NCT01679080

Brief Summary

Osteogenesis imperfecta (OI) is an inherited disease of the connective tissue. Symptoms are fractures, growth retardation, blue sclera, bad teeth, impaired hearing a.o. The aim of the present study is to investigate the effect of treatment of adult OI patients with bisphosphonate (zoledronic acid), parathyroid hormone (PTH) or placebo on bone mass, fracture risk and quality of life. The investigators will therefore conduct a double blind, placebo controlled trial, taking genotype and previous antiresorptive therapy into account.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
9

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Nov 2012

Longer than P75 for phase_2

Geographic Reach
1 country

3 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 16, 2012

Completed
20 days until next milestone

First Posted

Study publicly available on registry

September 5, 2012

Completed
2 months until next milestone

Study Start

First participant enrolled

November 1, 2012

Completed
7.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2020

Completed
11 months until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2021

Completed
Last Updated

June 25, 2021

Status Verified

June 1, 2021

Enrollment Period

7.7 years

First QC Date

August 16, 2012

Last Update Submit

June 22, 2021

Conditions

Keywords

Drug therapyAdult

Outcome Measures

Primary Outcomes (1)

  • Bone Mineral Density (BMD)

    Dual-energy X-ray absorptiometry scans are performed at the lumbar spine, hip and whole body twice yearly. The value of the lumbar BMD is the primary outcome.

    Three years

Secondary Outcomes (1)

  • Fracture risk

    Three years

Study Arms (3)

Zolendronic acid, 3 yr + placebo teriparatide, 2 yr

EXPERIMENTAL

yearly intravenous infusion of 5mg active zoledronic acid in 3 yr

Drug: Zoledronic acid

teriparatide 2 yr; active zol in 3rd yr

EXPERIMENTAL

daily injection of one dose active teriparatide for two years, active zoledronic acid in year 3.

Drug: Zoledronic acidDrug: Teriparatide

No active treatment

PLACEBO COMPARATOR

Observation in three years, no treatment

Other: No active treatment

Interventions

antiresorptive and calcium and vitamin D

Also known as: zolendronate, Aclasta
Zolendronic acid, 3 yr + placebo teriparatide, 2 yrteriparatide 2 yr; active zol in 3rd yr

anabolic and calcium and vitamin D

Also known as: PTH, Forsteo
teriparatide 2 yr; active zol in 3rd yr

Calcium and vitamin D

No active treatment

Eligibility Criteria

Age22 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • clinical diagnosis of osteogenesis imperfecta
  • BMD\<-1.0 or

You may not qualify if:

  • creatinine clearance \<30mL/min
  • treatment with glucocorticoids \> 5mg daily during the last 3 months
  • metabolic bone disease or vitamin d deficiency
  • liver or kidney disease
  • contradictions to zoledronic acid or teriparatide
  • increased baseline risk of osteosarcoma

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (3)

Osteoporosis clinic; department of endocrinology and metabolism

Aarhus, Aarhus C, 8000, Denmark

Location

Department of endocrinology

Hvidovre, 2650, Denmark

Location

Department of Endocrinology M

Odense, 6000, Denmark

Location

MeSH Terms

Conditions

Osteogenesis Imperfecta

Interventions

Zoledronic AcidTeriparatide

Condition Hierarchy (Ancestors)

OsteochondrodysplasiasBone Diseases, DevelopmentalBone DiseasesMusculoskeletal DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesCollagen DiseasesConnective Tissue DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

DiphosphonatesOrganophosphonatesOrganophosphorus CompoundsOrganic ChemicalsImidazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsParathyroid HormonePeptide HormonesHormonesHormones, Hormone Substitutes, and Hormone AntagonistsPeptidesAmino Acids, Peptides, and Proteins

Study Officials

  • Bente Langdahl, MD

    Aarhus University Hospital

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 16, 2012

First Posted

September 5, 2012

Study Start

November 1, 2012

Primary Completion

July 1, 2020

Study Completion

June 1, 2021

Last Updated

June 25, 2021

Record last verified: 2021-06

Locations