NCT00131118

Brief Summary

This is an extension study to examine the long-term safety and efficacy of zoledronic acid in patients who have completed the core CZOL446H2202 study.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
127

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jul 2004

Typical duration for phase_2

Geographic Reach
1 country

10 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2004

Completed
1.1 years until next milestone

First Submitted

Initial submission to the registry

August 15, 2005

Completed
2 days until next milestone

First Posted

Study publicly available on registry

August 17, 2005

Completed
1.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2007

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2007

Completed
Last Updated

June 1, 2017

Status Verified

November 1, 2016

Enrollment Period

2.8 years

First QC Date

August 15, 2005

Last Update Submit

May 31, 2017

Conditions

Keywords

Osteogenesis Imperfecta, Brittle bone disease, bisphosphonate, children

Outcome Measures

Primary Outcomes (1)

  • Long-term safety of two different zoledronic acid doses over an additional 12 months in patients who have completed one year treatment in CZOL446H2202

Secondary Outcomes (1)

  • Measure percentage change of lumbar spine bone mineral density at month 18 and 24 compared to baseline in the core study.

Interventions

Eligibility Criteria

Age1 Year - 17 Years
Sexall
Age GroupsChild (0-17)

You may qualify if:

  • Have completed the core CZOL446H2202 study
  • Males or females between 1-17 years of age

You may not qualify if:

  • Deformity or abnormality which would prevent spine bone density from being done
  • Any surgical bone-lengthening procedure
  • Any kidney diseases or abnormalities
  • Low calcium or vitamin D levels in the blood

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (10)

UCLA Medical Center-Dept of Pediatric Nephrology

Los Angeles, California, 90095, United States

Location

Alfred Dupont Hospital for Children

Wilmington, Delaware, 19899, United States

Location

Intermountains Orthopedics

Boise, Idaho, 83702, United States

Location

Children's Hospital

Omaha, Nebraska, 68198, United States

Location

For information regarding facilities, please contact the Central Contact

Multiple Locations, New Jersey, United States

Location

Children's Hospital Medical Center

Cincinnati, Ohio, 45229, United States

Location

Children's Hospital

Columbus, Ohio, 43205, United States

Location

Oregon Health Sciences University

Portland, Oregon, 97239, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232, United States

Location

Texas Children's Hospital

Houston, Texas, 77030, United States

Location

Related Links

MeSH Terms

Conditions

Osteogenesis Imperfecta

Interventions

Zoledronic Acid

Condition Hierarchy (Ancestors)

OsteochondrodysplasiasBone Diseases, DevelopmentalBone DiseasesMusculoskeletal DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesCollagen DiseasesConnective Tissue DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

DiphosphonatesOrganophosphonatesOrganophosphorus CompoundsOrganic ChemicalsImidazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 15, 2005

First Posted

August 17, 2005

Study Start

July 1, 2004

Primary Completion

May 1, 2007

Study Completion

May 1, 2007

Last Updated

June 1, 2017

Record last verified: 2016-11

Locations