin =\< 2 mg/dl
  • AST(SGOT)/ALT(SGPT) =\< 5 X institutional upper limit of normal
  • Serum creatinine within normal institutional limits OR creatinine clearance \>= 60 mL/min/1.73 m\^2 for patients with creatinine levels above institutional normal
  • All women of child-bearing potential and men must agree to use adequate contraception (hormonal or barrier method of birth control; abstinence) prior to study entry and for the duration of study participation; the effects of BAY 43-9006 on the developing human fetus at the recommended therapeutic dose are unknown; however, kinase inhibitors are known to be teratogenic; should a woman become pregnant or suspect she is pregnant while participating in this study, she should inform her treating physician immediately
  • +1 more criteria

You may not qualify if:

  • Patients with APL are not eligible for this clinical trial
  • Patients who have not recovered from adverse events due to agents administered more than 3 weeks earlier
  • Patients with rapidly increasing peripheral blood blast counts (increase in the absolute peripheral blast count \> 50% within one week) or uncontrolled (absolute blast count \> 30,000) while on hydroxyurea will be excluded
  • Patients with uncontrolled hypertension (i.e., persistent grade 3 while undergoing treatment)
  • Patients may not be actively receiving any other investigational agents
  • Patients active and / or untreated CNS leukemia will not be eligible
  • History of allergic reactions attributed to compounds of similar chemical or biologic composition to BAY 43-9006
  • Pregnant women are excluded from this study; breastfeeding should be discontinued if the mother is treated with BAY 43-9006
  • Patients with immune deficiency are at increased risk of lethal infections when treated with marrow suppressive therapy; therefore, HIV-positive patients receiving combination anti-retroviral therapy are excluded from the study because of possible pharmacokinetic interactions with BAY 43-9006; appropriate studies will be undertaken in patients receiving combination anti-retroviral therapy when indicated
  • Uncontrolled intercurrent illness including, but not limited to, ongoing or active infection, symptomatic congestive heart failure, unstable angina pectoris, cardiac arrhythmia, or psychiatric illness/social situations that would limit compliance with study requirements
  • Patients must not have any evidence of bleeding diathesis
  • Patients must not be on therapeutic anticoagulation; prophylactic anticoagulation (i.e. low dose warfarin) of venous or arterial access devices is allowed provided that the requirements for PT, INR or PTT are met
  • Patients must not be taking the cytochrome P450 enzyme-inducing antiepileptic drugs (phenytoin, carbamazepine, or phenobarbital), rifampin or St. John's wort

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Johns Hopkins University

Baltimore, Maryland, 21287-8936, United States

Location

MeSH Terms

Conditions

Leukemia, Basophilic, AcuteLeukemia, Eosinophilic, AcuteLeukemia, Megakaryoblastic, AcuteLeukemia, Monocytic, AcuteLeukemia, Myeloid, AcuteCongenital AbnormalitiesLeukemia, Myelomonocytic, AcuteLeukemia, Erythroblastic, AcutePrecursor Cell Lymphoblastic Leukemia-Lymphoma

Interventions

Sorafenib

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesMyeloproliferative DisordersBone Marrow DiseasesLeukemia, LymphoidLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

Phenylurea CompoundsUreaAmidesOrganic ChemicalsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsNiacinamideNicotinic AcidsAcids, HeterocyclicHeterocyclic CompoundsPyridinesHeterocyclic Compounds, 1-Ring

Study Officials

  • B. Smith

    Johns Hopkins University

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
NIH
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 16, 2005

First Posted

August 19, 2005

Study Start

June 1, 2005

Primary Completion

April 1, 2007

Last Updated

January 9, 2013

Record last verified: 2013-01

Locations